TB006 for Autism Spectrum Disorder

NCT ID: NCT06500637

Last Updated: 2024-08-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

45 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-08-03

Study Completion Date

2026-07-31

Brief Summary

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Multisite 14-week prospective double-blind placebo controlled parallel-group randomized clinical trial with 14-week open-label extension at the end of double-blind treatment phase for placebo subjects. Eligible subjects will be randomized within each site in 2:1 ratio to receive either TB006 or placebo treatment.

Detailed Description

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A key molecular mechanism implicated in ASD is immune dysregulation and unchecked neuroinflammation marked by increased microglial activation. Galectin-3 (Gal-3), a galactoside-binding lectin, is critical to activation of neuroinflammation resulting in the proliferation of microglia.7 Gal-3 has been shown to be elevated in individuals with ASD. To inhibit Gal-3's contribution to neuroinflammation, Truebinding has developed TB006, a neutralizing monoclonal antibody against Gal-3. Our overall hypothesis is that TB006 will significantly improve core and associated behavioral symptoms of ASD and be well tolerated with no significant adverse effects in adults with ASD.

Conditions

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Autism Spectrum Disorder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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TB006

TB006 is a humanized immunoglobulin G4 (IgG4) (S228P) type monoclonal antibody that is highly specific and has a high affinity to human Galectin-3 (hGal-3). Galectins are a ubiquitous group of proteins found in a variety of cells, tissues, and extravascular spaces, and are involved in numerous metabolic processes and functions. The galectins preferentially bind to β-galactoside derivatives and can cross-link surface glycoproteins by binding galactose residues. The Gal-3 protein plays an important role in different pathogenic conditions, including neurodegenerative and neuroinflammatory disorders. Serum levels of Gal-3 have been found to be elevated in ASD.

Group Type EXPERIMENTAL

TB006

Intervention Type DRUG

TB006 is a humanized immunoglobulin G4 (IgG4) (S228P) type monoclonal antibody that is highly specific and has a high affinity to human Galectin-3 (hGal-3).

Placebo

Identical IV solution without TB006 product

Group Type PLACEBO_COMPARATOR

TB006

Intervention Type DRUG

TB006 is a humanized immunoglobulin G4 (IgG4) (S228P) type monoclonal antibody that is highly specific and has a high affinity to human Galectin-3 (hGal-3).

Interventions

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TB006

TB006 is a humanized immunoglobulin G4 (IgG4) (S228P) type monoclonal antibody that is highly specific and has a high affinity to human Galectin-3 (hGal-3).

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Autism Spectrum Disorder as defined below by the ADOS or ADI-R.
2. Between 18 and 35 years of age at baseline.
3. English included in the languages in which the individual is being raised.
4. Autism severity of moderate or higher (≥4) under the 7-item clinical global impression-severity scale.
5. Ability to maintain all ongoing complementary, dietary, traditional, and behavioral treatments constant for the study period.
6. Unchanged complementary, dietary, traditional, and behavioral treatments for two months prior to study entry.
7. In males and females of childbearing age, two forms of birth control must be used unless they are not sexually active.
8. A caretaker who will accompany the patient to all procedures and has adequate contact with the participant to complete caregiver questionnaires.

Exclusion Criteria

1. LGALS3 rs4644 single nucleotide polymorphism with two copies of the Variant-type allele.
2. History of infusion reactions to immunoglobulin product.
3. Significant self-abusive or violent behavior or evidence of suicidal ideation, plan or behavior.
4. Severely affected as defined by CGI-Severity Standard Score = 7 (Extremely Ill).
5. Severe prematurity (\<34 weeks gestation) as determined by medical history.
6. Current uncontrolled gastroesophageal disorders.
7. Current or history of liver or kidney disease as determined by medical history and safety labs (See Laboratory Values Monitoring Plan for specific laboratory values).
8. Genetic syndromes.
9. Congenital brain malformations.
10. Active Epilepsy Diagnosis (Epilepsy Diagnosis is defined as History of two or more unprovoked seizures; Patient with a history of epilepsy who have been off medication without seizures for more than two years do not qualify as active epilepsy).
11. Any medical condition that the PI determines could jeopardize the safety of the study subject or compromise the integrity of the data.
12. Significant negative reaction (i.e., fainting, vomiting, etc.) because of a previous blood draw.
13. Failure to thrive or \< 5%ile for Body Mass Index or weight at the time of screening.
14. Concurrent treatment with drug that would significantly interact with the investigational product.
15. Allergy or Sensitivity to ingredients in the investigational product or placebo.
16. Evaluation with the NIH Toolbox or BOSCC within 3 months of entering the study.
17. Planned evaluation with the NIH Toolbox or BOSCC during the study.
18. Pregnancy
19. Current DSM-5 diagnosis requiring alternative pharmacotherapy, e.g., Major Depression, Bipolar Disorder, a psychotic disorder (based on clinical assessment assisted by the Child and Adolescent Symptom Inventory).
20. Refusal to comply with the use of birth control if sexually active.
21. Abnormal vital signs (systolic blood pressure \> 180 mmHg or \< 90 mmHg; heart rate \> 120 beats per minute or \< 55 beats per minute; temperature \> 101.0o F; oxygen saturation \< 90%)
22. Prolonged QTc (defined as \> 450ms for males and \>470ms for female) or any abnormalities felt by the investigator to be of concern.
Minimum Eligible Age

18 Years

Maximum Eligible Age

35 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Autism Discovery and Treatment Foundation

UNKNOWN

Sponsor Role collaborator

Rossignol Medical Center

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Richard E Frye, M.D., Ph.D

Role: STUDY_DIRECTOR

Rossignol Medical Center

Daniel A Rossignol, MD

Role: PRINCIPAL_INVESTIGATOR

Rossignol Medical Center

Locations

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Rossignol Medical Center

Phoenix, Arizona, United States

Site Status RECRUITING

Rossignol Medical Center

Aliso Viejo, California, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Alina Espinoza

Role: CONTACT

844-ADTF-Research ext. 0

Facility Contacts

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Richard E Frye, M.D., PhD

Role: primary

321-259-7111

Desiree Chandler, PA

Role: primary

321-259-7111

References

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Rodriguez JI, Kern JK. Evidence of microglial activation in autism and its possible role in brain underconnectivity. Neuron Glia Biol. 2011 May;7(2-4):205-13. doi: 10.1017/S1740925X12000142. Epub 2012 Jul 6.

Reference Type BACKGROUND
PMID: 22874006 (View on PubMed)

Garcia-Revilla J, Boza-Serrano A, Espinosa-Oliva AM, Soto MS, Deierborg T, Ruiz R, de Pablos RM, Burguillos MA, Venero JL. Galectin-3, a rising star in modulating microglia activation under conditions of neurodegeneration. Cell Death Dis. 2022 Jul 20;13(7):628. doi: 10.1038/s41419-022-05058-3.

Reference Type BACKGROUND
PMID: 35859075 (View on PubMed)

Wang X, Zhang S, Lin F, Chu W, Yue S. Elevated Galectin-3 Levels in the Serum of Patients With Alzheimer's Disease. Am J Alzheimers Dis Other Demen. 2015 Dec;30(8):729-32. doi: 10.1177/1533317513495107. Epub 2013 Jul 2.

Reference Type BACKGROUND
PMID: 23823143 (View on PubMed)

Artik A, Kocaman O, Kara H, Tuncer SC. Galectin-3 levels in school aged children with autism spectrum disorder. Int J Dev Disabil. 2022 Dec 1;69(5):757-761. doi: 10.1080/20473869.2022.2150035. eCollection 2023.

Reference Type BACKGROUND
PMID: 37547549 (View on PubMed)

Other Identifiers

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TB-RMC

Identifier Type: -

Identifier Source: org_study_id

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