A Study Comparing the Efficacy and Safety of Zanidatamab to Trastuzumab, Each in Combination With Physician's Choice Chemotherapy, for the Treatment of Participants With Metastatic HER2-positive Breast Cancer

NCT ID: NCT06435429

Last Updated: 2025-12-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

550 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-08-13

Study Completion Date

2031-11-26

Brief Summary

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The efficacy and safety of zanidatamab in combination with physician's choice of chemotherapy compared with trastuzumab in combination with physician's choice of chemotherapy will be evaluated for the treatment of participants with metastatic HER2-positive breast cancer who have progressed on, or are intolerant to, previous T-DXd treatment.

Detailed Description

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Zanidatamab, as a monotherapy or in combination with other antineoplastic agents, has shown clinically meaningful efficacy against multiple HER2-positive advanced/metastatic tumors, including in patients with metastatic breast cancer (mBC). Zanidatamab may offer a viable treatment option for patients with metastatic HER2-positive breast cancer.

The primary objective of the study is to compare the efficacy of zanidatamab plus chemotherapy versus trastuzumab plus chemotherapy. The secondary objectives of the study will include further comparing the efficacy, safety and tolerability, patient-reported tolerability, and patient-reported physical functioning of zanidatamab plus chemotherapy versus trastuzumab plus chemotherapy. The pharmacokinetics and immunogenicity of zanidatamab in combination with chemotherapy will also be evaluated.

Conditions

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Metastatic HER2-positive Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Zanidatamab plus physician's choice of chemotherapy

Participants with HER2-positive metastatic breast cancer (mBC) who have progressed on, or are intolerant to, previous T-DXd treatment will be randomized to receive intravenous infusion of zanidatamab plus physician's choice of chemotherapy (eribulin, or vinorelbine, or gemcitabine, or capecitabine).

Group Type EXPERIMENTAL

Zanidatamab

Intervention Type DRUG

Administered by intravenous infusion

Eribulin

Intervention Type DRUG

Administered by intravenous infusion

Vinorelbine

Intervention Type DRUG

Administered by intravenous infusion

Gemcitabine

Intervention Type DRUG

Administered by intravenous infusion

Capecitabine

Intervention Type DRUG

Given orally

Trastuzumab plus physician's choice of chemotherapy

Participants with HER2-positive metastatic breast cancer (mBC) who have progressed on, or are intolerant to, previous T-DXd treatment will be randomized to receive intravenous infusion of trastuzumab plus physician's choice of chemotherapy (eribulin, or gemcitabine, or vinorelbine, or capecitabine).

Group Type ACTIVE_COMPARATOR

Trastuzumab

Intervention Type DRUG

Administered by intravenous infusion

Eribulin

Intervention Type DRUG

Administered by intravenous infusion

Vinorelbine

Intervention Type DRUG

Administered by intravenous infusion

Gemcitabine

Intervention Type DRUG

Administered by intravenous infusion

Capecitabine

Intervention Type DRUG

Given orally

Interventions

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Zanidatamab

Administered by intravenous infusion

Intervention Type DRUG

Trastuzumab

Administered by intravenous infusion

Intervention Type DRUG

Eribulin

Administered by intravenous infusion

Intervention Type DRUG

Vinorelbine

Administered by intravenous infusion

Intervention Type DRUG

Gemcitabine

Administered by intravenous infusion

Intervention Type DRUG

Capecitabine

Given orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Is 18 years of age or of the legal adult age per local standard at the time of signing the informed consent.
2. Has histologically confirmed HER2-positive breast cancer according to ASCO-CAP Guidelines as evaluated by a central laboratory
3. Participants with unresectable or metastatic HER2 positive breast cancer who have progressed on, or are intolerant to, previous T-DXd treatment.
4. Has measurable disease per RECIST version 1.1.
5. Is eligible to receive one of the chemotherapy options listed in the physician's choice of chemotherapy (eribulin, gemcitabine, vinorelbine, or capecitabine).
6. Participants with history of treated or clinically inactive CNS metastases are eligible as specified in the protocol.
7. Has a life expectancy of at least 6 months, in the opinion of the investigator.
8. Has adequate hematologic parameters as defined in the protocol.
9. Has adequate hepatic function as specified in the protocol.
10. Has creatinine clearance ≥ 30 mL/minute as calculated per local institutional guidelines.
11. Has LVEF ≥ 50% as determined by either echocardiogram or MUGA obtained within 4 weeks before the first dose of study intervention.
12. Has ECOG performance status of 0 or 1.
13. Participant agrees to the following based on sex assigned at birth.

1. Male participants:

Male participants are eligible to participate if they agree to the following during the study intervention period and for at least 5 months after the last dose of study intervention or the contraception period for the combination chemotherapy of choice per local guidance/standard practice, whichever is longer:
* Refrain from donating fresh unwashed semen.
* Use contraception as follows as specified in the protocol
2. Female participants:

* A female participant is eligible to participate if she is not pregnant or breastfeeding, and one of the following conditions applies:

* Is a women of nonchildbearing potential OR
* Is a woman of childbearing potential (WOCBP) and using a contraceptive method that is highly effective (with a failure rate of \< 1% per year), with low user dependency during the study intervention period and for at least 5 months after the last dose of study intervention or the contraception period for the combination chemotherapy of choice per local guidance/standard practice, whichever is longer.
* A WOCBP must have a negative highly sensitive pregnancy test (urine or serum as required by local regulations) within 3 days before the first dose of study intervention.
* Additional requirements for pregnancy testing during and after study intervention are provided in the protocol.
* The investigator is responsible for review of medical history, menstrual history, and recent sexual activity to decrease the risk for inclusion of a woman with an early undetected pregnancy.
14. Is capable of giving signed informed consent, which includes compliance with the requirements and restrictions listed in the informed consent form and in the protocol.

Participants are excluded from the study if any of the following criteria apply:

Medical Conditions

1. Has known or suspected leptomeningeal disease.
2. Has uncontrolled or significant cardiovascular disease.
3. Has toxicity related to prior cancer therapy that has not resolved to ≤ Grade 1, with exceptions as stated in the protocol.
4. Has uncontrolled infection requiring IV antibiotics, antivirals, or antifungals.
5. Has known HIV infection.
6. Has active hepatitis B or C infection.
7. Has an active SARS-CoV-2 infection. Participants with prior infection that has resolved per local institutions' requirements and screening guidance are eligible.
8. Has a history of life-threatening hypersensitivity to monoclonal antibodies or to recombinant proteins or excipients in the drug formulation of zanidatamab.
9. Is unable to receive trastuzumab treatment due to medical contraindications.
10. Has any serious underlying medical or psychiatric condition that would impair the ability of the participant to receive or tolerate the planned treatment at the investigational site.
11. Has any condition that would prevent treatment with the physician's choice of chemotherapy.
12. Has any issue or condition that in the opinion of the investigator would contraindicate the participant's participation in the study or confound the results of the study.

Prior/Concomitant Therapy
13. Has a history of prior allogeneic bone marrow, stem cell, or solid organ transplantation.
14. Was treated with any local or systemic antineoplastic therapy (including hormonal therapies for breast cancer) or any investigational therapy within 4 weeks or 5 half-lives (whichever is longer) prior to randomization.
15. Has a history of trauma or major surgery within 4 weeks prior to randomization.

Other Exclusions
16. Has a known hypersensitivity to any components of the study drugs, including chemotherapy.
17. Female participants who are breastfeeding or pregnant, and female and male participants planning a pregnancy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Jazz Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Mayo Clinic Scottsdale - PPDS

Phoenix, Arizona, United States

Site Status RECRUITING

Arizona Oncology Tucson - Wilmot

Tucson, Arizona, United States

Site Status WITHDRAWN

University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status RECRUITING

The Oncology Institute Of Hope And Innovation

Cerritos, California, United States

Site Status RECRUITING

Los Angeles Hematology Oncology Medical Group Glendale

Glendale, California, United States

Site Status RECRUITING

USC-Norris Comprehensive Cancer Center - Investigational Drug Service IDS

Los Angeles, California, United States

Site Status RECRUITING

UCSF at Mission Bay MB

San Francisco, California, United States

Site Status RECRUITING

University of Colorado-Cancer Center-PPDS

Aurora, Colorado, United States

Site Status RECRUITING

Rocky Mountain Cancer Centers

Denver, Colorado, United States

Site Status RECRUITING

Medstar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Washington Cancer Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Florida Cancer Specialists Research South

Fort Myers, Florida, United States

Site Status RECRUITING

Mayo Clinic Jacksonville - PPDS

Jacksonville, Florida, United States

Site Status RECRUITING

Florida Cancer Specialists Research North

St. Petersburg, Florida, United States

Site Status RECRUITING

Florida Cancer Specialists Research East

West Palm Beach, Florida, United States

Site Status RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

Minnesota Oncology Hematology

Coon Rapids, Minnesota, United States

Site Status RECRUITING

Mayo Clinic - PPDS

Rochester, Minnesota, United States

Site Status RECRUITING

Saint Luke's Cancer Institute

Kansas City, Missouri, United States

Site Status RECRUITING

Hackensack Meridian Health

Hackensack, New Jersey, United States

Site Status RECRUITING

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

Site Status RECRUITING

Memorial Sloan Kettering

Long Island City, New York, United States

Site Status RECRUITING

Perlmutter Cancer Center 160 E 34th St

New York, New York, United States

Site Status RECRUITING

The Mount Sinai Hospital

New York, New York, United States

Site Status RECRUITING

Columbia University Medical Center 161 Fort Washington

New York, New York, United States

Site Status RECRUITING

Messino Cancer Center

Asheville, North Carolina, United States

Site Status RECRUITING

Duke Cancer Institute

Durham, North Carolina, United States

Site Status RECRUITING

UNC Central Investigational Drug Services

Morrisville, North Carolina, United States

Site Status RECRUITING

Oncology Hematology Care (OHC)

Cincinnati, Ohio, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center 11100 Euclid Ave

Cleveland, Ohio, United States

Site Status WITHDRAWN

Abramson Cancer Center of The University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status RECRUITING

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status RECRUITING

Texas Oncology - Fort Worth

Fort Worth, Texas, United States

Site Status RECRUITING

U.T. MD Anderson Cancer Center, Investigational Pharmacy Services

Houston, Texas, United States

Site Status RECRUITING

Millennium Research and Clinical Development

Houston, Texas, United States

Site Status WITHDRAWN

Maryland Oncology Hematology Healing Way - USOR

Irving, Texas, United States

Site Status RECRUITING

Medical Oncology Hematology Consultants

Irving, Texas, United States

Site Status RECRUITING

Nexus Health

Irving, Texas, United States

Site Status RECRUITING

Sansum Clinic 540 W - USOR

Irving, Texas, United States

Site Status RECRUITING

Texas Oncology Gulf Coast

Irving, Texas, United States

Site Status RECRUITING

Texas Oncology West

Irving, Texas, United States

Site Status RECRUITING

Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status RECRUITING

Virginia Oncology Associates, Sentara Health

Norfolk, Virginia, United States

Site Status RECRUITING

Blue Ridge Cancer Care

Roanoke, Virginia, United States

Site Status RECRUITING

Fred Hutchinson Cancer Center

Seattle, Washington, United States

Site Status RECRUITING

Froedtert and The Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Sunshine Coast University Private Hospital

Birtinya, Queensland, Australia

Site Status RECRUITING

Box Hill Hospital

Melbourne, Victoria, Australia

Site Status RECRUITING

Peninsula and South Eastern Haematology and Oncology Group

Mount Waverly, Victoria, Australia

Site Status RECRUITING

HPS Pharmacies - Adelaide

Adelaide, , Australia

Site Status RECRUITING

The Kinghorn Cancer Centre

Mount Kuring-Gai, , Australia

Site Status RECRUITING

St John of God Hospital Subiaco

Subiaco, , Australia

Site Status RECRUITING

Medizinische Universitat Innsbruck

Innsbruck, , Austria

Site Status RECRUITING

Ordensklinikum Barmherzige Schwestern

Linz, , Austria

Site Status RECRUITING

Medizinische Universitat Wien

Vienna, , Austria

Site Status RECRUITING

Klinikum Wels-Grieskirchen GmbH - Abteilung für Innere Medizin IV

Wels, , Austria

Site Status RECRUITING

Institute Jules Bordet

Anderlecht, , Belgium

Site Status RECRUITING

UZ Antwerpen

Edegem, , Belgium

Site Status RECRUITING

Grand Hôpital de Charleroi

Gilly, , Belgium

Site Status RECRUITING

CHU UCL Namur - Site Sainte-Elisabeth

Namur, , Belgium

Site Status RECRUITING

AZ Delta- Campus Rumbeke

Roeselare, , Belgium

Site Status RECRUITING

Hospital Nossa Senhora Da Conceição

Porto Alegre, Rio Grande do Sul, Brazil

Site Status RECRUITING

IEPE Unimed Sorocaba

Sorocaba, São Paulo, Brazil

Site Status RECRUITING

DASA Hospital Brasilia

Brasília, , Brazil

Site Status RECRUITING

Centro Regional Integrado de Oncologia

Ceará, , Brazil

Site Status RECRUITING

Catarina Pesquisa Clinica

Itajaí, , Brazil

Site Status RECRUITING

Irmandade Da Santa Casa de Misericordia de Porto Alegre

Portalegre, , Brazil

Site Status RECRUITING

Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul PUCRS

Porto Alegre, , Brazil

Site Status RECRUITING

Real Hospital Portugues de Beneficiencia Em Pernambuco

Recife, , Brazil

Site Status RECRUITING

Nucleo de Oncologia Da Bahia

Salvador, , Brazil

Site Status RECRUITING

Ceon Pesquisas Ltda

São Caetano do Sul, , Brazil

Site Status RECRUITING

Hospital Beneficiencia Portuguesa

São Paulo, , Brazil

Site Status RECRUITING

Onco Star Sp Oncologia LTDA

São Paulo, , Brazil

Site Status RECRUITING

Jewish General Hospital

Montreal, , Canada

Site Status RECRUITING

The Ottawa Hospital Cancer Centre

Ottawa, , Canada

Site Status RECRUITING

CHU de Québec Université Laval Hôpital du Saint Sacrement

Québec, , Canada

Site Status RECRUITING

Sunnybrook Research Institute

Toronto, , Canada

Site Status RECRUITING

BC Cancer-Vancouver Center

Vancouver, , Canada

Site Status RECRUITING

Institut Bergonie

Bordeaux, , France

Site Status RECRUITING

Centre François Baclesse

Caen, , France

Site Status RECRUITING

Centre Georges François Leclerc

Dijon, , France

Site Status RECRUITING

Pharmacie Centre de Cancerologie de la Sarthe

Le Mans, , France

Site Status RECRUITING

Centre Oscar Lambret

Lille, , France

Site Status RECRUITING

AP HM Hopital de La Timone

Marseille, , France

Site Status RECRUITING

Institut Paoli Calmettes

Marseille, , France

Site Status RECRUITING

Pharmacie ICM Val d'Aurelle

Montpellier, , France

Site Status RECRUITING

ICANS - Institut de cancérologie Strasbourg Europe

Strasbourg, , France

Site Status RECRUITING

Oncopôle Claudius Regaud Pharmacie

Toulouse, , France

Site Status RECRUITING

Gustave Roussy

Villejuif, , France

Site Status RECRUITING

Helios Klinikum Berlin Buch GmbH Klinik für Gynäkologie und Geburtshilfe

Berlin, , Germany

Site Status RECRUITING

Marienhospital Bottrop gGmbH

Dortmund, , Germany

Site Status RECRUITING

Universitätsklinikum Carl Gustav Carus an der TU

Dresden, , Germany

Site Status RECRUITING

LMU Klinikum - Apotheke

München, , Germany

Site Status RECRUITING

Universitätsklinikum Ulm

Ulm, , Germany

Site Status RECRUITING

Aretaieio Hospital

Athens, , Greece

Site Status RECRUITING

Athens Medical Center

Athens, , Greece

Site Status RECRUITING

University General Hospital of Patras

Pátrai, , Greece

Site Status RECRUITING

European Interbalkan Medical Center

Thessaloniki, , Greece

Site Status RECRUITING

IRCCS Centro di Riferimento Oncologico di Aviano CRO

Aviano, , Italy

Site Status RECRUITING

Asst Papa Giovanni Xxiii

Bergamo, , Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria Di Bologna Policlinico S Orsola Malpighi Via Massarenti

Bologna, , Italy

Site Status RECRUITING

Ospedale San Raffaele S.r.l PPDS

Milan, , Italy

Site Status RECRUITING

Istituto Europeo di Oncologia

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria di Modena

Modena, , Italy

Site Status RECRUITING

Fondazione IRCCS San Gerardo dei Tintori

Monza, , Italy

Site Status RECRUITING

Istituto Oncologico Veneto - I.R.C.C.S.

Padua, , Italy

Site Status RECRUITING

Fondazione IRCCS Policlinico San Matteo

Pavia, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario A. Gemelli IRCCS

Rome, , Italy

Site Status RECRUITING

IRCCS Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

Chiba Cancer Center

Chiba, , Japan

Site Status RECRUITING

National Cancer Center Hospital

Chūōku, , Japan

Site Status RECRUITING

Osaka International Cancer Institute

Chūōku, , Japan

Site Status RECRUITING

National Hospital Organization Kyushu Cancer Center

Fukuoka, , Japan

Site Status RECRUITING

Fukushima Medical University Hospital

Fukushima, , Japan

Site Status RECRUITING

Saitama Medical University International Medical Center

Hidaka-shi, , Japan

Site Status RECRUITING

Tokai University Hospital

Isesaki-shi, , Japan

Site Status RECRUITING

Sagara Hospital

Kagoshima, , Japan

Site Status RECRUITING

Kyoto University Hospital

Kyoto, , Japan

Site Status RECRUITING

Aichi Cancer Center

Nagoya, , Japan

Site Status RECRUITING

Nagoya City University Hospital

Nagoya, , Japan

Site Status RECRUITING

Okayama University Hospital

Okayama, , Japan

Site Status RECRUITING

National Hospital Organization Osaka National Hospital

Osaka, , Japan

Site Status RECRUITING

National Hospital Organization Hokkaido Cancer Center

Sapporo, , Japan

Site Status RECRUITING

Juntendo University Hospital

Tokyo, , Japan

Site Status RECRUITING

Showa University Hospital

Tokyo, , Japan

Site Status RECRUITING

Kanagawa Cancer Center

Yokohama, , Japan

Site Status RECRUITING

Białostockie Centrum Onkologii im. Marii Skłodowskiej-Curie w Białymstoku

Bialystok, , Poland

Site Status RECRUITING

Wojewódzki Szpital Specjalistyczny W Białej Podlaskiej

Biała Podlaska, , Poland

Site Status RECRUITING

Pratia MCM Kraków

Krakow, , Poland

Site Status RECRUITING

Pratia Poznan

Poznan, , Poland

Site Status RECRUITING

Uniwersytecki Szpital Kliniczny w Poznaniu

Poznan, , Poland

Site Status RECRUITING

Narodowy Instytut Onkologii im. Marii Sklodowskiej-Curie Panstwowy Instytut Badawczy w Warszawie

Warsaw, , Poland

Site Status RECRUITING

Soon Chun Hyang University Cheonan Hospital

Cheonan-si, , South Korea

Site Status RECRUITING

Gachon University Gil Medical Center

Namdong-gu, , South Korea

Site Status RECRUITING

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status RECRUITING

Severance Hospital Yonsei University Health System

Seoul, , South Korea

Site Status RECRUITING

Gangnam Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status RECRUITING

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status RECRUITING

Hospital Universitario A Coruña

A Coruña, , Spain

Site Status RECRUITING

Hospital Universitario de Badajoz

Badajoz, , Spain

Site Status RECRUITING

Hospital Universitari Vall d Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status RECRUITING

ICO Badalona-H.U. Germans Trias i Pujol

Barcelona, , Spain

Site Status RECRUITING

Hospital General Universitario de Elche

Elche, , Spain

Site Status RECRUITING

Hospital Universitario Clinico San Cecilio

Granada, , Spain

Site Status RECRUITING

Hospital Beata Maria Ana

Madrid, , Spain

Site Status RECRUITING

MD Anderson Cancer Center

Madrid, , Spain

Site Status RECRUITING

Hospital Clinico San Carlos

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario de Canarias

San Cristóbal de La Laguna, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Clínico Universitario de Valencia

Valencia, , Spain

Site Status RECRUITING

CHUVI - H.U. Alvaro Cunqueiro

Vigo, , Spain

Site Status RECRUITING

Royal United Hospital

Bath, , United Kingdom

Site Status RECRUITING

Beatson West Of Scotland Cancer Centre

Glasgow, , United Kingdom

Site Status RECRUITING

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status RECRUITING

Guy's Hospital

London, , United Kingdom

Site Status RECRUITING

Charring Cross Hospital

London, , United Kingdom

Site Status RECRUITING

The Christie - PPDS

Manchester, , United Kingdom

Site Status RECRUITING

Churchill Hospital

Oxford, , United Kingdom

Site Status RECRUITING

New Cross Hospital

Wolverhampton, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Austria Belgium Brazil Canada France Germany Greece Italy Japan Poland South Korea Spain United Kingdom

Central Contacts

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Clinical Trial Disclosure & Transparency

Role: CONTACT

215-832-3750

Other Identifiers

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2023-508960-31-00

Identifier Type: OTHER

Identifier Source: secondary_id

JZP598-303

Identifier Type: -

Identifier Source: org_study_id

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