Endothelin Receptor Antagonism With Ambrisentan to Treat Hepatorenal Syndrome

NCT ID: NCT06256432

Last Updated: 2025-01-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

54 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-04-17

Study Completion Date

2026-02-28

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Patients with advanced cirrhosis of the liver develop kidney problems occasionally. This condition is called Hepatorenal Syndrome, requires hospitalization and frequently results in death.

The goal of this clinical trial is to test whether the administration of low doses of ambrisentan can help patients with Hepatorenal Syndrome and to determine if it is safe. Ambrisentan is a drug that is approved for the treatment of high blood pressure in the lungs at higher doses.

This clinical trial will compare the safety and effects of ambrisentan to another drug called terlipressin, which is commonly used to treat patients with hepatorenal syndrome.

The main questions the clinical trial aims to answer are:

* Does ambrisentan help the kidney function of the patient?
* Does ambrisentan help prevent death in patients with Hepatorenal Syndrome?
* Does ambrisentan prevent Hepatorenal Syndrome from reappearing?

While in the hospital, trial participants will receive either one of two doses of ambrisentan or terlipressin. If in the first 4 days, ambrisentan is not helpful, the patient may be eligible to receive terlipressin. Patients assigned to receive ambrisentan will continue taking this medication at home after leaving the hospitals and until they complete 60 days of treatment.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Hepatorenal Syndrome Liver Cirrhosis Acute Kidney Injury Ascites Hepatic

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Ambrisentan - Low Dose 1

Liquid solution for oral administration, dose \< 250 µg/day, up to 60 days

Group Type EXPERIMENTAL

Ambrisentan

Intervention Type DRUG

Endothelin receptor antagonist

Ambrisentan - Low Dose 2

Liquid solution for oral administration, dose \< 250 µg/day, up to 60 days

Group Type EXPERIMENTAL

Ambrisentan

Intervention Type DRUG

Endothelin receptor antagonist

Terlipressin

Sterile lyophilized powder, to be reconstituted for intravenous administration, at a dose indicated by the study investigator and administered for up to 14 days, considering the following recommendation: 1 mg terlipressin administered in 2-minute bolus every 6 hours for 3 days, and dose of terlipressin increased to 2 mg every 6 hours in the absence of a decrease of at least 30% in serum creatinine by day 4

Group Type ACTIVE_COMPARATOR

Terlipressin

Intervention Type DRUG

Terlipressin

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Ambrisentan

Endothelin receptor antagonist

Intervention Type DRUG

Terlipressin

Terlipressin

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Written Informed consent prior to any study-related procedures.
* Age ≥ 18 years and ≤ 70 years.
* Male or non-pregnant, non-lactating female. Women of child-bearing potential must have a confirmed negative serum pregnancy test at the time of screening and must use a highly effective contraceptive method throughout the study such as combined (oestrogen and progestogen containing) hormonal contraception associated with inhibition of ovulation (oral, intravaginal, transdermal), progestogen-only hormonal contraception associated with inhibition of ovulation (oral, injectable, implantable), intrauterine device (IUD), intrauterine hormone-releasing system (IUS), bilateral tube occlusion, vasectomised partner, and sexual abstinence and until one month after completing treatment with the study medication. In the case of hormonal contraception, women should have been on a stable regimen for a minimum of three months before study enrolment. Women not of child-bearing potential include post-menopausal females (defined as having a history of amenorrhea for at least one year) or a documented status as being surgically sterile (hysterectomy, bilateral oophorectomy, tubal ligation/salpingectomy). Men must use an effective contraception method (i.e., condom + diaphragm/spermicidal gel or foam, or vasectomy), and should not donate semen during the study. Men are considered to be fertile from the time of puberty, except for those men with permanent sterility secondary to bilateral orchiectomy.
* Cirrhosis of the liver by laboratory examination, clinical history or biopsy.
* History of ascites.
* Increase in serum creatinine ≥ 0.3 mg/dl (26.5 µmol/L) from a value obtained in the 7 days prior to admission, OR a serum creatinine ≥ 1.5 mg/dl (132.6 µmol/L) and is ≥ 1.5-fold above the most recent and lowest value obtained in the last 3 months.
* The subject has no clinical and/or haemodynamic evidence of intravascular volume depletion; or has undergone at least 12 hours of diuretic withdrawal and fluid resuscitation to discard or treat intravascular volume depletion (such as difficulty in establishing volume status, volume status is assessed as equivocal, or there is clinical and/or haemodynamic evidence of intravascular volume depletion), and no significant improvement in serum creatinine has been observed.

Exclusion Criteria

* Serum creatinine \> 5 mg/dL (442 µmol/L).
* Mean arterial pressure (MAP) \< 60 mmHg.
* Large Volume Paracentesis (LVP) in the 3 days prior to screening.
* Sepsis, uncontrolled bacterial infection or less than 2 days anti-infective therapy for documented or suspected bacterial infection.
* Total bilirubin \> 8 mg/dL (137 µmol/L).
* Serum sodium \< 125 mmol/L.
* International Normalised Ratio (INR) ≥ 3.5.
* Proteinuria ≥ 1000 mg/dL.
* Microhaematuria \> 50 red blood cells per high power field.
* Clinically significant casts on urinalysis, including granular casts.
* History or evidence of obstructive uropathy or parenchymal renal disease on ultrasound or other imaging.
* Subject with a recent history of circulatory shock defined as MAP \< 60 mmHg within 5 days prior to screening requiring vasopressors or subjects requires circulatory support with vasopressors during screening.
* Subject requiring oxygen supplementation or mechanical ventilation.
* Recent exposure to nephrotoxic agents or exposure to radiographic contrast agents within 72 hrs prior to screening.
* Superimposed acute liver failure/injury due to factors other than alcohol, including acute viral hepatitis, drugs, medications (e.g., acetaminophen), or other toxins (e.g., mushroom \[Amanita\] poisoning).
* Severe cardiovascular disease, including, but not limited to, unstable angina, pulmonary oedema, congestive heart failure (NYHA ≥ II), or persisting symptomatic peripheral vascular disease, myocardial infarction or stable chronic angina within the past 12 months, or any other cardiovascular disease judged by the Investigator to be severe.
* Subject has a history of Transjugular Intrahepatic Portosystemic shunt (TIPS).
* Subject with acute variceal bleeding at the time of screening who may undergo pre-emptive TIPS or is anticipated to be treated with terlipressin.
* Current or recent Renal Replacement Therapy (RRT) within 30 days of enrolment, or anticipation of RRT in the next 3 days after screening.
* Hepatocellular Carcinoma (HCC) beyond the Milan criteria or other malignancy affecting survival beyond 6 months.
* Participation in a study of an investigational medical product or device within the last 30 days preceding screening.
* Hepatic Encephalopathy with West Haven Grade III or IV.
* Current or recent (30 days prior to enrolment) treatment with endothelin receptor antagonists, including ambrisentan.
* Estimated life expectancy of less than 3 days.
* Known allergy or sensitivity to ambrisentan or propylene glycol.
* History of Idiopathic Pulmonary Fibrosis.
* Subject is unable or unwilling to follow instructions or comply with study procedures.
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Noorik Biopharmaceuticals AG

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Iker Navarro, MD

Role: STUDY_DIRECTOR

Noorik Biopharmaceuticals AG

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Aster CMI Hospital

Bangalore, Karnataka, India

Site Status RECRUITING

Sir HN Reliance Hospital Foundation

Mumbai, Maharashtra, India

Site Status RECRUITING

All India Institute of Medical Sciences

New Delhi, National Capital Territory of Delhi, India

Site Status RECRUITING

Asian Institute of Gastroenterology (AIG)

Hyderabad, Telangana, India

Site Status RECRUITING

Ganesh Shankar Vidyarthi Memorial (GSVM) Medical College

Kanpur, Uttar Pradesh, India

Site Status RECRUITING

Medanta Multi Super Specialty Hospital

Lucknow, Uttar Pradesh, India

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

India

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Iker Navarro, MD

Role: CONTACT

+41 76 398 7007

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Mallikarjun Sakpal, MD

Role: primary

Ranjini R, MD

Role: backup

Akash Shukla, MD

Role: primary

Dr Shalimar, MD

Role: primary

Clinical Research Coordinator

Role: primary

+91 40 2337 8888

Vinay Kumar, MD

Role: primary

Abhai Verna, MD

Role: primary

References

Explore related publications, articles, or registry entries linked to this study.

Angeli P, Gines P, Wong F, Bernardi M, Boyer TD, Gerbes A, Moreau R, Jalan R, Sarin SK, Piano S, Moore K, Lee SS, Durand F, Salerno F, Caraceni P, Kim WR, Arroyo V, Garcia-Tsao G; International Club of Ascites. Diagnosis and management of acute kidney injury in patients with cirrhosis: revised consensus recommendations of the International Club of Ascites. Gut. 2015 Apr;64(4):531-7. doi: 10.1136/gutjnl-2014-308874. Epub 2015 Jan 28. No abstract available.

Reference Type BACKGROUND
PMID: 25631669 (View on PubMed)

Soper CP, Latif AB, Bending MR. Amelioration of hepatorenal syndrome with selective endothelin-A antagonist. Lancet. 1996 Jun 29;347(9018):1842-3. No abstract available.

Reference Type BACKGROUND
PMID: 8667963 (View on PubMed)

Mindikoglu AL, Weir MR. Current concepts in the diagnosis and classification of renal dysfunction in cirrhosis. Am J Nephrol. 2013;38(4):345-54. doi: 10.1159/000355540. Epub 2013 Oct 5.

Reference Type BACKGROUND
PMID: 24107793 (View on PubMed)

Ring-Larsen H. Renal blood flow in cirrhosis: relation to systemic and portal haemodynamics and liver function. Scand J Clin Lab Invest. 1977 Nov;37(7):635-42. doi: 10.3109/00365517709100657.

Reference Type BACKGROUND
PMID: 594643 (View on PubMed)

Moore K. Endothelin and vascular function in liver disease. Gut. 2004 Feb;53(2):159-61. doi: 10.1136/gut.2003.024703.

Reference Type BACKGROUND
PMID: 14724140 (View on PubMed)

Moore K, Wendon J, Frazer M, Karani J, Williams R, Badr K. Plasma endothelin immunoreactivity in liver disease and the hepatorenal syndrome. N Engl J Med. 1992 Dec 17;327(25):1774-8. doi: 10.1056/NEJM199212173272502.

Reference Type BACKGROUND
PMID: 1435931 (View on PubMed)

Zipprich A, Gittinger F, Winkler M, Dollinger MM, Ripoll C. Effect of ET-A blockade on portal pressure and hepatic arterial perfusion in patients with cirrhosis: A proof of concept study. Liver Int. 2021 Mar;41(3):554-561. doi: 10.1111/liv.14757. Epub 2021 Jan 5.

Reference Type BACKGROUND
PMID: 33295121 (View on PubMed)

Dhaun N, Macintyre IM, Melville V, Lilitkarntakul P, Johnston NR, Goddard J, Webb DJ. Blood pressure-independent reduction in proteinuria and arterial stiffness after acute endothelin-a receptor antagonism in chronic kidney disease. Hypertension. 2009 Jul;54(1):113-9. doi: 10.1161/HYPERTENSIONAHA.109.132670. Epub 2009 Jun 8.

Reference Type BACKGROUND
PMID: 19506099 (View on PubMed)

Wong F, Moore K, Dingemanse J, Jalan R. Lack of renal improvement with nonselective endothelin antagonism with tezosentan in type 2 hepatorenal syndrome. Hepatology. 2008 Jan;47(1):160-8. doi: 10.1002/hep.21940.

Reference Type BACKGROUND
PMID: 17886336 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

N-003-CRD005

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Terlipressin in Septic Shock in Cirrhosis
NCT00628160 COMPLETED PHASE2/PHASE3
Angiotensin 2 for Hepatorenal Syndrome
NCT04048707 WITHDRAWN PHASE2