Phase 2 Study Evaluating Rapcabtagene Autoleucel in Participants With Severe Active GPA or MPA

NCT ID: NCT06868290

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

126 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-13

Study Completion Date

2030-05-24

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to evaluate the efficacy and safety of rapcabtagene autoleucel versus comparator in participants with severe active Granulomatosis with Polyangiitis (GPA) or Microscopic Polyangiitis (MPA)

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is a Phase 2, randomized, assessor-blinded active controlled study. This study comprises two cohorts:

* A lead-in cohort enrolling participants to receive rapcabtagene autoleucel
* A randomized cohort with participants receiving either rapcabtagene autoleucel or comparator.

After end of study (EOS), participants who received rapcabtagene autoleucel infusion will enter a long-term follow-up (LTFU) period lasting up to 15 years after rapcabtagene autoleucel infusion. This LTFU will be described in a separate study protocol.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

ANCA Associated Vasculitis (AAV)

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Chimeric Antigen Receptor-T (CAR-T) rapcabtagene autoleucel anti-neutrophil cytoplasmic antibody (ANCA) ANCA-associated vasculitis/vasculitides (AAV) Granulomatosis with Polyangiitis (GPA) Microscopic Polyangiitis (MPA)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Outcome Assessors
The study investigator and the participant will be unblinded to the study treatment. A blinded assessor will perform the efficacy assessments to minimize bias in data collection.

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Rapcabtagene autoleucel

Single infusion of rapcabtagene autoleucel (YTB323) and concomitant glucocorticoids as per protocol

Group Type EXPERIMENTAL

Rapcabtagene autoleucel

Intervention Type BIOLOGICAL

Single infusion of rapcabtagene autoleucel

Glucocorticoids

Intervention Type DRUG

Concomitant glucocorticoids as per protocol

Active comparator

Comparator and concomitant glucocorticoids as per protocol

Group Type ACTIVE_COMPARATOR

Active Comparator

Intervention Type OTHER

Active comparator option as per protocol

Glucocorticoids

Intervention Type DRUG

Concomitant glucocorticoids as per protocol

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Rapcabtagene autoleucel

Single infusion of rapcabtagene autoleucel

Intervention Type BIOLOGICAL

Active Comparator

Active comparator option as per protocol

Intervention Type OTHER

Glucocorticoids

Concomitant glucocorticoids as per protocol

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Men and women, aged ≥18 and ≤ 75 years with a diagnosis of GPA or MPA according to the American College of Rheumatology/ European League Against Rheumatism 2022 (ACR/EULAR 2022) classification criteria
2. Positive test for ANCA-autoantibodies
3. GPA and MPA participants with severe active disease

Exclusion Criteria

1. Any condition that could prevent a complete washout of medications or could otherwise make the participant ineligible for anti-CD19 CAR-T therapy and further participation in the study
2. Hypersensitivity and/or contraindications to any product to be given to the participant as part of the study protocol
3. Other systemic autoimmune diseases requiring therapy
4. Any medical conditions that are not related to GPA/MPA that would jeopardize the ability of the participant to tolerate CD19 CAR-T cell therapy
5. Inadequate organ function
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University Of Colorado

Aurora, Colorado, United States

Site Status RECRUITING

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status RECRUITING

Northwestern University

Chicago, Illinois, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

Oregon Health Sciences University

Portland, Oregon, United States

Site Status RECRUITING

Houston Methodist Hospital

Houston, Texas, United States

Site Status RECRUITING

LDS Hospital

Salt Lake City, Utah, United States

Site Status RECRUITING

Novartis Investigative Site

Salvador, Estado de Bahia, Brazil

Site Status RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status RECRUITING

Novartis Investigative Site

São Paulo, , Brazil

Site Status RECRUITING

Novartis Investigative Site

Haifa, , Israel

Site Status RECRUITING

Novartis Investigative Site

Ramat Gan, , Israel

Site Status RECRUITING

Novartis Investigative Site

Sapporo, Hokkaido, Japan

Site Status RECRUITING

Novartis Investigative Site

Kobe, Hyōgo, Japan

Site Status RECRUITING

Novartis Investigative Site

Kanazawa, Ishikawa-ken, Japan

Site Status RECRUITING

Novartis Investigative Site

Sendai, Miyagi, Japan

Site Status RECRUITING

Novartis Investigative Site

Suita, Osaka, Japan

Site Status RECRUITING

Novartis Investigative Site

Shinjuku-ku, Tokyo, Japan

Site Status RECRUITING

Novartis Investigative Site

Chiba, , Japan

Site Status RECRUITING

Novartis Investigative Site

Fukuoka, , Japan

Site Status RECRUITING

Novartis Investigative Site

Kyoto, , Japan

Site Status RECRUITING

Novartis Investigative Site

Riyadh, , Saudi Arabia

Site Status RECRUITING

Novartis Investigative Site

Singapore, , Singapore

Site Status RECRUITING

Novartis Investigative Site

Singapore, , Singapore

Site Status RECRUITING

Novartis Investigative Site

Basel, , Switzerland

Site Status RECRUITING

Novartis Investigative Site

Bern, , Switzerland

Site Status RECRUITING

Novartis Investigative Site

Cambridge, , United Kingdom

Site Status RECRUITING

Novartis Investigative Site

London, , United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Brazil Israel Japan Saudi Arabia Singapore Switzerland United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Novartis Pharmaceuticals

Role: CONTACT

Phone: 1-888-669-6682

Email: [email protected]

Novartis Pharmaceuticals

Role: CONTACT

Phone: +41613241111

Email: [email protected]

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Chong Pedrick

Role: primary

John Hatzimouratides Jr.

Role: primary

Matthew Selle

Role: primary

Michael Rabinovich

Role: primary

Josephine Baum

Role: primary

Rosy Quinn

Role: primary

Jennifer Garrett

Role: primary

Tara Sou

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

CYTB323I12201

Identifier Type: -

Identifier Source: org_study_id