Study of BLU-808 in Chronic Inducible Urticaria (CIndU) and Chronic Spontaneous Urticaria (CSU)

NCT ID: NCT06931405

Last Updated: 2025-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

105 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-05-28

Study Completion Date

2026-12-31

Brief Summary

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This is a 2-part, proof-of-concept study to be conducted globally, designed to evaluate the safety, tolerability, clinical activity, pharmacokinetics, and pharmacodynamics of BLU-808, a wild type KIT inhibitor, in participants with CIndU (Part A) or CSU (Part B).

Detailed Description

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Conditions

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Chronic Inducible Urticaria Chronic Spontaneous Urticaria

Keywords

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Chronic Inducible Urticaria Chronic Spontaneous Urticaria BLU-808 CIndU CSU Chronic Urticaria CU Cold Urticaria ColdU Symptomatic Dermographism SD

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Arms A1 and A3 are non-randomized and open label. Arm B is randomized and double blind.

Study Groups

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Arm A1 (Part A): BLU-808

BLU-808 will be administered orally.

Group Type EXPERIMENTAL

BLU-808

Intervention Type DRUG

Oral administration

Arm A3 (Part A): BLU-808

BLU-808 will be administered orally.

Group Type EXPERIMENTAL

BLU-808

Intervention Type DRUG

Oral administration

Arm B (Part B): BLU-808/Placebo

BLU-808 or matching placebo will be administered orally.

Group Type EXPERIMENTAL

BLU-808

Intervention Type DRUG

Oral administration

Placebo

Intervention Type DRUG

Oral administration

Interventions

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BLU-808

Oral administration

Intervention Type DRUG

Placebo

Oral administration

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Part A: Confirmed diagnosis of CIndU for ≥3 months prior to Day 1 that is inadequately controlled with second generation H1-antihistamines.
* Part B: Confirmed diagnosis of CSU for ≥3 months prior to Day 1 that is inadequately controlled with second generation H1-antihistamines.

Exclusion Criteria

* Part A: Any active urticaria that may interfere with study assessments.
* Part B: Participant has a clearly defined predominant cause of chronic urticaria or sole trigger such as symptomatic dermographism and cold-induced urticaria.
* Part A and Part B: Any other skin disease associated with chronic itching or angioedema that might influence the study evaluations and results, skin diseases associated with only wheals and no itch, or autoinflammatory diseases with urticarial lesions.
* Part A and Part B: Significant medical, psychiatric, or surgical conditions, or physical findings that may affect participant safety, study drug metabolism, study participation, or assessment of study results.
* Part A and Part B: Abnormal laboratory values that may pose risks or interfere with study participation.
* Part A and Part B: Pregnancy or plans for pregnancy; breastfeeding.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Blueprint Medicines Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Allervie Clinical Research

Birmingham, Alabama, United States

Site Status RECRUITING

Acuro Research, Inc.

Little Rock, Arkansas, United States

Site Status RECRUITING

Modena Allergy & Asthma Clinical Research - La Jolla

La Jolla, California, United States

Site Status RECRUITING

Allergy & Asthma Medical Group and Research Center

San Diego, California, United States

Site Status RECRUITING

Allergy Affiliates Inc.

Bradenton, Florida, United States

Site Status RECRUITING

University of South Florida

Tampa, Florida, United States

Site Status RECRUITING

Treasure Valley Medical Research

Boise, Idaho, United States

Site Status RECRUITING

Endeavor Health

Northbrook, Illinois, United States

Site Status RECRUITING

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, United States

Site Status RECRUITING

Southern Indiana Clinical Trials

New Albany, Indiana, United States

Site Status RECRUITING

The Indiana Clinical Trials Center

Plainfield, Indiana, United States

Site Status RECRUITING

Equity Medical - Bowling Green

Bowling Green, Kentucky, United States

Site Status RECRUITING

Johns Hopkins University

Baltimore, Maryland, United States

Site Status RECRUITING

Institute For Asthma & Allergy

Wheaton, Maryland, United States

Site Status RECRUITING

Chesapeake Clinical Research

White Marsh, Maryland, United States

Site Status RECRUITING

Henry Ford Health

Detroit, Michigan, United States

Site Status RECRUITING

Mayo Clinic

Rochester, Minnesota, United States

Site Status RECRUITING

The Clinical Research Center LLC.

St Louis, Missouri, United States

Site Status RECRUITING

Montana Medical Research, Inc.

Missoula, Montana, United States

Site Status RECRUITING

Equity Medical (at Cameron Dermatology) - New York

New York, New York, United States

Site Status RECRUITING

Bernstein Clinical Research Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Allergy & Clinical Immunology Associates

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

National Allergy, Asthma & Urticaria Centers of Charleston

Charleston, South Carolina, United States

Site Status RECRUITING

Reveal Research Institute

Dallas, Texas, United States

Site Status RECRUITING

Odense University Hospital - Odense

Odense, , Denmark

Site Status RECRUITING

Fraunhofer-Institut fuer Translationale Medizin und Pharmakologie ITMP - Standort Berlin

Berlin, , Germany

Site Status RECRUITING

Universitaetsklinikum Carl Gustav Carus Dresden

Dresden, , Germany

Site Status RECRUITING

Universitaetsklinikum Frankfurt - Klinikum der Johann Wolfgang Goethe Universitaet

Frankfurt am Main, , Germany

Site Status RECRUITING

Medizinische Hochschule Hannover (MHH)

Hanover, , Germany

Site Status RECRUITING

Universitaetsmedizin der Johannes Gutenberg - Universitaet Mainz

Mainz, , Germany

Site Status RECRUITING

Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status RECRUITING

Centro Ricerche Cliniche di Verona s.r.l.

Verona, , Italy

Site Status RECRUITING

Hospital del Mar

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari de Bellvitge

Barcelona, , Spain

Site Status RECRUITING

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status RECRUITING

Taipei Medical University - Shuang Ho Hospital

New Taipei City, , Taiwan

Site Status RECRUITING

Countries

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United States Denmark Germany Italy Spain Taiwan

Central Contacts

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Blueprint Medicines

Role: CONTACT

Phone: 1-888-258-7768

Email: [email protected]

Blueprint Medicines, EU Contact

Role: CONTACT

Phone: +31 85 064 4001

Email: [email protected]

Other Identifiers

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2024-520031-33-00

Identifier Type: OTHER

Identifier Source: secondary_id

BLU-808-1201

Identifier Type: -

Identifier Source: org_study_id