A Study of Eptinezumab in Pediatric Participants With Episodic Migraine

NCT ID: NCT05897320

Last Updated: 2025-11-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

315 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-06-08

Study Completion Date

2027-08-31

Brief Summary

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The main goal of this trial is to learn whether eptinezumab helps reduce the number of days with episodic migraine in pediatric participants.

Detailed Description

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Conditions

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Episodic Migraine

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Eptinezumab 300 mg

Participants will receive a single intravenous (IV) infusion of eptinezumab 300 mg (weight adjusted).

Group Type EXPERIMENTAL

Eptinezumab

Intervention Type DRUG

Solution for infusion

Placebo

Participants will receive a single IV infusion of matching placebo to eptinezumab.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Solution for infusion

Eptinezumab 100 mg

Participants will receive a single IV infusion of eptinezumab 100 mg (weight adjusted).

Group Type EXPERIMENTAL

Eptinezumab

Intervention Type DRUG

Solution for infusion

Interventions

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Eptinezumab

Solution for infusion

Intervention Type DRUG

Placebo

Solution for infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of migraine (with or without aura) according to the International Classification of Headache Disorders, 3rd edition (ICHD-3; in the opinion of the investigator) with history of migraine headaches of at least 6 months prior to the Screening Visit.
* During the 28-day screening period, the participant (and their parent/caregiver, when applicable) must adequately complete the headache eDiary (≥23 of the 28 days) following the day of the Screening Visit.
* During the 28-day screening period, the participant must have ≤14 headache days, of which at least 4 are migraine days as documented in the eDiary.

Exclusion Criteria

* History or diagnosis of chronic tension-type headache, hypnic headache, cluster headache, hemicrania continua, new daily persistent headache, or unusual migraine subtypes (previously referred to as complicated migraine), such as hemiplegic migraine (sporadic and familial), migraine with brainstem aura, recurrent painful ophthalmic neuropathy, or migraine with neurological accompaniments that are not typical of migraine aura (diplopia, altered consciousness, or long duration, e.g., \>60 min).
* History of moderate or severe head trauma or other neurological disorder or systemic medical disease that is, in the investigator's opinion, likely to affect the functions of the central nervous system.
* Current psychiatric condition that is uncontrolled and/or untreated for a minimum of 6 months prior to the Screening Visit. Participants with a lifetime history of psychosis and/or mania are excluded.
* Any other disorder for which the treatment takes priority over treatment of migraine or is likely to interfere with study treatment or impair treatment compliance.
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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H. Lundbeck A/S

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Email contact via H. Lundbeck A/S

Role: STUDY_DIRECTOR

[email protected]

Locations

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Ki Health Partners LLC DBA New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status RECRUITING

Child Neurology of NW Florida

Gulf Breeze, Florida, United States

Site Status RECRUITING

A G A Clinical Trials

Hialeah, Florida, United States

Site Status RECRUITING

University of South Florida

Tampa, Florida, United States

Site Status RECRUITING

University of Kentucky HealthCare (UKHC) Kentucky Clinic

Lexington, Kentucky, United States

Site Status RECRUITING

University of Maryland School of Medicine

Baltimore, Maryland, United States

Site Status RECRUITING

Michigan Head Pain and Neurological Institute

Ann Arbor, Michigan, United States

Site Status COMPLETED

North Suffolk Neurology-Commack

Commack, New York, United States

Site Status RECRUITING

OnSite Clinical Solutions, LLC - Randolph Rd - Charlotte

Charlotte, North Carolina, United States

Site Status COMPLETED

Childrens Hospital Medical Center of Akron

Akron, Ohio, United States

Site Status RECRUITING

Cincinnati Children's Hospital Medical Center - PIN

Cincinnati, Ohio, United States

Site Status RECRUITING

Road Runner Research Ltd

San Antonio, Texas, United States

Site Status RECRUITING

Children's Specialty Group - 3 Commercial Place

Norfolk, Virginia, United States

Site Status RECRUITING

Childrens Hospital of Wisconsin

New Berlin, Wisconsin, United States

Site Status RECRUITING

Clínica Privada Independencia

Munro, Buenos Aires, Argentina

Site Status COMPLETED

Hospital Britanico de Buenos Aires

Barracas, Ciudad Autónoma de BuenosAires, Argentina

Site Status RECRUITING

Expertia S.A- Mautalén Salud e Investigación

Buenos Aires, Ciudad Autónoma de BuenosAires, Argentina

Site Status RECRUITING

Instituto Médico Río Cuarto

Río Cuarto, Córdoba Province, Argentina

Site Status RECRUITING

INECO Neurociencias Oroño

Rosario, Santa Fe Province, Argentina

Site Status RECRUITING

Centro de Investigaciones Médicas Tucumán - PPDS

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status RECRUITING

Hospital de Niños de La Santisima Trinidad

Córdoba, , Argentina

Site Status RECRUITING

Medical Arts Health Research Group - Penticton

Penticton, British Columbia, Canada

Site Status COMPLETED

Vancouver Island Health Authority

Victoria, British Columbia, Canada

Site Status RECRUITING

The Kids Clinic

Ajax, Ontario, Canada

Site Status RECRUITING

London Health Sciences Centre -800 Commissioners Rd E

London, Ontario, Canada

Site Status RECRUITING

Ospedale Pediatrico Bambino Gesù IRCCS

Rome, Lazio, Italy

Site Status RECRUITING

Istituto G Gaslini Ospedale Pediatrico IRCCS

Genoa, Liguria, Italy

Site Status RECRUITING

Ospedale San Raffaele S.r.l. - PPDS

Milan, Lombardy, Italy

Site Status RECRUITING

Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, Lombardy, Italy

Site Status RECRUITING

Fondazione Istituto Neurologico Nazionale Casimiro Mondino IRCCS

Pavia, Lombardy, Italy

Site Status RECRUITING

AO Brotzu - Clinica di Neuropsichiatria dell'Infanzia e dell'Adolescenza - INCIPIT - PIN

Cagliari, Sardinia, Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria A Meyer - INCIPIT - PIN

Florence, Tuscany, Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria Pisana - Stabilimento Santa Chiara

Pisa, Tuscany, Italy

Site Status RECRUITING

Clinical Research Institute SC-Mexico

Tepetlacolco, , Mexico

Site Status RECRUITING

AthleticoMed

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status RECRUITING

ETG Neuroscience - PPDS

Warsaw, Masovian Voivodeship, Poland

Site Status RECRUITING

Centrum Medyczne Plejady Magdalena Celinska - Lowenhoff, Michal Zolnowski Spolka komandytowa

Krakow, , Poland

Site Status RECRUITING

ETG Lublin - PPDS

Lublin, , Poland

Site Status RECRUITING

Instytut Zdrowia Dr Boczarska-Jedynak Sp. z o.o. Sp. k.

Oświęcim, , Poland

Site Status RECRUITING

MTZ Clinical Research Powered by PRATIA - PPDS

Warsaw, , Poland

Site Status RECRUITING

MIGRE Polskie Centrum Leczenia Migreny Anna Gryglas-Dworak

Wroclaw, , Poland

Site Status RECRUITING

ULS de Santo António, EPE - Centro Materno Infantil Norte

Porto Covo, Setúbal District, Portugal

Site Status RECRUITING

Centro Clínico Académico, Braga - Hospital de Braga

Braga, , Portugal

Site Status RECRUITING

ULS de Coimbra, EPE - Hospital Pediátrico de Coimbra

Coimbra, , Portugal

Site Status RECRUITING

Hospital CUF Descobertas

Lisbon, , Portugal

Site Status COMPLETED

ULS de São João, EPE - Hospital de São João

Porto Covo, , Portugal

Site Status RECRUITING

Childrens University Hospital

Belgrade, , Serbia

Site Status RECRUITING

University Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

University Clinical Center Nis

Niš, , Serbia

Site Status RECRUITING

Children and Youth Health Care Institute of Vojvodina

Novi Sad, , Serbia

Site Status RECRUITING

Clinical Centre of Vojvodina

Novi Sad, , Serbia

Site Status RECRUITING

CHUVI - H.U. Alvaro Cunqueiro

Vigo, Pontevedra, Spain

Site Status RECRUITING

Hospital Universitario Vall d'Hebron - PPDS

Barcelona, , Spain

Site Status RECRUITING

Hospital Clinico San Carlos

Madrid, , Spain

Site Status RECRUITING

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status RECRUITING

Izmir City Hospital

Bayraklı, İzmir, Turkey (Türkiye)

Site Status RECRUITING

Eskisehir Osmangazi Universitesi Tip Fakultesi Hastanesi

Eskişehir, , Turkey (Türkiye)

Site Status RECRUITING

Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi

Fatih/Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Mersin Universitesi Tip Fakultesi Hastanesi

Mersin, , Turkey (Türkiye)

Site Status RECRUITING

Royal Hospital for Children (Glasgow) - PPDS - PIN

Glasgow, Glasgow City, United Kingdom

Site Status RECRUITING

Royal Hospital for Children and Young People - PIN

Edinburgh, Midlothian, United Kingdom

Site Status RECRUITING

James Paget University Hospitals NHS Foundation Trust

Great Yarmouth, Norfolk, United Kingdom

Site Status RECRUITING

Great Ormond Street Hospital

London, , United Kingdom

Site Status RECRUITING

Countries

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United States Argentina Canada Italy Mexico Poland Portugal Serbia Spain Turkey (Türkiye) United Kingdom

Central Contacts

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Email contact via H. Lundbeck A/S

Role: CONTACT

Phone: +45 36301311

Email: [email protected]

Other Identifiers

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2022-502538-14-00

Identifier Type: OTHER

Identifier Source: secondary_id

19357A

Identifier Type: -

Identifier Source: org_study_id