Study of the Efficacy and Safety of Inhaled Treprostinil in Subjects With Progressive Pulmonary Fibrosis (TETON-PPF)

NCT ID: NCT05943535

Last Updated: 2025-12-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

698 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-10-30

Study Completion Date

2027-11-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Study RIN-PF-305 is designed to evaluate the safety and efficacy of inhaled treprostinil in subjects with progressive pulmonary fibrosis (PPF) over a 52-week period.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Study RIN-PF-305 is a Phase 3, multinational, randomized, double-blind, placebo-controlled study to evaluate the safety and efficacy of inhaled treprostinil in subjects with PPF over a 52-week period. Subjects will be randomly allocated 1:1 to receive inhaled treprostinil or placebo. All subjects will initiate inhaled treprostinil or placebo at a dose of 3 breaths administered 4 times daily (QID) and will titrate to a target dosing regimen of 12 breaths QID. Study drug doses may be titrated up as tolerated, until the target dose or maximum clinically tolerated dose is achieved. Once eligible, 6 Treatment Period visits to the clinic will be required at Weeks 4, 8, 16, 28, 40, and 52.

Efficacy assessments include spirometry (forced vital capacity \[FVC\]), time to clinical worsening, time to first acute exacerbation of interstitial lung disease (ILD), overall survival, King's Brief Interstitial Lung Disease (K-BILD) questionnaire, plasma N-terminal pro-brain natriuretic peptide (NT-proBNP) concentration, supplemental oxygen use, and lung diffusion capacity (DLCO). Safety assessments include the development of adverse events (AEs)/serious adverse events (SAEs), vital signs, clinical laboratory parameters, and electrocardiogram (ECG) parameters.

Subjects who complete the Week 52 Visit may be offered the opportunity to enter an open-label extension (OLE) study after completing the final study visit.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Progressive Pulmonary Fibrosis Interstitial Lung Disease

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Treprostinil PPF ILD

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Placebo

Matching placebo inhaled using an ultrasonic nebulizer QID

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered QID

Treprostinil Ultrasonic Nebulizer

Intervention Type DEVICE

Treprostinil ultrasonic nebulizer which emits a dose of approximately 6 mcg per breath.

Inhaled Treprostinil

Treprostinil for inhalation solution (0.6 mg/mL) delivered via an ultrasonic nebulizer which emits a dose of approximately 6 mcg per breath. Inhaled QID and titrated up to a target of 12 breaths QID or until the subject reaches their maximum clinically tolerated dose.

Group Type EXPERIMENTAL

Inhaled Treprostinil

Intervention Type DRUG

Inhaled treprostinil (6 mcg/breath) administered QID

Treprostinil Ultrasonic Nebulizer

Intervention Type DEVICE

Treprostinil ultrasonic nebulizer which emits a dose of approximately 6 mcg per breath.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Placebo

Placebo administered QID

Intervention Type DRUG

Inhaled Treprostinil

Inhaled treprostinil (6 mcg/breath) administered QID

Intervention Type DRUG

Treprostinil Ultrasonic Nebulizer

Treprostinil ultrasonic nebulizer which emits a dose of approximately 6 mcg per breath.

Intervention Type DEVICE

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Tyvaso

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Subject gives voluntary informed consent to participate in the study.
2. Subject is ≥18 years of age, inclusive, at the time of signing informed consent.
3. Subject has radiological evidence of pulmonary fibrosis of \>10% extent on an HRCT scan in the previous 12 months (confirmed by central review).
4. Subject has a diagnosis of PPF (other than IPF) that fulfills at least 1 of the following criteria for progression within 24 months of screening despite standard treatment of ILD, as assessed by the Investigator:

1. Clinically significant decline in % predicted FVC based on ≥10% relative decline
2. Marginal decline in % predicted FVC based on ≥5% to \<10% relative decline combined with worsening of respiratory symptoms
3. Marginal decline in % predicted FVC based on ≥5% to \<10% relative decline combined with increasing extent of fibrotic changes on chest imaging
4. Worsening of respiratory symptoms as well as increasing extent of fibrotic changes on chest imaging
5. FVC ≥45% predicted at Screening (confirmed by central review).
6. Subjects must be on 1 of the following:

1. On nintedanib or pirfenidone for ≥90 days prior to Baseline and in the Investigator's opinion, are planning to continue treatment through the study
2. Not on treatment with nintedanib or pirfenidone for ≥90 days prior to Baseline and in the Investigator's opinion, not planning to initiate either treatment during the study.

Concomitant use of both nintedanib and pirfenidone is not permitted.
7. Subjects treated with immunosuppressive agents (eg, mycophenolate, methotrexate, azathioprine, oral corticosteroids, rituximab) need to be on treatment for at least 120 days prior to Baseline and, in the Investigator's clinical opinion, must be refractory to treatment.
8. Women of childbearing potential must be non-pregnant (as confirmed by a urine pregnancy test at Screening and Baseline) and non-lactating, and will agree to do 1 of the following:

1. Abstain from intercourse (when it is in line with their preferred and usual lifestyle)
2. Use 2 medically acceptable, highly effective forms of contraception for the duration of the study, and at least 30 days after discontinuing study drug.

i. Medically acceptable, highly effective forms of contraception can include approved hormonal contraceptives (oral, injectable, and implantable) and barrier methods (such as a condom or diaphragm) when used with a spermicide.

Women who are successfully sterilized (including hysterectomy, bilateral salpingectomy, or bilateral oophorectomy) or postmenopausal (defined as amenorrhea for at least 12 consecutive months) are not considered to be of reproductive potential.
9. Males with a partner of childbearing potential must agree to use a condom for the duration of treatment and for at least 48 hours after discontinuing study drug.
10. In the opinion of the Investigator, the subject is able to communicate effectively with study personnel, and is considered reliable, willing, and likely to be cooperative with protocol requirements, including attending all study visits.

Exclusion Criteria

1. Subject is pregnant or lactating.
2. Subject has primary obstructive airway physiology (forced expiratory volume in 1 second/FVC \<0.70 at Screening) or greater extent of emphysema than fibrosis on HRCT (confirmed by central review).
3. Subject has a diagnosis of IPF.
4. Subject has shown intolerance or significant lack of efficacy to a prostacyclin or prostacyclin analogue that resulted in discontinuation or inability to effectively titrate that therapy.
5. Subject has received any PAH-approved therapy, including prostacyclin therapy (epoprostenol, treprostinil, iloprost, or beraprost; except for acute vasoreactivity testing), IP receptor agonists (selexipag), endothelin receptor antagonists, phosphodiesterase type 5 inhibitors (PDE5-Is), soluble guanylate cyclase stimulators, or activin signaling inhibitors (sotatercept) within 60 days prior to Baseline. As needed use of a PDE5-I for erectile dysfunction is permitted, provided no doses are taken within 48 hours prior to any study-related efficacy assessments.
6. Subject is receiving \>10 L/min of oxygen supplementation by any mode of delivery at rest at Baseline.
7. Exacerbation of ILD or active pulmonary or upper respiratory infection within 30 days prior to Baseline. Subjects must have completed any antibiotic or steroid regimens for treatment of the infection or acute exacerbation more than 30 days prior to Baseline to be eligible. If hospitalized for an acute exacerbation of ILD or a pulmonary or upper respiratory infection, subjects must have been discharged more than 90 days prior to Baseline to be eligible.
8. Subject has uncontrolled cardiac disease, defined as myocardial infarction within 6 months prior to Baseline or unstable angina within 30 days prior to Baseline.
9. Use of any other investigational drug/device or participation in any investigational study in which the subject received a medical intervention (ie, procedure, device, medication/supplement) within 30 days prior to Screening. Subjects participating in non-interventional, observational, or registry studies are eligible.
10. Acute pulmonary embolism within 90 days prior to Baseline.
11. In the opinion of the Investigator, the subject has any condition that would interfere with the interpretation of study assessments or would impair study participation or cooperation.
12. In the opinion of the Investigator, life expectancy \<12 months due to ILD or a concomitant illness.
13. Subject has received nerandomilast within 60 days prior to Baseline.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

United Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

UAB Lung Health Center

Birmingham, Alabama, United States

Site Status RECRUITING

Norton Thoracic Institute

Phoenix, Arizona, United States

Site Status RECRUITING

Peter Morton Medical Building

Los Angeles, California, United States

Site Status RECRUITING

NewportNativeMD, Inc.

Newport Beach, California, United States

Site Status RECRUITING

University of California Irvine Medical Center

Orange, California, United States

Site Status RECRUITING

Paradigm Clinical Research

Redding, California, United States

Site Status RECRUITING

UC Davis Health Medical Center

Sacramento, California, United States

Site Status RECRUITING

Paradigm Clinical Research

San Diego, California, United States

Site Status RECRUITING

Stanford University Medical Center

Stanford, California, United States

Site Status RECRUITING

Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Ascension Medical Group St. Vincent's Lung Institute

Jacksonville, Florida, United States

Site Status RECRUITING

Mayo Clinic

Jacksonville, Florida, United States

Site Status RECRUITING

TGH/USF Center for Advanced Lung Disease and Lung Transplant

Tampa, Florida, United States

Site Status RECRUITING

The Emory Clinic

Atlanta, Georgia, United States

Site Status RECRUITING

Northwestern Memorial Hospital, Clinical Research Unit

Chicago, Illinois, United States

Site Status RECRUITING

Rush University Medical Center Outpatient Pulmonary Clinic

Chicago, Illinois, United States

Site Status RECRUITING

UI Health Hospital

Chicago, Illinois, United States

Site Status RECRUITING

Loyola University Medical Center

Maywood, Illinois, United States

Site Status RECRUITING

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status RECRUITING

University of Kentucky

Lexington, Kentucky, United States

Site Status RECRUITING

University of Louisville Healthcare Outpatient Research Clinic

Louisville, Kentucky, United States

Site Status RECRUITING

Tulane Medical Center

New Orleans, Louisiana, United States

Site Status RECRUITING

Johns Hopkins Asthma and Allergy Center

Baltimore, Maryland, United States

Site Status RECRUITING

Adventist Healthcare White Oak Medical Center

Silver Spring, Maryland, United States

Site Status RECRUITING

Tufts Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Infinity Medical Center

North Dartmouth, Massachusetts, United States

Site Status RECRUITING

Beaumont Hospital, Royal Oak

Royal Oak, Michigan, United States

Site Status RECRUITING

University of Minnesota Health Clinical Research Unit (CRU)

Minneapolis, Minnesota, United States

Site Status RECRUITING

Mayo Clinic

Rochester, Minnesota, United States

Site Status RECRUITING

The Lung Research Center, LLC

Chesterfield, Missouri, United States

Site Status RECRUITING

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

University of New Mexico

Albuquerque, New Mexico, United States

Site Status RECRUITING

Northwell Health

New Hyde Park, New York, United States

Site Status RECRUITING

Weill Cornell Medicine, New York-Presbyterian Hospital

New York, New York, United States

Site Status RECRUITING

Stony Brook Advanced Specialty Care

Stony Brook, New York, United States

Site Status RECRUITING

Montefiore Medical Center

The Bronx, New York, United States

Site Status RECRUITING

Duke University Medical Center

Durham, North Carolina, United States

Site Status RECRUITING

PulmonIx LLC

Greensboro, North Carolina, United States

Site Status RECRUITING

East Carolina University

Greenville, North Carolina, United States

Site Status RECRUITING

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

The Ohio State University Wexner Medical CEnter

Columbus, Ohio, United States

Site Status RECRUITING

Mercy Health St.Vincent Medical Center LLC

Toledo, Ohio, United States

Site Status RECRUITING

Pennsylvania State Hershey Medical Center and College of Medicine

Hershey, Pennsylvania, United States

Site Status RECRUITING

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Temple University Hospital

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Medical University of South Carolina-Nexus

Charleston, South Carolina, United States

Site Status RECRUITING

Prisma Health Pulmonology-Richland

Columbia, South Carolina, United States

Site Status RECRUITING

Clinical Trials Center of Middle Tennessee, LLC

Franklin, Tennessee, United States

Site Status RECRUITING

StatCare Pulmonary Consultants, PLLC

Knoxville, Tennessee, United States

Site Status RECRUITING

The Vanderbilt Lung Institute

Nashville, Tennessee, United States

Site Status RECRUITING

Baylor University Medical Center

Dallas, Texas, United States

Site Status RECRUITING

UT Southwestern Medical Center-Advanced Lung Clinic

Dallas, Texas, United States

Site Status RECRUITING

Houston Methodist Outpatient Center

Houston, Texas, United States

Site Status RECRUITING

The University of Texas Health Science Center at Houston, McGovern Medical School

Houston, Texas, United States

Site Status RECRUITING

A & A Research Consultants, LLC

McAllen, Texas, United States

Site Status RECRUITING

Metroplex Pulmonary and Sleep Center

McKinney, Texas, United States

Site Status RECRUITING

Intermountain Medical Center

Murray, Utah, United States

Site Status RECRUITING

University of Utah Health

Salt Lake City, Utah, United States

Site Status RECRUITING

University of Virginia Health System

Charlottesville, Virginia, United States

Site Status RECRUITING

Christopher King, MD

Falls Church, Virginia, United States

Site Status RECRUITING

Pulmonary Associates of Richmond, Inc.

Richmond, Virginia, United States

Site Status RECRUITING

University Hospital and UW Health Clinics

Madison, Wisconsin, United States

Site Status RECRUITING

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Instituto Ave Pulmo - Fundacion enfisema

Mar del Plata, Buenos Aires, Argentina

Site Status RECRUITING

Instituto Medico Rio Cuarto

Río Cuarto, Córdoba Province, Argentina

Site Status RECRUITING

Sanatorio Parque de Rosario - Consultorios Externos

Rosario, Santa Fe Province, Argentina

Site Status RECRUITING

Investigaciones en Patologias Respiratorias

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status RECRUITING

CIMER-Centro Integral de Medicina Respiratoria

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status RECRUITING

CINME Centro de Investigaciones Metabolicas

Buenos Aires, , Argentina

Site Status RECRUITING

Fundación Respirar

Buenos Aires, , Argentina

Site Status RECRUITING

Instituto de Medicina Respiratoria

Córdoba, , Argentina

Site Status RECRUITING

Sanatorio Allende Cerro

Córdoba, , Argentina

Site Status RECRUITING

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status RECRUITING

St George Hospital

Kogarah, New South Wales, Australia

Site Status RECRUITING

The Prince Charles Hospital

Brisbane, Queensland, Australia

Site Status RECRUITING

Eastern Health Box Hill Hospital

Box Hill, Victoria, Australia

Site Status RECRUITING

Monash Health-Monash Medical Centre

Clayton, Victoria, Australia

Site Status RECRUITING

Austin Health

Heidelberg, Victoria, Australia

Site Status RECRUITING

Institute for Respiratory Health - Midland

Midland, Western Australia, Australia

Site Status RECRUITING

Institute for Respiratory Health

Nedlands, Western Australia, Australia

Site Status RECRUITING

AZORG

Aalst, , Belgium

Site Status RECRUITING

ZAS Middelheim

Antwerp, , Belgium

Site Status RECRUITING

CUB Hopital Erasmde

Brussels, , Belgium

Site Status RECRUITING

Cliniques Universitaires St.-Luc

Brussels, , Belgium

Site Status RECRUITING

UZ Leuven

Leuven, , Belgium

Site Status RECRUITING

CHU de Liège

Liège, , Belgium

Site Status RECRUITING

St.Paul's Hospital

Vancouver, British Columbia, Canada

Site Status RECRUITING

Dynamic Drug Advancement Limited

Ajax, Ontario, Canada

Site Status RECRUITING

St.Joseph's Healthcare Hamilton

Hamilton, Ontario, Canada

Site Status RECRUITING

Hôpital Maisonneuve-Rosemont

Montreal, Quebec, Canada

Site Status RECRUITING

CIC Mauricie inc.

Québec, Quebec, Canada

Site Status RECRUITING

Centro de Investigacion Curico

Curicó, Maule Region, Chile

Site Status RECRUITING

Centro Respiratorio Integral LTDA. (CENRESIN)

Quillota, Región de Valparaíso, Chile

Site Status RECRUITING

Centro de Investigación de Enfermedades Respiratorias e Inmunológicas (CIERI)

Viña del Mar, Región de Valparaíso, Chile

Site Status RECRUITING

CEC Centro Estudios Clinicos

Santiago, Santiago Metropolitan, Chile

Site Status RECRUITING

Fundacion Medica San Cristobal

Santiago, Santiago Metropolitan, Chile

Site Status RECRUITING

Biocinetic Ltda.

Santiago, Santiago Metropolitan, Chile

Site Status RECRUITING

Hôpital Avicennes

Bobigny, , France

Site Status RECRUITING

Hospices civils de Lyon - Hôpital Louis Pradel

Bron, , France

Site Status RECRUITING

CHU Caen Normandie

Caen, , France

Site Status RECRUITING

Assistance Publique Hôpitaux de Marseille - centre Hospitalier Régional de Marseille

Marseille, , France

Site Status RECRUITING

Rouen University Hospital

Rouen, , France

Site Status RECRUITING

Centre Hospitalier Régional Universitaire de Tours

Tours, , France

Site Status RECRUITING

RoMed Klinikum Rosenheim-Ellmaierstr. 23

Rosenheim, Bavaria, Germany

Site Status RECRUITING

Zentralklinik Bad Berka GmbH Klinik für Pneumologie, Zentrum für Schlaf-und Beatmungsmedizin

Bad Berka, , Germany

Site Status RECRUITING

Prufstelle der GWT am Fachkrankenhaus Coswig

Coswig, , Germany

Site Status RECRUITING

uhrlandklinik Westdeutsches Lungenzentrum am Universitätsklinikum Essen gGmbH

Essen, , Germany

Site Status RECRUITING

SLK Kliniken Heilbronn GmbH

Löwenstein, , Germany

Site Status RECRUITING

LMU Klinikum Medizinische Klinik und Poliklinik V

München, , Germany

Site Status RECRUITING

Barzilai Medical Center

Ashkelon, , Israel

Site Status RECRUITING

Hillel Yaffe Medical Center

Hadera, , Israel

Site Status RECRUITING

Rabin Medical Center

Haifa, , Israel

Site Status RECRUITING

Shaare Zedek Medical Center

Jerusalem, , Israel

Site Status RECRUITING

The Hadassah University Medical Center Ein Kerem Hospital

Jerusalem, , Israel

Site Status RECRUITING

Meir Medical Center

Kfar Saba, , Israel

Site Status RECRUITING

Rabin Medical Center

Petah Tikva, , Israel

Site Status RECRUITING

Kaplan Medical Center

Rehovot, , Israel

Site Status RECRUITING

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status RECRUITING

Azienda Ospedaliero Universitaria Policlinico "G. Rodolico - San Marco" Presidio Ospedaliero Gaspare Rodolico

Catania, , Italy

Site Status RECRUITING

Azienda Unita Sanitaria Locale Della Romagna Ospedale "Gian Battista Morgagni - Luigi Pierantoni" di Forlì

Forlì, , Italy

Site Status RECRUITING

Azienda Ospedaliero-Universitaria di Modena Policlinico di Modena

Modena, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

Site Status RECRUITING

Azienda Ospedaliero-Universitaria Senese

Siena, , Italy

Site Status RECRUITING

Canterbury Respiratory Research Group

Christchurch, Canterbury, New Zealand

Site Status RECRUITING

Aotearoa Clinical Trials Trust- Middlemore Hospital

Auckland, , New Zealand

Site Status RECRUITING

Hospital Nacional Adolfo Guevara Velasco

Cusco, , Peru

Site Status RECRUITING

Clinica Internacional - Sede Lima

Lima, , Peru

Site Status RECRUITING

Unidad de Investigacion de Enfermedades Respiratorias- Clinica San Pablo -Surco

Lima, , Peru

Site Status RECRUITING

Clinica Ricardo Palma

Lima, , Peru

Site Status RECRUITING

Hospital Central de la Fuerza Aerea del Peru

Lima, , Peru

Site Status RECRUITING

Centro de Investigacion de Enfermedades Respiratorias - Clinica Providencia

Lima, , Peru

Site Status RECRUITING

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status RECRUITING

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status RECRUITING

Korea University Anam Hospital

Seoul, , South Korea

Site Status RECRUITING

Asan Medical Center

Seoul, , South Korea

Site Status RECRUITING

The Catholic University of Korea, Eunpyeong St. Mary's Hospital

Seoul, , South Korea

Site Status RECRUITING

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, , Taiwan

Site Status RECRUITING

Chang Gung Medical Foundation Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status RECRUITING

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status RECRUITING

Birmingham Heartlands Hospital

Birmingham, , United Kingdom

Site Status RECRUITING

Royal Papworth Hospital

Cambridge, , United Kingdom

Site Status RECRUITING

NHS Lothian, Royal INfirmary of Edingburgh

Edinburgh, , United Kingdom

Site Status RECRUITING

Guy's Hospital

London, , United Kingdom

Site Status RECRUITING

Manchester University NHS Foundation Trust, North Manchester General Hospital

Manchester, , United Kingdom

Site Status RECRUITING

NHS Tayside, Perth Royal Infirmary

Perth, , United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Belgium Canada Chile France Germany Israel Italy New Zealand Peru South Korea Taiwan United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

United Therapeutics Global Medical Information

Role: CONTACT

Phone: 919-485-8350

Email: [email protected]

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Melessia Wells

Role: primary

Gabrielle Ambrose

Role: primary

Jennifer Perez

Role: primary

Grace Harvey

Role: primary

Jordan Perkins

Role: primary

Mandy Swanson

Role: primary

Sarah Natera

Role: primary

Chery Bolovits

Role: primary

Jannet Estrada

Role: primary

Amen Hamed

Role: primary

Jennifer McWilliams

Role: primary

Inna Dawson

Role: primary

Brenda Farlow

Role: primary

Mitzi Near

Role: primary

Aaron Gundersheimer

Role: primary

Kimberly Saulsberry

Role: primary

Hannah Carlson

Role: primary

Adriana Martinez

Role: primary

Kimberly Lovell

Role: primary

Srushan Shankara bhaktula

Role: primary

Belica Graf

Role: primary

Sandy Ditta

Role: primary

Sarah Collins

Role: primary

Jennifer Hernandez

Role: primary

Mary Hays

Role: primary

Layla Rahimi

Role: primary

Cheryl O'Neil

Role: primary

Beverly Mauer

Role: primary

Amanda DeGrote

Role: primary

Teng Moua

Role: primary

Anna Shipp

Role: primary

Rosann Gans

Role: primary

Megan Baldenweck

Role: primary

Frederick Gentry

Role: primary

Sara Khan

Role: primary

Christine Wu

Role: primary

Jacqueline Skarre

Role: primary

Jane Wilson

Role: primary

Lisa Holmes

Role: primary

Lauren Hinshaw

Role: primary

Shravya Dharambhat

Role: primary

Emillie Hoh

Role: primary

Benjamin Hood

Role: primary

Joseph Bandi

Role: primary

Timothy Sheehan

Role: primary

Sarah Alam

Role: primary

Kim Selwood

Role: primary

Angela Francisco

Role: primary

Keera McKenna

Role: primary

Lindsey Robbs

Role: primary

Tabitha McCauley

Role: primary

Phyllis Young

Role: primary

Brianna Kamran

Role: primary

Maria Goralski

Role: primary

Nelson Villasmil Hernandez

Role: primary

Mary Rangel

Role: primary

Jaedan Chapa

Role: primary

Ambreen Ahmed

Role: primary

Danielle Nasson

Role: primary

Heather Hammerschmidt

Role: primary

Yousef Althulth

Role: primary

Priscila Dauphin

Role: primary

Betsy Daniel

Role: primary

Maggie Chilsen

Role: primary

Kiley Timler

Role: primary

Mario Fernando Sabas

Role: primary

Sebastián Etchevers

Role: primary

Julieta Nasurdi

Role: primary

Maria Jose Guzman

Role: primary

Natalia Juarez Babiano

Role: primary

Yesica Castillo

Role: primary

Antonela Iannazzo

Role: primary

Angélica Baima

Role: primary

Maria Gracia de la Vega

Role: primary

Alan Teoh

Role: primary

Ajantha Raguparan

Role: primary

Alan Carew

Role: primary

Alan Young

Role: primary

Yvonne Ng

Role: primary

Yet Khor

Role: primary

Kaye McMullan

Role: primary

Michelle Young, MD

Role: primary

Elke Hardeman

Role: primary

Johan Clukers

Role: primary

Sebastien Van Laethem

Role: primary

Sophie Gohy

Role: primary

Nico De Crem

Role: primary

Fanny Gester

Role: primary

Jeff Wong

Role: primary

Cynthia Lee

Role: primary

Sarah Goodwin

Role: primary

Danae Tassy

Role: primary

Mireille Devost

Role: primary

Reinaldo Eduardo Cortez de la Fuente

Role: primary

Leon Fernando Ovalle Jarpa

Role: primary

Magdalena Reyes

Role: primary

Nicolas Cataldo

Role: primary

Eliana Andahur Orellana

Role: primary

Beatriz Diaz

Role: primary

Morgane Didier

Role: primary

François Lestelle

Role: primary

Aurélien Justet

Role: primary

Benjamin Coiffard

Role: primary

Hélène Morisse Pradier

Role: primary

Laurent Plantier

Role: primary

Stefan Jungbauer

Role: primary

Veronika Gath

Role: primary

Marcus Vogler

Role: primary

Eda Burcur Börner

Role: primary

Biljana Joves

Role: primary

Tobias Veit

Role: primary

Mohamed Alamor

Role: primary

Marinella Beckerman

Role: primary

Michal Shteinberg

Role: primary

Ariel Rokach

Role: primary

Rottem Kuint

Role: primary

Lilach Israeli-Shani

Role: primary

Maayan Flaschner

Role: primary

Nina Azarov

Role: primary

Irina Fomin

Role: primary

Antonio Galia

Role: primary

Luca Donati

Role: primary

Valentina Ruggieri

Role: primary

Diana Verdirosi

Role: primary

Benedetta Di Ruggiero

Role: primary

Sara Pure

Role: primary

Jennifer Treacy

Role: primary

Rosa Alfaro Carrasco

Role: primary

Eneyda Llerena Zegarra

Role: primary

Alva Silvia

Role: primary

Judith Armas

Role: primary

Franklin Gutierrez Torres

Role: primary

Marjorie Gaviria Haxhuell

Role: primary

Huiyeong Hwang

Role: primary

LeeNa Kim

Role: primary

Mija Kim

Role: primary

Yebin Park

Role: primary

SunHwa Ryu

Role: primary

Hung Yuan-Chen

Role: primary

Yi-Chun Shih

Role: primary

Yi-Chun Shih

Role: primary

Caroline Gallagher

Role: primary

Helen Parfrey

Role: primary

Manjit Cartlidge

Role: primary

Alexandra Lawrence

Role: primary

Huda Badri

Role: primary

Moses Effiong

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

RIN-PF-305

Identifier Type: -

Identifier Source: org_study_id