An Open-Label, Nonrandomized, Multicenter Extension Study to Evaluate the Long-term Safety and Efficacy of Pegcetacoplan in Participants With C3 Glomerulopathy or Immune-Complex Membranoproliferative Glomerulonephritis

NCT ID: NCT05809531

Last Updated: 2025-03-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

100 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-05-29

Study Completion Date

2027-07-31

Brief Summary

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This study is designed as a long-term extension to Study APL2-C3G-310, and is being conducted to establish the long-term safety and efficacy of pegcetacoplan in patients with C3 glomerulopathy (C3G) or immune-complex membranoproliferative glomerulonephritis (IC-MPGN).

Detailed Description

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Conditions

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C3G IC-MPGN C3 Glomerulopathy C3 Glomerulonephritis Complement 3 Glomerulopathy Complement 3 Glomerulopathy (C3G) Complement 3 Glomerulonephritis Dense Deposit Disease DDD Membranoproliferative Glomerulonephritis Membranoproliferative Glomerulonephritis (MPGN) Immune Complex Membranoproliferative Glomerulonephritis (IC-MPGN)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pegcetacoplan administered subcutaneously

Pegcetacoplan administered subcutaneously twice weekly according to protocol defined dosing regimen

Group Type EXPERIMENTAL

Pegcetacoplan

Intervention Type DRUG

Complement (C3) Inhibitor

Interventions

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Pegcetacoplan

Complement (C3) Inhibitor

Intervention Type DRUG

Other Intervention Names

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APL-2

Eligibility Criteria

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Inclusion Criteria

* Completed participation in Study APL2-C3G-310 through the week 52 visit requirements
* Experienced clinical benefit from pegcetacoplan while participating in the previous trial, in the opinion of the investigator
* Must remain on a stable regimen for C3G or IC-MPGN treatment according to the requirements of Study APL2-C3G-310
* Received vaccinations against S pneumoniae, N meningitidis (types A, C, W, Y, and B), and H influenzae (type B) according to the requirements of Study APL2-C3G-310 and agree to receive any additional vaccinations recommended according to ACIP recommendations for adults or children with complement deficiencies and/or immunocompromising conditions or other similar local applicable guidelines
* Female participants of childbearing potential, defined as any woman who has experienced menarche and who is not permanently sterile or postmenopausal, must have a negative urine pregnancy test at visit 1 and must agree to use protocol-defined methods of contraception for the duration of the study through at least 90 days after receiving the last dose of pegcetacoplan
* Male participants must agree to use protocol-defined methods of contraception and agree to refrain from donating semen for the duration of the study through at least 90 days after receiving the last dose of pegcetacoplan
* Participants above the legal age of consent, in accordance with local regulations, must be willing and able to provide informed consent. The legally authorized representative of participants under the legal age of consent must be willing and able to provide informed consent; where appropriate, participants under the legal age of consent must also give their assent to participation in the study
* Willing and able to self-administer pegcetacoplan or have an identified caregiver who can perform the administration

Exclusion Criteria

* Female participants who are or are planning to become pregnant or who are currently breastfeeding and are unwilling to discontinue for the duration of the study and for at least 90 days after the final dose of study drug
* Inability or unwillingness to cooperate with the requirements of the protocol
* Any condition that, in the opinion of the investigator, creates an undue risk for the participant by participating in the study or is likely to confound interpretation of the study results
* Evidence of ongoing drug or alcohol abuse or dependence, in the opinion of the investigator
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Apellis Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Academic Medical Research Institute (01034)

Los Angeles, California, United States

Site Status

Children's Hospital Colorado (01037)

Aurora, Colorado, United States

Site Status

University of Florida, Department of Pediatric Nephrology (01010)

Gainesville, Florida, United States

Site Status

Emory Investigational Drug Service (01021)

Atlanta, Georgia, United States

Site Status

University of Iowa Hospital and Clinics (01030)

Iowa City, Iowa, United States

Site Status

University of Michigan Hospital (01008)

Ann Arbor, Michigan, United States

Site Status

Hackensack Meridian Health (01036)

Hackensack, New Jersey, United States

Site Status

Cohen Children Hospital, Pediatric Pharmacy (01022)

Hyde Park, New York, United States

Site Status

Columbia Nephrology (01039)

New York, New York, United States

Site Status

Oregon Health & Science Univ., Dept. Pediatrics (01038)

Portland, Oregon, United States

Site Status

Northeast Clinical Research Center LLC (01009)

Bethlehem, Pennsylvania, United States

Site Status

Texas Children's Hospital (01027)

Houston, Texas, United States

Site Status

Hospital Privado-Universitario de Cordoba (54004)

Córdoba, , Argentina

Site Status

Clinica Privada Velez Sarsfield (54007)

Córdoba, , Argentina

Site Status

Kidney Trials Unit, Princess Alexandra Hospital (61007)

Woolloongab, Queensland, Australia

Site Status

St. Vincent's Hospital Melbourne (61003)

Fitzroy, , Australia

Site Status

Catholic University of Leuven (32001)

Leuven, , Belgium

Site Status

Santa Casa de Misericordia de Belo Horizonte (55017)

Belo Horizonte, Minas Gerais, Brazil

Site Status

Irmandade da Santa Casa Misericordia Porto Alegre (55016)

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

HC UNESP Botucatu (55010)

Botucatu, , Brazil

Site Status

Hospital de Clinicas de Porto Alegre (55018)

Porto Alegre, , Brazil

Site Status

Real Hospital Portugues de Beneficencia (55015)

Recife, , Brazil

Site Status

Ruschel Medicina E Pesquisa Clinica (55012)

Rio de Janeiro, , Brazil

Site Status

Hospital De Base (55014)

São José do Rio Preto, , Brazil

Site Status

Hospital do Rim - Fundacao Oswaldo Ramos (55005)

São Paulo, , Brazil

Site Status

Univ Sao Paulo, Av. Dr Eneas Carvalho de Aguiar, 155 (55007)

São Paulo, , Brazil

Site Status

Institute for Clinical and Experimental Medicine (42001)

Prague, , Czechia

Site Status

CHU de Bordeaux - Hopital Pellegrin (33010)

Bordeaux, , France

Site Status

Institut de transplantation urologie-nephrologie (33011)

Nantes, , France

Site Status

Schneider Childrens Medical Center (97204)

Petah Tikva, , Israel

Site Status

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (39004)

Milan, , Italy

Site Status

Istituto di Ricerche Farmacologiche Mario Negri IRCCS (39003)

Ranica, , Italy

Site Status

Ospesale Pediatrico bambino Gesu (39005)

Rome, , Italy

Site Status

Nagasaki University Hospital (81005)

Nagasaki, Nagasaki, Japan

Site Status

Seirei Hamamatsu General Hospital (81004)

Hamamatsu, Shizuoka, Japan

Site Status

AMC Apotheek Goederenontvangst (31002)

Amsterdam, , Netherlands

Site Status

University Medical Center Groningen (31004)

Groningen de Brug, , Netherlands

Site Status

Radboud University Medical Center (31003)

Nijmegen, , Netherlands

Site Status

Yonsei University College of Medicine, Sinchon Severance Hospital (82002)

Seoul, , South Korea

Site Status

Seoul National University Hospital (82003 & 82005)

Soeul, , South Korea

Site Status

Hosp. Universit. Materno-Infantil Vall d' Hebron (34006)

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre (34008)

Madrid, , Spain

Site Status

Hospital Universitario Dr Peset (34009)

Valencia, , Spain

Site Status

CHUV Lausanne (41002)

Lausanne, , Switzerland

Site Status

Imperial College Hammersmith Hospital (44013)

London, , United Kingdom

Site Status

Royal Manchester Children's Hospital (44011)

Manchester, , United Kingdom

Site Status

Nottingham University Hospitals NHS Trust (44012)

Nottingham, , United Kingdom

Site Status

Countries

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United States Argentina Australia Belgium Brazil Czechia France Israel Italy Japan Netherlands South Korea Spain Switzerland United Kingdom

Other Identifiers

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2023-504625-39-00

Identifier Type: OTHER

Identifier Source: secondary_id

U1111-1290-7826

Identifier Type: OTHER

Identifier Source: secondary_id

2022-002833-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

APL2-C3G-314

Identifier Type: -

Identifier Source: org_study_id

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