A Study of ONO-2020 in Participants With Mild to Moderate Alzheimer's Disease

NCT ID: NCT06881836

Last Updated: 2025-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-04-24

Study Completion Date

2026-08-31

Brief Summary

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This is a Phase 2, double-blind, parallel-group, placebo-controlled study to assess safety, tolerability, pharmacokinetics, and efficacy of ONO-2020 in participants with mild to moderate Alzheimer's disease (AD). This study aims to determine whether administering ONO-2020, an epigenetic regulator, may improve cognitive functions like memory and cognition in individuals with Alzheimer's disease dementia.

Detailed Description

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In the study, participants will undergo a screening period of up to 6 weeks (42 days). Eligible participants will be assigned to receive one of 2 dose levels of ONO-2020 or placebo control arm. ONO-2020 or placebo will be administered orally QD for 26 weeks. All participants who received study intervention will be followed up for 4 weeks after treatment discontinuation. The target sample size is 240 participants , out of which up to 45 participants will undergo additional special CSF biomarker evaluation. After enrollment, participants will be randomized in a 1:1:1 ratio to one of 3 treatment arms.

Conditions

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Alzheimer Disease

Keywords

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Alzheimer Disease mild to moderate Alzheimer Disease Dementia ONO-2020

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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ONO-2020 Dose 1

Participants will receive ONO-2020 Dose 1 administered orally, once a day (QD) for 26 weeks.

Group Type EXPERIMENTAL

ONO-2020

Intervention Type DRUG

ONO-2020 group: Two ONO-2020 tablets will be orally administered once daily.

ONO-2020 Dose 2

Participants will receive ONO-2020 Dose 2 administered orally, once a day (QD) for 26 weeks.

Group Type EXPERIMENTAL

ONO-2020

Intervention Type DRUG

ONO-2020 group: Two ONO-2020 tablets will be orally administered once daily.

Placebo

Participants will receive Placebo administered orally, once a day (QD) for 26 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo group: Two ONO-2020 placebo tablets will be orally administered once daily.

Interventions

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ONO-2020

ONO-2020 group: Two ONO-2020 tablets will be orally administered once daily.

Intervention Type DRUG

Placebo

Placebo group: Two ONO-2020 placebo tablets will be orally administered once daily.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Have a diagnosis of Alzheimer's disease according to the recommendations from the revised criteria for diagnosis and staging of Alzheimer's disease: Alzheimer's Association Workgroup , along with any positive AD-specific biomarker results (abnormal Core 1 or Core 2 biomarkers) from a previous diagnosis or at screening.
2. Have a previous MRI or CT scan of the brain, which was performed within 1 year prior to enrollment in the study, to confirm that more recent neurological events (e.g., stroke) would not potentially constitute a confounder in the assessment of the etiology of the participant's cognitive status.
3. MMSE score of 15 to 24, inclusive, and MMSE score cannot deviate more than 3 points in either direction between the screening and baseline visits.
4. AD numeric clinical stage 4 or stage 5 based on NIA-AA criteria 2024, at screening and baseline visits
5. Participants receiving concurrent AD treatment (acetylcholinesterase inhibitors and /or memantine) must be on a stable dose for at least 90 days prior to randomization, and the participant must be willing to remain on the same dose for the duration of the study.
6. Have the ability to comply with procedures for cognitive and other tests in the opinion of the investigator
7. If female, postmenopausal for at least 1 year
8. Non-vasectomized male participants with female partners of childbearing potential must agree to use an effective method of contraception from dosing on Day 1 until 3 months after the last administration of study intervention and agree not to donate sperm until 3 months after the last administration of study intervention.
9. Participant must have a Caregiver who has frequent contact with the participant (defined as at least 8 hours per week spread across 3\~4 visits per week) to provide support to the participant to ensure compliance with study requirements. The Caregiver must be willing to consent to participate in this study, to provide a rating of the extent and severity of change of the participant's memory, problem-solving abilities, or activities of daily living from prior abilities.
10. General health status acceptable for participation in the study, and the participant must be able to ingest pills.
11. Participant and his/her Caregiver have provided full written informed consent prior to the performance of any protocol-specified procedure; or if a participant is unable to provide informed consent due to cognitive status, he/she has provided assent, and a legally acceptable representative (LAR) has provided full written informed consent on behalf of the participant.

Exclusion Criteria

1. Participants with dementia or other memory impairment not due to Alzheimer's disease, including, but not limited to, dementia with Lewy bodies, vascular dementia, Parkinson's disease, Huntington disease, corticobasal degeneration, Creutzfeldt-Jakob disease, progressive supranuclear palsy, frontotemporal degeneration, normal pressure hydrocephalus, hypoxia, severe sleep apnea or other chronic sleep disturbance, or baseline intellectual disability.
2. Participants with a history of stroke, well-documented transient ischemic attack, or pulmonary or cerebral embolism.
3. History of significant psychiatric illness such as schizophrenia or bipolar affective disorder, or history or current major depressive disorder in the past year and any other significant psychiatric illness that in the opinion of the investigator could interfere with participation in the study.
4. Participants with delirium or history of delirium within the 30 days prior to the screening visit.
5. Have suicide ideation according to the investigator's clinical judgment as per the Columbia-Suicide Severity Rating Scale (C-SSRS) at screening or have made a suicide attempt in the 6 months prior to screening.
6. Clinically significant ECG abnormality as judged by the investigator.
7. Confirmed absolute QTcF \>450 msec for males or \>470 msec for females.
8. Positive results at screening for active viral infections that include human immunodeficiency virus (HIV), hepatitis B surface antigen (HBsAg), and hepatitis C virus (HCV) RNA PCR test.
9. Participants with total bilirubin, alanine transaminase (ALT) or aspartate transaminase (AST) greater than 1.5×upper limit of normal (ULN), or international normalized ratio (INR) greater than 1.7 at screening.
10. Participants with estimated creatinine clearance (CrCL, Cockcroft-Gault equation) ≤30 mL/min at screening.
11. Participants with a history of treatment, and/or current treatment, with anti-Aβ antibodies
12. Changes in any medications that, in the opinion of the investigator, may potentially impair participants' ability to perform cognitive testing or study procedures during the study period (from Screening to EOT), and their dosing should be stable for at least 1 month before Screening (such as benzodiazepines and sedatives/hypnotics). All concomitant medications must be kept as stable as medically possible during the study.
13. Participants who have taken any investigational products, or used investigational medical devices, within 3 months or five half-lives of the therapy (whichever is longer) with respect to first dosing and throughout the study
Minimum Eligible Age

55 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Project Leader

Role: STUDY_DIRECTOR

Ono Pharmaceutical Co. Ltd

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status RECRUITING

Banner Alzheimer's Institute (BAI)

Phoenix, Arizona, United States

Site Status RECRUITING

Clinical Endpoints

Scottsdale, Arizona, United States

Site Status RECRUITING

Banner Sun Health Research Institute

Sun City, Arizona, United States

Site Status RECRUITING

Center for Neurosciences-Research

Tucson, Arizona, United States

Site Status RECRUITING

Baptist Health Center for Clinical Research

Little Rock, Arkansas, United States

Site Status TERMINATED

Advanced Research Center; Inc

Anaheim, California, United States

Site Status RECRUITING

Profound Research LLC at The Neurology Center of Southern California

Carlsbad, California, United States

Site Status RECRUITING

Ark Clinical Research

Fountain Valley, California, United States

Site Status WITHDRAWN

Neurology Center of North Orange County

Fullerton, California, United States

Site Status RECRUITING

Neurology Center of North Orange County

Fullerton, California, United States

Site Status RECRUITING

Stanford University

Palo Alto, California, United States

Site Status RECRUITING

Sunwise Clinical Research

Walnut Creek, California, United States

Site Status RECRUITING

CenExel Rocky Mountain Clinical Research

Englewood, Colorado, United States

Site Status RECRUITING

Brain Matters Research

Delray Beach, Florida, United States

Site Status RECRUITING

Neuropsychiatric Research Center of Southwest Florida

Fort Myers, Florida, United States

Site Status WITHDRAWN

Velocity Clinical Research, Hallandale Beach

Hallandale, Florida, United States

Site Status RECRUITING

Premier Clinical Research Institute; Inc.

Miami, Florida, United States

Site Status RECRUITING

Quantum Clinical Trials

Miami Beach, Florida, United States

Site Status RECRUITING

Suncoast Clinical Research

New Port Richey, Florida, United States

Site Status RECRUITING

Renstar Medical Research

Ocala, Florida, United States

Site Status RECRUITING

Charter Research - Orlando

Orlando, Florida, United States

Site Status RECRUITING

Accel Research Sites - Brain and Spine Institute

Port Orange, Florida, United States

Site Status RECRUITING

USF Health Byrd Alzheimer's Institute

Tampa, Florida, United States

Site Status RECRUITING

ForCare Clinical Research

Tampa, Florida, United States

Site Status RECRUITING

Charter Research - The Villages

The Villages, Florida, United States

Site Status RECRUITING

Conquest Research LLC

Winter Park, Florida, United States

Site Status RECRUITING

Sandhill Research, LLC d/b/a Accel Research Sites - NeuroStudies CRU

Decatur, Georgia, United States

Site Status RECRUITING

CenExel iResearch, LLC

Savannah, Georgia, United States

Site Status RECRUITING

Velocity Clinical Research, Boise

Meridian, Idaho, United States

Site Status RECRUITING

Re:Cognition Health-Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Charter Research - Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Ascension Alexian Brothers Medical Center

Elk Grove Village, Illinois, United States

Site Status RECRUITING

University of Kansas Medical Center

Fairway, Kansas, United States

Site Status RECRUITING

Univ of Kentucky Sanders-Brown Center on Aging

Lexington, Kentucky, United States

Site Status RECRUITING

Boston Clinical Trials

Boston, Massachusetts, United States

Site Status RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

ActivMed Research

Methuen, Massachusetts, United States

Site Status RECRUITING

Quest Research Institute

Farmington Hills, Michigan, United States

Site Status RECRUITING

Cleveland Clinic Lou Ruvo Center for Brain Health

Las Vegas, Nevada, United States

Site Status NOT_YET_RECRUITING

Vector Clinical Trials

Las Vegas, Nevada, United States

Site Status RECRUITING

The Cognitive and Research Center of New Jersey

Springfield, New Jersey, United States

Site Status RECRUITING

Advanced Memory Research Institute of NJ (CenExel AMRI)

Toms River, New Jersey, United States

Site Status RECRUITING

Advanced Clinical Institute Inc.

West Long Branch, New Jersey, United States

Site Status RECRUITING

Integrative Clinical Trials

Brooklyn, New York, United States

Site Status RECRUITING

University at Buffalo

Buffalo, New York, United States

Site Status RECRUITING

Velocity Clinical Research; Syracuse

East Syracuse, New York, United States

Site Status RECRUITING

The Feinstein Institutes for Medical Research

Manhasset, New York, United States

Site Status RECRUITING

NYU Center for Cognitive Neurology

New York, New York, United States

Site Status RECRUITING

AD-CARE; University of Rochester

Rochester, New York, United States

Site Status RECRUITING

Stony Brook University Hospital

Stony Brook, New York, United States

Site Status RECRUITING

New Hope Clinical Research

Charlotte, North Carolina, United States

Site Status TERMINATED

Eximia Research-Raleigh

Raleigh, North Carolina, United States

Site Status RECRUITING

Velocity Clinical Research at Raleigh Neurology

Raleigh, North Carolina, United States

Site Status RECRUITING

NeuroScience Research Center

Canton, Ohio, United States

Site Status RECRUITING

University of Cincinnati

Cincinnati, Ohio, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

The Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

Neurology Diagnostics Research

Dayton, Ohio, United States

Site Status RECRUITING

Neuro Behavioral Clinical Research, Inc.

North Canton, Ohio, United States

Site Status RECRUITING

Neural Net Research / Center for Cognitive Health

Portland, Oregon, United States

Site Status RECRUITING

Oregon Health & Science University

Portland, Oregon, United States

Site Status RECRUITING

Penn Medicine

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status RECRUITING

Neurology Clinic, P.C.

Cordova, Tennessee, United States

Site Status RECRUITING

Alliance for Multispecialty Research;LLC-Knoxville

Knoxville, Tennessee, United States

Site Status RECRUITING

Vanderbilt UMC-Cognitive Med

Nashville, Tennessee, United States

Site Status RECRUITING

FutureSearch Trials of Neurology

Austin, Texas, United States

Site Status COMPLETED

Horizon Clinical Research Group

Cypress, Texas, United States

Site Status RECRUITING

Texas Neurology

Dallas, Texas, United States

Site Status RECRUITING

FutureSearch Trials of Dallas LLC

Dallas, Texas, United States

Site Status RECRUITING

Re:Cognition Health - Fort Worth

Fort Worth, Texas, United States

Site Status RECRUITING

Re:Cognition Health - Houston

Houston, Texas, United States

Site Status RECRUITING

Olympus Clinical Research - Katy

Katy, Texas, United States

Site Status RECRUITING

Be Well Clinical Studies

Round Rock, Texas, United States

Site Status RECRUITING

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status RECRUITING

Grayline Research Center

Wichita Falls, Texas, United States

Site Status RECRUITING

Velocity Clinical Research, Salt Lake City

Salt Lake City, Utah, United States

Site Status WITHDRAWN

Wasatch Clinical Research; LLC

Salt Lake City, Utah, United States

Site Status RECRUITING

Re:Cognition Health - Fairfax

Fairfax, Virginia, United States

Site Status RECRUITING

Sentara Neurology Specialists

Norfolk, Virginia, United States

Site Status RECRUITING

Northwest Clinical Research Center

Bellevue, Washington, United States

Site Status RECRUITING

Kingfisher Cooperative; LLC

Spokane, Washington, United States

Site Status RECRUITING

National Center for Geriatrics and Gerontology

Aichi, , Japan

Site Status RECRUITING

Inage Neurology and Memory Clinic

Chiba, , Japan

Site Status RECRUITING

Mabashi Clinic

Chiba, , Japan

Site Status RECRUITING

Southern Tohoku Medical Clinic

Fukushima, , Japan

Site Status RECRUITING

Ikuseikai Shinozuka Hospital

Gunma, , Japan

Site Status RECRUITING

Imon Yukari Neurology Clinic

Hiroshima, , Japan

Site Status RECRUITING

NHO Hiroshima-Nishi Medical Center

Hiroshima, , Japan

Site Status RECRUITING

Himeji Central Hospital Clinic

Hyōgo, , Japan

Site Status RECRUITING

Kobe City Medical Center General Hospital

Hyōgo, , Japan

Site Status RECRUITING

Memory Clinic Toride

Ibaraki, , Japan

Site Status RECRUITING

Kagawa Prefectural Central Hospital

Kagawa, , Japan

Site Status RECRUITING

Meiwakai Izaki Clinic

Nagasaki, , Japan

Site Status RECRUITING

Katayama Medical Clinic

Okayama, , Japan

Site Status RECRUITING

Takesato Hospital

Saitama, , Japan

Site Status RECRUITING

Jichiidai Station Brain Clinic

Tochigi, , Japan

Site Status RECRUITING

Ichiekai Itsuki Hospital

Tokushima, , Japan

Site Status RECRUITING

Federation of National Public Service Personnel Mutual Aid Associations Tachikawa Hospital

Tokyo, , Japan

Site Status RECRUITING

Memory Clinic Ochanomizu

Tokyo, , Japan

Site Status RECRUITING

Tokyo Medical University Hospital

Tokyo, , Japan

Site Status RECRUITING

Tokyo Metropolitan Institute for Geriatrics and Gerontology

Tokyo, , Japan

Site Status RECRUITING

Countries

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United States Japan

Central Contacts

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North America Clinical Trial Support Desk

Role: CONTACT

Phone: +18665877745(Toll-Free)

Email: [email protected]

International Clinical Trial Support Desk

Role: CONTACT

Phone: +17162141777(Standard)

Email: [email protected]

Facility Contacts

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LaToya Conner-Gaiters

Role: primary

Anna Crossland

Role: primary

Emma Peacock

Role: primary

Jennifer Crowley

Role: primary

Gwendolyn Gabriec

Role: primary

Sara Veerman

Role: primary

Morgan Hussey

Role: primary

Priyanka Huilgol

Role: primary

Priyanka Huilgol

Role: primary

Pragya Tripathi

Role: primary

Jamie Flores

Role: primary

Emily Birney

Role: primary

Jennifer Blasi

Role: primary

William Torres

Role: primary

Vivian Torres

Role: primary

Jordan Herman

Role: primary

Rebecca Ramkumar

Role: primary

Angella Pitts

Role: primary

Emilio Lorenzo

Role: primary

Karen garceau

Role: primary

Karen Colombo

Role: primary

Kaylie LoCascio

Role: primary

Wendy Giselbach

Role: primary

Jairo Argueta

Role: primary

Adrienne Hilliard

Role: primary

Skyler McPherson

Role: primary

Audra Weslowski

Role: primary

Daisy Aleman

Role: primary

Amber Holst

Role: primary

Quinlan Smith

Role: primary

Reagan Smith

Role: primary

Muna Amry

Role: primary

Joanne Monaghan

Role: primary

Dylan Hruskar

Role: primary

Chloe Armstrong

Role: primary

Freddrenia Holmes

Role: primary

Michelle Torreliza

Role: primary

Josephine Sanchez

Role: primary

Kamela Chandrika

Role: primary

Maria Gencova

Role: primary

Rebecca Ornstein

Role: primary

Bella Yevseva

Role: primary

Nicholas Audino

Role: primary

Jennifer Wolf

Role: primary

Erica Christen

Role: primary

Emilie Geesey

Role: primary

Susan Salem-Spencer

Role: primary

Melanie Rooney

Role: primary

Eric Henderson

Role: primary

Tracey Pate

Role: primary

Shandell Mooney

Role: primary

Jessica Marchbank

Role: primary

Janel Thomas

Role: primary

Teagan Lucas

Role: primary

Joyce Berhold

Role: primary

Jax Harvey

Role: primary

Emma Moorehead

Role: primary

Alexandra Ruhf

Role: primary

Martha Combs

Role: primary

Marie Amoyaw

Role: primary

Ye Lui

Role: primary

Jada S Thomas

Role: primary

Meagan Adams

Role: primary

Shatabdi Satpathi

Role: primary

Michelle Washington

Role: primary

Karl Wolff

Role: primary

Zobaida Shakur

Role: primary

Laura Vaquerano

Role: primary

Wendy Benitez

Role: primary

Stephen Shay

Role: primary

Koni Lopez

Role: primary

Dessirae Perez

Role: primary

Karen R George

Role: primary

Oumayma Driouche

Role: primary

Lisa Richardson

Role: primary

Nicole Harper

Role: backup

Sasha Kapal

Role: primary

Kasey Wills

Role: primary

Other Identifiers

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jRCT2031240712

Identifier Type: REGISTRY

Identifier Source: secondary_id

ONO-2020-02

Identifier Type: -

Identifier Source: org_study_id