Study of Circular RNA Treatment in Patients With Radiation Induced Xerostomia-1

NCT ID: NCT06714253

Last Updated: 2025-11-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

42 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-05

Study Completion Date

2027-08-31

Brief Summary

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This is a first-in-human clinical study to evaluate the safety, tolerability and efficacy of RXRG001 administered in the ducts of the parotid glands in adult patients with radiation-induced xerostomia (dry mouth) and hyposalivation (reduced saliva production).

In Part 1 of the study (open-label, single-arm), patients will receive unilateral administrations of RXRG001 in 3 single ascending dose cohorts and in 3 multiple ascending dose cohorts.

Part 2 of the study has a randomized, double-blind, placebo-controlled design. Patients will receive bilateral administrations of RXRG001 in 3 multiple ascending dose cohorts.

Detailed Description

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Conditions

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Radiation-Induced Xerostomia and Hyposalivation

Keywords

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Radiation Induced Xerostomia First-in-human Hyposalivation Circular ribonucleic acid Aquaporin 1

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Part 1 (Phase 1): single-arm, open-label Part 2 (Phase 2): randomized, double-blind, placebo-controlled, parallel-group
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Part 1 (Phase 1): single-arm open-label Part 2 (Phase2): randomized, double-blind, placebo-controlled, parallel-group

Study Groups

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RXRG001 Part 1

Open-label, single arm with 6 subsequent dose cohorts (3 single dose and 3 multiple dose cohorts) of RXRG001 administered intraductally in the salivary gland (unilateral)

Group Type EXPERIMENTAL

RXRG001

Intervention Type BIOLOGICAL

Circular ribonucleic acid encoding human aquaporin 1 encapsulated in a lipid nanoparticle

RXRG001 Part 2

Randomized double-blind with 3 subsequent multiple dose cohorts. RXRG001 is administered intraductally in the salivary gland (bilateral)

Group Type EXPERIMENTAL

RXRG001

Intervention Type BIOLOGICAL

Circular ribonucleic acid encoding human aquaporin 1 encapsulated in a lipid nanoparticle

Placebo Part 2

Randomized double-blind with 3 subsequent multiple dose cohorts. Placebo is administered intraductally in the salivary gland (bilateral)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Placebo (saline)

Interventions

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RXRG001

Circular ribonucleic acid encoding human aquaporin 1 encapsulated in a lipid nanoparticle

Intervention Type BIOLOGICAL

Placebo

Placebo (saline)

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

1. At least 18 years of age
2. History of radiation treatment or chemoradiotherapy for head and neck cancer for stage 2 or higher
3. Free from recurrence of your cancer and never have had another form of cancer for at least 2 years
4. Suffering from xerostomia and/or hyposalivation and have xerostomia symptoms which were not resolved after treatment for at least 3 months
5. Both parotid glands on imaging examination

Exclusion Criteria

1. Any active infection
2. Heart failure, reduced kidney function or uncontrolled diabetes (Hemoglobin A1c \>=8%)
3. History of autoimmune diseases known to potentially affect the salivary glands
4. Any malignancy, other than head and neck cancer within the past 3 years except for certain skin and cervical cancers
5. Active smoker or use tobacco products or have a history of substance or alcohol abuse

* Other criteria apply
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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RiboX Therapeutics Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status RECRUITING

John Hopkins University, Sidney Kimmel Comprehensive Cancer Center

Baltimore, Maryland, United States

Site Status RECRUITING

NYU Langone Medical Center

New York, New York, United States

Site Status RECRUITING

Penn Medicine - Otorhinolaryngology - Head and Neck Surgery Perelman

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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RiboX Therapeutics Ltd.

Role: CONTACT

Phone: 609 212 2832

Email: [email protected]

Facility Contacts

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Principal Investigator

Role: primary

Principal Investigator

Role: primary

Principal Investigator

Role: primary

Principal Investigator

Role: primary

Other Identifiers

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RX-RIX-CS101

Identifier Type: -

Identifier Source: org_study_id