A Phase 3 Efficacy and Safety Study of Fosmanogepix for the Treatment of Adult Patients With Invasive Mold Infections.

NCT ID: NCT06925321

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

219 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-08-26

Study Completion Date

2028-02-29

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of fosmanogepix (administered IV or oral) for the treatment of adult patients with invasive mold infections. The study is looking for patients who have been diagnosed with invasive mold infections. The maximum study duration will be approximately 8 months, including a target study treatment duration of 84 days which can be extended up to 180 days and follow-up period.

The patient will be assigned to one of two treatment cohorts:

Cohort A (primary therapy): Patients will receive either the study drug or institutional standard of care antifungal treatment.

Cohort B (salvage treatment; i.e. treatment given after patients did not respond to previous treatments or did not tolerate them): Patients will receive the study drug

The primary aim is to compare the all cause mortality with a fixed threshold at Day 42.

Detailed Description

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Conditions

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Invasive Mold Infections

Keywords

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Fungal infection Antifungal Mold infection Rare molds Multidrug resistant mold Aspergillus spp. Fusarium spp. Lomentospora prolificans Mucorales fungi Scedosporium spp.

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

An open-label, 2-cohort study
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort A: Experimental Treatment

Patients will receive the study drug.

Fosmanogepix will be administered as an Intravenous (IV) infusion or in oral form.

Group Type EXPERIMENTAL

Fosmanogepix IV infusion

Intervention Type DRUG

Fosmanogepix will be administered IV

Fosmanogepix oral tablet

Intervention Type DRUG

Fosmanogepix will be administered orally.

Cohort A: Comparator Antifungal Treatment

Best available therapy (BAT) administered as IV or orally per standard guidelines.

Group Type ACTIVE_COMPARATOR

Standard of care antifungal therapy

Intervention Type DRUG

Standard of care antifungal therapy will be administered in accordance with their respective product labels and/or standard practice guidelines

Cohort B

Patients will receive the study drug.

Fosmanogepix will be administered as an Intravenous (IV) infusion or in oral form.

Group Type EXPERIMENTAL

Fosmanogepix IV infusion

Intervention Type DRUG

Fosmanogepix will be administered IV

Fosmanogepix oral tablet

Intervention Type DRUG

Fosmanogepix will be administered orally.

Interventions

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Fosmanogepix IV infusion

Fosmanogepix will be administered IV

Intervention Type DRUG

Standard of care antifungal therapy

Standard of care antifungal therapy will be administered in accordance with their respective product labels and/or standard practice guidelines

Intervention Type DRUG

Fosmanogepix oral tablet

Fosmanogepix will be administered orally.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of proven or probable Invasive mold infection (IMI) defined in accordance with the Revision and Update of the Consensus Definitions of Invasive Fungal Disease from the EORTC/MSGERC as adapted for this study and caused by Aspergillus spp. (in patients with limited treatment options), Fusarium spp., Lomentospora prolificans, Mucorales fungi, or other multi-drug resistant molds.
2. Patient's condition allows for appropriate infection source control measures.

Main Exclusion Critera:

1. Refractory hematologic malignancy.
2. Chronic aspergillosis, aspergilloma, or allergic bronchopulmonary aspergillosis.
3. COVID-19 associated mucormycosis.
4. Invasive fungal disease caused by more than one fungal pathogen is not permitted in Cohort A but is permitted in Cohort B.
5. Patients with a Karnofsky Performance Status \< 20 at Screening.
6. Requirement, or anticipated requirement, for hemodialysis, peritoneal dialysis, or hemofiltration.
7. Patients with known human immunodeficiency virus infection.
8. Ongoing neurological disorders.
9. Patients receiving hospice/comfort care only.
10. Other medical or psychiatric condition.
11. Current use of any prohibited concomitant medication(s).
12. Current/ previous administration of an investigational drug within 30 days.
13. Prior enrollment in this or any previous study of fosmanogepix.
14. Moderate or severe hepatic impairment.
15. Patient who is pregnant or lactating.
16. Known hypersensitivity to fosmanogepix, manogepix, or any of their excipients.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biomedical Advanced Research and Development Authority

FED

Sponsor Role collaborator

Basilea Pharmaceutica

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Daniel Ionescu, MD

Role: STUDY_DIRECTOR

Basilea Pharmaceutica International Ltd, Allschwil

Locations

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University of Alabama at Birmingham School of Medicine, Department of Medicine

Birmingham, Alabama, United States

Site Status RECRUITING

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status RECRUITING

Karmanos Cancer Institute - Detroit

Detroit, Michigan, United States

Site Status RECRUITING

University of Minnesota, M Health Fairview Medical Center

Minneapolis, Minnesota, United States

Site Status RECRUITING

Washington University School of Medicine, Infectious Diseases Clinical Research Unit

St Louis, Missouri, United States

Site Status RECRUITING

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Duke University Medical Center, Duke Infectious Diseases

Durham, North Carolina, United States

Site Status RECRUITING

Princess Alexandra Hospital

Woolloongabba, , Australia

Site Status RECRUITING

Chaim Sheba Medical Center, Department of Infectious Diseases

Ramat Gan, , Israel

Site Status RECRUITING

The Tel Aviv Sourasky Medical Center, Infectious Diseases Unit

Tel Aviv, , Israel

Site Status RECRUITING

Faculty of Medicine, Siriraj Hospital

Bangkok, , Thailand

Site Status RECRUITING

Maharaj Nakorn Chiang Mai Hospital

Chiang Mai, , Thailand

Site Status RECRUITING

Songklanagarind Hospital

Hat Yai, , Thailand

Site Status RECRUITING

Countries

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United States Australia Israel Thailand

Central Contacts

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Daniel Ionescu, MD

Role: CONTACT

Phone: +41763192318

Email: [email protected]

Marc Engelhardt, MD

Role: CONTACT

Phone: +41797010551

Email: [email protected]

Other Identifiers

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FMGX-CS-302

Identifier Type: -

Identifier Source: org_study_id