Cryoablation Versus Medical Therapy in Desmoid Tumors Progressing After Watchful Waiting

NCT ID: NCT06081400

Last Updated: 2025-11-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

NA

Total Enrollment

150 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-03-04

Study Completion Date

2029-06-30

Brief Summary

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"Wait \& see" is currently the standard of care of recently diagnosed desmoid tumors (DT). In case of progression or symptomatic disease, medical therapy is nowadays widely used including chemotherapy.

Cryoablation has proven to be beneficial for the treatment of large, progressive and symptomatic DT.

This randomized phase II trial aims to compare cryoablation versus medical therapy in DT patients progressing after the "wait \& see" period. Moreover, a cross-over design has been anticipated to allow all patients to undergo cryoablation if necessary.

Detailed Description

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Conditions

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Desmoid Tumor

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cryoablation

One single cryoablation of the desmoid tumor at Day 0

Group Type EXPERIMENTAL

Cryoablation

Intervention Type PROCEDURE

Percutaneous imaging-guided cryoablation

Medical therapy

Chemotherapy: at the investigator's discretion: either

* methotrexate 30mg/m² + vinblastine 6mg/m² (IV infusion) once/week for 6 months, then every other week from months 7 to 12, or
* vinorelbine : for adults: 90mg/week (per os: 3x30mg, soft capsules) for 12 months. for adolescents: 60mg/m2/week (capped at 90mg/week) for 12 months

Group Type ACTIVE_COMPARATOR

Chemotherapy drug

Intervention Type DRUG

Either :

methotrexate 30mg/m² + vinblastine 6mg/m² (IV infusion) once/week for 6 months, then every other week from months 7 to 12, or vinorelbine : for adults : 90mg/week (per os: 3x30mg, soft capsules) for 12 months; for adolescents: 60mg/m2/week (capped at 90mg/week) for 12 months

Interventions

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Cryoablation

Percutaneous imaging-guided cryoablation

Intervention Type PROCEDURE

Chemotherapy drug

Either :

methotrexate 30mg/m² + vinblastine 6mg/m² (IV infusion) once/week for 6 months, then every other week from months 7 to 12, or vinorelbine : for adults : 90mg/week (per os: 3x30mg, soft capsules) for 12 months; for adolescents: 60mg/m2/week (capped at 90mg/week) for 12 months

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subject (male or female) with extra-peritoneal desmoid tumor (confirmed by prior biopsy by an experienced pathologist within the RRePS network)
* 13 years of age or older
* Measurable viable tumor (according to the mRECIST criteria using MRI. The baseline MRI imaging is mandatory in the 2 months prior to treatment initiation (D0).
* Progressive disease (according to the mRECIST criteria) after the watchful waiting period or significant increase in symptoms requiring an active therapy, as advised in a multidisciplinary sarcoma tumor board
* Tumor deemed accessible for cryoablation procedure by the operator in a type I center. (In pediatric cases, a careful site tumor analysis will be performed with interventional radiologist to ensure for limited consequence of cryoablation in pediatric patients especially regarding growth plates).
* 100 % of destruction of the tumor achievable in one procedure of cryoablation with 1cm security margin according to assessment by referral center (type 1) for cryoablation
* ECOG performance status 0-2 at inclusion visit
* Biological and hematological parameters (neutrophils ≥ 1,5.109/L ; platelet count ≥ 100.109/L ; no significant hemostatic abnormalities) in the 4 weeks prior to treatment initiation (D0)
* Subject able to understand the objectives and risks of the research and to give dated and signed informed consent. For minors, the consent of the 2 parents must be obtained.
* Subject affiliated to a social health insurance plan
* For a woman of childbearing age: negative blood pregnancy test at screening/inclusion visit
* Subject agreeing to use a contraceptive method

Exclusion Criteria

* Intra-peritoneal or multifocal desmoid tumor
* Concurrent or prior use of any antitumor agent for the current desmoid tumor
* Relapse after surgery for desmoid tumor
* Any contraindication including known hypersensitivity to vinorelbine or other vinca-alkaloids, or other constituents to navelbine, to vinblastine, to methotrexate or any excipients, such as, but not limited to current or recent (within 2 weeks) severe infection, severe renal failure, severe hepatic injury, chronic respiratory failure
* Any contraindication including hypersensitivity to gadoteric acid, meglumine or any drug containing gadolinium
* Concomitant treatment with: yellow fever vaccine, prophylactic treatment with phenytoin, trimethoprim, ciprofloxacin, penicillins, probenecid, acetylsalicylic acid, NSAIDs, PPIs, acitretin, azote protoxide, St John's wort
* Any contra-indication for the procedure as stated by the interventional radiologist in terms of tumor size, proximity to neural/vascular structures or adjacent organs at risk making the procedure at unacceptable risk
* Impaired hemostasis, that may interfere with the conduct of the cryoablation
* Contraindication to any form of sedation
* Others contra-indications to MRI
* Pregnancy or breastfeeding
* Concurrent participation in other experimental studies that could affect endpoints of the present study
* Impossibility to give the subject informed information (subject in an emergency situation, patient with comprehension difficulties ...)
* Psychiatric disorders
* Incompetent subject (subject to a legal protection measure: curatorship, guardianship, future protection mandate, family habilitation)
Minimum Eligible Age

13 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Direction Générale de l'Offre des Soins (DGOS)

UNKNOWN

Sponsor Role collaborator

University Hospital, Strasbourg, France

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Afshin GANGI, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Hôpitaux Universitaires de Strasbourg

Locations

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Service d'oncologie/CHU de Besançon

Besançon, , France

Site Status NOT_YET_RECRUITING

Service d'Oncologie Médicale, Service de Radiologie Interventionnelle, Institut BERGONNIE

Bordeaux, , France

Site Status RECRUITING

Service d'Oncologie Médicale, Service de Radiologie Interventionnelle-Centre François BACLESSE

Caen, , France

Site Status RECRUITING

Service d'Oncologie Médicale -Centre Georges François LECLERC

Dijon, , France

Site Status RECRUITING

Service d'Oncologie Médicale, Service de Radiologie Interventionnelle-Centre Léon BERARD

Lyon, , France

Site Status RECRUITING

Service d'Oncologie Médicale, service de Radiologie Interventionnelle,CHU de Marseille, Hopital La Timone

Marseille, , France

Site Status RECRUITING

Service de Radiologie-CHU de Nantes

Nantes, , France

Site Status RECRUITING

Service d'Oncologie Médicale-Centre Antoine LACASSAGNE

Nice, , France

Site Status RECRUITING

Service d'Oncologie Médicale

Saint-Herblain, , France

Site Status RECRUITING

Institut de cancérologie Strasbourg Europe (ICANS)

Strasbourg, , France

Site Status RECRUITING

Service d'Imagerie Interventionnelle, Hôpitaux Universitaires de Strasbourg , France, 67091

Strasbourg, , France

Site Status RECRUITING

Service d'Oncologie Médicale-Institut Claudius Régaud et Service de Radiologie Interventionnelle, CHU de Toulouse

Toulouse, , France

Site Status NOT_YET_RECRUITING

Service d'Oncologie médicale, Service de Radiologie Interventionnelle- Institut Gustave ROUSSY

Villejuif, , France

Site Status RECRUITING

Countries

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France

Central Contacts

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Afshin GANGI, MD,PhD

Role: CONTACT

0369550304 ext. 33

Roberto Luigi CAZZATO, MD

Role: CONTACT

0369550304 ext. 33

Facility Contacts

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Clément BOLOGNINI, MD

Role: primary

Maud TOULMONDE, MD

Role: primary

Marie-Aude THENINT, MD

Role: primary

Alice HERVIEU, MD

Role: primary

Mehdi BRAHMI, MD

Role: primary

Florence DUFFAUD, MD, PhD

Role: primary

Arthur DAVID, MD

Role: primary

Agnès DUCOULOMBIER, MD

Role: primary

Emmanuelle BOMPAS, MD

Role: primary

Jean-Emmanuel KURTZ, MD PhD

Role: primary

Afshin GANGI, MD, PhD

Role: primary

Thibaud VALENTIN, MD

Role: primary

Frédéric DESCHAMPS, MD

Role: primary

Other Identifiers

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7361

Identifier Type: -

Identifier Source: org_study_id

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