Study to Assess the Efficacy & Safety of KHK4951 in Patients With Neovascular Age-Related Macular Degeneration

NCT ID: NCT06116890

Last Updated: 2025-10-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

180 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-01-31

Study Completion Date

2026-09-30

Brief Summary

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The purpose of this study is to evaluate efficacy and safety of KHK4951 eye drops in patients with nAMD.

Detailed Description

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Conditions

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Neovascular Age-Related Macular Degeneration (nAMD)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Arm A

KHK4951 High dose

Group Type EXPERIMENTAL

KHK4951

Intervention Type DRUG

KHK4951 eye drop for 44 weeks until end of the trial

Aflibercept Injection

Intervention Type DRUG

Intravitreal injection (IVT) of aflibercept will be given as specified in the protocol

Arm B

KHK4951 Middle dose

Group Type EXPERIMENTAL

KHK4951

Intervention Type DRUG

KHK4951 eye drop for 44 weeks until end of the trial

Aflibercept Injection

Intervention Type DRUG

Intravitreal injection (IVT) of aflibercept will be given as specified in the protocol

Arm C

KHK4951 Low dose

Group Type EXPERIMENTAL

KHK4951

Intervention Type DRUG

KHK4951 eye drop for 44 weeks until end of the trial

Aflibercept Injection

Intervention Type DRUG

Intravitreal injection (IVT) of aflibercept will be given as specified in the protocol

Interventions

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KHK4951

KHK4951 eye drop for 44 weeks until end of the trial

Intervention Type DRUG

Aflibercept Injection

Intravitreal injection (IVT) of aflibercept will be given as specified in the protocol

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Voluntary written informed consent to participate in the study
* Active subfoveal MNV (any subtype) or juxtafoveal/extrafoveal MNV secondary to AMD with a subfoveal component related to the MNV activity in the study eye as assessed by FA (evidence of leakage) or SD-OCT (presence of fluid) judged by the central reading center at screening
* BCVA ETDRS letter score of 78 letters to 35 letters in the study eye as measured by the ETDRS visual acuity chart at screening
* CST ≥ 450 μm at screening

Exclusion Criteria

* Subretinal hemorrhage, fibrosis, or atrophy of \> 50% of the total lesion area and/or that involves the fovea in the study eye
* Uncontrolled glaucoma in the study eye
* Aphakia or pseudophakia with AC-IOL in the study eye
* Active intraocular inflammation in the study eye
* Any current ocular condition for which visual acuity loss would not improve from resolution of macular edema in the study eye
* History of rhegmatogenous retinal detachment in the study eye
* Any current or history of ocular disease other than nAMD in the study eye that may confound assessment of the macula or affect central vision
* History of the following therapies in the study eye:

* History of vitrectomy surgery, submacular surgery, or other surgical intervention for AMD
* Prior treatment PDT with Visudyne®, external-beam radiation therapy, transpupillary thermotherapy, or panretinal photocoagulation
* Periocular or intraocular (sub-Tenon or IVT) corticosteroids within 12 weeks prior to Day 1
* Previous intraocular device implantation except PC-IOL
* Previous laser (any type) to the macular area
* Previous treatment with IVT anti-VEGF drugs other than ranibizumab, bevacizumab, aflibercept 2 mg, and their biosimilars;
* Treatment with ranibizumab, bevacizumab, aflibercept 2 mg, or their biosimilars within 12 weeks prior to Day 1. Previously treated patients who received these medications more than 12 weeks prior to Day 1 can be enrolled, but the patients should be diagnosed with nAMD within 3 years prior to Day 1
* Any current or history of endophthalmitis in either eye
* History of idiopathic or autoimmune-associated uveitis in either eye
* Active infectious conjunctivitis, keratitis, scleritis, or endophthalmitis in either eye
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kyowa Kirin Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sotaro Takigawa

Role: STUDY_DIRECTOR

Kyowa Kirin Co., Ltd.

Locations

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Barnet Dulaney Perkins Eye Center - Phoenix

Mesa, Arizona, United States

Site Status

Retina Associates Southwest, P.C.

Tucson, Arizona, United States

Site Status

Win Retina

Arcadia, California, United States

Site Status

Retina Vitreous Associates Medical Group

Beverly Hills, California, United States

Site Status

The Retina Partners

Encino, California, United States

Site Status

Salehi Retina Institute, Inc

Huntington Beach, California, United States

Site Status

Payam Amini

Pasadena, California, United States

Site Status

Retina Consultants of Southern CO

Colorado Springs, Colorado, United States

Site Status

Blue Ocean Clinical Research West

Clearwater, Florida, United States

Site Status

Florida Eye Associates

Melbourne, Florida, United States

Site Status

Eye Associates of Pinellas

Pinellas Park, Florida, United States

Site Status

Ft. Lauderdale Eye Institute

Plantation, Florida, United States

Site Status

Retina Vitreous Associates of Florida - Saint Petersburg

St. Petersburg, Florida, United States

Site Status

Southern Vitreoretinal Associates

Tallahassee, Florida, United States

Site Status

Center for Retina and Macular Disease - Ophthalmology

Winter Haven, Florida, United States

Site Status

Southeast Retina Center

Augusta, Georgia, United States

Site Status

Massachusetts Eye and Ear

Boston, Massachusetts, United States

Site Status

Associated Retinal Consultants (ARC) P.C. - Opthalmology

Royal Oak, Michigan, United States

Site Status

Sierra Eye Associates

Reno, Nevada, United States

Site Status

Retina Center of New Jersey

Bloomfield, New Jersey, United States

Site Status

Vision Research Center Eye Associates of New Mexico

Albuquerque, New Mexico, United States

Site Status

Retina Vitreous Surgeons of Central NY, PC

Liverpool, New York, United States

Site Status

Ophthalmic Consultants of Long Island

Oceanside, New York, United States

Site Status

Retina Vitreous Center in Edmond Oklahoma

Edmond, Oklahoma, United States

Site Status

Eye Health Northwest

Portland, Oregon, United States

Site Status

Eye Care Specialists

Kingston, Pennsylvania, United States

Site Status

Charleston Neuroscience Institute (RCA Network Site)

Ladson, South Carolina, United States

Site Status

Black Hills Regional Eye Institute - Ophthalmology

Rapid City, South Dakota, United States

Site Status

Charles Retina Institute

Germantown, Tennessee, United States

Site Status

Retina Research Institute of Texas

Abilene, Texas, United States

Site Status

Austin Retina Associates - Ophthalmology/Retina (RCA Network site)

Austin, Texas, United States

Site Status

Austin Clinical Research, LLC

Austin, Texas, United States

Site Status

Retina Consultants of Texas

Bellaire, Texas, United States

Site Status

Texas Retina Associates

Fort Worth, Texas, United States

Site Status

Retinal Consultants of Texas- San Antonio (RCA Network site)

San Antonio, Texas, United States

Site Status

Retina Consultants of Texas (RCA Network Site)

The Woodlands, Texas, United States

Site Status

Strategic Clinical Research Group, LLC

Willow Park, Texas, United States

Site Status

Retina Group of Washington

Fairfax, Virginia, United States

Site Status

Eye Clinic Albury Wodonga

Albury, New South Wales, Australia

Site Status

Marsden Eye Specialists

Parramatta, New South Wales, Australia

Site Status

Strathfield Retina Clinic

Strathfield, New South Wales, Australia

Site Status

Sydney Eye Hospital

Sydney, New South Wales, Australia

Site Status

Adelaide Eye and Retina Centre

Adelaide, South Australia, Australia

Site Status

Centre for Eye Research Australia

East Melbourne, Victoria, Australia

Site Status

Aichi Medical University Hospital - Ophthalmology

Nagakute, Aichi-ken, Japan

Site Status

MIYAKE Eye Hospital

Nagoya, Aichi-ken, Japan

Site Status

Toho University Medical Center Sakura Hospital

Sakura, Chiba, Japan

Site Status

Matsuyama Red Cross Hospital

Matsuyama, Ehime, Japan

Site Status

Hayashi Eye Hospital - Ophthalmology

Fukuoka, Fukuoka, Japan

Site Status

Kurume University Hospital

Kurume, Fukuoka, Japan

Site Status

Minamitohoku Eye Clinic

Kōriyama, Fukushima, Japan

Site Status

Caress Sapporo Tokeidai Memorial Hospital

Sapporo, Hokkaido, Japan

Site Status

Kobe University Hospital - Ophthalmology

Kobe, Hyôgo, Japan

Site Status

Kozawa Eye Hospital and Diabetes Center

Mito, Ibaraki, Japan

Site Status

Kagawa University Hospital

Kita-gun, Kanagawa, Japan

Site Status

Shinshu University Hospital - Ophthalmology

Matsumoto, Nagano, Japan

Site Status

Nara Medical University Hospital - Ophthalmology

Kashihara, Nara, Japan

Site Status

University of the Ryukyus Hospital

Nakagami-gun, Okinawa, Japan

Site Status

Kansai Medical University Medical Center

Hirakata, Osaka, Japan

Site Status

Kindai University Hospital

Sayama, Osaka, Japan

Site Status

Jichi Medical University Hospital

Shimotsuke, Tochigi, Japan

Site Status

The University of Tokyo Hospital

Bunkyō, Tokyo, Japan

Site Status

Nihon University Hospital

Chiyoda City, Tokyo, Japan

Site Status

Tokyo Medical University Hachioji Medical Center

Hachiōji, Tokyo, Japan

Site Status

Tokyo Medical Center

Meguro City, Tokyo, Japan

Site Status

Keio University Hospital - Ophthalmology

Shinjuku, Tôkyô, Japan

Site Status

Fukushima Medical University Hospital - Ophthalmology

Fukushima, , Japan

Site Status

Rakuwakai Otowa Hospital

Kyoto, , Japan

Site Status

Okayama University Hospital - Ophthalmology

Okayama, , Japan

Site Status

Saitama Red Cross Hospital

Saitama, , Japan

Site Status

Osaka Metropolitan University Hospital

Osaka, Ôsaka, Japan

Site Status

Keimyung University Dongsan Hospital

Daegu, Dalseo-gu, South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam, Gyeonggido, South Korea

Site Status

CHA Bundang Medical Center, CHA University

Seongnam-si, Gyeonggido, South Korea

Site Status

Yeungnam University Hospital

Daegu, Nam-gu, South Korea

Site Status

Gachon University Gil Medical Center

Incheon, Namdong-gu, South Korea

Site Status

Kyung Hee University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Korea University Anam Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Seoul National University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Asan Medical Center

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Samsung Medical Center

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Kim Eye Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Countries

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United States Australia Japan South Korea

Other Identifiers

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4951-002

Identifier Type: -

Identifier Source: org_study_id

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