A Study to Investigate the Efficacy and Safety of Baxdrostat in Participants With Uncontrolled Hypertension on Two or More Medications Including Participants With Resistant Hypertension

NCT ID: NCT06034743

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

796 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-11-22

Study Completion Date

2025-10-10

Brief Summary

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This is a Phase III, multicentre, randomised, double-blinded, placebo-controlled, parallel group study to evaluate the safety, tolerability and effect of 1 or 2 mg baxdrostat versus placebo, administered once daily (QD) orally, on the reduction of systolic blood pressure in approximately 720 participants aged ≥ 18 years with hypertension, despite a stable regimen of 2 antihypertensive agents at baseline, one of which is a diuretic (uncontrolled hypertension); or ≥ 3 antihypertensive agents at baseline, one of which is a diuretic (treatment-resistant hypertension).

Detailed Description

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Conditions

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Uncontrolled Hypertension Resistant Hypertension

Keywords

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Hypertension Uncontrolled hypertension Resistant hypertension Blood pressure Baxdrostat CIN-107 Aldosterone Aldosterone synthase

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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2 mg baxdrostat

2 mg baxdrostat administered orally, once daily (QD).

Group Type EXPERIMENTAL

Baxdrostat

Intervention Type DRUG

Baxdrostat tablet administered orally, once daily (QD). Unit dose strengths:

* 1 mg per tablet for 1 mg baxdrostat Arm;
* 2 mg per tablet for 2 mg baxdrostat Arm.

1 mg baxdrostat

1 mg baxdrostat administered orally, once daily (QD).

Group Type EXPERIMENTAL

Baxdrostat

Intervention Type DRUG

Baxdrostat tablet administered orally, once daily (QD). Unit dose strengths:

* 1 mg per tablet for 1 mg baxdrostat Arm;
* 2 mg per tablet for 2 mg baxdrostat Arm.

Placebo

Placebo administered orally, once daily (QD).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo tablet matching baxdrostat, administered orally, once daily (QD).

Interventions

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Baxdrostat

Baxdrostat tablet administered orally, once daily (QD). Unit dose strengths:

* 1 mg per tablet for 1 mg baxdrostat Arm;
* 2 mg per tablet for 2 mg baxdrostat Arm.

Intervention Type DRUG

Placebo

Placebo tablet matching baxdrostat, administered orally, once daily (QD).

Intervention Type DRUG

Other Intervention Names

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CIN-107

Eligibility Criteria

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Inclusion Criteria

* Male or female participants must be ≥ 18 years old
* Mean sitting systolic blood pressure on automated office blood pressure measurement ≥ 140 mmHg and \< 170 mmHg at Screening
* Fulfil at least 1 of the following 2 criteria:

1. uHTN subpopulation: have a stable regimen of 2 antihypertensive medications, from different therapeutic classes (at least one must be a diuretic), at maximum tolerated dose in the judgement of the Investigator
2. rHTN subpopulation: have a stable regimen of ≥ 3 antihypertensive medications, from different therapeutic classes (at least one must be a diuretic), at maximum tolerated dose in the judgement of the Investigator
* Estimated glomerular filtration rate ≥ 45 mL/min/1.73m2 at Screening
* Serum potassium (K+) level ≥ 3.5 and \< 5.0 mmol/L at Screening
* Randomisation Criterion:
* Sitting systolic blood pressure on attended automated office blood pressure measurement of ≥ 135 mmHg at the Baseline Visit

Exclusion Criteria

* Mean sitting systolic blood pressure on attended automated office blood pressure measurement ≥ 170 mmHg
* Mean seated diastolic blood pressure on attended automated office blood pressure measurement ≥ 110 mmHg
* Serum sodium level \< 135 mmol/L at Screening
* Has the following known secondary causes of hypertension: renal artery stenosis, uncontrolled or untreated hyperthyroidism, uncontrolled or untreated hypothyroidism, pheochromocytoma, Cushing's syndrome, aortic coarctation
* New York Heart Association functional heart failure class IV at Screening
* Persistent atrial fibrillation
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Saraland, Alabama, United States

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Scottsdale, Arizona, United States

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Sun City West, Arizona, United States

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Surprise, Arizona, United States

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Little Rock, Arkansas, United States

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Fresno, California, United States

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Lincoln, California, United States

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Orange, California, United States

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Rancho Cucamonga, California, United States

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Stanford, California, United States

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New Haven, Connecticut, United States

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Clearwater, Florida, United States

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Jacksonville, Florida, United States

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Port Orange, Florida, United States

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Atlanta, Georgia, United States

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Decatur, Georgia, United States

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Springfield, Illinois, United States

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Munster, Indiana, United States

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Lexington, Kentucky, United States

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Detroit, Michigan, United States

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Rochester, Minnesota, United States

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Olive Branch, Mississippi, United States

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Kansas City, Missouri, United States

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Kansas City, Missouri, United States

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Kansas City, Missouri, United States

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Rosedale, New York, United States

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The Bronx, New York, United States

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Chapel Hill, North Carolina, United States

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New Bern, North Carolina, United States

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Toledo, Ohio, United States

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Grants Pass, Oregon, United States

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Bethlehem, Pennsylvania, United States

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Langhorne, Pennsylvania, United States

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East Providence, Rhode Island, United States

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Memphis, Tennessee, United States

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Brownsville, Texas, United States

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Corpus Christi, Texas, United States

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Houston, Texas, United States

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Sugar Land, Texas, United States

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Manassas, Virginia, United States

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Suffolk, Virginia, United States

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Madison, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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CABA, , Argentina

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CABA, , Argentina

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Ciudad de Buenos Aires, , Argentina

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Córdoba, , Argentina

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Córdoba, , Argentina

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Mar del Plata, , Argentina

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Mendoza, , Argentina

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Rosario, , Argentina

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San Miguel de Tucumán, , Argentina

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San Nicolás, , Argentina

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San Vicente, , Argentina

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Clayton, , Australia

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Darlinghurst, , Australia

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Epping, , Australia

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Geelong, , Australia

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Liverpool, , Australia

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New Lambton Heights, , Australia

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Perth, , Australia

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Wollongong, , Australia

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Woolloongabba, , Australia

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Braunau am Inn, , Austria

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Sankt Pölten, , Austria

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Vienna, , Austria

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Ghent, , Belgium

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Liège, , Belgium

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Mons, , Belgium

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Pleven, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Edmonton, Alberta, Canada

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North Vancouver, British Columbia, Canada

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Cambridge, Ontario, Canada

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Markham, Ontario, Canada

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Newmarket, Ontario, Canada

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Ottawa, Ontario, Canada

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Scarborough Village, Ontario, Canada

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Toronto, Ontario, Canada

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Waterloo, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Saint-Jean-sur-Richelieu, Quebec, Canada

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Benešov, , Czechia

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Brandýs nad Labem, , Czechia

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Broumov, , Czechia

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Louny, , Czechia

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Ostrava, , Czechia

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Příbram, , Czechia

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Uherské Hradiště, , Czechia

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Aarhus, , Denmark

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Herning, , Denmark

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Holbæk, , Denmark

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Bobigny, , France

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Bordeaux, , France

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Paris, , France

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Paris, , France

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Saint-Priest-en-Jarez, , France

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Toulon, , France

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Toulouse, , France

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Tours, , France

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Bad Homburg, , Germany

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Bad Oeynhausen, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Dortmund, , Germany

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Düsseldorf, , Germany

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Elsterwerda, , Germany

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Erlangen, , Germany

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Essen, , Germany

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Frankfurt, , Germany

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Frankfurt, , Germany

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Hanover, , Germany

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Hanover, , Germany

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Homburg, , Germany

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Kaiserslautern, , Germany

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Leipzig, , Germany

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Mannheim, , Germany

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Wermsdorf, , Germany

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Balatonfüred, , Hungary

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Budapest, , Hungary

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Kalocsa, , Hungary

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Kaposvár, , Hungary

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Nyíregyháza, , Hungary

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Pécs, , Hungary

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Delhi, , India

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Delhi, , India

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Guntur, , India

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Kanpur, , India

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Kolkata, , India

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Kolkata, , India

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Mysuru, , India

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Mysuru, , India

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New Delhi, , India

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New Delhi, , India

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Surat, , India

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Ashdod, , Israel

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Haifa, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Rehovot, , Israel

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Acquaviva delle Fonti, , Italy

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Bologna, , Italy

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Brescia, , Italy

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Milan, , Italy

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Milan, , Italy

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Milan, , Italy

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Pisa, , Italy

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Roma, , Italy

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Torino, , Italy

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Udine, , Italy

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Adachi-ku, , Japan

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Chūōku, , Japan

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Chūōku, , Japan

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Kanazawa, , Japan

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Koga-shi, , Japan

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Kyoto, , Japan

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Nagasaki, , Japan

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Okayama, , Japan

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Osaka, , Japan

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Sapporo, , Japan

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Tsuchiura-shi, , Japan

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Yufu-shi, , Japan

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Kajang, , Malaysia

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Kota Bharu, , Malaysia

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Kuching, , Malaysia

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Malacca, , Malaysia

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Muar town, , Malaysia

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Sarawak Miri, , Malaysia

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Seri Manjung, , Malaysia

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Hoogeveen, , Netherlands

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Nijmegen, , Netherlands

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Utrecht, , Netherlands

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Bialystok, , Poland

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Bydgoszcz, , Poland

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Chrzanów, , Poland

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Gdansk, , Poland

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Gdynia, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Poznan, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Brezno, , Slovakia

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Košice, , Slovakia

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Moldava nad Bodvou, , Slovakia

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Prešov, , Slovakia

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Rimavská Sobota, , Slovakia

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Svidník, , Slovakia

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Cape Town, , South Africa

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Centurion, , South Africa

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Claremont, , South Africa

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Durban, , South Africa

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Kwadwesi, , South Africa

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Somerset West, , South Africa

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Worcester, , South Africa

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Bucheon-si, , South Korea

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Busan, , South Korea

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Daejeon, , South Korea

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Incheon, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Barcelona, , Spain

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Barcelona, , Spain

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Ferrol, , Spain

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Granada, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Majadahonda, , Spain

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Seville, , Spain

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Terrassa (Barcelona), , Spain

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Gothenburg, , Sweden

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Uppsala, , Sweden

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taichung, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Yung Kang City, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Hat Yai, , Thailand

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Khon Kaen, , Thailand

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Pathum Thani, , Thailand

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Adana, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Bursa, , Turkey (Türkiye)

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Dinar, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Kütahya, , Turkey (Türkiye)

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Odunpazari, , Turkey (Türkiye)

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Bollington, , United Kingdom

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Bristol, , United Kingdom

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Chesterfield, , United Kingdom

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Dundee, , United Kingdom

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Glasgow, , United Kingdom

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Harrow, , United Kingdom

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Hownslow, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Prescot, , United Kingdom

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Weston-super-Mare, , United Kingdom

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Yate, , United Kingdom

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Da Nang, , Vietnam

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Hanoi, , Vietnam

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Ho Chi Minh City, , Vietnam

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Ho Chi Minh City, , Vietnam

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Hochiminh City, , Vietnam

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Countries

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United States Argentina Australia Austria Belgium Bulgaria Canada Czechia Denmark France Germany Hungary India Israel Italy Japan Malaysia Netherlands Poland Slovakia South Africa South Korea Spain Sweden Taiwan Thailand Turkey (Türkiye) United Kingdom Vietnam

References

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Flack JM, Azizi M, Brown JM, Dwyer JP, Fronczek J, Jones ESW, Olsson DS, Perl S, Shibata H, Wang JG, Wilderang U, Wittes J, Williams B; BaxHTN Investigators. Efficacy and Safety of Baxdrostat in Uncontrolled and Resistant Hypertension. N Engl J Med. 2025 Oct 9;393(14):1363-1374. doi: 10.1056/NEJMoa2507109. Epub 2025 Aug 30.

Reference Type DERIVED
PMID: 40888730 (View on PubMed)

Other Identifiers

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2023-505499-32-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

D6970C00002

Identifier Type: -

Identifier Source: org_study_id