A Study of CC-97540, CD-19-Targeted Nex-T CAR T Cells, in Participants With Severe, Refractory Autoimmune Diseases (Breakfree-1)

NCT ID: NCT05869955

Last Updated: 2026-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

270 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-13

Study Completion Date

2028-08-29

Brief Summary

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The purpose of this study is to establish the tolerability, preliminary efficacy, and pharmacokinetics of CC-97540 in participants with severe, refractory autoimmune diseases (Breakfree-1).

Detailed Description

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Conditions

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Systemic Lupus Erythematosus Idiopathic Inflammatory Myopathy Systemic Sclerosis Rheumatoid Arthritis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Administration of CC-97540

Group Type EXPERIMENTAL

CC-97540

Intervention Type DRUG

Specified dose on specified days

Fludarabine

Intervention Type DRUG

Specified dose on specified days

Cyclophosphamide

Intervention Type DRUG

Specified dose on specified days

Tocilizumab

Intervention Type DRUG

Specified dose on specified days

Interventions

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CC-97540

Specified dose on specified days

Intervention Type DRUG

Fludarabine

Specified dose on specified days

Intervention Type DRUG

Cyclophosphamide

Specified dose on specified days

Intervention Type DRUG

Tocilizumab

Specified dose on specified days

Intervention Type DRUG

Other Intervention Names

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BMS-986353

Eligibility Criteria

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Inclusion Criteria

\- Diagnosis of Systemic Lupus Erythematosus (SLE) defined as follows:.

i) Fulfilling the 2019 European League Against Rheumatism (EULAR) / American College of Rheumatology (ACR) classification criteria of SLE.

ii) Presence of anti-dsDNA, anti-histone, anti-chromatin, anti-Ro (anti-SS-A), anti-La (anti-SS-B), or anti-Sm antibodies at screening.

\- SLE disease activity:.

i) Active disease at screening, with recent ≥ 1 major organ system with a BILAG A score (excluding musculoskeletal, mucocutaneous, and/or constitutional organ system).

ii) Inadequate response to glucocorticoids and to at least 2 of the following treatments, used for at least 3 months each: cyclophosphamide, mycophenolic acid or its derivatives, belimumab, azathioprine, anifrolumab, methotrexate, rituximab, obinutuzumab, cyclosporin, tacrolimus or voclosporin.

* Diagnosis of Idiopathic Inflammatory Myopathy (IIM) defined as follows:.

i) Fulfilling the 2017 EULAR/ACR classification criteria for probable or definite IIM.

ii) Participant diagnosed with the following IIM subgroups: dermatomyositis (DM), immune-mediated necrotizing myopathy (IMNM), anti-synthetase syndrome (ASyS), and polymyositis (PM).

iii) Presence of at least 1 myositis specific antibody (MSA), associated antibody (MAA), or ANA at screening or prior to screening.

* IIM disease activity:.

i) Severe/moderate muscle AND/OR skin involvement.

ii) Proof of activity as documented by:.

A. An active myositis-associated rash OR.

B. A recent muscle biopsy OR.

C. An elevated CK \> 3 times the upper limit of normal OR.

D. Participants diagnosed IIM AND progressive Interstitial Lung Disease (ILD) on high-resolution computed tomography (HRCT)

iii) Inadequate response to glucocorticoids and at least 2 of the following treatments used for at least 3 months: azathioprine, methotrexate, cyclosporin A, tacrolimus, MMF, cyclophosphamide, IVIG, JAK inhibitors, and rituximab.

* Diagnosis of Systemic Sclerosis (SSc) defined as follows:.

i) Fulfilling 2013 EULAR/ACR classification criteria for SSc.

ii) Antinuclear Antibody (ANA) positive at screening or prior to screening.

\- SSc disease activity:.

i) Participants diagnosed with diffuse cutaneous SSc OR diffuse or limited cutaneous SSc AND progressive ILD, AND.

ii) Inadequate response to at least 1 of the following treatments used for at least 3 months: mycophenolate, cyclophosphamide, rituximab, nintedanib, azathioprine, tocilizumab, or intravenous immunoglobulins (IVIG).

\- Rheumatoid Arthritis (RA) disease activity:.

i) Minimum of 3 SJC and 3 TJC on a 66/68 joint count (SJC/TJC).

ii) OR participants diagnosed with progressive ILD (interstitial lung disease).

iii) AND Inadequate disease response or intolerance to at least one conventional synthetic disease-modifying antirheumatic drug (DMARD) and as well as ≥ 2 DMARDs with different mechanisms of action from the categories biologic disease-modifying antirheumatic drug (bDMARDs) or targeted synthetic disease-modifying anti-rheumatic drug (tsDMARD) for a minimum of 3 months.

A. Participants qualifying on progressive ILD may have exhausted the therapies above OR have demonstrated inadequate disease response or intolerance to at least one of the following treatments used for at least 3 months: mycophenolate, tocilizumab, cyclophosphamide, rituximab, azathioprine, nintedinib, pirfenidone.

Exclusion Criteria

\- Diagnosis of drug-induced SLE rather than idiopathic SLE.

\- Other systemic autoimmune diseases (eg, multiple sclerosis, psoriasis, inflammatory bowel disease, etc) are excluded. Participants with type I autoimmune diabetes mellitus, thyroid autoimmune disease, Celiac disease, or secondary Sjögren's syndrome are not excluded.

* SLE overlap syndromes including, but not limited to, rheumatoid arthritis, scleroderma, and mixed connective tissue disease, are excluded.
* Present or recent clinically significant CNS pathology, within 12 months.
* IIM disease activity:.

i) Other forms of IIM: Inclusion Body Myositis, Amyopathic DM, any form of juvenile myositis.

ii) Myositis other than IIM, eg, drug-induced myositis and PM associated with HIV.

iii) Participants with severe muscle damage (Physician VAS for muscle damage in Myositis Damage Index \> 7 cm on a 10 cm scale), permanent weakness due to a non-IIM cause (eg, stroke), or myositis with cardiac involvement.

\- SSc disease activity:.

i) SSc related PAH requiring active treatment.

ii) Rapidly progressive SSc related lower GI (small and large intestines) involvement (requiring parenteral nutrition); active gastric antral vascular ectasia.

iii) Prior scleroderma renal crisis.

\- RA disease activity:.

i) Prior history of or current inflammatory joint disease other than RA.

ii) Joint damage and/or deformity that may confound the investigator's ability to accurately assess disease activity.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb Services Unlimited Company

UNKNOWN

Sponsor Role collaborator

Juno Therapeutics, Inc., a Bristol-Myers Squibb Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Site Status RECRUITING

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status RECRUITING

Local Institution - 0048

New Haven, Connecticut, United States

Site Status WITHDRAWN

Mayo Clinic in Florida

Jacksonville, Florida, United States

Site Status RECRUITING

University of Miami Hospital and Clinics, Sylvester Cancer Center

Miami, Florida, United States

Site Status RECRUITING

Local Institution - 0053

Chicago, Illinois, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 0030

Baltimore, Maryland, United States

Site Status WITHDRAWN

Local Institution - 0038

Boston, Massachusetts, United States

Site Status NOT_YET_RECRUITING

Local Institution - 0046

Boston, Massachusetts, United States

Site Status WITHDRAWN

University of Massachusetts Chan Medical School

Worcester, Massachusetts, United States

Site Status NOT_YET_RECRUITING

University of Massachusetts Chan Medical School

Worcester, Massachusetts, United States

Site Status RECRUITING

University of Michigan

Ann Arbor, Michigan, United States

Site Status RECRUITING

Henry Ford Medical Center - New Center One

Detroit, Michigan, United States

Site Status RECRUITING

Mayo Clinic in Rochester, Minnesota

Rochester, Minnesota, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Local Institution - 0028

Omaha, Nebraska, United States

Site Status COMPLETED

Atlantic Health System Overlook Medical Center

Summit, New Jersey, United States

Site Status RECRUITING

NYU Langone Health

New York, New York, United States

Site Status RECRUITING

Local Institution - 0054

New York, New York, United States

Site Status WITHDRAWN

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status RECRUITING

Columbia University Irving Medical Center

New York, New York, United States

Site Status RECRUITING

Local Institution - 0055

New York, New York, United States

Site Status WITHDRAWN

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Local Institution - 0027

Columbus, Ohio, United States

Site Status WITHDRAWN

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status RECRUITING

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status RECRUITING

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Swedish Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Local Institution - 0057

Seattle, Washington, United States

Site Status NOT_YET_RECRUITING

Fred Hutchinson Cancer Center

Seattle, Washington, United States

Site Status RECRUITING

UZ Leuven

Leuven, Vlaams-Brabant, Belgium

Site Status RECRUITING

Local Institution - 0043

Strasbourg, Alsace, France

Site Status NOT_YET_RECRUITING

CHU Bordeaux Haut-Leveque

Pessac, Aquitaine, France

Site Status RECRUITING

CHU Montpellier Lapeyronie Hospital

Montpellier, Hérault, France

Site Status RECRUITING

Hopital Claude Huriez - CHU de Lille

Lille, , France

Site Status RECRUITING

Centre Hospitalier Universitaire de Nice - Hôpital l'Archet

Nice, , France

Site Status RECRUITING

Hôpital Saint-Louis

Paris, , France

Site Status RECRUITING

Local Institution - 0052

Paris, , France

Site Status WITHDRAWN

Centre Hospitalier Universitaire de Rennes - Hôpital Pontchaillou

Rennes, , France

Site Status RECRUITING

Universitaetsklinikum Wuerzburg

Würzburg, Bavaria, Germany

Site Status RECRUITING

Universitaetsklinikum Koeln

Cologne, North Rhine-Westphalia, Germany

Site Status RECRUITING

Universitätsklinikum Leipzig

Leipzig, Saxony, Germany

Site Status RECRUITING

Universitaetsklinikum Magdeburg

Magdeburg, Saxony-Anhalt, Germany

Site Status RECRUITING

Charité - Universitaetsmedizin Berlin - Campus Bejnamin Franklin

Berlin, , Germany

Site Status RECRUITING

Universitaetsklinikum Duesseldorf

Düsseldorf, , Germany

Site Status RECRUITING

Universitaetsklinikum Erlangen

Erlangen, , Germany

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Università Cattolica del Sacro Cuore

Rome, Lazio, Italy

Site Status RECRUITING

Humanitas

Rozzano, Milano, Italy

Site Status RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, Barcelona [Barcelona], Spain

Site Status RECRUITING

Hospital Universitario Marqués de Valdecilla

Santander, Cantabria, Spain

Site Status RECRUITING

Hospital Clínic de Barcelona

Barcelona, Catalunya [Cataluña], Spain

Site Status RECRUITING

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status RECRUITING

H.R.U Málaga - Hospital General

Málaga, , Spain

Site Status RECRUITING

Countries

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United States Belgium France Germany Italy Spain

Central Contacts

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BMS Clinical Trials Contact Center www.BMSClinicalTrials.com

Role: CONTACT

855-907-3286

First line of the email MUST contain the NCT# and Site #.

Role: CONTACT

Facility Contacts

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Melissa Griffith, Site 0035

Role: primary

720-848-7700

Richard Nash, Site 0024

Role: primary

303-981-2305

Vikas Majithia, Site 0006

Role: primary

904-953-2000

Lazaros Lekakis, Site 0056

Role: primary

305-748-0641

Site 0038

Role: primary

Jonathan Gerber, Site 0032

Role: primary

508-635-7093

Roberto Caricchio, Site 0033

Role: primary

267-968-7826

Monalisa Ghosh, Site 0031

Role: primary

734-936-4000

Alireza Meysami, Site 0037

Role: primary

313-916-9328

Uma Thanarajasingam, Site 0022

Role: primary

507-422-9855

Alfred Kim, Site 0010

Role: primary

314-326-4785

Neil Kramer, Site 0008

Role: primary

646-734-2774

Amit Saxena, Site 0002

Role: primary

646-501-7387

Margrit Wiesendanger, Site 0011

Role: primary

646-285-7881

Anca Askanase, Site 0007

Role: primary

555-555-5555

Saira Sheikh, Site 0003

Role: primary

919-966-0545

Emily Littlejohn, Site 0005

Role: primary

216-445-5559

Heidi Jacobe, Site 0036

Role: primary

214-648-3348

Maureen Mayes, Site 0029

Role: primary

713-500-6905

Chitra Hosing, Site 0034

Role: primary

713-745-3219

Philip Mease, Site 0004

Role: primary

206-386-2000

Site 0057

Role: primary

Alexandre Hirayama, Site 0058

Role: primary

206-606-1024

Ellen De Langhe, Site 0019

Role: primary

003216342542

Site 0043

Role: primary

Edouard Forcade, Site 0044

Role: primary

+33557656511

Jacques Morel, Site 0015

Role: primary

33467338710

Ibrahim YAKOUB-AGHA, Site 0016

Role: primary

+33320445551

Nihal Martis, Site 0040

Role: primary

+33492035444

Dominique Farge, Site 0018

Role: primary

33 1 42 49 97 64

Roch Houot, Site 0020

Role: primary

33299289873

Marc Schmalzing, Site 0049

Role: primary

+4993120140100

Philipp Koehler, Site 0042

Role: primary

4922147884774

Vladan Vucinic, Site 0041

Role: primary

493419713841

Dimitrios Mougiakakos, Site 0045

Role: primary

49-391-67-21233

David Simon, Site 0025

Role: primary

+49(0)9131-85-43253

Joerg Distler, Site 0047

Role: primary

00492118117817

Georg Schett, Site 0017

Role: primary

004991318539131

MARIA ANTONIETTA D'AGOSTINO, Site 0012

Role: primary

+393495458711

Armando Santoro, Site 0023

Role: primary

390282244080

JOSEFINA CORTES-HERNANDEZ, Site 0014

Role: primary

934894171

Ricardo Blanco, Site 0013

Role: primary

+34 942 20 25 10

Ignasi Rodriguez-Pintó, Site 0021

Role: primary

932275774

ALEJANDRO ESCUDERO, Site 0050

Role: primary

957011631

Antonio Fernandez Nebro, Site 0039

Role: primary

+34951290360

Related Links

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Other Identifiers

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2023-503823-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA061-1001

Identifier Type: -

Identifier Source: org_study_id

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