Trial Outcomes & Findings for A Study to Assess the Efficacy, Safety and Tolerability of Different Doses of AZD0780 in Patients With Dyslipidemia (NCT NCT06173570)

NCT ID: NCT06173570

Last Updated: 2025-11-17

Results Overview

Percent change was calculated as (Week 12 LDL-C - Baseline LDL-C) / Baseline LDL-C \* 100. Negative values indicate reduction in LDL-C. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

428 participants

Primary outcome timeframe

From first day of treatment up to week 12

Results posted on

2025-11-17

Participant Flow

The study was conducted from January 2024 to September 2024 in 55 research sites in 8 countries (United States, Canada, Czech Republic, Denmark, Hungary, Japan, Slovakia, and Spain).

Of 428 enrolled participants, two randomized participants - one screen failure and one withdrawal by subject - did not start treatment.

Participant milestones

Participant milestones
Measure
AZD0780 1 mg
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
Participants received placebo administered orally once daily for up to 12 weeks
Overall Study
STARTED
86
85
85
85
87
Overall Study
Started Treatment
86
85
84
85
86
Overall Study
COMPLETED
81
81
84
80
82
Overall Study
NOT COMPLETED
5
4
1
5
5

Reasons for withdrawal

Reasons for withdrawal
Measure
AZD0780 1 mg
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
Participants received placebo administered orally once daily for up to 12 weeks
Overall Study
Adverse Event
1
0
0
2
0
Overall Study
Lost to Follow-up
1
0
0
0
2
Overall Study
Protocol Violation
0
2
0
0
1
Overall Study
Withdrawal by Subject
0
1
1
1
1
Overall Study
Non-compliance with Study Drug
1
0
0
0
0
Overall Study
Screen Failure
0
0
0
0
1
Overall Study
Other
2
1
0
2
0

Baseline Characteristics

A Study to Assess the Efficacy, Safety and Tolerability of Different Doses of AZD0780 in Patients With Dyslipidemia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Total
n=426 Participants
Total of all reporting groups
Ethnicity (NIH/OMB)
Hispanic or Latino
5 Participants
n=202 Participants
10 Participants
n=283 Participants
6 Participants
n=120 Participants
12 Participants
n=122 Participants
8 Participants
n=79 Participants
41 Participants
n=806 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
81 Participants
n=202 Participants
75 Participants
n=283 Participants
78 Participants
n=120 Participants
73 Participants
n=122 Participants
78 Participants
n=79 Participants
385 Participants
n=806 Participants
Age, Categorical
<=18 years
0 Participants
n=202 Participants
0 Participants
n=283 Participants
0 Participants
n=120 Participants
0 Participants
n=122 Participants
0 Participants
n=79 Participants
0 Participants
n=806 Participants
Age, Categorical
Between 18 and 65 years
47 Participants
n=202 Participants
59 Participants
n=283 Participants
39 Participants
n=120 Participants
50 Participants
n=122 Participants
47 Participants
n=79 Participants
242 Participants
n=806 Participants
Age, Categorical
>=65 years
39 Participants
n=202 Participants
26 Participants
n=283 Participants
45 Participants
n=120 Participants
35 Participants
n=122 Participants
39 Participants
n=79 Participants
184 Participants
n=806 Participants
Age, Continuous
62.7 Years
STANDARD_DEVIATION 7.9 • n=202 Participants
60.9 Years
STANDARD_DEVIATION 7.2 • n=283 Participants
63.9 Years
STANDARD_DEVIATION 7.2 • n=120 Participants
62.3 Years
STANDARD_DEVIATION 7.9 • n=122 Participants
62.3 Years
STANDARD_DEVIATION 7.8 • n=79 Participants
62.4 Years
STANDARD_DEVIATION 7.6 • n=806 Participants
Sex: Female, Male
Female
41 Participants
n=202 Participants
41 Participants
n=283 Participants
37 Participants
n=120 Participants
41 Participants
n=122 Participants
44 Participants
n=79 Participants
204 Participants
n=806 Participants
Sex: Female, Male
Male
45 Participants
n=202 Participants
44 Participants
n=283 Participants
47 Participants
n=120 Participants
44 Participants
n=122 Participants
42 Participants
n=79 Participants
222 Participants
n=806 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=202 Participants
0 Participants
n=283 Participants
0 Participants
n=120 Participants
0 Participants
n=122 Participants
0 Participants
n=79 Participants
0 Participants
n=806 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=202 Participants
1 Participants
n=283 Participants
0 Participants
n=120 Participants
0 Participants
n=122 Participants
0 Participants
n=79 Participants
1 Participants
n=806 Participants
Race (NIH/OMB)
Asian
8 Participants
n=202 Participants
6 Participants
n=283 Participants
6 Participants
n=120 Participants
6 Participants
n=122 Participants
6 Participants
n=79 Participants
32 Participants
n=806 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=202 Participants
0 Participants
n=283 Participants
0 Participants
n=120 Participants
0 Participants
n=122 Participants
0 Participants
n=79 Participants
0 Participants
n=806 Participants
Race (NIH/OMB)
Black or African American
5 Participants
n=202 Participants
3 Participants
n=283 Participants
4 Participants
n=120 Participants
4 Participants
n=122 Participants
6 Participants
n=79 Participants
22 Participants
n=806 Participants
Race (NIH/OMB)
White
73 Participants
n=202 Participants
75 Participants
n=283 Participants
73 Participants
n=120 Participants
74 Participants
n=122 Participants
73 Participants
n=79 Participants
368 Participants
n=806 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=202 Participants
0 Participants
n=283 Participants
0 Participants
n=120 Participants
0 Participants
n=122 Participants
1 Participants
n=79 Participants
1 Participants
n=806 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=202 Participants
0 Participants
n=283 Participants
1 Participants
n=120 Participants
1 Participants
n=122 Participants
0 Participants
n=79 Participants
2 Participants
n=806 Participants
Low-Density Lipoprotein Cholesterol (LDL-C)
2.6822 mmol/L
STANDARD_DEVIATION 0.6918 • n=202 Participants
2.7258 mmol/L
STANDARD_DEVIATION 0.8960 • n=283 Participants
2.4784 mmol/L
STANDARD_DEVIATION 0.7122 • n=120 Participants
2.5500 mmol/L
STANDARD_DEVIATION 0.6939 • n=122 Participants
2.5769 mmol/L
STANDARD_DEVIATION 0.6620 • n=79 Participants
2.6031 mmol/L
STANDARD_DEVIATION 0.7378 • n=806 Participants

PRIMARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 LDL-C - Baseline LDL-C) / Baseline LDL-C \* 100. Negative values indicate reduction in LDL-C. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change in Low-Density Lipoprotein Cholesterol (LDL-C) Level From Baseline to Week 12
-31.19 Percent Change (%)
Interval -37.06 to -25.32
-33.83 Percent Change (%)
Interval -39.78 to -27.88
-41.09 Percent Change (%)
Interval -46.92 to -35.25
-46.62 Percent Change (%)
Interval -52.48 to -40.76
4.08 Percent Change (%)
Interval -1.84 to 10.0

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 LDL-C - Baseline LDL-C) / Baseline LDL-C \* 100. Negative values indicate reduction in LDL-C. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Low-Density Lipoprotein Cholesterol (LDL-C) at Week 12
-30.47 Percent Change (%)
Interval -36.45 to -24.49
-33.35 Percent Change (%)
Interval -39.44 to -27.26
-40.47 Percent Change (%)
Interval -46.42 to -34.53
-46.41 Percent Change (%)
Interval -52.48 to -40.35
3.39 Percent Change (%)
Interval -2.63 to 9.4

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Total Cholesterol at Week 12
-18.93 Percent Change (%)
Interval -22.48 to -15.38
-20.09 Percent Change (%)
Interval -23.7 to -16.48
-24.84 Percent Change (%)
Interval -28.36 to -21.32
-27.06 Percent Change (%)
Interval -30.62 to -23.51
2.29 Percent Change (%)
Interval -1.29 to 5.88

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of High-Density Lipoprotein Cholesterol (HDL-C) at Week 12
0.12 Percent Change (%)
Interval -2.96 to 3.19
4.03 Percent Change (%)
Interval 0.93 to 7.12
1.97 Percent Change (%)
Interval -1.07 to 5.0
4.66 Percent Change (%)
Interval 1.6 to 7.72
3.65 Percent Change (%)
Interval 0.58 to 6.71

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Triglycerides at Week 12
3.06 Percent Change (%)
Interval -5.05 to 11.17
2.90 Percent Change (%)
Interval -5.29 to 11.08
1.93 Percent Change (%)
Interval -5.99 to 9.85
-0.44 Percent Change (%)
Interval -8.52 to 7.63
9.56 Percent Change (%)
Interval 1.47 to 17.65

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Non-High-Density Lipoprotein Cholesterol (Non-HDL-C) at Week 12
-26.85 Percent Change (%)
Interval -32.65 to -21.04
-29.86 Percent Change (%)
Interval -35.75 to -23.97
-35.13 Percent Change (%)
Interval -40.92 to -29.35
-41.65 Percent Change (%)
Interval -47.45 to -35.85
3.53 Percent Change (%)
Interval -2.33 to 9.39

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Very-Low-Density Lipoprotein Cholesterol (VLDL-C) at Week 12
1.13 Percent Change (%)
Interval -6.55 to 8.81
4.02 Percent Change (%)
Interval -3.69 to 11.73
2.21 Percent Change (%)
Interval -5.26 to 9.68
0.46 Percent Change (%)
Interval -7.15 to 8.07
7.19 Percent Change (%)
Interval -0.52 to 14.9

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Apolipoprotein A1 at Week 12
1.67 Percent Change (%)
Interval -1.0 to 4.34
3.25 Percent Change (%)
Interval 0.58 to 5.93
3.61 Percent Change (%)
Interval 1.02 to 6.21
5.72 Percent Change (%)
Interval 3.08 to 8.36
4.46 Percent Change (%)
Interval 1.8 to 7.12

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Hypothetical estimand: data collected after intercurrent events (ICEs) defined in the CSP excluded.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Apolipoprotein B at Week 12
-24.08 Percent Change (%)
Interval -28.37 to -19.8
-25.39 Percent Change (%)
Interval -29.71 to -21.07
-34.33 Percent Change (%)
Interval -38.53 to -30.12
-36.95 Percent Change (%)
Interval -41.2 to -32.71
2.92 Percent Change (%)
Interval -1.39 to 7.23

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Total Cholesterol at Week 12
-18.23 Percent Change (%)
Interval -21.88 to -14.58
-19.80 Percent Change (%)
Interval -23.54 to -16.07
-24.54 Percent Change (%)
Interval -28.14 to -20.94
-26.90 Percent Change (%)
Interval -30.6 to -23.2
1.73 Percent Change (%)
Interval -1.88 to 5.34

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of High-Density Lipoprotein Cholesterol (HDL-C) at Week 12
0.80 Percent Change (%)
Interval -2.29 to 3.89
3.66 Percent Change (%)
Interval 0.58 to 6.75
2.17 Percent Change (%)
Interval -0.85 to 5.19
4.65 Percent Change (%)
Interval 1.61 to 7.7
3.11 Percent Change (%)
Interval 0.11 to 6.12

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Triglycerides at Week 12
2.81 Percent Change (%)
Interval -5.25 to 10.86
2.17 Percent Change (%)
Interval -5.93 to 10.28
1.72 Percent Change (%)
Interval -6.09 to 9.54
-0.83 Percent Change (%)
Interval -8.87 to 7.22
9.04 Percent Change (%)
Interval 1.16 to 16.92

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Non-High-Density Lipoprotein Cholesterol (Non-HDL-C) at Week 12
-26.13 Percent Change (%)
Interval -31.94 to -20.32
-29.42 Percent Change (%)
Interval -35.34 to -23.49
-34.77 Percent Change (%)
Interval -40.59 to -28.95
-41.35 Percent Change (%)
Interval -47.27 to -35.43
2.86 Percent Change (%)
Interval -2.91 to 8.62

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Very-Low-Density Lipoprotein Cholesterol (VLDL-C) at Week 12
0.81 Percent Change (%)
Interval -6.81 to 8.43
2.67 Percent Change (%)
Interval -4.91 to 10.26
1.77 Percent Change (%)
Interval -5.59 to 9.13
0.42 Percent Change (%)
Interval -7.18 to 8.02
6.74 Percent Change (%)
Interval -0.68 to 14.15

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Apolipoprotein A1 at Week 12
2.52 Percent Change (%)
Interval -0.18 to 5.22
2.89 Percent Change (%)
Interval 0.14 to 5.64
3.79 Percent Change (%)
Interval 1.19 to 6.39
5.55 Percent Change (%)
Interval 2.88 to 8.22
3.82 Percent Change (%)
Interval 1.15 to 6.48

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Treatment policy estimand: data collected after ICEs defined in the CSP retained.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=86 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Apolipoprotein B at Week 12
-23.35 Percent Change (%)
Interval -27.79 to -18.91
-24.53 Percent Change (%)
Interval -29.06 to -19.99
-33.85 Percent Change (%)
Interval -38.18 to -29.51
-36.86 Percent Change (%)
Interval -41.35 to -32.37
2.44 Percent Change (%)
Interval -2.0 to 6.89

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment. For this outcome, only participants with both baseline and week 12 values were included in the analysis.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Descriptive statistics only.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=75 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=75 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=81 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=76 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=78 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Lipoprotein-a at Week 12
-7.48 Percent Change (%)
Interval -64.6 to 319.6
-11.16 Percent Change (%)
Interval -56.7 to 2582.3
-19.57 Percent Change (%)
Interval -66.3 to 36.6
-19.43 Percent Change (%)
Interval -71.3 to 55.6
0.00 Percent Change (%)
Interval -46.3 to 98.9

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment. For this outcome, only participants with both baseline and week 12 values were included in the analysis.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Descriptive statistics only.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=75 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=75 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=79 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=77 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=80 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of Remnant Cholesterol at Week 12
-9.09 Percent Change (%)
Interval -77.8 to 160.0
-8.33 Percent Change (%)
Interval -169.7 to 671.4
-22.95 Percent Change (%)
Interval -1200.0 to 266.7
-18.31 Percent Change (%)
Interval -200.0 to 420.0
-5.00 Percent Change (%)
Interval -85.7 to 558.3

SECONDARY outcome

Timeframe: From first day of treatment up to week 12

Population: Full Analysis Set: all randomized participants who received at least one dose of study treatment. For this outcome, only participants with both baseline and week 12 values were included in the analysis.

Percent change was calculated as (Week 12 value - Baseline value) / Baseline value \* 100. Negative values indicate reduction in lipid parameter. Baseline is the last non-missing value prior to first administration of study treatment. Descriptive statistics only.

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=75 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=75 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=82 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=77 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=79 Participants
Participants received placebo administered orally once daily for up to 12 weeks
Percent Change From Baseline of High Sensitivity C-reactive Protein (hsCRP) at Week 12
0.00 Percent Change (%)
Interval -96.8 to 2500.0
0.00 Percent Change (%)
Interval -79.8 to 716.7
0.00 Percent Change (%)
Interval -98.1 to 4950.0
-22.22 Percent Change (%)
Interval -93.3 to 2603.0
0.00 Percent Change (%)
Interval -75.7 to 1358.3

SECONDARY outcome

Timeframe: From week 1 up to week 12

Population: PK Analysis Set: all participants who received at least one dose of study treatment and who had evaluable PK data.

Geometric mean plasma concentration; LLOQ = 0.01 umol/L; BLQ values are handled as Not Quantified (NQ)

Outcome measures

Outcome measures
Measure
AZD0780 1 mg
n=85 Participants
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=83 Participants
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 Participants
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=84 Participants
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
Participants received placebo administered orally once daily for up to 12 weeks
AZD0780 Plasma Concentrations Summarized by Sampling Timepoint
Week 1
0.0790 umol/L
Geometric Coefficient of Variation 76.7603
0.2523 umol/L
Geometric Coefficient of Variation 54.0463
0.8120 umol/L
Geometric Coefficient of Variation 72.6051
2.6420 umol/L
Geometric Coefficient of Variation 58.0213
AZD0780 Plasma Concentrations Summarized by Sampling Timepoint
Week 2
0.0926 umol/L
Geometric Coefficient of Variation 71.7485
0.2639 umol/L
Geometric Coefficient of Variation 75.6804
0.8156 umol/L
Geometric Coefficient of Variation 95.1545
2.6676 umol/L
Geometric Coefficient of Variation 55.8538
AZD0780 Plasma Concentrations Summarized by Sampling Timepoint
Week 4
0.0901 umol/L
Geometric Coefficient of Variation 81.2970
0.2380 umol/L
Geometric Coefficient of Variation 98.8448
0.8393 umol/L
Geometric Coefficient of Variation 74.6636
2.7059 umol/L
Geometric Coefficient of Variation 47.5671
AZD0780 Plasma Concentrations Summarized by Sampling Timepoint
Week 8
0.0932 umol/L
Geometric Coefficient of Variation 68.6270
0.2359 umol/L
Geometric Coefficient of Variation 102.5351
0.8350 umol/L
Geometric Coefficient of Variation 92.9640
2.4911 umol/L
Geometric Coefficient of Variation 102.6420
AZD0780 Plasma Concentrations Summarized by Sampling Timepoint
Week 12
0.0957 umol/L
Geometric Coefficient of Variation 61.8573
0.2317 umol/L
Geometric Coefficient of Variation 111.2636
0.7221 umol/L
Geometric Coefficient of Variation 119.9436
2.4373 umol/L
Geometric Coefficient of Variation 134.1014

Adverse Events

AZD0780 1 mg

Serious events: 2 serious events
Other events: 4 other events
Deaths: 0 deaths

AZD0780 3 mg

Serious events: 2 serious events
Other events: 2 other events
Deaths: 0 deaths

AZD0780 10 mg

Serious events: 2 serious events
Other events: 2 other events
Deaths: 0 deaths

AZD0780 30 mg

Serious events: 1 serious events
Other events: 3 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
AZD0780 1 mg
n=86 participants at risk
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 participants at risk
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 participants at risk
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 participants at risk
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 participants at risk
Participants received placebo administered orally once daily for up to 12 weeks
Infections and infestations
Osteomyelitis
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
1.2%
1/84 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Psychiatric disorders
Major Depression
1.2%
1/86 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/84 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Infections and infestations
Colonic abscess
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
1.2%
1/85 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/84 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Lentigo maligna
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
1.2%
1/84 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Nervous system disorders
Syncope
1.2%
1/86 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/84 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Nervous system disorders
Transient ischaemic attack
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/84 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
1.2%
1/85 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Cardiac disorders
Angina pectoris
1.2%
1/86 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/84 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
Gastrointestinal disorders
Inguinal hernia
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
1.2%
1/85 • Number of events 1 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/84 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/85 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
0.00%
0/86 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.

Other adverse events

Other adverse events
Measure
AZD0780 1 mg
n=86 participants at risk
Participants received 1 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 3 mg
n=85 participants at risk
Participants received 3 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 10 mg
n=84 participants at risk
Participants received 10 mg of AZD0780 administered orally once daily for up to 12 weeks
AZD0780 30 mg
n=85 participants at risk
Participants received 30 mg of AZD0780 administered orally once daily for up to 12 weeks
Placebo
n=86 participants at risk
Participants received placebo administered orally once daily for up to 12 weeks
Vascular disorders
Hypertension
4.7%
4/86 • Number of events 4 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
2.4%
2/85 • Number of events 2 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
2.4%
2/84 • Number of events 2 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
3.5%
3/85 • Number of events 3 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.
5.8%
5/86 • Number of events 5 • Adverse events were collected from start of study treatment, throughout the 12-week treatment period, and the 2-weeks follow-up period.

Additional Information

Global Clinical Lead

AstraZeneca

Phone: 1-877-240-9479

Results disclosure agreements

  • Principal investigator is a sponsor employee No unpublished information may be disclosed without prior written approval from AstraZeneca AB.
  • Publication restrictions are in place

Restriction type: OTHER