A Study of JNJ-88549968 for the Treatment of Calreticulin (CALR)-Mutated Myeloproliferative Neoplasms

NCT ID: NCT06150157

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

100 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-20

Study Completion Date

2027-12-15

Brief Summary

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The purpose of this study is to characterize safety and to determine the Recommended Phase 2 Dose (RP2D\[s\]) and optimal dosing schedule(s) of JNJ-88549968, in part 1 (Dose Escalation); to characterize the safety of JNJ- 88549968 at RP2D(s), in part 2 (Cohort Expansion).

Detailed Description

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Conditions

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Myeloproliferative Disorders Essential Thrombocythemia Neoplasms Myelofibrosis

Study Design

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Allocation Method

NA

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Dose Escalation (Part 1) and Dose Expansion (Part 2)

In dose escalation (Part 1), participants will receive JNJ-88549968. The dose will be escalated sequentially to determine the recommended phase 2 dose (RP2D) and optimal dosing schedule(s) based on safety, pharmacokinetic, pharmacodynamic, and preliminary assessment of efficacy across several dose regimens. In dose expansion (Part 2), participants will receive JNJ-88549968 at the RP2D regimen(s) determined in dose escalation (Part 1).

Group Type EXPERIMENTAL

JNJ-88549968

Intervention Type DRUG

JNJ-88549968 will be administered.

Interventions

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JNJ-88549968

JNJ-88549968 will be administered.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Be greater than or equal to (\>=) 18 years of age (or the legal age of majority in the jurisdiction in which the study is taking place, whichever the greater) at the time of informed consent
* Positive for a calreticulin (CALR) driver mutation of essential thrombocythemia (ET) or myelofibrosis (MF)
* Participants with ET and MF with risk characteristics as described in the protocol
* Have an Eastern Cooperative Oncology Group (ECOG) performance status grade of less than or equal to (\<=) 2

Exclusion Criteria

* Known allergies, hypersensitivity, or intolerance to the excipients of the study treatment
* Concurrent or recently diagnosed or treated malignancies present at the time of participant screening. Exceptions are squamous and basal cell carcinoma of the skin, carcinoma in situ of the cervix, and any malignancy that is considered cured or has minimal risk of recurrence within 1 year of first dose of study treatment in the opinion of both the investigator and sponsor's medical monitor. Participants cured of another malignant disease with no sign of relapse greater than or equal to (\>=) 3 years after treatment ended are allowed to enter the study
* Prior solid organ transplantation
* Either of the following regarding hematopoietic stem cell transplantation:

1. Prior treatment with allogenic stem cell transplant less than or equal to (\<=) 6 months before the first dose of JNJ-88549968 or
2. Evidence of graft versus host disease (GVHD) that requires immunosuppressant therapy
* History of clinically significant cardiovascular disease within 6 months prior to the first dose of study treatment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

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City of Hope

Duarte, California, United States

Site Status RECRUITING

Moffit Cancer center

Tampa, Florida, United States

Site Status RECRUITING

University of Michigan

Ann Arbor, Michigan, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status RECRUITING

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Sarah Cannon Cancer Institute

Nashville, Tennessee, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Princess Margaret Cancer Centre University Health Network

Toronto, Ontario, Canada

Site Status RECRUITING

Jewish General Hospital

Montreal, Quebec, Canada

Site Status RECRUITING

Hopital Saint Louis

Paris, , France

Site Status RECRUITING

CH LYON SUD - Hematology

Pierre-Bénite, , France

Site Status RECRUITING

Universitaetsklinikum der RWTH Aachen

Aachen, , Germany

Site Status RECRUITING

Charite Campus Benjamin Franklin

Berlin, , Germany

Site Status RECRUITING

Med. Universitatsklinik Essen

Essen, , Germany

Site Status RECRUITING

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status RECRUITING

Universitaetsklinikum Heidelberg

Heidelberg, , Germany

Site Status RECRUITING

Universitaetsklinikum Regensburg

Regensburg, , Germany

Site Status RECRUITING

Carmel Medical Center

Haifa, , Israel

Site Status RECRUITING

Hadassah University Hospita Ein Kerem

Jerusalem, , Israel

Site Status RECRUITING

Sheba Medical Center

Ramat Gan, , Israel

Site Status RECRUITING

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status RECRUITING

Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status RECRUITING

Policlinico di Milano

Milan, , Italy

Site Status RECRUITING

Hosp. Univ. Germans Trias I Pujol

Badalona, , Spain

Site Status RECRUITING

Hosp. Clinico Univ. de Valencia

Valencia, , Spain

Site Status RECRUITING

University College London Hospitals Nhs Foundation Trust

London, , United Kingdom

Site Status RECRUITING

Guy's and St Thomas' Hospital

London, , United Kingdom

Site Status RECRUITING

Churchill Hospital

Oxford, , United Kingdom

Site Status RECRUITING

Countries

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United States Canada France Germany Israel Italy Spain United Kingdom

Central Contacts

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Study Contact

Role: CONTACT

Phone: 844-434-4210

Email: [email protected]

Other Identifiers

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88549968MPN1001

Identifier Type: OTHER

Identifier Source: secondary_id

2023-505584-36-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

88549968MPN1001

Identifier Type: -

Identifier Source: org_study_id