ML-004 Open-Label Extension Study in Adults and Adolescents With Autism Spectrum Disorders (ASD)

NCT ID: NCT05889273

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ENROLLING_BY_INVITATION

Clinical Phase

PHASE2

Total Enrollment

120 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-06-01

Study Completion Date

2027-12-31

Brief Summary

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ML-004-003 is a multi-center, open-label extension study that will enroll approximately 120 adolescent and adult subjects with ASD that have completed study ML-004-002. The primary objective of the study will be to evaluate the safety of ML-004 in subjects with ASD.

Detailed Description

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Conditions

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Autism Spectrum Disorder

Keywords

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ASD Autism Autism Spectrum Disorder Social Communication

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Multi-center, open-label study
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ML-004 (IR)/(ER) tablet

ML-004 is a bilayer immediate-release (IR)/extended-release (ER, gastroretentive) oral tablet formulation. ML-004 is taken orally once daily and provided as a tablet in two dose strengths of 12 mg (3 mg IR/9 mg ER) and 24 mg tablet (6 mg IR/18 mg ER). Dose levels for this study are 12 mg (provided as one 12 mg tablet), 24 mg (one 24 mg tablet), 48 mg (two 24 mg tablets), and 72 mg (three 24 mg tablets).

Group Type EXPERIMENTAL

ML-004 (IR)/(ER) tablet

Intervention Type DRUG

Participants will receive ML-004 once daily.

Interventions

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ML-004 (IR)/(ER) tablet

Participants will receive ML-004 once daily.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Has completed Study ML-004-002 within the past 90 days
* Age 12 years to 46 years at screening
* Has a designated care/study partner who can reliably report on symptoms
* Has a diagnosis of Autism Spectrum Disorder (ASD)
* Has a body mass index (BMI) ≥18 kg/m²
* Psychoactive medications and adjunctive therapies stable for 4 weeks prior to screening
* Must be able to swallow study medication

Exclusion Criteria

* Has Rett syndrome or Child Disintegrative Disorder
* History of epilepsy without current adequate control, or any seizure in the 6 months preceding screening
* Has a positive response to C-SSRS questions 4 and/or 5, or is a significant risk for suicidal behavior
* Has a clinical history of uncontrolled or severe hypertension
* If female, is pregnant or lactating
Minimum Eligible Age

12 Years

Maximum Eligible Age

46 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MapLight Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Harmonex Neuroscience Research

Dothan, Alabama, United States

Site Status

Southwest Autism Research and Resource Center

Phoenix, Arizona, United States

Site Status

Cortica Healthcare

Glendale, California, United States

Site Status

NRC Research Institute

Orange, California, United States

Site Status

Yale Child Study Center

New Haven, Connecticut, United States

Site Status

The Children's Research Institute

Washington D.C., District of Columbia, United States

Site Status

Abba Medical Group

Miami, Florida, United States

Site Status

APG Research, LLC

Orlando, Florida, United States

Site Status

University of South Florida Psychiatry and Behavioral Neurosciences

Tampa, Florida, United States

Site Status

Neurobehavioral Medicine Group

Bloomfield Hills, Michigan, United States

Site Status

University of Missouri, Thompson Center for Autism & Neurodevelopment

Columbia, Missouri, United States

Site Status

Nathan Kline Institute for Psychiatric Research

Orangeburg, New York, United States

Site Status

Richmond Behavioral Associates

Staten Island, New York, United States

Site Status

Suburban Research Associates

Media, Pennsylvania, United States

Site Status

BioBehavioral Research of Austin

Austin, Texas, United States

Site Status

Road Runner Research, Ltd.

San Antonio, Texas, United States

Site Status

Family Psychiatry of The Woodlands

The Woodlands, Texas, United States

Site Status

Brain and Mind Centre

Camperdown, New South Wales, Australia

Site Status

The Royal Children's Hospital, Murdoch Children's Research Institute

Parkville, Victoria, Australia

Site Status

Holland Bloorview Kids Rehabilitation Hospital

Toronto, Ontario, Canada

Site Status

Countries

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United States Australia Canada

Related Links

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Other Identifiers

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ML-004-003

Identifier Type: -

Identifier Source: org_study_id