A Study to Test Whether Spesolimab Helps People With a Skin Condition Called Pyoderma Gangrenosum

NCT ID: NCT06624670

Last Updated: 2025-11-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-02-04

Study Completion Date

2028-02-01

Brief Summary

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The purpose of this study is to find out whether a medicine called spesolimab helps people with pyoderma gangrenosum (PG). The main aim is to see whether spesolimab leads to closure of PG ulcers. This study is open to adults with ulcerative PG with at least 1 ulcer that measures between 5 cm\^2 to 80 cm\^2 in size.

This study has 2 parts. In Part 1, participants are put into groups randomly, which means by chance. 1 group gets spesolimab and the other group gets placebo. Placebo injections look like spesolimab injections, but do not contain any medicine. Every participant has a 2 in 3 chance of getting spesolimab. For the first 8 weeks, participants also take corticosteroid medicine by mouth.

In Part 2, participants are put into groups again. Participants without open ulcers have an equal chance of getting spesolimab or placebo. Participants with open skin ulcers will get spesolimab.

In both parts, participants receive spesolimab or placebo as an infusion into a vein every 4 weeks.

Participants are in the study for about 1.5 years. During this time, they visit the study site 20 times. At study visits, doctors check the participant's skin for signs of PG. The doctors also regularly check participants' health and take note of any unwanted effects. The results of the groups are compared to see whether the treatment works.

Detailed Description

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Conditions

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Pyoderma Gangrenosum

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Spesolimab

Group Type EXPERIMENTAL

Spesolimab

Intervention Type DRUG

Solution for infusion

Prednisone

Intervention Type DRUG

Prednisone

Prednisolone

Intervention Type DRUG

Prednisolone

Placebo

Group Type PLACEBO_COMPARATOR

Placebo matching to spesolimab

Intervention Type DRUG

Placebo matching to spesolimab

Prednisone

Intervention Type DRUG

Prednisone

Prednisolone

Intervention Type DRUG

Prednisolone

Interventions

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Spesolimab

Solution for infusion

Intervention Type DRUG

Placebo matching to spesolimab

Placebo matching to spesolimab

Intervention Type DRUG

Prednisone

Prednisone

Intervention Type DRUG

Prednisolone

Prednisolone

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Adult trial participants, aged ≥18 years (if local legislation for age of consent differs, then local legislation will be followed) at screening.
2. Signed and dated written informed consent in accordance with International Council on Harmonisation-Good Clinical Practice (ICH-GCP) and local legislation prior to admission to the trial.
3. A confirmed diagnosis of ulcerative pyoderma gangrenosum (PG) (≥10 points on the PARACELSUS score) that requires systemic therapy in the opinion of the investigator. The diagnosis needs to be confirmed by an Adjudication Committee. Trial participants with mixed PG subtypes are eligible as long as the target lesion is of the ulcerative subtype.
4. At least one measurable (defined as measuring ≥5 cm\^2) PG ulcer. In trial participants with more than one PG ulcer, the target PG ulcer will be selected by the investigator and confirmed by external Adjudication Committee.
5. At the time of the Screening Visit, a maximum duration of 6 months since the target ulcer in the current PG episode was diagnosed. Target ulcers \>6 months since diagnosis are allowed if they are active and progressing, as judged by the investigator and confirmed by an Adjudication Committee.
6. Women of childbearing potential (WOCBP) must be ready and able to use highly effective methods of birth control per ICH M3 (R2) that result in a low failure rate of less than 1% per year when used consistently and correctly. A list of contraception methods meeting these criteria and instructions on the duration of use is provided in the participant information and in the protocol.

Exclusion Criteria

1. Trial participants with non-PG lesions.
2. Trial participants with a target PG ulcer measuring \>80 cm\^2.
3. Trial participants with chronic, non-inflamed PG wounds or ulcers that are not responsive to immunosuppressive therapy, as determined by an Adjudication Committee.
4. Presence of active ulcer infection at the Screening Visit (unless treated and resolved prior to administration of the first dose of trial medication) based on investigator assessment.
5. Presence of persistent or recurring bacterial infection requiring systemic antibiotic therapy; or clinically significant viral, fungal, or parasitic infections within 2 weeks prior to the Screening Visit. Any such infection must be resolved, with treatment completed ≥2 weeks prior to the Screening Visit. No new/recurrent infections should have occurred prior to Visit 2.
6. "Active or latent tuberculosis (TB)

* Participants with active TB are excluded
* Participants with latent TB may be included if treatment of latent TB, as per local guidelines, is initiated prior to randomization and completed during the course of the trial."
7. Chronic or acute infections including Human immunodeficiency virus (HIV) infections and viral hepatitis (including occult hepatitis); the corresponding laboratory tests will be performed during screening. A trial participant can be re-screened if the trial participant was treated and is cured from the acute infection.
8. Severe, progressive, or uncontrolled hepatic disease, defined as \>3x Upper Limit of Normal (ULN) elevation in Aspartate aminotransferase (AST) or Alanine aminotransferase (ALT) or alkaline phosphatase, or \>2x ULN elevation in total bilirubin.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Boehringer Ingelheim

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status RECRUITING

Medical Dermatology Specialists Phoenix

Phoenix, Arizona, United States

Site Status NOT_YET_RECRUITING

University of California Irvine

Irvine, California, United States

Site Status NOT_YET_RECRUITING

University of Miami

Miami, Florida, United States

Site Status RECRUITING

University of South Florida

Tampa, Florida, United States

Site Status RECRUITING

Dawes Fretzin Clinical Research Group, LLC-Indianapolis -68995

Indianapolis, Indiana, United States

Site Status RECRUITING

Tulane University Hospital and Clinic

New Orleans, Louisiana, United States

Site Status NOT_YET_RECRUITING

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status NOT_YET_RECRUITING

University of Michigan Health System

Ann Arbor, Michigan, United States

Site Status RECRUITING

Dartmouth Hitchcock Clinics Heater Road

Lebanon, New Hampshire, United States

Site Status NOT_YET_RECRUITING

Dermatology at Lake Success

Lake Success, New York, United States

Site Status RECRUITING

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status NOT_YET_RECRUITING

Red River Research Partners, LLC

Fargo, North Dakota, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status NOT_YET_RECRUITING

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

Site Status RECRUITING

Oregon Health and Sciences University

Portland, Oregon, United States

Site Status NOT_YET_RECRUITING

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status NOT_YET_RECRUITING

Epiphany Dermatology

Lewisville, Texas, United States

Site Status RECRUITING

CIPREC

CABA, , Argentina

Site Status COMPLETED

Hospital Italiano de Buenos Aires

CABA, , Argentina

Site Status COMPLETED

Instituto de Especialidades de la Salud Rosario

Rosario, , Argentina

Site Status COMPLETED

Skin and Cancer Foundation

Darlinghurst, New South Wales, Australia

Site Status RECRUITING

Royal North Shore Hospital-St Leonards-20807

St Leonards, New South Wales, Australia

Site Status RECRUITING

Alfred Hospital

Melbourne, Victoria, Australia

Site Status RECRUITING

Medical University of Graz State Hospital - University Hospital Graz

Graz, , Austria

Site Status NOT_YET_RECRUITING

LKH Salzburg University Hospital

Salzburg, , Austria

Site Status RECRUITING

UZ Leuven

Leuven, , Belgium

Site Status RECRUITING

Chronos Pesquisa Clinica

Brasília, , Brazil

Site Status RECRUITING

Faculdade de Medicina do ABC

Santo André, , Brazil

Site Status NOT_YET_RECRUITING

Rejuvenation Dermatology Clinic

Edmonton, Alberta, Canada

Site Status RECRUITING

University of Alberta Hospital (University of Alberta)

Edmonton, Alberta, Canada

Site Status NOT_YET_RECRUITING

Women's College Hospital

Toronto, Ontario, Canada

Site Status RECRUITING

McGill University Health Centre (MUHC)

Montreal, Quebec, Canada

Site Status NOT_YET_RECRUITING

Centre de Recherche Saint-Louis

Québec, , Canada

Site Status NOT_YET_RECRUITING

Peking University People's Hospital

Beijing, , China

Site Status RECRUITING

Peking University Third Hospital

Beijing, , China

Site Status RECRUITING

The First Hospital of Jilin University

Changchun, , China

Site Status RECRUITING

The Second Xiangya Hospital Of Central South University

Changsha, , China

Site Status RECRUITING

West China Hospital of Sichuan University

Chengdu, , China

Site Status RECRUITING

The First Affiliated Hospital, Zhejiang University

Hangzhou, , China

Site Status NOT_YET_RECRUITING

The Second Affiliated Hospital Zhejiang University School of Medicine

Hangzhou, , China

Site Status RECRUITING

Hangzhou Third People's Hospital

Hangzhou, , China

Site Status NOT_YET_RECRUITING

Shandong Provincial Hospital of Dermatology

Jinan, , China

Site Status RECRUITING

Shanghai Skin Disease Hospital

Shanghai, , China

Site Status RECRUITING

The University of Hong Kong-Shenzhen Hospital

Shenzhen, , China

Site Status RECRUITING

Wuhan Union Hospital

Wuhan, , China

Site Status NOT_YET_RECRUITING

Second Affiliated Hospital of Xi'an JiaoTong University

Xi'an, , China

Site Status RECRUITING

HUS Tulehduskeskus /Ihosairauksien linja

Helsinki, , Finland

Site Status NOT_YET_RECRUITING

HOP Privé Antony

Antony, , France

Site Status RECRUITING

HOP l'Archet

Nice, , France

Site Status NOT_YET_RECRUITING

HOP Saint-Louis

Paris, , France

Site Status NOT_YET_RECRUITING

Charite Universitätsmedizin Berlin KöR

Berlin, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum Erlangen

Erlangen, , Germany

Site Status RECRUITING

Universitätsklinikum Essen AöR

Essen, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum Würzburg AÖR

Würzburg, , Germany

Site Status NOT_YET_RECRUITING

Fondazione IRCCS Ca'Granda-Ospedale Maggiore Policlinico

Milan, , Italy

Site Status NOT_YET_RECRUITING

Azienda Ospedaliera Universitaria Pisana

Pisa, , Italy

Site Status RECRUITING

Istituti Fisioterapici Ospitalieri

Roma, , Italy

Site Status RECRUITING

AOU Policlinico Umberto I

Roma, , Italy

Site Status NOT_YET_RECRUITING

Fondazione Policlinico Universitario A. Gemelli IRCCS

Roma, , Italy

Site Status NOT_YET_RECRUITING

Istituto Clinico Humanitas

Rozzano (MI), , Italy

Site Status NOT_YET_RECRUITING

AO Città della Salute e Scienza

Torino, , Italy

Site Status NOT_YET_RECRUITING

Fujita Health University Hospital

Aichi, Toyoake, , Japan

Site Status NOT_YET_RECRUITING

Hokkaido University Hospital

Hokkaido, Sapporo, , Japan

Site Status NOT_YET_RECRUITING

Hyogo College of Medicine Hospital

Hyogo, Nishinomiya, , Japan

Site Status NOT_YET_RECRUITING

Mie University Hospital

Mie, Tsu, , Japan

Site Status RECRUITING

Tohoku University Hospital

Miyagi, Sendai, , Japan

Site Status NOT_YET_RECRUITING

Jichi Medical University Hospital

Tochigi, Shimotsuke, , Japan

Site Status RECRUITING

Teikyo University Hospital

Tokyo, Itabashi-ku, , Japan

Site Status RECRUITING

Nihon University Itabashi Hospital

Tokyo, Itabashi-ku, , Japan

Site Status RECRUITING

Hospital Raja Permaisuri Bainun

Ipoh, , Malaysia

Site Status RECRUITING

Sarawak General Hospital

Kuching, , Malaysia

Site Status NOT_YET_RECRUITING

Hospital Pulau Pinang-Pulau Pinang-21953

Pulau Pinang, , Malaysia

Site Status RECRUITING

Oslo Universitetssykehus HF, Rikshospitalet

Oslo, , Norway

Site Status RECRUITING

Helse Stavanger, Stavanger Universitetssykehus

Stavanger, , Norway

Site Status RECRUITING

Military Medical Institute- National Research Institute

Warsaw, , Poland

Site Status RECRUITING

Cityclinic Medical and Psychological Clinic Matusiak Partnership

Wroclaw, , Poland

Site Status RECRUITING

ULS de Coimbra, E.P.E.

Coimbra, , Portugal

Site Status NOT_YET_RECRUITING

ULS de São José, E.P.E. - Hospital Sto. António Capuchos

Lisbon, , Portugal

Site Status NOT_YET_RECRUITING

ULS de Santa Maria, E.P.E

Lisbon, , Portugal

Site Status RECRUITING

ULS de Santo Antônio, E.P.E - Centro Hospitalar Universitário de Santo António

Porto, , Portugal

Site Status NOT_YET_RECRUITING

Hospital Universitario Ramon Y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Virgen de la Victoria

Málaga, , Spain

Site Status RECRUITING

Karolinska Universitetssjukhuset Solna

Stockholm, , Sweden

Site Status RECRUITING

University Hospital Zurich

Zurich, , Switzerland

Site Status NOT_YET_RECRUITING

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status RECRUITING

Chang Gung Medical Foundation (CGMF) - Linkou Bran

Linkou District, , Taiwan

Site Status RECRUITING

National Taiwan University Hospital

Taipei, , Taiwan

Site Status NOT_YET_RECRUITING

Countries

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Hungary Puerto Rico United States Argentina Australia Austria Belgium Brazil Canada China Finland France Germany Italy Japan Malaysia Norway Poland Portugal Spain Sweden Switzerland Taiwan

Central Contacts

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Boehringer Ingelheim

Role: CONTACT

Phone: 1-800-243-0127

Email: [email protected]

Facility Contacts

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Boehringer Ingelheim

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Related Links

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Other Identifiers

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2024-514306-31-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1306-8055

Identifier Type: REGISTRY

Identifier Source: secondary_id

1368-0140

Identifier Type: -

Identifier Source: org_study_id