Trial of Nadofaragene Firadenovec vs. Observation in Participants With Intermediate Risk Non-Muscle Invasive Bladder Cancer

NCT ID: NCT06510374

Last Updated: 2026-02-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

454 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-01

Study Completion Date

2031-06-30

Brief Summary

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A phase 3b, Randomized, Controlled Trial of Nadofaragene Firadenovec vs. Observation in Participants with Intermediate Risk Non-Muscle Invasive Bladder Cancer (IR NMIBC)

Detailed Description

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Conditions

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Intermediate Risk Non-Muscle Invasive Bladder Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm 1 Nadofaragene Firadenovec

Participants in the nadofaragene firadenovec arm will receive quarterly instillations with nadofaragene firadenovec for 24 months. For these subjects, the disease evaluation visits will occur within 2 weeks prior to the investigation medicinal products instillation visits.

Group Type EXPERIMENTAL

Nadofaragene Firadenovec

Intervention Type DRUG

Vector-based gene therapy for NMIBC treatment to potentiate durable therapeutic responses by interferon (IFN) alfa-2b (IFN-α2b) amplification.

Arm 2 - Observation

Subjects will be followed based on the surveillance schedule of the AUA/SUO guideline (quarterly) over the 24 months treatment period.

.

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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Nadofaragene Firadenovec

Vector-based gene therapy for NMIBC treatment to potentiate durable therapeutic responses by interferon (IFN) alfa-2b (IFN-α2b) amplification.

Intervention Type DRUG

Other Intervention Names

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Adstiladrin

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with intermediate risk non-muscle invasive bladder cancer (IR NMIBC) as defined by American Urological Association (AUA)/Society of Urologic Oncology \[SUO\] Guideline (2020)
* Has undergone adequate transurethral resection of bladder tumor (TURBT; with or without peri-operative chemotherapy) within 60 days prior to randomization:

* Recurrence within 1 year, low-grade Ta
* Solitary low-grade Ta \>3 cm
* Low-grade Ta, multifocal
* Solitary high-grade Ta, ≤3 cm
* Low-grade T1

* Restage TURBT may be done at the discretion of the investigator

Exclusion Criteria

* Current or previous evidence of muscle invasive (muscularis propria) or metastatic disease presented at the screening visit

High risk NMIBC defined as:

* High-grade T1
* Any recurrent, high-grade Ta
* High-grade Ta \>3 cm (or multifocal)
* Any carcinoma in situ (CIS)
* Any Bacillus Calmette-Guérin (BCG) failure in high-grade subject
* Any variant histology
* Any prostatic urethral involvement

Low risk NMIBC defined as:

* First occurrence of low-grade solitary Ta ≤3 cm
* Recurrence of low-grade solitary Ta ≤3 cm \>12 months from previous occurrence
* Papillary urothelial neoplasm of low malignant potential
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ferring Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Global Clinical Compliance

Role: STUDY_DIRECTOR

Ferring Pharmaceutical

Locations

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University of South Alabama (USA) Health System - USACM

Mobile, Alabama, United States

Site Status RECRUITING

Urology Associates of Mobile

Mobile, Alabama, United States

Site Status RECRUITING

Mayo Clinic Arizona

Phoenix, Arizona, United States

Site Status RECRUITING

Urology Associates of Central California

Fresno, California, United States

Site Status RECRUITING

American Institute of Research

Los Angeles, California, United States

Site Status RECRUITING

Urology Center of Southern California

Murrieta, California, United States

Site Status RECRUITING

University of California, Irvine

Orange, California, United States

Site Status RECRUITING

Advent Health

Denver, Colorado, United States

Site Status RECRUITING

Medstar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Mayo Clinic

Jacksonville, Florida, United States

Site Status RECRUITING

Advanced Urology institute - Pinellas

Largo, Florida, United States

Site Status RECRUITING

Sarasota Memorial Healthcare System

Sarasota, Florida, United States

Site Status RECRUITING

Emory University

Atlanta, Georgia, United States

Site Status RECRUITING

Blessing Health System

Quincy, Illinois, United States

Site Status RECRUITING

Wichita Urology Group

Wichita, Kansas, United States

Site Status RECRUITING

University of Kentucky (UK) - Markey Cancer Center

Lexington, Kentucky, United States

Site Status RECRUITING

Mayo Clinic - Rochester Minnesota

Rochester, Minnesota, United States

Site Status RECRUITING

Specialty Clinical Research of St. Louis

St Louis, Missouri, United States

Site Status RECRUITING

Adult and Pediatric Urology P.C.

Omaha, Nebraska, United States

Site Status RECRUITING

Atlantic Health

Morristown, New Jersey, United States

Site Status RECRUITING

Albany Medical College

Albany, New York, United States

Site Status RECRUITING

Great Lakes Physician PC d/b/a Western New York Urology Associates

Cheektowaga, New York, United States

Site Status RECRUITING

AccuMed Research Associates

Garden City, New York, United States

Site Status RECRUITING

Northwell Health -The Arthur Smith Institute for Urology

Lake Success, New York, United States

Site Status RECRUITING

Veterans Affairs New York Harbor Healthcare System - Manhattan VA Medical Center

New York, New York, United States

Site Status RECRUITING

Integrated Medical Professionals, PLLC

New York, New York, United States

Site Status RECRUITING

James J. Peters VA Medical Center

The Bronx, New York, United States

Site Status RECRUITING

University of Cincinnati

Cincinnati, Ohio, United States

Site Status RECRUITING

Oregon Health and Science University (Portland)

Portland, Oregon, United States

Site Status RECRUITING

MidLantic Urology

Bala-Cynwyd, Pennsylvania, United States

Site Status RECRUITING

Keystone Urology Specialists

Lancaster, Pennsylvania, United States

Site Status RECRUITING

University of Pennsylvania - Perelman Center for Advanced Medicine - Penn Urology

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Carolina Urologic Research Center

Myrtle Beach, South Carolina, United States

Site Status RECRUITING

Urology Clinics of North Texas PLLC (Dallas)

Dallas, Texas, United States

Site Status RECRUITING

Houston Methodist Hospital (Houston)

Houston, Texas, United States

Site Status RECRUITING

Urology of Virginia

Virginia Beach, Virginia, United States

Site Status RECRUITING

Prostate Cancer Centre

Calgary, Alberta, Canada

Site Status RECRUITING

G kenneth Jansz Medicine Professional Corporation

Burlington, Ontario, Canada

Site Status RECRUITING

CHU Clermont Ferrand - Hopital Gabriel Montpied

Clermont-Ferrand, Auvergne-Rhône-Alpes, France

Site Status RECRUITING

CHU Toulouse - Hopital Rangueil

Toulouse, Haute-Garonne, France

Site Status RECRUITING

CHU Nantes - Hotel Dieu

Nantes, Nantes, France

Site Status RECRUITING

CHU de Rouen - Hopital Charles-Nicolle

Rouen, Normandy, France

Site Status RECRUITING

CHU de Bordeaux - Hôpital Pellegrin

Bordeaux, Nouvelle-Aquitaine, France

Site Status RECRUITING

Centre Hospitalier Universitaire De Nimes (Nîmes)

Nîmes, Occitanie, France

Site Status RECRUITING

Hospices Civils de Lyon - Edouard Herriot Hosp.

Lyon, Rhône-Alps, France

Site Status RECRUITING

Hopital La Pitie Salpetriere

Paris, , France

Site Status RECRUITING

APHP - Hopital Bichat

Paris, Île-de-France Region, France

Site Status RECRUITING

Aichi Medical University Hospital

Nagakute, Aichi-ken, Japan

Site Status RECRUITING

Nagoya University Hospital

Nagoya, Aichi-ken, Japan

Site Status RECRUITING

Japanese Red Cross Narita Hospital

Narita, Chiba, Japan

Site Status RECRUITING

National Hospital Organization Shikoku Cancer Center

Matsuyama, Ehime, Japan

Site Status RECRUITING

Kyushu University Hospital

Fukuoka, Fukuoka, Japan

Site Status RECRUITING

Hiroshima University Hospital

Hiroshima, Hiroshima, Japan

Site Status RECRUITING

Hitachi General Hospital

Hitachi, Ibaraki, Japan

Site Status RECRUITING

University of Tsukuba Hospital

Tsukuba, Ibaraki, Japan

Site Status RECRUITING

St. Marianna University Hospital

Kawasaki, Kanagawa, Japan

Site Status RECRUITING

Yokohama City University Hospital

Yokohama, Kanagawa, Japan

Site Status RECRUITING

Kochi Medical School Hospital

Nankoku, Kochi, Japan

Site Status RECRUITING

Mie University Hospital

Tsu, Mie-ken, Japan

Site Status RECRUITING

Nara Medical University Hospital

Kashihara, Nara, Japan

Site Status RECRUITING

Institute of Science Tokyo Hospital

Bunkyō-Ku, Tokyo, Japan

Site Status RECRUITING

Wakayama Medical University Hospital

Wakayama, Wakayama, Japan

Site Status RECRUITING

Samsung Medical Center

Seoul, Seoul, South Korea

Site Status RECRUITING

Instituto de Investigacion Valdecilla (IDIVAL) / Hospital universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status RECRUITING

Hospital del Mar

Barcelona, Catalonia, Spain

Site Status RECRUITING

Hospital Universitario Reina Sofia

Córdoba, Córdoba, Spain

Site Status RECRUITING

Hospital Universitario de A Coruna

A Coruña, Galicia, Spain

Site Status RECRUITING

Hospital Universitario Virgen De Las Nieves

Granada, Granada, Spain

Site Status RECRUITING

Hospital Universitario Basurto

Bilbao, Vizcaya, Spain

Site Status RECRUITING

Hospital Universitario 12 De Octubre (Madrid)

Madrid, , Spain

Site Status RECRUITING

Countries

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United States Canada France Japan South Korea Spain

Central Contacts

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Ferring Pharmaceuticals

Role: CONTACT

833-548-1402

Other Identifiers

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U1111-1284-0685

Identifier Type: OTHER

Identifier Source: secondary_id

000423

Identifier Type: -

Identifier Source: org_study_id

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