A Study of GDX012 in Adults With Relapsed or Refractory Acute Myeloid Leukemia

NCT ID: NCT05886491

Last Updated: 2025-12-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

14 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-07-11

Study Completion Date

2026-05-12

Brief Summary

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GDX012 is a novel cell therapy developed for the treatment of certain types of cancer, including Acute Myeloid Leukemia (AML). The main aims of the study are to learn how safe GDX012 is, how treatment with GDX012 is tolerated and to determine the best dose of GDX012.

Detailed Description

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The drug being tested in this study is called GDX012. GDX012 is being tested to evaluate the safety and tolerability in adult participants with AML.

The study will enroll approximately 53 patients in two phases, dose escalation and dose expansion.

During Phase 1 (sequential dose escalation), participants will be assigned to one of the following treatment groups each consisting of 3 to 6 participants to receive GDX012 at one of the three dose levels:

1. GDX012 Dose 1
2. GDX012 Dose 2
3. GDX012 Dose 3

Upon completion of Phase 1, 1 to 2 dose levels will be selected for Phase 2a of the study. At the completion of Phase 2a of the study a single dose may be selected by the sponsor and investigators as the recommended phase 2 dose (RP2D) for future study.

This multi-center trial will be conducted in the United States. The overall time to participate in the study is approximately 14 months.

Conditions

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Leukemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Phase 1: Dose Escalation of GDX012

Participants will receive GDX012 weight-based dose as intravenous (IV) infusion on Day 1 of Phase 1 after lymphodepleting chemotherapy. Three dose levels of GDX012 will be tested in Phase 1. Some participants may be eligible for a second dose.

Group Type EXPERIMENTAL

GDX012

Intervention Type DRUG

GDX012 suspension for IV infusion.

Chemotherapy Agents

Intervention Type DRUG

Chemotherapy agents (fludarabine/cyclophosphamide) as per standard of care.

Phase 2a: GDX012

Participants will receive GDX012 (weight-based) IV infusion at pre-selected one or two dose levels from Phase 1, on Day 1 after lymphodepleting chemotherapy. Some participants may be eligible for a second dose.

Group Type EXPERIMENTAL

GDX012

Intervention Type DRUG

GDX012 suspension for IV infusion.

Chemotherapy Agents

Intervention Type DRUG

Chemotherapy agents (fludarabine/cyclophosphamide) as per standard of care.

Interventions

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GDX012

GDX012 suspension for IV infusion.

Intervention Type DRUG

Chemotherapy Agents

Chemotherapy agents (fludarabine/cyclophosphamide) as per standard of care.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Total body weight of ≥40 kg.
2. Must have pathologically confirmed relapsed or refractory acute myeloid leukemia (R/R AML) including:

1. Relapsed AML is defined as ≥5% blasts in the bone marrow (BM) or peripheral blood at any time after achieving a CR, CRh, Cri, or MLFS.
2. Refractory AML is defined as failure to achieve a CR, CRh, Cri, or MLFS after 1 of the following regimens:

i. Two courses of intensive induction chemotherapy. ii. At least 2 cycles of hypomethylating agent (HMA) or low-dose, cytarabine-based combination regimen.

iii. At least 4 cycles of HMA monotherapy.
3. During dose escalation, participants must be ineligible for hematopoietic stem cell transplantation (HSCT).
4. Must have an anticipated life expectancy of \>3 months before lymphodepletion.
5. Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 1.
6. Participants must have adequate renal, cardiac, hepatic, pulmonary and bone marrow function as defined by the protocol.

Exclusion Criteria

1. Diagnosis of acute promyelocytic leukemia.
2. Has received or plans to receive any of the excluded therapy/treatment within the specified timeframe before lymphodepleting chemotherapy as defined by the protocol.
3. Prior allogeneic HSCT within 3 months of signing informed consent form (ICF) or with ongoing requirement for systemic graft-versus-host therapy.
4. Active central nervous system (CNS) involvement.
5. History of malignancy other than non-melanoma skin cancer or carcinoma in situ (eg. cervix, bladder, breast) low grade prostate cancer without treatment requirement unless in remission without treatment for ≥2 years.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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University of Alabama at Birmingham (UAB) Hospital

Birmingham, Alabama, United States

Site Status

City of Hope

Duarte, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Sarah Cannon/CBCI

Denver, Colorado, United States

Site Status

Comprehensive Cancer Center of Northwestern University

Chicago, Illinois, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status

Thomas Jefferson University

New York, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

OHSU Knight Cancer Institute

Portland, Oregon, United States

Site Status

Tri-Star BMT/Sarah Cannon Nashville

Nashville, Tennessee, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Related Links

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https://clinicaltrials.takeda.com/study-detail/fb2158ec7a43459e??page=1&idFilter=TAK-012-1501

Click here for more information about this trial in easy-to-understand language, including a Plain Language Summary of the results if the trial has been completed.

Other Identifiers

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jRCT2033240022

Identifier Type: REGISTRY

Identifier Source: secondary_id

TAK-012-1501

Identifier Type: -

Identifier Source: org_study_id

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