A Study of Ranolazine in ALS

NCT ID: NCT06527222

Last Updated: 2025-10-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

72 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-04-29

Study Completion Date

2026-05-31

Brief Summary

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The purpose of this study is to evaluate safety, effect on cramps, function and quality of life of ranolazine versus placebo for the treatment of ALS.

Detailed Description

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A prospective, multi center, double-blind, placebo-controlled, parallel group study of 2 doses of ranolazine (500 mg and 1000 mg twice daily) compared to placebo in patients with ALS.

Approximately 72 adults with ALS will be enrolled into the study in the United States at approximately 7 ALS treatment sites.

Participants will take oral ranolazine or placebo twice daily, attend a minimum of 5 onsite research visits, and 4 remote research visits.

The study is estimated to last 28 weeks for each participant.

Conditions

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Amyotrophic Lateral Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ranolazine low dose

Participants receive Ranolazine 500mg orally twice daily for 24 weeks.

Group Type EXPERIMENTAL

Ranolazine

Intervention Type DRUG

500mg twice daily

Ranolazine high dose

Participants receive Ranolazine 1000mg orally twice daily for 24 weeks.

Group Type EXPERIMENTAL

Ranolazine

Intervention Type DRUG

1000 mg twice daily

Placebo

Participants receive Ranolazine placebo orally twice daily for 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Ranolazine placebo twice daily

Interventions

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Ranolazine

500mg twice daily

Intervention Type DRUG

Ranolazine

1000 mg twice daily

Intervention Type DRUG

Placebo

Ranolazine placebo twice daily

Intervention Type DRUG

Other Intervention Names

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Ranexa Ranexa

Eligibility Criteria

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Inclusion Criteria

* 18 years or older
* Diagnosed with clinically definite, possible, probably, or lab-supported probable ALS per revised El Escorial criteria
* Breathing assessment called forced vital capacity (FVC) greater than or equal to 50%.
* Able to swallow pills at the start of the study and expected to for the length of the study.
* If on ALS modifying medications must be on a stable dose at least 30 days.
* Experiencing 4 or more cramps per week during a 2-week screening period.

Exclusion Criteria

* Disease duration \< 5 years
* Tracheostomy invasive ventilation, or noninvasive ventilation of more than 12 hours/day
* Pregnant or lactating, adults unable to consent, and prisoners
* Taking ranolazine or investigational drug or has received an investigational drug within 30 days (or 5 half-lives for drugs, whichever is longer) prior to screening
* Medically uncontrolled comorbidities (heart, liver, kidney disease)
* Baseline QTc interval prolongation \>450 ms for men/ \>470 ms for women, history of long QT syndrome, or medications which prolong the QT interval
* Participation in an experimental drug trial less than 30 days before screening
* Patients have to be on a stable dosage of any medications used to treat muscle cramps for ≥30 days or have been off these medications ≥30 days prior to randomization.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ALS Association

OTHER

Sponsor Role collaborator

Swathy Chandrashekhar, MBBS

OTHER

Sponsor Role lead

Responsible Party

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Swathy Chandrashekhar, MBBS

Principal Investigator

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Jeffrey Statland, MD

Role: PRINCIPAL_INVESTIGATOR

University of Kansas Medical Center

Locations

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University of California, San Francisco

San Francisco, California, United States

Site Status RECRUITING

Mayo Clinic Florida

Jacksonville, Florida, United States

Site Status RECRUITING

University of Kansas Medical Center

Fairway, Kansas, United States

Site Status RECRUITING

University of Kansas Medical Center: Wichita

Wichita, Kansas, United States

Site Status RECRUITING

University of Missouri Health Care

Columbia, Missouri, United States

Site Status RECRUITING

The Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

National Neuromuscular Research Institute, PLLC.

Austin, Texas, United States

Site Status NOT_YET_RECRUITING

Countries

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United States

Central Contacts

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Katie Lillig, BS

Role: CONTACT

913-945-9932

Facility Contacts

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Abby Straight

Role: primary

415-353-2981

Role: backup

Huy B. Tran

Role: primary

904-953-4503

Nick Staudenmier, BS

Role: primary

913-945-9922

Katie Lillig, BS

Role: backup

913-945-9932

KUMC CTSU Wichita

Role: primary

316-293-1833

Hannah Hancock

Role: backup

Amanda Heider

Role: primary

573-884-6852

Atchayah Balakrishna

Role: primary

Kaneshia Hives

Role: backup

Emil Hussain

Role: primary

Other Identifiers

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24-43175

Identifier Type: -

Identifier Source: org_study_id

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