BGB-43395 Alone or as Part of Combination Therapies in Participants With Breast Cancer and Other Advanced Solid Tumors

NCT ID: NCT06120283

Last Updated: 2025-12-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

300 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-01

Study Completion Date

2028-06-30

Brief Summary

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This is a dose escalation and dose expansion study to compare how well BGB-43395, a selective cyclin-dependent kinase 4 (CDK4) inhibitor, works as monotherapy or in combination with fulvestrant, letrozole, or elacestrant in participants with hormone receptor positive (HR+) and human epidermal growth factor 2 negative (HER2-) breast cancer (BC) and other advanced solid tumors. The main purpose of this study is to explore the recommended dosing for BGB-43395.

Detailed Description

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Conditions

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Advanced Solid Tumor Advanced Breast Cancer Metastatic Breast Cancer Hormone-receptor-positive Breast Cancer Hormone Receptor Positive Breast Carcinoma Hormone Receptor Positive Malignant Neoplasm of Breast HER2-negative Breast Cancer Hormone Receptor Positive HER-2 Negative Breast Cancer Non-small Cell Lung Cancer

Keywords

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breast cancer advanced solid tumor advanced breast cancer hormone receptor positive breast cancer HER2-negative breast cancer Hormone Receptor Positive HER-2 Negative Breast Cancer BGB-43395 non-small cell lung cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Dose Escalation and Safety Expansion

Phase 1a: Sequential cohorts of increasing dose levels of BGB-43395 will be evaluated as monotherapy and in combination with either fulvestrant, letrozole, or elacestrant to assess for safety and tolerability.

Group Type EXPERIMENTAL

BGB-43395

Intervention Type DRUG

Planned doses administered orally.

Fulvestrant

Intervention Type DRUG

Standard dose administered via intramuscular injection.

Letrozole

Intervention Type DRUG

Standard dose administered orally as a tablet.

Elacestrant

Intervention Type DRUG

Standard dose administered orally as a tablet.

Dose Expansion

Phase 1b: The recommended dose for expansion (RFDE) for BGB-43395 (in combination with fulvestrant or letrozole) from Phase 1a will be evaluated in HR+ breast cancer and selected tumor-specific cohorts.

Group Type EXPERIMENTAL

BGB-43395

Intervention Type DRUG

Planned doses administered orally.

Fulvestrant

Intervention Type DRUG

Standard dose administered via intramuscular injection.

Letrozole

Intervention Type DRUG

Standard dose administered orally as a tablet.

Interventions

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BGB-43395

Planned doses administered orally.

Intervention Type DRUG

Fulvestrant

Standard dose administered via intramuscular injection.

Intervention Type DRUG

Letrozole

Standard dose administered orally as a tablet.

Intervention Type DRUG

Elacestrant

Standard dose administered orally as a tablet.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Phase 1a (Dose Escalation) and 1b (Dose Expansion): Participants with histologically or cytologically confirmed advanced, metastatic, or unresectable solid tumors associated with dependency on CDK4, including HR+ breast cancer, ovarian cancer, endometrial cancer, non-small cell lung cancer, and others.
* Phase 1a: Received prior therapy for their condition (if available) and should be refractory to, or intolerant of standard-of-care therapies. In regions where approved and available, participants with HR+ breast cancer must have received at least 2 prior lines of treatment including endocrine therapy and a CDK4/6 inhibitor. For combination with elacestrant, participants must have received at least 1 prior line of treatment for advanced/metastatic disease including prior endocrine therapy and CDK4/6 inhibitor in either the adjuvant or advanced/metastatic setting.
* Phase 1b: Selected tumor cohorts will include HR+/HER2- breast cancer and additional tumor types.
* Phase 1b: Participants with HR+/HER2- breast cancer enrolled in regions where CDK4/6 inhibitors are approved and available must have received at least one line of therapy for advanced disease including endocrine therapy and a CDK4/6 inhibitor. Participants can have received up to 2 lines of prior cytotoxic chemotherapy for advanced disease.
* Stable Eastern Cooperative Oncology Group (ECOG) Performance Status ≤ 1.
* Female participants with metastatic HR+/HER2- breast cancer must be postmenopausal or receiving ovarian function suppression treatment.
* Adequate organ function without symptomatic visceral disease.

Exclusion Criteria

* Prior therapy selectively targeting CDK4 (prior CDK4/6 inhibitor therapy is permitted and required in local regions where it is approved and available).
* Known leptomeningeal disease or uncontrolled, untreated brain metastases.
* Any malignancy ≤ 3 years before the first dose of study treatment(s) except for the specific cancer under investigation in this study and any locally recurring cancer that has been treated with curative intent (eg, resected basal or squamous cell skin cancer, superficial bladder cancer, or carcinoma in situ of the cervix or breast).
* Uncontrolled diabetes.
* Infection requiring systemic antibacterial, antifungal, or antiviral therapy ≤ 28 days before the first dose of study drug(s), or symptomatic COVID-19 infection.
* Participants with untreated chronic hepatitis B or chronic hepatitis B virus (HBV) carriers with HBV DNA ≥ 500 IU/mL (or ≥ 2500 copies/mL) at screening.
* Participants with active hepatitis C infection.
* Prior allogeneic stem cell transplantation, or organ transplantation.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BeiGene

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

BeiGene

Locations

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Sarah Cannon Research Institute (Scri) At Health One

Denver, Colorado, United States

Site Status RECRUITING

Florida Cancer Specialists and Research Institute

Lake Mary, Florida, United States

Site Status RECRUITING

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status COMPLETED

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Duke Cancer Center

Durham, North Carolina, United States

Site Status RECRUITING

James Cancer Hospital and Solove Research Institute

Columbus, Ohio, United States

Site Status RECRUITING

Scri Oncology Partners

Nashville, Tennessee, United States

Site Status RECRUITING

Next Oncology

Austin, Texas, United States

Site Status RECRUITING

The University of Texas Md Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Next Dallas

Irving, Texas, United States

Site Status RECRUITING

Blacktown Cancer and Haematology Centre

Blacktown, New South Wales, Australia

Site Status RECRUITING

Southern Highlands Private Hospital

Bowral, New South Wales, Australia

Site Status RECRUITING

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status RECRUITING

Macquarie University

North Ryde, New South Wales, Australia

Site Status RECRUITING

Townsville University Hospital

Douglas, Queensland, Australia

Site Status RECRUITING

Genesiscare St Andrews

Adelaide, South Australia, Australia

Site Status RECRUITING

Austin Health

Heidelberg, Victoria, Australia

Site Status RECRUITING

Peter Maccallum Cancer Centre

Melbourne, Victoria, Australia

Site Status RECRUITING

Fundacao Pio Xii Hospital de Amor de Barretos

Barretos, , Brazil

Site Status RECRUITING

Hospital Sirio Libanes Brasilia

Brasília, , Brazil

Site Status RECRUITING

Centro de Pesquisas Oncologicas Cepon

Florianópolis, , Brazil

Site Status RECRUITING

Liga Norte Riograndene Contra O Cancer

Natal, , Brazil

Site Status RECRUITING

Fundacao Universidade de Caxias Do Sul Instituto de Pesquisas Em Saude

Petrópolis, , Brazil

Site Status RECRUITING

Hospital Sao Lucas Da Pucrs Uniao Brasileira de Educacao E Assistencia

Porto Algre, , Brazil

Site Status RECRUITING

Instituto Nacional de Cancer

Rio de Janeiro, , Brazil

Site Status RECRUITING

Instituto Dor de Pesquisa E Ensino Hospital Sao Rafael

Salvador, , Brazil

Site Status RECRUITING

Icesp Instituto Do Cancer Do Estado de Sao Paulo Octavio Frias de Oliveira

São Paulo, , Brazil

Site Status RECRUITING

Clinica de Pesquisa E Centro de Estudos Em Oncologia Ginecologica E Mamaria

São Paulo, , Brazil

Site Status RECRUITING

Hospital Israelita Albert Einstein

São Paulo, , Brazil

Site Status RECRUITING

Beijing Cancer Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

Fujian Cancer Hospital

Fuzhou, Fujian, China

Site Status RECRUITING

Sun Yat Sen Memorial Hospital, Sun Yat Sen University (South)

Guangzhou, Guangdong, China

Site Status RECRUITING

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, China

Site Status RECRUITING

The First Affiliated Hospital of Nanchang University Branch Donghu

Nanchang, Jiangxi, China

Site Status RECRUITING

Liaoning Cancer Hospital and Institute

Shenyang, Liaoning, China

Site Status RECRUITING

Fudan University Shanghai Cancer Centerpudong

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Centre de Lutte Contre Le Cancer Institut Bergonie

Bordeaux, , France

Site Status RECRUITING

Centre Francois Baclesse

Caen, , France

Site Status RECRUITING

Centre Oscar Lambret

Lille, , France

Site Status RECRUITING

Institut Paoli Calmettes

Marseille, , France

Site Status RECRUITING

Institut Curie

Paris, , France

Site Status RECRUITING

Centre Eugene Marquis

Rennes, , France

Site Status RECRUITING

Institut de Cancerologie de Louest

Saint-Herblain, , France

Site Status RECRUITING

Institut Gustave Roussy

Villejuif, , France

Site Status RECRUITING

Nagoya University Hospital

Nagoya, Aichi-ken, Japan

Site Status RECRUITING

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status RECRUITING

Shizuoka Cancer Center

Suntogun, Shizuoka, Japan

Site Status RECRUITING

Pulau Pinang Hospital

George Town, , Malaysia

Site Status RECRUITING

University Malaya Medical Centre

Kuala Lumpur, , Malaysia

Site Status RECRUITING

Sarawak General Hospital

Kuching, , Malaysia

Site Status RECRUITING

National Cancer Institute (Institut Kanser Negara)

Putrajaya, , Malaysia

Site Status RECRUITING

The Institute of Oncology, Arensia Exploratory Medicine

Chisinau, , Moldova

Site Status ACTIVE_NOT_RECRUITING

Harbour Cancer and Wellness

Auckland, , New Zealand

Site Status RECRUITING

Nzcr Christchurch

Christchurch, , New Zealand

Site Status RECRUITING

Seoul National University Bundang Hospital

BundangGu SeongnamSi, Gyeonggi-do, South Korea

Site Status RECRUITING

Gachon University Gil Medical Center

NamdongGu, Incheon Gwang'yeogsi, South Korea

Site Status RECRUITING

Samsung Medical Center

GangnamGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

The Catholic University of Korea, Seoul St Marys Hospital

SeochoGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Severance Hospital Yonsei University Health System

SeodaemunGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Korea University Anam Hospital

SeongbukGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Asan Medical Center

SongpaGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Srinagarind Hospital (Khon Kaen University)

Muang, , Thailand

Site Status ACTIVE_NOT_RECRUITING

Countries

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United States Australia Brazil China France Japan Malaysia Moldova New Zealand South Korea Thailand

Central Contacts

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Study Director

Role: CONTACT

Phone: 1.877.828.5568

Email: [email protected]

Other Identifiers

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2023-506888-34-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CTR20243370

Identifier Type: REGISTRY

Identifier Source: secondary_id

BGB-43395-101

Identifier Type: -

Identifier Source: org_study_id