Patient Interview Study to Explore the Impact of Gene Therapy in Hemophilia A & B

NCT ID: NCT06634836

Last Updated: 2025-08-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

WITHDRAWN

Study Classification

OBSERVATIONAL

Study Start Date

2025-03-17

Study Completion Date

2025-12-31

Brief Summary

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The purpose of this study is to learn about experiences of patients with hemophilia A and B after taking gene therapy. The experiences of patients will be studied through online interviews.

This study is seeking participants who are:

* part of the Pfizer's gene therapy clinical studies or
* in the long-term follow up for these clinical programs. Participants will have one study visit at the clinic and one online interview. The planned duration for each participant will be 1 to 2 months. This covers the time from entering the study to end of the online interview.

Detailed Description

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Conditions

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Hemophilia A Hemophilia B

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Study Groups

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Hemophilia A and Hemophilia B patients

Patients who are participating in the Pfizer's gene therapy clinical trials for Hemophilia A or Hemophilia B or are in the long-term follow up for these clinical programs

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Participation in the Pfizer's gene therapy clinical trials for Hemophilia A or B .
* Participants will be one year or more post-gene therapy
* Participants will be willing to provide written consent and will be willing to comply with the study requirements
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Other Identifiers

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NCT06634836

Identifier Type: REGISTRY

Identifier Source: secondary_id

C3731011

Identifier Type: -

Identifier Source: org_study_id

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