A Study to Evaluate the Safety, Tolerability and Efficacy of RZ-001 With Valganciclovir (VGCV) in Subjects With Glioblastoma

NCT ID: NCT06102525

Last Updated: 2025-09-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

43 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-08

Study Completion Date

2029-05-31

Brief Summary

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This is a Phase 1/2a, open-label study to evaluate the safety, tolerability, immunogenicity, and preliminary clinical activity of RZ-001 administered in combination with VGCV in subjects with hTERT-positive GBM.

Detailed Description

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The study consists of 2 parts: a dose-escalation part (Part 1) and a dose-expansion part (Part 2).

Part 1 consists of dose escalation exploring MTD/RP2D for intratumoral (IT) injection.

Part 2 will consist of dose expansion exploring clinical activity for the optimal fixed dose based on the results of Part 1.

Conditions

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Glioblastoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1 Cohort 1

RZ-001 Dose 1 and VGCV

Group Type EXPERIMENTAL

RZ-001

Intervention Type DRUG

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

VGCV

Intervention Type COMBINATION_PRODUCT

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Part 1 Cohort 2

RZ-001 Dose 2 and VGCV

Group Type EXPERIMENTAL

RZ-001

Intervention Type DRUG

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

VGCV

Intervention Type COMBINATION_PRODUCT

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Part 1 Cohort 3

RZ-001 Dose 3 and VGCV

Group Type EXPERIMENTAL

RZ-001

Intervention Type DRUG

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

VGCV

Intervention Type COMBINATION_PRODUCT

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Part 1 Cohort 4

RZ-001 Dose 4 and VGCV

Group Type EXPERIMENTAL

RZ-001

Intervention Type DRUG

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

VGCV

Intervention Type COMBINATION_PRODUCT

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Part 1 Cohort 5

RZ-001 Dose 5 and VGCV

Group Type EXPERIMENTAL

RZ-001

Intervention Type DRUG

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

VGCV

Intervention Type COMBINATION_PRODUCT

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Part 2

RZ-001 Dose 6 and VGCV

Group Type EXPERIMENTAL

RZ-001

Intervention Type DRUG

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

VGCV

Intervention Type COMBINATION_PRODUCT

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Interventions

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RZ-001

Recombinant adenovirus harboring the modified ribozyme construct with HSV-tk as a therapeutic transgene

Intervention Type DRUG

VGCV

VGCV, used in a subject after RZ-001 administration, is a nucleoside analog that is metabolized by HSV-tk and other cellular kinases to form the cytotoxic nucleotide analog ganciclovir triphosphate. An approved oral VGCV will be used in the proposed clinical study of RZ-001.

Intervention Type COMBINATION_PRODUCT

Other Intervention Names

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Ad-ECRT-122T Valganciclovir

Eligibility Criteria

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Inclusion Criteria

* Adult males and females
* Histologically-confirmed grade 4 astrocytoma, GBM, per The 2021 WHO Classification of CNS Tumors.
* hTERT positive expression confirmed during the screening period
* ECOG score of ≤ 2
* KPS ≥ 60
* Life expectancy ≥ 3 months

Exclusion Criteria

* Diagnosis of other malignant tumors within 5 years prior to RZ-001 administration.
* Have extracranial metastases of the tumor cells
* Current or history of HIV positive
* Not suitable for inclusion judged by the investigator
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Rznomics, Inc.

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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The Catholic University of Korea, Incheon St. Mary's Hospital

Incheon, , South Korea

Site Status RECRUITING

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status RECRUITING

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status RECRUITING

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status RECRUITING

Asan Medical Center

Seoul, , South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status RECRUITING

Countries

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South Korea

Central Contacts

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Rznomics Inc.

Role: CONTACT

+82317068730

Facility Contacts

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The Catholic University of Korea, Incheon St. Mary's Hospital

Role: primary

Gachon University Gil Medical Center

Role: primary

Seoul National University Bundang Hospital

Role: primary

Severance Hospital, Yonsei University Health System

Role: primary

Asan Medical Center

Role: primary

Samsung Medical Center

Role: primary

Other Identifiers

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RZ-001-201

Identifier Type: -

Identifier Source: org_study_id

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