Ivosidenib in Participants With Locally Advanced or Metastatic Conventional Chondrosarcoma Untreated or Previously Treated With 1 Systemic Treatment Regimen

NCT ID: NCT06127407

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

136 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-07-09

Study Completion Date

2030-11-26

Brief Summary

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Study CL3-95031-007 (CHONQUER) is a Phase 3, international, multicenter, double-blind, randomized, placebo-controlled study of orally administered ivosidenib. Participants are required to have a histopathological diagnosis consistent with isocitrate dehydrogenase-1 (IDH1) gene-mutated, locally advanced or metastatic conventional chondrosarcoma Grades 1, 2, or 3 and not eligible for curative resection. IDH1 mutant status will be determined during pre-screening/screening phase. Participant must have radiographic progression/recurrence of disease according to Response Evaluation Criteria in Solid Tumors (RECIST v1.1) and have received 0 to 1 prior systemic treatment regimen in the advanced/metastatic setting for conventional chondrosarcoma. The primary endpoint is progression-free survival (PFS) in Grades 1 and 2 participants. Key secondary endpoints are PFS in all randomized participants, overall survival (OS) in Grades 1 and 2 participants, and OS in all randomized participants.

Participants who meet enrollment criteria will be randomized 1:1 to receive oral ivosidenib 500mg once daily, or a matching placebo once daily.

Detailed Description

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Conditions

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Locally Advanced or Metastatic Conventional Chondrosarcoma With an IDH1 Mutation, Untreated or Previously Treated With 1 Systemic Treatment Regimen

Keywords

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Conventional chondrosarcoma IDH1 ivosidenib locally advanced metastatic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Ivosidenib

Taken continuously until BICR-confirmed disease progression, unacceptable toxicity, confirmed pregnancy, death, withdrawal of consent, lost to follow-up, or the Sponsor ends the study (estimated average treatment duration of two years).

Group Type EXPERIMENTAL

Ivosidenib 500mg

Intervention Type DRUG

Provided as tablets, taken orally as two 250mg tablets once daily.

Placebo

Taken continuously until BICR-confirmed disease progression, unacceptable toxicity, confirmed pregnancy, death, withdrawal of consent, lost to follow-up, or the Sponsor ends the study (estimated average treatment duration of two years). Participants randomized to the placebo arm who experience BICR-confirmed disease progression and meet the crossover eligibility criteria will be given the opportunity to cross over and receive ivosidenib.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Provided as tablets, taken orally once daily.

Interventions

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Ivosidenib 500mg

Provided as tablets, taken orally as two 250mg tablets once daily.

Intervention Type DRUG

Placebo

Provided as tablets, taken orally once daily.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Have a histopathological diagnosis (fresh or banked tumor biopsy sample collected within the last 3 years) consistent with locally advanced or metastatic conventional chondrosarcoma Grades 1, 2, or 3 and not eligible for curative resection.
* Have at least one BICR-confirmed measurable lesion as defined by RECIST v1.1. Participants who have received prior radiation therapy are eligible provided measurable disease falls outside of the treatment field or within the field and has shown ≥20% growth in size since post-treatment assessment.
* Have received 0 or 1 prior systemic treatment regimen in the advanced/metastatic setting for chondrosarcoma.
* Have radiographic progression/recurrence of disease according to RECIST v1.1 defined as:

1. Radiographic progression of disease (local and/or distant) documented by 2 imaging assessments performed no more than 6 months (±2 weeks) apart within 12 months before randomization.

OR
2. Any recurrence of disease (local and/or distant) after complete surgical resection and documented by imaging within 6 months (±2 weeks) before randomization.
* Have documented IDH1 gene-mutated disease (from a fresh tumor biopsy or the most recent banked tumor tissue available that was sourced from either a primary or metastatic tumor lesion) based on central laboratory testing (R132C/L/G/H/S mutation variants tested)
* Have recovered from any clinically relevant sequelae and toxic effects of any prior surgery, radiotherapy, or other therapy intended for the treatment of cancer.

Exclusion Criteria

* Are unable to swallow oral medication.
* Pregnant or lactating women.
* Are participating in another interventional study at the same time; participation in noninterventional registries or epidemiological studies is allowed.
* Have received prior therapy with an IDH1 inhibitor
* Have received systemic anticancer therapy \<2 weeks prior to randomization (for investigational or immune-based anticancer therapy \<4 weeks).
* Have received radiotherapy \<2 weeks prior to randomization.
* Have known symptomatic brain metastases requiring steroids \>10 mg per day prednisone (or equivalent). Participants with previously diagnosed brain metastases are eligible if they have completed their treatment and have recovered from the acute effects of radiation therapy or surgery prior to randomization, have discontinued or reduced corticosteroid treatment \<=10 mg per day for these metastases for at least 4 weeks and have radiographically stable disease of brain lesions for at least 3 months prior to randomization.
* Have a history of another primary cancer, with the exception of: a) curatively resected non-melanoma skin cancer; b) curatively treated carcinoma in situ; or c) pT1-2 prostatic cancer Gleason score \<6 or d) participant is free of other primary solid or liquid tumor for ≥ 1 year prior to the start of study treatment and, in the opinion of the Investigator, the disease will not affect participant's outcome in the setting of current chondrosarcoma diagnosis.
* Have had major surgery within 4 weeks prior to randomization.
* Have significant active cardiac disease within 6 months prior to randomization, including New York Heart Association (NYHA) Class III or IV congestive heart failure; myocardial infarction; unstable angina; and/or stroke.
* Have LVEF \<40% by ECHO scan (or by other methods according to institutional practice) obtained within 28 days prior to randomization.
* Have a heart-rate corrected QT interval (using Fridericia's formula) (QTcF) ≥ 450 msec or other factors that increase the risk of QT prolongation or arrhythmic events (eg, heart failure, hypokalemia, family history of long QT interval syndrome). Participants with a bundle branch block combined with a prolonged QTcF interval may be permitted based on local cardiology assessment.
* Have known medical history of progressive multifocal leukoencephalopathy (PML).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Institut de Recherches Internationales Servier

OTHER

Sponsor Role collaborator

Servier Bio-Innovation LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Usc Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status RECRUITING

Sarcoma Oncology Research Center

Santa Monica, California, United States

Site Status RECRUITING

University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status RECRUITING

Yale Cancer Center

New Haven, Connecticut, United States

Site Status RECRUITING

Mayo Clinic - Jacksonville, Fl

Jacksonville, Florida, United States

Site Status RECRUITING

University of Miami

Miami, Florida, United States

Site Status RECRUITING

Emory Winship Cancer Institute

Atlanta, Georgia, United States

Site Status RECRUITING

Robert H. Lurie Comprehensive Cancer Center of Northwestern University

Chicago, Illinois, United States

Site Status RECRUITING

University of Iowa Hospitals & Clinics- Holden Comprehensive Cancer Center

Iowa City, Iowa, United States

Site Status RECRUITING

Johns Hopkins University

Baltimore, Maryland, United States

Site Status RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

Mayo Clinic - Rochester, Mn

Rochester, Minnesota, United States

Site Status RECRUITING

The Washington University

St Louis, Missouri, United States

Site Status RECRUITING

Nebraska Methodist Hospital

Omaha, Nebraska, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

Duke University

Durham, North Carolina, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States

Site Status RECRUITING

Oregon Health & Science University Knight Cancer Institute

Portland, Oregon, United States

Site Status RECRUITING

University of Pittsburgh Medical Center-Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status RECRUITING

The Univeristy of Texas Md Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Flinders Medical Centre

Bedford Park, , Australia

Site Status RECRUITING

Chris O'Brien Lifehouse

Camperdown, , Australia

Site Status NOT_YET_RECRUITING

Chris O'Brien Lifehouse

Camperdown, , Australia

Site Status RECRUITING

St Vincent'S Hospital Melbourne

Fitzroy, , Australia

Site Status RECRUITING

Sir Charles Gairdner Hospital

Nedlands, , Australia

Site Status RECRUITING

Princess Alexandra Hospital

Woolloongabba, , Australia

Site Status RECRUITING

Cliniques Universitaires St. Luc

Brussels, , Belgium

Site Status RECRUITING

U.Z. Gent

Ghent, , Belgium

Site Status RECRUITING

Centre Multidisciplinaire de Oncologie Medicale

Liège, , Belgium

Site Status RECRUITING

Liga Norte Riograndense Contra O Cancer

Natal, Rio Grande do Norte, Brazil

Site Status RECRUITING

Hospital de Amor - Barretos

Barretos, , Brazil

Site Status RECRUITING

Hospital Das Clínicas Da Ufmg

Belo Horizonte, , Brazil

Site Status RECRUITING

CIONC

Curitiba, , Brazil

Site Status RECRUITING

Cepon - Centro de Pesquisas Oncologicas

Florianópolis, , Brazil

Site Status RECRUITING

Fundação Amaral Carvalho - Jaú/ Sp

Jaú, , Brazil

Site Status RECRUITING

Instituto Nacional Do Câncer - Inca

Rio de Janeiro, , Brazil

Site Status RECRUITING

Icesp - Instituto Do Câncer Do Estado de São Paulo

São Paulo, , Brazil

Site Status RECRUITING

Impar Serviços Hospitalares S.A. - Hospital Nove de Julho

São Paulo, , Brazil

Site Status RECRUITING

Hospital A C Camargo

São Paulo, , Brazil

Site Status RECRUITING

Hospital Albert Einstein

São Paulo, , Brazil

Site Status RECRUITING

Alberta Health Services

Calgary, Alberta, Canada

Site Status RECRUITING

University Health Network

Toronto, Ontario, Canada

Site Status RECRUITING

Muhc Glen Site

Montreal, Quebec, Canada

Site Status RECRUITING

The First Affiliated Hospital of Sun Yat-Sen University

Guangzhou, Guangdong, China

Site Status RECRUITING

Union Hospital, Tongji Medical College, Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status RECRUITING

Shanghai Changzheng Hospital

Shang'ai, Shanghai Municipality, China

Site Status RECRUITING

Shanghai Ruijin Hospital

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Shanghai General Hospital

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

West China Hopital of Sichuan University

Chengdu, Sichuan, China

Site Status RECRUITING

The Second Affiliated Hospital Zhejiang University School of Medical

Hangzhou, Zhejiang, China

Site Status RECRUITING

Beijing Cancer Hospital

Beijing, , China

Site Status RECRUITING

Beijing Jishuitan Hospital

Beijing, , China

Site Status RECRUITING

Henan Cancer Hospital

Guangzhou, , China

Site Status RECRUITING

Aarhus Universitetshospital

Aarhus, , Denmark

Site Status RECRUITING

Herlev & Gentofte Hospital

Herlev, , Denmark

Site Status RECRUITING

Institut Bergonié

Bordeaux, , France

Site Status RECRUITING

Centre Oscar Lambret

Lille, , France

Site Status RECRUITING

Hôpital Léon Bérard

Lyon, , France

Site Status RECRUITING

Hopital de La Timone

Marseille, , France

Site Status RECRUITING

Hôpital Cochin

Paris, , France

Site Status RECRUITING

INSTITUT de CANCEROLOGIE de l'Ouest

Saint-Herblain, , France

Site Status RECRUITING

Iuct-Oncopole Institut Universitaire Du Cancer

Toulouse, , France

Site Status RECRUITING

Institut Gustave Roussy

Villejuif, , France

Site Status RECRUITING

Helios Klinikum Bad Saarow

Bad Saarow, , Germany

Site Status RECRUITING

Charite Universitatsmedizin

Berlin, , Germany

Site Status RECRUITING

Universitätsklinikum Carl Gustav Carus Dresden

Dresden, , Germany

Site Status RECRUITING

Universitatsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status RECRUITING

Universitätsmedizin Mannheim (Umm)

Mannheim, , Germany

Site Status NOT_YET_RECRUITING

Lmu Klinikum

München, , Germany

Site Status NOT_YET_RECRUITING

Ukm - Sarkom-Zentrum

Münster, , Germany

Site Status RECRUITING

Universitaetsklinikum Ulm

Ulm, , Germany

Site Status RECRUITING

Irccs Istituto Ortopedico Rizzoli

Bologna, , Italy

Site Status RECRUITING

Irccs Fondazione Istituto Nazionale Dei Tumori

Milan, , Italy

Site Status RECRUITING

San Luigi Gonzaga University Hospital of Turin

Orbassano, , Italy

Site Status RECRUITING

Istituto Oncologico Veneto Iov - Irccs

Padua, , Italy

Site Status RECRUITING

Aou Policlinico Paolo Giaccone

Palermo, , Italy

Site Status RECRUITING

Ospedale Santo Stefano

Prato, , Italy

Site Status RECRUITING

Policlinico Universitario Campus Biomedico

Roma, , Italy

Site Status RECRUITING

Istituti Fisioterapici Ospitalieri (Ifo) - Istituto Nazionale Tumori Regina Elena (Ire)

Roma, , Italy

Site Status RECRUITING

Hokkaido Cancer Center

Sapporo, Hokkaido, Japan

Site Status RECRUITING

Kanazawa University Hospital

Kanazawa, Ishikawa-ken, Japan

Site Status RECRUITING

Nagoya University Hospital

Shōwaku, Nagoya-shi, Aichi, Japan

Site Status RECRUITING

Niigata University Medical and Dental General Hospital

Chūōku, Niigata City, Japan

Site Status RECRUITING

Oita University Hospital

Yufu-Shi, Oita Prefecture, Japan

Site Status RECRUITING

Osaka International Cancer Institute

Chūōku, Osaka-shi, Osaka, Japan

Site Status RECRUITING

National Cancer Center Hospital

Chuo-ku, Tokyo, , Japan

Site Status RECRUITING

Fukushima Medical University Hospital

Fukushima, , Japan

Site Status RECRUITING

Kyushu University Hospital

Higashi, , Japan

Site Status RECRUITING

Cancer Institute Hospital of Jfcr

Koto-Ku, Tokyo, , Japan

Site Status RECRUITING

Okayama University Hospital

Okayama, , Japan

Site Status RECRUITING

Universitair Medisch Centrum Groningen (Umcg)

Groningen, , Netherlands

Site Status RECRUITING

Leids Universitair Medisch Centrum

Leiden, , Netherlands

Site Status RECRUITING

Radboud Umc

Nijmegen, , Netherlands

Site Status RECRUITING

Pan American Center For Oncology Trials, LLC

Rio Piedras, , Puerto Rico

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status RECRUITING

Severance Hospital

Seoul, , South Korea

Site Status RECRUITING

Asan Medical Center

Seoul, , South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status RECRUITING

Hospital Universitario Valle de Hebrón - Vhio

Barcelona, , Spain

Site Status RECRUITING

Hospital de La Santa Creu I Sant Pau

Barcelona, , Spain

Site Status RECRUITING

Hospital de Bellvitge - Ico

L'Hospitalet de Llobregat, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Fundación Jiménez Díaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Y Politecnico La Fe

Valencia, , Spain

Site Status RECRUITING

National Taiwan University Hospital

Taipei, , Taiwan

Site Status RECRUITING

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status RECRUITING

Western General Hospital

Edinburgh, , United Kingdom

Site Status RECRUITING

Royal Marsden Hospital

London, , United Kingdom

Site Status RECRUITING

UCLH

London, , United Kingdom

Site Status RECRUITING

Christie Hospital

Manchester, , United Kingdom

Site Status RECRUITING

Churchill Hospital

Oxford, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Belgium Brazil Canada China Denmark France Germany Italy Japan Netherlands Puerto Rico South Korea Spain Taiwan United Kingdom

Central Contacts

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Institut de Recherches Internationales Servier (I.R.I.S.), Clinical Studies Department

Role: CONTACT

Phone: +33 1 55 72 60 00

Email: [email protected]

Facility Contacts

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Victoria Chua-Alcala, MD

Role: primary

Sharon Huie

Role: primary

Steven Attia, Dr

Role: primary

William Read

Role: primary

DFCI Sarcoma Center

Role: primary

Role: primary

Richard Riedel, MD

Role: primary

Role: primary

Luiza Stoeva

Role: primary

OHSU Clinical Trials Office

Role: primary

Clinical Research Coordinator

Role: primary

Role: primary

Role: backup

Vivek Bhadri, MD

Role: primary

Melissa Moore, Dr

Role: primary

Vladimir Andelkovic, Dr

Role: primary

Matthew Young

Role: primary

Role: primary

Role: primary

Daniel Pink, MD

Role: primary

Simone Micheel

Role: backup

Uniklinik Dresden Studiensekretariat Onkologie

Role: primary

PD. Dr. med. Torsten Keßler

Role: primary

Dr. Lorenzo D'Ambrosio

Role: primary

Baldi Giacomo Giulio

Role: primary

Role: backup

Bruno Vincenzi, MD

Role: primary

Role: primary

Role: primary

Role: primary

Jacco de Haan

Role: primary

Hans Gelderblom

Role: primary

Ingrid Desar

Role: primary

Claudia Valverde

Role: primary

Nadia Hindi

Role: primary

Javier Martin Broto

Role: backup

Roberto Díaz Beveridge, MD

Role: primary

Wei-Wu Chen

Role: primary

Po-Kuei Wu

Role: primary

Carla Dalton

Role: primary

Anna Mazepa

Role: backup

References

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Tap WD, Cote GM, Burris H, Gore L, Elias A, Beeram M, Conley AP, Gianolio DA, Qu Z, Pandya S, Trent JC. Phase I Study of the Mutant IDH1 Inhibitor Ivosidenib: Long-term Safety and Clinical Activity in Patients with Conventional Chondrosarcoma. Clin Cancer Res. 2025 Jun 3;31(11):2108-2114. doi: 10.1158/1078-0432.CCR-24-4128.

Reference Type DERIVED
PMID: 40100120 (View on PubMed)

Related Links

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https://chonquer.com/en-us/

CHONQUER Study Website

Other Identifiers

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CL3-95031-007

Identifier Type: -

Identifier Source: org_study_id