Dynamics of the Anti-factor VIII Antibody Signature During Treatment With Emicizumab

NCT ID: NCT05802836

Last Updated: 2023-07-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

100 participants

Study Classification

OBSERVATIONAL

Study Start Date

2023-04-26

Study Completion Date

2029-12-31

Brief Summary

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The goal of this observational study is to learn about the changes of antibodies and inhibitors against the coagulation factor VIII in patients with severe hemophilia A receiving emicizumab therapy. No additional visits or procedures are planned. Patients in this study will continue to receive their routine care and analysis will be done from left over samples from routine visits.

Detailed Description

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Conditions

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Severe Hemophilia A Severe Hemophilia A With Inhibitor Severe Hemophilia A Without Inhibitor

Study Design

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Observational Model Type

OTHER

Study Time Perspective

OTHER

Study Groups

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Inhibitor negative, FVIII on demand or regularly

Patients with severe hemophilia A receiving emicizumab therapy which are negative for factor VIII Inhibitor (including patients post ITI) and are receiving factor VIII therapy either on demand or regularly,

no interventions

Intervention Type OTHER

no intervention, only 3 different patients groups

Inhibitor positive, FVIII therapy regularly (ITI)

Patients with severe hemophilia A receiving emicizumab therapy which are positive for factor VIII Inhibitor and are receiving regularly factor VIII therapy (ITI)

no interventions

Intervention Type OTHER

no intervention, only 3 different patients groups

Inhibitor positive, no FVIII therapy

Patients with severe hemophilia A receiving emicizumab therapy which are positive for factor VIII Inhibitor and are receiving no factor VIII therapy

no interventions

Intervention Type OTHER

no intervention, only 3 different patients groups

Interventions

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no interventions

no intervention, only 3 different patients groups

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Severe congenital hemophilia A (CHA)
* Treatment with emicizumab irrespective of any other treatment
* Informed consent

Exclusion Criteria

* No therapy with emicizumab
* Immunosuppressive therapy
* HIV-infection with CD4 (cluster of differentiation 4) cells \<200/µl
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Roche Pharma AG

INDUSTRY

Sponsor Role collaborator

Chugai Pharma Germany GmbH

UNKNOWN

Sponsor Role collaborator

Christoph Königs

OTHER

Sponsor Role lead

Responsible Party

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Christoph Königs

Principal Investigator, Head of molecular and clinical Haemostasis

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Christoph Koenigs, PD Dr. Dr

Role: PRINCIPAL_INVESTIGATOR

Goethe University

Locations

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University Hospital Frankfurt, Goethe University

Frankfurt am Main, Hesse, Germany

Site Status RECRUITING

Countries

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Germany

Central Contacts

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Stephan Schultze-Strasser, Dr.

Role: CONTACT

+496963016998

Christoph Koenigs, PD Dr. Dr

Role: CONTACT

+4969630183030

Facility Contacts

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Stephan Schultze-Strasser, Dr.

Role: primary

00496963016998

Christoph Koenigs, PD Dr. Dr.

Role: backup

004969630183030

Other Identifiers

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DRKS00031196

Identifier Type: REGISTRY

Identifier Source: secondary_id

ML44394

Identifier Type: -

Identifier Source: org_study_id

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