A Phase 3 Study to Assess Efficacy Safety and Tolerability of Remibrutinib in Adult and Adolescent Patients With Moderate to Severe Hidradenitis Suppurativa (RECHARGE 1)

NCT ID: NCT06799000

Last Updated: 2026-01-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

555 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-01-31

Study Completion Date

2028-02-18

Brief Summary

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The purpose of this study is to establish the efficacy, safety, and tolerability of remibrutinib (LOU064) Dose A and Dose B compared to placebo in participants with moderate to severe hidradenitis suppurativa (HS).

Detailed Description

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The total duration of the study is 76 weeks and consists of: Screening (up to 4 weeks), Treatment Period 1 (16 weeks, double-blind treatment with remibrutinib (Dose A or Dose B) or placebo, Treatment Period 2 (52 weeks, treatment with remibrutinib (Dose A or Dose B) and Safety Follow-Up (treatment-free follow-up for 4 weeks).

Participants who prematurely discontinue study treatment (either during Treatment Period 1 or Treatment Period 2) are encouraged to remain in the study. Participants who do not wish to remain in the study will enter a 4-week Safety Follow-Up period.

Conditions

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Hidradenitis Suppurativa

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Remibrutinib Dose A (Treatment Period 1 and 2)

Participants randomized to receive remibrutinib Dose A during Treatment Period 1 and 2

Group Type EXPERIMENTAL

Remibrutinib Dose A

Intervention Type DRUG

Remibrutinib Dose A (oral)

Remibrutinib Dose B (Treatment Period 1 and 2)

Participants randomized to receive remibrutinib Dose B during Treatment Period 1 and 2

Group Type EXPERIMENTAL

Remibrutinib Dose B

Intervention Type DRUG

Remibrutinib Dose B (oral)

Placebo (Treatment Period 1) + remibrutinib Dose B (Treatment Period 2)

Participants randomized to receive placebo during Treatment Period 1 followed by remibrutinib dose B during Treatment Period 2

Group Type PLACEBO_COMPARATOR

Remibrutinib Dose B

Intervention Type DRUG

Remibrutinib Dose B (oral)

Placebo 1

Intervention Type DRUG

Placebo matching to remibrutinib Dose A (oral)

Placebo 2

Intervention Type DRUG

Placebo matching to remibrutinib Dose B (oral)

Interventions

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Remibrutinib Dose A

Remibrutinib Dose A (oral)

Intervention Type DRUG

Remibrutinib Dose B

Remibrutinib Dose B (oral)

Intervention Type DRUG

Placebo 1

Placebo matching to remibrutinib Dose A (oral)

Intervention Type DRUG

Placebo 2

Placebo matching to remibrutinib Dose B (oral)

Intervention Type DRUG

Other Intervention Names

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LOU064 LOU064

Eligibility Criteria

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Inclusion Criteria

1. Male and female participants ≥ 12 years of age at the time of signing of the informed consent.
2. Diagnosis of HS based on clinical history and physical examination for at least 6 months prior to the Baseline visit.
3. Participants with moderate to severe HS defined as:

* A total of at least 5 AN count (abscesses and/or inflammatory nodules) AND
* Inflammatory lesions should affect at least 2 distinct anatomic areas (e.g., left and right axillae)

Exclusion Criteria

1. Presence of more than 20 fistulae/tunnels (both draining and non-draining) in total at baseline.
2. Any active skin disease or conditions that may interfere with the assessment of HS.
3. Previous exposure to remibrutinib or other BTK inhibitors.
4. Use of other investigational drugs within 5 half-lives of enrollment, or within 30 days (for small molecules) prior to randomization, or until the pharmacodynamic effect has returned to baseline (for biologics), whichever is longer.
5. Significant bleeding risk or coagulation disorders.
6. History of gastrointestinal bleeding.
7. Requirement for anti-platelet (except for acetylsalicylic acid up to 100 mg/d or clopidogrel up to 75 mg/d) or anti-coagulant medication.
8. History or current hepatic disease.
9. Evidence of clinically significant cardiovascular, neurological, psychiatric, pulmonary, renal, hepatic, endocrine, metabolic, hematological disorders, gastrointestinal disease or immunodeficiency that, in the Investigator's opinion, would compromise the safety of the participant, interfere with the interpretation of the study results or otherwise preclude participation or protocol adherence of the participant.
10. History of hypersensitivity to any of the study drug constituents.
11. Known or suspected infectious disease that is active, chronic or recurrent which precludes the participant from participating in the trial as per investigator's assessment. These infectious diseases include and are not limited to opportunistic infections (e.g., tuberculosis, atypical mycobacterioses, listeriosis or aspergillosis) and/or known or suspected Human Immunodeficiency Virus (HIV) infection. Should it be required by local regulations and/or considered appropriate by the investigator, an HIV test can be performed to confirm eligibility.
12. History of live attenuated vaccine administration within 6 weeks prior to randomization or requirement to receive these vaccinations at any time while on study treatment.
13. Major surgery within 8 weeks prior to screening or planned surgery for the duration of the study.
Minimum Eligible Age

12 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Medical Dermatology Specialists

Phoenix, Arizona, United States

Site Status RECRUITING

Johnson Dermatology

Fort Smith, Arkansas, United States

Site Status RECRUITING

Arkansas Research Trials

North Little Rock, Arkansas, United States

Site Status RECRUITING

Cheryl Effron MD Inc

Anaheim, California, United States

Site Status RECRUITING

Physioseq

Sacramento, California, United States

Site Status RECRUITING

Olive View UCLA Medical Center

Sylmar, California, United States

Site Status RECRUITING

Clinical Trials Research Institute

Thousand Oaks, California, United States

Site Status RECRUITING

Howard University College of Medicine

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Florida Academic Centers Research and Education LLC

Coral Gables, Florida, United States

Site Status RECRUITING

University of MiamiHealth System

Miami, Florida, United States

Site Status RECRUITING

Ziaderm Research LLC

North Miami Beach, Florida, United States

Site Status RECRUITING

Revival Research Institute LLC

Evans, Georgia, United States

Site Status RECRUITING

Gwinnett Clinical Research Center

Snellville, Georgia, United States

Site Status RECRUITING

Immunology-Rheumatology Research

Suwanee, Georgia, United States

Site Status RECRUITING

Illinois Dermatology Institute

Chicago, Illinois, United States

Site Status RECRUITING

Dawes Fretzin Clinical Rea Group

Indianapolis, Indiana, United States

Site Status RECRUITING

Equity Medical LLC

Bowling Green, Kentucky, United States

Site Status RECRUITING

Dermat. and Adv. Aesthetics

Lake Charles, Louisiana, United States

Site Status RECRUITING

Michigan Center for Rsrch Company

Clarkston, Michigan, United States

Site Status RECRUITING

Henry Ford Hospital

Detroit, Michigan, United States

Site Status RECRUITING

Revival Research Institute

Troy, Michigan, United States

Site Status RECRUITING

University of Mississippi Med Ctr

Jackson, Mississippi, United States

Site Status RECRUITING

Care Access Hoboken

Hoboken, New Jersey, United States

Site Status RECRUITING

Forest Hills Dermatology Group

New York, New York, United States

Site Status RECRUITING

Icahn School Of Med At Mount Sinai

New York, New York, United States

Site Status RECRUITING

Skinsearch of Rochester Inc

Rochester, New York, United States

Site Status RECRUITING

OnSite Clinical Solutions LLC

Huntersville, North Carolina, United States

Site Status RECRUITING

Wake Forest Baptist Health

Winston-Salem, North Carolina, United States

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Unity Clinical Research

Oklahoma City, Oklahoma, United States

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Essential Medical Research

Tulsa, Oklahoma, United States

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UP Medical Center H System

Pittsburgh, Pennsylvania, United States

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Medical University of South Carolina MUSC

Charleston, South Carolina, United States

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Advanced Research Experts

Nashville, Tennessee, United States

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Bellaire Dermatology Associates

Bellaire, Texas, United States

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RFSA Dermatology

San Antonio, Texas, United States

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Virginia Clinical Research

Norfolk, Virginia, United States

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Novartis Investigative Site

Caba, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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Rosario, Santa Fe Province, Argentina

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CABA, , Argentina

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Phillip, Australian Capital Territory, Australia

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Sydney, New South Wales, Australia

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Westmead, New South Wales, Australia

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Melbourne, Victoria, Australia

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Parkville, Victoria, Australia

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Sofia, Bulgaria, Bulgaria

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Stara Zagora, Bulgaria, Bulgaria

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Pleven, , Bulgaria

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Sofia, , Bulgaria

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Surrey, British Columbia, Canada

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St. John's, Newfoundland and Labrador, Canada

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Hamilton, Ontario, Canada

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Richmond Hill, Ontario, Canada

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Québec, Quebec, Canada

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Saint-Jérôme, Quebec, Canada

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Fuzhou, Fujian, China

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Guangzhou, Guangdong, China

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Wuhan, Hubei, China

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Changsha, Hunan, China

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Changchun, Jilin, China

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Shenyang, Liaoning, China

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Xian, Shanxi, China

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Chengdu, Sichuan, China

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Ürümqi, Xinjiang, China

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Ningbo, Zhejiang, China

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Beijing, , China

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Jinan, , China

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Barranquilla, Atlántico, Colombia

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Bogota, Cundinamarca, Colombia

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Cali, Valle del Cauca Department, Colombia

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Medellín, , Colombia

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Kobenhavn N V, , Denmark

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Roskilde, , Denmark

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Langenau, Baden-Wurttemberg, Germany

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Darmstadt, Hesse, Germany

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Dresden, Saxony, Germany

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Halle, Saxony-Anhalt, Germany

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Aachen, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bochum, , Germany

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Bonn, , Germany

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Erlangen, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Kiel, , Germany

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Mainz, , Germany

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Memmingen, , Germany

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Münster, , Germany

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Stade, , Germany

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Chaïdári, , Greece

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Heraklion Crete., , Greece

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Thessaloniki, , Greece

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Ancona, AN, Italy

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Brescia, BS, Italy

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Cona, FE, Italy

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Florence, FI, Italy

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Milan, MI, Italy

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Rozzano, MI, Italy

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Modena, MO, Italy

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Pisa, PI, Italy

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Roma, RM, Italy

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Torino, TO, Italy

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Muar town, Johor, Malaysia

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Kota Bharu, Kelantan, Malaysia

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George Town, Pulau Pinang, Malaysia

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Kuching, Sarawak, Malaysia

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Kuala Terengganu, Terengganu, Malaysia

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Kuala Lumpur, , Malaysia

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Guadalajara, Jalisco, Mexico

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Guadalajara, Jalisco, Mexico

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Cuauhtémoc, Mexico City, Mexico

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Chihuahua City, , Mexico

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Bydgoszcz, , Poland

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Gdansk, , Poland

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Lodz, , Poland

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Almada, , Portugal

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Braga, , Portugal

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Coimbra, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Bratislava, Slovakia, Slovakia

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Trnava, Slovakia, Slovakia

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Bratislava, , Slovakia

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Prešov, , Slovakia

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Raslouw Centurion, Gauteng, South Africa

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Soweto, Gauteng, South Africa

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Cape Town, , South Africa

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Durban, , South Africa

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Cadiz, Andalusia, Spain

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Badalona, Barcelona, Spain

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Sabadell, Barcelona, Spain

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Barcelona, Catalonia, Spain

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Manises, Valencia, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Valencia, , Spain

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Basel, , Switzerland

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Bern, , Switzerland

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Zurich, , Switzerland

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Kaohsiung City, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Countries

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United States Argentina Australia Bulgaria Canada China Colombia Denmark Germany Greece Italy Malaysia Mexico Poland Portugal Slovakia South Africa Spain Switzerland Taiwan

Central Contacts

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Novartis Pharmaceuticals

Role: CONTACT

1-888-669-6682

Novartis Pharmaceuticals

Role: CONTACT

+41613241111

Facility Contacts

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Nayeli Carreto

Role: primary

+1 602 354 5770

Christa Elliott

Role: primary

+1 479 649 3376

Shawna Owens

Role: primary

+1 501 621 1100

Kani Kubari

Role: primary

Carissa Garrity

Role: primary

Shaliz Aflatooni

Role: primary

Luke Park

Role: primary

+1 888 367 1850

Edward Bauer

Role: primary

+1 202 865 7272

Martha Gutierrez

Role: primary

+1 305 324 2110

Aliete Espinosa

Role: primary

+1 305 689 3376

Katelyn Louis

Role: primary

+1 305 652 8600

Chandana Janardhan

Role: primary

Colleen Ethridge

Role: primary

+1 770 972 2241

Jerry Wilkerson

Role: primary

Sahithi Gangavarapu

Role: primary

Joannie Prusa

Role: primary

+1 317 516 5030#102

Kristen Newman

Role: primary

Cindi Reed

Role: primary

+1 337 477 0011

Brianna Cole

Role: primary

+1 248 620 3376

Jennifer Creasor

Role: primary

+1 313 876 1850

Navya Kamath

Role: primary

Tekka Johnson

Role: primary

+1 601 815 5374

Sameer Verma

Role: primary

+1 201 800 1485

Tazrin Tripti

Role: primary

Vaishnavi Shreedhar

Role: primary

Angela Malizia

Role: primary

April Page

Role: primary

+1 800 785 3150

Leslie Moorefield

Role: primary

Charlotte Tinsley

Role: primary

+1 405 606 3900

Angela Swanson

Role: primary

+1 918 645 1992

Charity Ruhl

Role: primary

+1 412 647 2013

Rithi John Chandy

Role: primary

+1 843 792 9784

Diana Carrasquero

Role: primary

Hannah Green

Role: primary

+1 832 553 2308

Jonathan Joseph

Role: primary

Brandy Hartman

Role: primary

Other Identifiers

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2024-513282-39-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CLOU064J12301

Identifier Type: -

Identifier Source: org_study_id

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