Study of Tilpisertib Fosmecarbil in Participants With Moderately to Severely Active Ulcerative Colitis

NCT ID: NCT06029972

Last Updated: 2025-12-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

176 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-05

Study Completion Date

2027-05-31

Brief Summary

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The goal of this study is to learn if tilpisertib fosmecarbil (formerly known as GS-5290) is effective and safe in treating participants with moderate to severe ulcerative colitis. The study will compare participants in different treatment groups treated with tilpisertib fosmecarbil with participants treated with placebo.

The primary objective of this study is to demonstrate the efficacy of tilpisertib fosmecarbil, compared to placebo control, in achieving Clinical Response at Week 12.

Detailed Description

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Conditions

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Ulcerative Colitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Tilpisertib Fosmecarbil Dose A

Blinded Treatment Phase:

Participants will receive tilpisertib fosmecarbil Dose A for up to 12 weeks. An efficacy assessment will be performed at Week 12.

• Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52.

Non-responder Treatment Phase:

• Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose A for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve clinical response at Non-responder Treatment Phase Week 12 will discontinue study drug.

Group Type EXPERIMENTAL

Tilpisertib Fosmecarbil

Intervention Type DRUG

Tablets administered orally

Tilpisertib Fosmecarbil Dose B

Blinded Treatment Phase:

Participants will receive tilpisertib fosmecarbil Dose B for up to 12 weeks. An efficacy assessment will be performed at Week 12.

• Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52.

Non-responder Treatment Phase:

• Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose B for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve clinical response at Non-responder Treatment Phase Week 12 will discontinue study drug.

Group Type EXPERIMENTAL

Tilpisertib Fosmecarbil

Intervention Type DRUG

Tablets administered orally

Tilpisertib Fosmecarbil Dose C

Blinded Treatment Phase:

Participants will receive tilpisertib fosmecarbil Dose C for up to 12 weeks. An efficacy assessment will be performed at Week 12.

• Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose C for up to Week 52.

Non-responder Treatment Phase:

• Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose B for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve clinical response at Non-responder Treatment Phase Week 12 will discontinue study drug.

Group Type EXPERIMENTAL

Tilpisertib Fosmecarbil

Intervention Type DRUG

Tablets administered orally

Tilpisertib Fosmecarbil Placebo

Blinded Treatment Phase:

Participants will receive tilpisertib fosmecarbil placebo for up to 12 weeks. An efficacy assessment will be performed at Week 12.

• Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose C for up to Week 52.

Non-responder Treatment Phase:

• Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose A for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved Clinical Response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve Clinical Response at Non-responder Treatment Phase Week 12 will discontinue study drug.

Group Type PLACEBO_COMPARATOR

Tilpisertib Fosmecarbil

Intervention Type DRUG

Tablets administered orally

Placebo

Intervention Type DRUG

Tablets administered orally

Interventions

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Tilpisertib Fosmecarbil

Tablets administered orally

Intervention Type DRUG

Placebo

Tablets administered orally

Intervention Type DRUG

Other Intervention Names

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GS-5290

Eligibility Criteria

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Inclusion Criteria

* Individuals assigned male at birth, or nonpregnant, nonlactating individuals assigned female at birth, 18 to 75 years of age based on the date of the screening visit.
* Ulcerative colitis (UC) of at least 90-day duration before randomization confirmed by endoscopy and histology at any time in the past AND a minimum disease extent of 15 cm from the anal verge. Documentation of endoscopy and histology consistent with the diagnosis of UC must be available in the source documents prior to the initiation of screening.
* Moderately to severely active UC as determined during screening with a modified Mayo Clinic Score based on the sum of Stool Frequency, Rectal Bleeding, and Endoscopic Finding of 5 to 9 points and an endoscopic subscore of 2 to 3 (determined by central reader).
* Previous treatment history of approved UC therapy with at least one advanced therapy mechanisms of action but failure (ie, loss of response or lack of response) of no more than 3 different advanced therapy mechanisms of action.
* A surveillance colonoscopy for dysplasia is required prior to randomization if indicated by regional guidelines for individuals with UC.

Exclusion Criteria

* Current diagnosis of Crohn's Disease (CD) or diagnosis of indeterminate colitis due to an enteric pathogen, lymphocytic or collagenous colitis.
* Individuals with disease limited to the rectum (ulcerative proctitis) during screening endoscopy.
* Requirement for ongoing therapy with or prior use of any prohibited medications.
* Active clinically significant infection, or any infection requiring hospitalization or treatment with intravenous anti-infectives within 8 weeks.

of randomization; or any infection requiring oral anti-infective therapy within 6 weeks of randomization.

* History of opportunistic infection.
* Current diagnosis of acute severe colitis, fulminant colitis, or toxic megacolon.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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GI Alliance

Sun City, Arizona, United States

Site Status RECRUITING

GastroSb Weight Loss Clinic

Chula Vista, California, United States

Site Status RECRUITING

Southern California Research Centers

Coronado, California, United States

Site Status RECRUITING

VVCRD Research

Garden Grove, California, United States

Site Status RECRUITING

UC San Diego Health System

La Jolla, California, United States

Site Status RECRUITING

Gastro Care Institute

Lancaster, California, United States

Site Status RECRUITING

Om Research LLC

Lancaster, California, United States

Site Status RECRUITING

United Medical Doctors

Murrieta, California, United States

Site Status WITHDRAWN

University of California, Davis

Sacramento, California, United States

Site Status RECRUITING

University of California San Francisco

San Francisco, California, United States

Site Status RECRUITING

Amicis Research Center

Valencia, California, United States

Site Status WITHDRAWN

Luna Research

Coral Gables, Florida, United States

Site Status RECRUITING

University of Florida

Gainesville, Florida, United States

Site Status RECRUITING

The Medici Medical Research

Hollywood, Florida, United States

Site Status RECRUITING

Encore Medical Research, LLC

Hollywood, Florida, United States

Site Status WITHDRAWN

Clinical Research of Osceola

Kissimmee, Florida, United States

Site Status RECRUITING

Florida Research Institute

Largo, Florida, United States

Site Status RECRUITING

Wellness Research Center

Miami, Florida, United States

Site Status WITHDRAWN

IMIC Inc

Miami, Florida, United States

Site Status WITHDRAWN

Reserka LLC

Miami, Florida, United States

Site Status WITHDRAWN

GI PROS Research

Naples, Florida, United States

Site Status RECRUITING

Clinical One Research

Orlando, Florida, United States

Site Status RECRUITING

Digestive and Liver Center of Florida, LLC

Orlando, Florida, United States

Site Status RECRUITING

Advanced Medical Research Center

Port Orange, Florida, United States

Site Status RECRUITING

Gastroenterology Associates of Florida - GI Alliance

Wellington, Florida, United States

Site Status WITHDRAWN

Atlanta Center For Gastroenterology P.C.

Decatur, Georgia, United States

Site Status WITHDRAWN

Corewell Health

Grand Rapids, Michigan, United States

Site Status RECRUITING

Mayo Clinic

Rochester, Minnesota, United States

Site Status RECRUITING

Gastroenterology Associates of North Mississippi

Oxford, Mississippi, United States

Site Status RECRUITING

Digestive Health Specialists

Tupelo, Mississippi, United States

Site Status RECRUITING

St. Charles Clinical Research

St Louis, Missouri, United States

Site Status RECRUITING

Ellipsis Research Group

Brooklyn, New York, United States

Site Status ACTIVE_NOT_RECRUITING

NYU Langone Long Island Clinical Research Associates

Great Neck, New York, United States

Site Status RECRUITING

Gastroenterology & Hepatology Specialists Inc

Canton, Ohio, United States

Site Status RECRUITING

Ohio Gastroenterology & Liver Institute

Cincinnati, Ohio, United States

Site Status WITHDRAWN

The Ohio State University Wexner Medical Centre

Columbus, Ohio, United States

Site Status RECRUITING

Dayton Gastroenterology, LLC

Dayton, Ohio, United States

Site Status RECRUITING

Great Lakes Gastroenterology Research, LLC

Mentor, Ohio, United States

Site Status RECRUITING

Hightower Clinical

Oklahoma City, Oklahoma, United States

Site Status WITHDRAWN

Skyline Gastroenterology of West Tennessee

Jackson, Tennessee, United States

Site Status NOT_YET_RECRUITING

Gastroenterology Research of Hill Country

Boerne, Texas, United States

Site Status RECRUITING

Gastroenterology Research of America

El Paso, Texas, United States

Site Status WITHDRAWN

DHAT Research Institute

Garland, Texas, United States

Site Status WITHDRAWN

Southwest Clinical Trials

Houston, Texas, United States

Site Status WITHDRAWN

GI Alliance

Lubbock, Texas, United States

Site Status RECRUITING

GI Associates and Endoscopy Center - GI Alliance

Mansfield, Texas, United States

Site Status RECRUITING

Clinical Associates in Research Therapeutics of America

San Antonio, Texas, United States

Site Status RECRUITING

Gastroenterology Research of San Antonio

San Antonio, Texas, United States

Site Status RECRUITING

Tyler Research Institute, LLC

Tyler, Texas, United States

Site Status RECRUITING

Gastroenterology Associates of Tidewater

Chesapeake, Virginia, United States

Site Status RECRUITING

Emeritas Group Research

Lansdowne Town Center, Virginia, United States

Site Status RECRUITING

Gastroenterology Consultants of Southwest Virginia

Roanoke, Virginia, United States

Site Status RECRUITING

Swedish Medical Center

Seattle, Washington, United States

Site Status WITHDRAWN

Sunshine Coast University Hospital

Birtinya, Queensland, Australia

Site Status RECRUITING

Mater Adult Hospital

South Brisbane, Queensland, Australia

Site Status RECRUITING

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status RECRUITING

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status RECRUITING

Queen Elizabeth Hospital

Woodville, South Australia, Australia

Site Status RECRUITING

Monash Medical Centre

Clayton, Victoria, Australia

Site Status WITHDRAWN

Northern Health

Epping, Victoria, Australia

Site Status RECRUITING

Footscray Hospital

Footscray, Victoria, Australia

Site Status RECRUITING

Fiona Stanley Hospital

Murdoch, Western Australia, Australia

Site Status RECRUITING

Medical University of Innsbruck

Innsbruck, , Austria

Site Status RECRUITING

University of Salzburg, Universitätsklinik für Innere Medizin III

Salzburg, , Austria

Site Status NOT_YET_RECRUITING

Universitätsklinikum St. Pölten

Sankt Pölten, , Austria

Site Status RECRUITING

Medical University Vienna, Department of Internal Medicine III, Division Gastroenterology and Hepatology

Vienna, , Austria

Site Status RECRUITING

Universitaire Ziekenhuis Leuven

Leuven, , Belgium

Site Status RECRUITING

London Health Sciences Centre-University Hospital

London, , Canada

Site Status RECRUITING

Physician's Clinical Research, Inc. (PCRI)

Toronto, , Canada

Site Status WITHDRAWN

Mount Sinai Hospital

Toronto, , Canada

Site Status RECRUITING

TDDA Speciality Research

Vaughan, , Canada

Site Status RECRUITING

Centre Hospitalier Universitaire Grenoble

Grenoble, , France

Site Status RECRUITING

Hôpital Claude Huriez

Little Cedex, , France

Site Status RECRUITING

Hopital Saint Eloi

Montpellier, , France

Site Status RECRUITING

Centre Hospitalier Universitaire de Nantes

Nantes, , France

Site Status RECRUITING

Institut des MICI

Neuilly-sur-Seine, , France

Site Status RECRUITING

CHU de Saint Etienne - Hopital Nord

Saint-Etienne, , France

Site Status RECRUITING

Hopital Rangueil

Toulouse, , France

Site Status RECRUITING

CHRU Nancy

Vandœuvre-lès-Nancy, , France

Site Status RECRUITING

Charite Universitaetsmedizin Berlin Campus CVK, Department of Hepatology and Gastroenterology

Berlin, , Germany

Site Status NOT_YET_RECRUITING

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status NOT_YET_RECRUITING

Universitatsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status RECRUITING

Eugastro Gmbh

Liepzig, , Germany

Site Status RECRUITING

Universitaetsklinikum Ulm Klinik fur Innere Medizin I CED Studien Ambulanz

Ulm, , Germany

Site Status NOT_YET_RECRUITING

Tolna Megye Balassa Janos Korhaz

Beri Balogh, , Hungary

Site Status RECRUITING

Szent Janos Korhaz es Eszak-budai Egyesitett Korhazak

Budapest, , Hungary

Site Status RECRUITING

AZIENDA UNICA OSPEDALIERO-UNIVERSITARIA"RENATO DULBECCO" - AOU"Mater Domini"

Catanzaro, , Italy

Site Status RECRUITING

IRCCS Istituto Clinico Humanitas

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliera San Camillo Forlanini

Roma, , Italy

Site Status RECRUITING

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

Azienda Sanitaria Universitaria Friuli Centrale

Udine, , Italy

Site Status WITHDRAWN

Hyogo Medical University Hospital

Hyōgo, , Japan

Site Status RECRUITING

Fukuoka University Hospital

Jonan-ku, , Japan

Site Status RECRUITING

The Jikei University Hospital

Minatoku, , Japan

Site Status RECRUITING

Kitasato University Kitasato Institute Hospital

Minatoku, , Japan

Site Status RECRUITING

Kyorin University Hospital

Mitaka-shi, , Japan

Site Status RECRUITING

Nagasaki University Hospital

Nagasaki, , Japan

Site Status RECRUITING

Ishida Clinic of IBD and Gastroenterology

Ōita, , Japan

Site Status RECRUITING

Saga University Hospital

Sagaken, , Japan

Site Status RECRUITING

Kitasato University Hospital

Sagamihara, , Japan

Site Status RECRUITING

Sapporo Medical University Hospital

Sapporo, , Japan

Site Status RECRUITING

Ginza Central Clinic

Tokyo, , Japan

Site Status RECRUITING

Institute of Science Tokyo Hospital

Toukiyouto, , Japan

Site Status RECRUITING

Economicus Sp. z o.o., Niepubliczny Zakład Opieki Zdrowotnej (NZOZ) ALL-MEDICUS

Katowice, , Poland

Site Status WITHDRAWN

Gabinet Endoskopii Przewodu Pokarmowego

Krakow, , Poland

Site Status RECRUITING

Medrise Sp. z o.o. Centrum Badań Klinicznych

Lublin, , Poland

Site Status NOT_YET_RECRUITING

SOLUMED Centrum Medyczne

Poznan, , Poland

Site Status NOT_YET_RECRUITING

Kliniczny Szpital Wojewódzki Nr 2 im. Sw. Jadwigi Królowej w Rzeszowie

Rzeszów, , Poland

Site Status RECRUITING

Specjalistyczna Praktyka Lekarska Leszek Bryniarski

Sopot, , Poland

Site Status RECRUITING

GASTROMED Kopon, Zmudzinski i wspolnicy Sp. J. Specialized Center of Gastroenterology and Endoscopy

Torun, , Poland

Site Status RECRUITING

Medical Network Sp. z o.o. WIP Warsaw IBD Point Profesor Kierkus

Warsaw, , Poland

Site Status RECRUITING

Nzoz Vivamed

Warsaw, , Poland

Site Status WITHDRAWN

Specjalistyczne Gabinety Lekarskie Body Clinic

Warsaw, , Poland

Site Status RECRUITING

Centrum Medyczne Oporow

Wroclaw, , Poland

Site Status RECRUITING

Yonsei University Severance Hospital

Seodaemun-Gu, VIC, South Korea

Site Status RECRUITING

Inje University

Busan, , South Korea

Site Status RECRUITING

Yeungnam University Hospital

Daegu, , South Korea

Site Status RECRUITING

Kyungpook National University Hospital

Junggu, , South Korea

Site Status RECRUITING

Kyung Hee University Medical Center

Seoul, , South Korea

Site Status RECRUITING

Kangbuk Samsung Hospital

Seoul, , South Korea

Site Status RECRUITING

Hanyang University Hospital

Seoul, , South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status RECRUITING

Wonju Severance Christian Hospital

Wŏnju, , South Korea

Site Status RECRUITING

Intesto, Gastroenterologische Praxis Crohn-Colitis-Zentrum

Bern, , Switzerland

Site Status RECRUITING

Fairfield General Hospital

Bury, , United Kingdom

Site Status RECRUITING

Cambridge University Hospitals NHS Foundation Trust

Cambridge, , United Kingdom

Site Status RECRUITING

Barts Health NHS Trust

London, , United Kingdom

Site Status RECRUITING

Norfolk and Norwich University Hospital Nhs Foundation Trust

Norwich, , United Kingdom

Site Status RECRUITING

University Hospital Southampton Nhs Foundation Trust

Southampton, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Austria Belgium Canada France Germany Hungary Italy Japan Poland South Korea Switzerland United Kingdom

Central Contacts

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Gilead Clinical Study Information Center

Role: CONTACT

Phone: 1-833-445-3230 (GILEAD-0)

Email: [email protected]

Related Links

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Other Identifiers

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2022-501119-14

Identifier Type: OTHER

Identifier Source: secondary_id

jRCT2031230403

Identifier Type: OTHER

Identifier Source: secondary_id

GS-US-457-6411

Identifier Type: -

Identifier Source: org_study_id