Artesunate Ointment for the Treatment of Anal HSIL in HIV-negative Participants

NCT ID: NCT06206564

Last Updated: 2025-05-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-01-12

Study Completion Date

2026-12-31

Brief Summary

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This is a phase II double blind, placebo-controlled, randomized study of artesunate ointment for the treatment of HIV-negative men and women who have anal high grade squamous intraepithelial lesions (anal HSIL)

Detailed Description

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Eligible participants in this study are randomized 2:1 to receive either artesunate or placebo ointment for the treatment of anal HSIL. Both groups receive four 5-day cycles of ointment, at weeks 0, 2, 4, and 6. Participants are followed closely with anoscopy or high resolution anoscopy (HRA) at weeks 8, 18, 30, and 42. After the week 18 HRA visit, participants who have at least partial response will be followed with HRA at week 30.

Participants who are found to be non-responders at week 18 will undergo standard of care ablation.

Participants who are found to have anal HSIL at weeks 30 or 42 will be followed according to standard of care procedures.

Primary Objective: To evaluate the complete and partial histopathologic response to four 5-day cycles of artesunate ointment in adult patients with biopsy-proven HPV-associated intra-anal HSIL (18 weeks).

Secondary Objectives:

Efficacy:

To evaluate the viral clearance after four 5-day cycles of artesunate ointment To evaluate complete and partial intra-anal response To evaluate complete and partial peri-anal response To evaluate persistence of response throughout the study window

Safety:

To evaluate the safety of artesunate ointment for the treatment of intra-anal HSIL.

Conditions

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Anal High-grade Squamous Intraepithelial Lesion Anal HSIL Anal HPV Infection AIN

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Double blind, placebo-controlled randomized trial
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Double-blind, placebo-controlled

Study Groups

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Artesunate

Group Type EXPERIMENTAL

Artesunate ointment

Intervention Type DRUG

Four 5-day cycles of artesunate ointment given at weeks 0, 2, 4, 6

Placebo ointment

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Four 5-day cycles of placebo ointment given at weeks 0, 2, 4, 6

Interventions

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Artesunate ointment

Four 5-day cycles of artesunate ointment given at weeks 0, 2, 4, 6

Intervention Type DRUG

Placebo

Four 5-day cycles of placebo ointment given at weeks 0, 2, 4, 6

Intervention Type DRUG

Other Intervention Names

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Artesunic acid Dihydroartemisinin (DHA) Artemisinin placebo ointment

Eligibility Criteria

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Inclusion Criteria

* Adult men and women age ≥ 18 years
* Capable of informed consent
* Biopsy-confirmed intra-anal high-grade dysplasia (AIN 2, AIN 3, anal HSIL) by HRA.
* Positive anal human papillomavirus (HPV) test.
* Women of childbearing potential agree to use birth control for the duration of the study.
* Laboratory values at Screening of:

1. Serum alanine transaminase (SGPT/ALT) \< 5 x upper limit of normal (ULN)
2. Serum aspartate transaminase (SGOT/AST) \< 5 x ULN
3. Serum Bilirubin (total) \< 2.5 x ULN
4. Serum Creatinine ≤ 1.5 x ULN
* Electrocardiogram (ECG) with no clinically significant findings as assessed by the Investigator.
* Weight ≥ 50kg

Exclusion Criteria

* Pregnant and nursing women
* Diagnosis of low-grade anal dysplasia (AIN 1, LSIL), without the concomitant diagnosis of anal HSIL, by HRA
* Concurrent anal, vulvar, cervical, or penile cancer
* HIV-seropositivity
* Currently receiving systemic chemotherapy or radiation therapy for another cancer.
* Patients who are on medical treatment with systemic immunosuppressants or steroids (e.g., active autoimmune disease). Participants using nasal steroid treatments for allergic conditions may participate in the study.
* Concomitant use of strong UGT (Uridine-diphosphate-glucuronosyltransferase) inhibitors
* Concomitant use of imiquimod or 5-fluorouracil (5-FU) for the duration of the study
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Laser Surgery Care, LLC

UNKNOWN

Sponsor Role collaborator

Anal Dysplasia Clinic MidWest

UNKNOWN

Sponsor Role collaborator

Frantz Viral Therapeutics, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Anal Dysplasia Clinic MidWest

Chicago, Illinois, United States

Site Status RECRUITING

Laser Surgery Care

New York, New York, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Mihaela Plesa

Role: CONTACT

440-255-1155

Ahmad Bayat, MD

Role: CONTACT

301-956-2523

Facility Contacts

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Gary Bucher, MD

Role: primary

312-623-2625

Emily Miller

Role: backup

3126232625

Taylor Ridley

Role: primary

212-242-6500

Other Identifiers

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ART-AIN IIB-2

Identifier Type: -

Identifier Source: org_study_id

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