Open-Label Safety, PK, and Efficacy Trial of Sebetralstat (KVD900) in Pediatric Patients (Ages 2-11) With HAE Type I or II

NCT ID: NCT06467084

Last Updated: 2026-01-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-06-24

Study Completion Date

2026-01-15

Brief Summary

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KVD900-303 is an open-label, multicenter clinical trial in patients aged 2 to 11 years old with HAE Type I or II.

Detailed Description

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Conditions

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Hereditary Angioedema

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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150 mg Dose Group

Patients will take a single 150 mg dose of KVD900.

Group Type OTHER

KVD900 150 mg

Intervention Type DRUG

KVD900 Tablet 150 mg (2 x 75 mg)

300 mg Dose Group

Patients will take a single 300 mg dose of KVD900.

Group Type OTHER

KVD900 300 mg

Intervention Type DRUG

KVD900 Tablet 300 mg (1 x 300 mg)

600 mg Dose Group

Patients will take a single 600 mg dose of KVD900.

Group Type OTHER

KVD900 600 mg

Intervention Type DRUG

KVD900 Tablet 600 mg (2 x 300 mg)

Interventions

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KVD900 150 mg

KVD900 Tablet 150 mg (2 x 75 mg)

Intervention Type DRUG

KVD900 300 mg

KVD900 Tablet 300 mg (1 x 300 mg)

Intervention Type DRUG

KVD900 600 mg

KVD900 Tablet 600 mg (2 x 300 mg)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male or female patients 2 to 11 years of age.
2. Confirmed diagnosis of HAE Type I or II.
3. For patients ≥20 kg at screening, patient has had at least 1 documented HAE attack in the last year prior to screening.
4. Caregiver, as assessed by the Investigator, must be able to appropriately store and administer IMP and be able to read, understand, and complete the diary.
5. Investigator believes that the patient and caregiver are willing and able to adhere to all protocol requirements.
6. Parent or Legally Authorized Representative (LAR) provides signed informed consent and patient provides assent (when applicable).

Exclusion Criteria

1. Any concomitant diagnosis of another form of chronic angioedema, such as acquired C1 inhibitor deficiency, HAE with normal C1-INH, idiopathic angioedema, or angioedema associated with urticaria.
2. A clinically significant history of poor response to bradykinin receptor 2 blocker, C1-INH therapy, or plasma kallikrein inhibitor therapy for the management of HAE, in the opinion of the Investigator.
3. Patient weighs \<9.5 kg.
4. Use of angiotensin-converting enzyme inhibitors after the Screening Visit.
5. Any estrogen-containing medications with systemic absorption (such as oral contraceptives including ethinylestradiol or hormonal replacement therapy) within 7 days prior to the Screening Visit.
6. Patients who require sustained use of strong cytochrome P450 3A4 (CYP3A4) inhibitors or inducers or moderate CYP3A4 inducers.
7. Any clinically significant comorbidity or systemic dysfunction, which in the opinion of the Investigator, would jeopardize the safety of the patient by participating in the trial.
8. Known hypersensitivity to sebetralstat or to any of the excipients.
9. Participation in any interventional investigational clinical trial within 4 weeks of the last dosing of investigational drug prior to the Screening Visit.
Minimum Eligible Age

2 Years

Maximum Eligible Age

11 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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KalVista Pharmaceuticals, Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

KalVista Pharmaceuticals, Ltd.

Locations

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KalVista Investigative Site

Birmingham, Alabama, United States

Site Status

KalVista Investigative Site

Scottsdale, Arizona, United States

Site Status

KalVista Investigative Site

San Diego, California, United States

Site Status

KalVista Investigative Site

Santa Monica, California, United States

Site Status

KalVista Investigative Site

Evansville, Indiana, United States

Site Status

KalVista Investigative Site

Wheaton, Maryland, United States

Site Status

KalVista Investigative Site

St Louis, Missouri, United States

Site Status

KalVista Investigative Site

Toledo, Ohio, United States

Site Status

KalVista Investigative Site

Hershey, Pennsylvania, United States

Site Status

KalVista Investigative Site

Dallas, Texas, United States

Site Status

KalVista Investigative Site

Edmonton, Alberta, Canada

Site Status

KalVista Investigative Site

Lille, , France

Site Status

KalVista Investigative Site

Marseille, , France

Site Status

KalVista Investigative Site

Paris, , France

Site Status

KalVista Investigative Site

Frankfurt am Main, , Germany

Site Status

KalVista Investigative Site

Frankfurt am Main, , Germany

Site Status

KalVista Investigative Site

Haifa, , Israel

Site Status

KalVista Investigative Site

Petah Tikva, , Israel

Site Status

KalVista Investigative Site

Tel Aviv, , Israel

Site Status

KalVista Investigative Site

Milan, , Italy

Site Status

KalVista Investigative Site

Padua, , Italy

Site Status

KalVista Investigative Site

Rome, , Italy

Site Status

KalVista Investigative Site

Kawagoe, , Japan

Site Status

KalVista Investigative Site

Tokyo, , Japan

Site Status

Countries

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United States Canada France Germany Israel Italy Japan

Other Identifiers

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KVD900-303

Identifier Type: -

Identifier Source: org_study_id

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