Evaluation of Eflornithine Plus Temozolomide in Patients With Newly Diagnosed Glioblastoma or Astrocytoma

NCT ID: NCT05879367

Last Updated: 2025-06-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

66 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-07-24

Study Completion Date

2026-06-30

Brief Summary

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The purpose of this study is to establish the recommended phase 2 dose of eflornithine in combination with temozolomide in patients whose glioblastoma or astrocytoma is newly diagnosed, and to evaluate safety and tolerability of this combination at that dose.

Detailed Description

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This open label dose escalation and expansion study will be conducted using a standard dose-escalation design with escalating doses of eflornithine plus temozolomide at the approved dose level, followed by an expansion cohort that will further evaluate safety and preliminary efficacy of the combination at the recommended phase 2 dose.

Duration of participation will be up to approximately 104 weeks in total per patient.

Screening Period - A maximum screening duration of 4 weeks.

Treatment Period - Up to approximately 104 weeks.

Follow-Up Visit - 4 weeks from last treatment.

Long-term Survival Follow-Up - up to 2 years from last treatment.

A total of up to 66 patients will be enrolled in a non-randomized fashion (patients may be added to any of the dose levels below the RP2D to a maximum of approximately 20 per dose level with the intent of further characterizing safety and pharmacokinetics).

Conditions

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Glioblastoma, IDH-wildtype Glioblastoma Glioblastoma Multiforme Glioblastoma IDH (Isocitrate Dehydrogenase) Wildtype GBM Astrocytoma Astrocytoma, IDH-Mutant

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Eflornithine Dose Level 1 + Temozolomide

Group Type EXPERIMENTAL

Eflornithine (Dose Level 1)

Intervention Type DRUG

Eflornithine 2.3 g/m2 administered orally every 8 hours on a 2 weeks on, 2 weeks off schedule

Temozolomide

Intervention Type DRUG

Temozolomide 150 mg/m2 (with option to escalate per USPI maintenance phase instructions) administered orally once daily on a 5 days on, 23 days off schedule

Eflornithine Dose Level 2 + Temozolomide

Group Type EXPERIMENTAL

Eflornithine (Dose Level 2)

Intervention Type DRUG

Eflornithine 2.8 g/m2 administered orally every 8 hours on a 2 weeks on, 2 weeks off schedule

Temozolomide

Intervention Type DRUG

Temozolomide 150 mg/m2 (with option to escalate per USPI maintenance phase instructions) administered orally once daily on a 5 days on, 23 days off schedule

Eflornithine Dose Level -1 + Temozolomide

Group Type EXPERIMENTAL

Eflornithine (Dose Level -1)

Intervention Type DRUG

Eflornithine 1.75 g/m2 administered orally every 8 hours on a 2 weeks on, 2 weeks off schedule

Temozolomide

Intervention Type DRUG

Temozolomide 150 mg/m2 (with option to escalate per USPI maintenance phase instructions) administered orally once daily on a 5 days on, 23 days off schedule

Interventions

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Eflornithine (Dose Level 1)

Eflornithine 2.3 g/m2 administered orally every 8 hours on a 2 weeks on, 2 weeks off schedule

Intervention Type DRUG

Eflornithine (Dose Level 2)

Eflornithine 2.8 g/m2 administered orally every 8 hours on a 2 weeks on, 2 weeks off schedule

Intervention Type DRUG

Eflornithine (Dose Level -1)

Eflornithine 1.75 g/m2 administered orally every 8 hours on a 2 weeks on, 2 weeks off schedule

Intervention Type DRUG

Temozolomide

Temozolomide 150 mg/m2 (with option to escalate per USPI maintenance phase instructions) administered orally once daily on a 5 days on, 23 days off schedule

Intervention Type DRUG

Other Intervention Names

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DFMO DFMO DFMO Temodar TMZ

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of World Health Organization (WHO) G4 classified GBM, IDH-wildtype (patients with GBM) or G3 astrocytoma (IDH1 or 2 mutant; CDKN2A/B intact) per WHO 2021 tumor classification.
* Completed external beam radiation therapy per standard of care.
* Patients with GBM: Must have received at least 80% of planned daily doses of TMZ during chemoradiation. Patients with astrocytoma: Must have tolerated adjuvant TMZ treatment through at least 2 and not more than 4 cycles.
* Adequate hematologic, renal, hepatic, and other organ function as indicated by hematology and serum chemistry testing.
* Willing to abstain from intercourse or use acceptable contraceptive methods.
* If taking corticosteroids, must be on a stable or decreasing dose.

Exclusion Criteria

* Recent history of recurrent or metastatic cancer that could confound response assessments
* Prior systemic chemotherapy other than temozolomide during external beam radiation therapy (for patients with GBM) or adjuvant temozolomide through up to 4 pre-study cycles (for patients with astrocytoma).
* Prior Optune treatment.
* Active infection or serious intercurrent medical illness.
* Poorly controlled seizures.
* Significant cardiac disease within 6 months of enrollment.
* Poorly controlled diabetes.
* Use of another investigational agent within 30 days of enrollment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Orbus Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Howard Colman, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Huntsman Cancer Institute/ University of Utah

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status WITHDRAWN

Henry Ford Hospital

Detroit, Michigan, United States

Site Status RECRUITING

Columbia University Medical Center - Herbert Irving Pavilion

New York, New York, United States

Site Status RECRUITING

Duke University

Durham, North Carolina, United States

Site Status RECRUITING

The Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Brown University Health/Rhode Island Hospital

Providence, Rhode Island, United States

Site Status RECRUITING

UT MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

University of Utah, Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Monika Varga

Role: CONTACT

6506569424

Facility Contacts

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Meghan Gauronskas

Role: primary

313-725-7871

Angela Dunn

Role: backup

313-725-7870

Maria Diaz, MD

Role: primary

212-342-0571

Nurse Navigators

Role: backup

212-342-5162

Erin Severance

Role: primary

919-668-6230

David Peereboom, MD

Role: primary

216-445-6068

Rachel Hufsey, RN

Role: backup

Nuno Rodrigues, RN

Role: primary

401.444.3059

Gada Alam

Role: backup

401-444-6217

Carlos Kamiya Matsuoka, MD

Role: primary

713-408-3538

Evguenia Gachimova, RN

Role: backup

832-266-3519

Rachel Kingsford

Role: primary

801-585-0115

Yuri Kida

Role: backup

801-646-4397

Other Identifiers

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OT-21-101

Identifier Type: -

Identifier Source: org_study_id

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