Study to Evaluate Avacopan in Combination With a Rituximab or Cyclophosphamide-containing Regimen, in Children From 6 Years to < 18 Years of Age With AAV.

NCT ID: NCT06321601

Last Updated: 2026-01-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-22

Study Completion Date

2028-09-26

Brief Summary

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The main objective of this study is to explore the efficacy of avacopan in participants affected by AAV.

Detailed Description

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Conditions

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Vasculitis

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Avacopan

Participants will receive avacopan twice-daily (BID) administered as oral tablets or liquid formula for 52 weeks.

Group Type EXPERIMENTAL

Avacopan

Intervention Type DRUG

Oral administration

Interventions

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Avacopan

Oral administration

Intervention Type DRUG

Other Intervention Names

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AMG 569

Eligibility Criteria

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Inclusion Criteria

* Male and female children and adolescents from 6 to \< 18 years of age
* Clinical diagnosis of granulomatosis with polyangiitis (GPA) or microscopic polyangiitis (MPA), consistent with Chapel-Hill Consensus Conference definitions (Jennette et al, 2013)
* Newly diagnosed or relapsed AAV with positive test for anti-PR3 or anti-MPO antibodies
* At least 1 PVAS major item, at least 3 PVAS nonmajor items, or at least the 2 renal items of proteinuria and hematuria.
* eGFR \> 15 mL/min/1.73 m2 (using modified Schwartz equation per central lab guidelines)
* Participants must have a bodyweight of ≥ 15 kg at day 1.

Exclusion Criteria

* Any other known multisystem autoimmune disease including eosinophilic granulomatosis with polyangiitis (Churg-Strauss), systemic lupus erythematosus , IgA vasculitis (Henoch-Schönlein), rheumatoid vasculitis, Sjogren's syndrome, anti-glomerular basement membrane disease, or cryoglobulinemic vasculitis
* Alveolar hemorrhage requiring invasive pulmonary ventilation support anticipated to last beyond the screening period of the study
* Any medical condition requiring or expected to require continued use of immunosuppressive treatments, including corticosteroids that may cause confoundment with study assessments and study conclusions.
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Emory University

Atlanta, Georgia, United States

Site Status RECRUITING

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Minnesota Masonic Childrens Hospital Discovery Clinic

Minneapolis, Minnesota, United States

Site Status RECRUITING

Cohen Children Medical Center

Lake Success, New York, United States

Site Status RECRUITING

University of North Carolina

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Wake Forest University Health Sciences

Charlotte, North Carolina, United States

Site Status RECRUITING

Akron Childrens Hospital

Akron, Ohio, United States

Site Status RECRUITING

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status RECRUITING

Upmc Childrens Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Texas Childrens Hospital

Houston, Texas, United States

Site Status RECRUITING

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status RECRUITING

Universitair Ziekenhuis Leuven - Gasthuisberg

Leuven, , Belgium

Site Status RECRUITING

Alberta Childrens Hospital

Calgary, Alberta, Canada

Site Status RECRUITING

Stollery Childrens Hospital

Edmonton, Alberta, Canada

Site Status RECRUITING

CHU Sainte Justine

Montreal, Quebec, Canada

Site Status RECRUITING

Vseobecna fakultni nemocnice v Praze

Prague, , Czechia

Site Status RECRUITING

Fakultni nemocnice v Motole

Prague, , Czechia

Site Status RECRUITING

Centre Hospitalier Universitaire de Bordeaux - Hopital Pellegrin

Bordeaux, , France

Site Status RECRUITING

Hospices Civils de Lyon Hopital Femme Mere Enfant

Bron, , France

Site Status RECRUITING

Hopital Necker Enfants Malades

Paris, , France

Site Status RECRUITING

Semmelweis Egyetem

Budapest, , Hungary

Site Status RECRUITING

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont Altalanos Orvostudomanyi Kar

Szeged, , Hungary

Site Status RECRUITING

Uniwersyteckie Centrum Kliniczne

Gdansk, , Poland

Site Status RECRUITING

Uniwersytecki Szpital Dzieciecy w Krakowie

Krakow, , Poland

Site Status RECRUITING

Dzieciecy Szpital Kliniczny im. Jozefa Polikarpa Brudzinskiego w Warszawie

Warsaw, , Poland

Site Status RECRUITING

Narodny ustav detskych chorob

Bratislava, , Slovakia

Site Status RECRUITING

Hospital Universitari Vall d Hebron

Barcelona, Catalonia, Spain

Site Status RECRUITING

Hospital Sant Joan de Deu

Esplugues de Llobregat, Catalonia, Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Countries

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United States Belgium Canada Czechia France Hungary Poland Slovakia Spain

Central Contacts

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Amgen Call Center

Role: CONTACT

866-572-6436

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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20230070

Identifier Type: -

Identifier Source: org_study_id

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