Trial Outcomes & Findings for A Study to Evaluate LTI-03 in Newly Diagnosed Idiopathic Pulmonary Fibrosis (IPF) Patients (NCT NCT05954988)

NCT ID: NCT05954988

Last Updated: 2025-07-31

Results Overview

Incidence of TEAEs by dose

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

24 participants

Primary outcome timeframe

21 days (dosing x 14 days; follow up x 7 days)

Results posted on

2025-07-31

Participant Flow

Participant milestones

Participant milestones
Measure
2.5 mg LTI-03 BID
2.5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
5 mg LTI-03 BID
5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
Placebo
Matching placebo BID x 14 days Placebo: Matching placebo
Overall Study
STARTED
9
9
6
Overall Study
COMPLETED
9
9
6
Overall Study
NOT COMPLETED
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Study to Evaluate LTI-03 in Newly Diagnosed Idiopathic Pulmonary Fibrosis (IPF) Patients

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
2.5 mg LTI-03 BID
n=9 Participants
2.5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
5 mg LTI-03 BID
n=9 Participants
5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
Placebo
n=6 Participants
Matching placebo BID x 14 days Placebo: Matching placebo
Total
n=24 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Age, Categorical
Between 18 and 65 years
4 Participants
n=5 Participants
3 Participants
n=7 Participants
1 Participants
n=5 Participants
8 Participants
n=4 Participants
Age, Categorical
>=65 years
5 Participants
n=5 Participants
6 Participants
n=7 Participants
5 Participants
n=5 Participants
16 Participants
n=4 Participants
Age, Continuous
67.8 years
STANDARD_DEVIATION 9.76 • n=5 Participants
68.4 years
STANDARD_DEVIATION 10.79 • n=7 Participants
71.7 years
STANDARD_DEVIATION 6.15 • n=5 Participants
69.0 years
STANDARD_DEVIATION 9.19 • n=4 Participants
Sex: Female, Male
Female
2 Participants
n=5 Participants
2 Participants
n=7 Participants
0 Participants
n=5 Participants
4 Participants
n=4 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
7 Participants
n=7 Participants
6 Participants
n=5 Participants
20 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
9 Participants
n=5 Participants
9 Participants
n=7 Participants
6 Participants
n=5 Participants
24 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
White
9 Participants
n=5 Participants
9 Participants
n=7 Participants
6 Participants
n=5 Participants
24 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Region of Enrollment
United States
2 participants
n=5 Participants
1 participants
n=7 Participants
0 participants
n=5 Participants
3 participants
n=4 Participants
Region of Enrollment
United Kingdom
3 participants
n=5 Participants
2 participants
n=7 Participants
3 participants
n=5 Participants
8 participants
n=4 Participants
Region of Enrollment
Germany
3 participants
n=5 Participants
4 participants
n=7 Participants
2 participants
n=5 Participants
10 participants
n=4 Participants
Region of Enrollment
Australia
1 participants
n=5 Participants
2 participants
n=7 Participants
1 participants
n=5 Participants
3 participants
n=4 Participants
Height
170.93 cm
STANDARD_DEVIATION 9.270 • n=5 Participants
169.56 cm
STANDARD_DEVIATION 9.530 • n=7 Participants
177.17 cm
STANDARD_DEVIATION 7.111 • n=5 Participants
171.98 cm
STANDARD_DEVIATION 9.067 • n=4 Participants
Weight
84.49 kg
STANDARD_DEVIATION 11.709 • n=5 Participants
85.36 kg
STANDARD_DEVIATION 25.108 • n=7 Participants
91.45 kg
STANDARD_DEVIATION 11.529 • n=5 Participants
86.55 kg
STANDARD_DEVIATION 17.446 • n=4 Participants
BMI
28.869 kg/m^2
STANDARD_DEVIATION 2.7335 • n=5 Participants
29.364 kg/m^2
STANDARD_DEVIATION 6.6335 • n=7 Participants
29.330 kg/m^2
STANDARD_DEVIATION 4.9868 • n=5 Participants
29.170 kg/m^2
STANDARD_DEVIATION 4.8340 • n=4 Participants
Number of Participants with Past and/or current tobacco use
Yes
8 Participants
n=5 Participants
7 Participants
n=7 Participants
4 Participants
n=5 Participants
19 Participants
n=4 Participants
Number of Participants with Past and/or current tobacco use
No
1 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
5 Participants
n=4 Participants
Cigarette smoking
18.25 pack-years
STANDARD_DEVIATION 10.327 • n=5 Participants
35.99 pack-years
STANDARD_DEVIATION 22.861 • n=7 Participants
26.88 pack-years
STANDARD_DEVIATION 26.772 • n=5 Participants
27.06 pack-years
STANDARD_DEVIATION 20.331 • n=4 Participants
Diffusion capacity of the lungs for carbon monoxide (DLCO)
5.123 mmol/min/kPa
STANDARD_DEVIATION 0.7913 • n=5 Participants
5.020 mmol/min/kPa
STANDARD_DEVIATION 1.5804 • n=7 Participants
5.354 mmol/min/kPa
STANDARD_DEVIATION 0.6776 • n=5 Participants
5.143 mmol/min/kPa
STANDARD_DEVIATION 1.1092 • n=4 Participants
Forced Vital Capacity (FVC)
3.214 L
STANDARD_DEVIATION 0.7744 • n=5 Participants
3.318 L
STANDARD_DEVIATION 0.6421 • n=7 Participants
3.085 L
STANDARD_DEVIATION 0.2733 • n=5 Participants
3.221 L
STANDARD_DEVIATION 0.6138 • n=4 Participants
FVC percent predicted
84.789 percent
STANDARD_DEVIATION 10.2189 • n=5 Participants
92.111 percent
STANDARD_DEVIATION 18.6644 • n=7 Participants
75.617 percent
STANDARD_DEVIATION 8.9410 • n=5 Participants
85.242 percent
STANDARD_DEVIATION 14.7507 • n=4 Participants
Leicester Cough Questionnaire (LCQ) Total Score
18.19 units on a scale
STANDARD_DEVIATION 3.264 • n=5 Participants
16.59 units on a scale
STANDARD_DEVIATION 3.236 • n=7 Participants
16.12 units on a scale
STANDARD_DEVIATION 3.373 • n=5 Participants
17.07 units on a scale
STANDARD_DEVIATION 3.262 • n=4 Participants
Cough Visual Analogue Scale (VAS) Score
29.6 units on a scale
STANDARD_DEVIATION 30.65 • n=5 Participants
38.1 units on a scale
STANDARD_DEVIATION 21.51 • n=7 Participants
35.3 units on a scale
STANDARD_DEVIATION 27.20 • n=5 Participants
34.2 units on a scale
STANDARD_DEVIATION 25.75 • n=4 Participants

PRIMARY outcome

Timeframe: 21 days (dosing x 14 days; follow up x 7 days)

Incidence of TEAEs by dose

Outcome measures

Outcome measures
Measure
2.5 mg LTI-03 BID
n=9 Participants
2.5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
5 mg LTI-03 BID
n=9 Participants
5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
Placebo
n=6 Participants
Matching placebo BID x 14 days Placebo: Matching placebo
Incidence of Treatment-emergent Adverse Events (TEAEs)
Any serious TEAE
0 percentage of participants
11.1 percentage of participants
0 percentage of participants
Incidence of Treatment-emergent Adverse Events (TEAEs)
Any TEAE
66.7 percentage of participants
77.8 percentage of participants
50.0 percentage of participants
Incidence of Treatment-emergent Adverse Events (TEAEs)
Any TEAE with CTCAE severity Grade 3 or higher
0 percentage of participants
0 percentage of participants
0 percentage of participants
Incidence of Treatment-emergent Adverse Events (TEAEs)
Any study drug-related TEAE
22.2 percentage of participants
55.6 percentage of participants
16.7 percentage of participants
Incidence of Treatment-emergent Adverse Events (TEAEs)
Any TEAE leading to treatment discontinuation
0 percentage of participants
0 percentage of participants
0 percentage of participants
Incidence of Treatment-emergent Adverse Events (TEAEs)
Any TEAE leading to death
0 percentage of participants
0 percentage of participants
0 percentage of participants

Adverse Events

2.5 mg LTI-03 BID

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

5 mg LTI-03 BID

Serious events: 1 serious events
Other events: 7 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
2.5 mg LTI-03 BID
n=9 participants at risk
2.5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
5 mg LTI-03 BID
n=9 participants at risk
5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
Placebo
n=6 participants at risk
Matching placebo BID x 14 days Placebo: Matching placebo
Injury, poisoning and procedural complications
Post-procedural fever
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21

Other adverse events

Other adverse events
Measure
2.5 mg LTI-03 BID
n=9 participants at risk
2.5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
5 mg LTI-03 BID
n=9 participants at risk
5 mg LTI-03 BID x 14 days LTI-03: Caveolin-1-Scaffolding-Protein-Derived Peptide
Placebo
n=6 participants at risk
Matching placebo BID x 14 days Placebo: Matching placebo
Cardiac disorders
Palpitations
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Nervous system disorders
Dizziness
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
16.7%
1/6 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Nervous system disorders
Dysgeusia
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Nervous system disorders
Ophthalmic migraine
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
General disorders
Chest discomfort
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
General disorders
Fatigue
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Ear and labyrinth disorders
Vertigo
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Gastrointestinal disorders
Dry mouth
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Gastrointestinal disorders
Hypoesthesia oral
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Gastrointestinal disorders
Esophageal spasm
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
16.7%
1/6 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Respiratory, thoracic and mediastinal disorders
Cough
33.3%
3/9 • Number of events 3 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
55.6%
5/9 • Number of events 5 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
33.3%
2/6 • Number of events 2 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Respiratory, thoracic and mediastinal disorders
Dyspnea exertional
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Respiratory, thoracic and mediastinal disorders
Productive cough
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Respiratory, thoracic and mediastinal disorders
Rhinorrhea
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Respiratory, thoracic and mediastinal disorders
Throat irritation
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Skin and subcutaneous tissue disorders
Cold sweat
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Musculoskeletal and connective tissue disorders
Back pain
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Infections and infestations
COVID-19
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Infections and infestations
Nasopharyngitis
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
Metabolism and nutrition disorders
Hyperkalemia
11.1%
1/9 • Number of events 1 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/9 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21
0.00%
0/6 • From ICF (if serious or related to protocol assessment) or Dosing Day 1 through End of Study Day 21

Additional Information

Shawna Evans

Rein Therapeutics, Inc.

Phone: 1 (737) 802-1989

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place