DETERMINE Trial Treatment Arm 01: Alectinib in Adult, Paediatric and Teenage/Young Adult Patients With ALK Positive Cancers

NCT ID: NCT05770037

Last Updated: 2025-11-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

30 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-18

Study Completion Date

2029-10-31

Brief Summary

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This clinical trial is looking at a drug called alectinib. Alectinib is approved as standard of care treatment for adult patients with certain types of lung cancer. This means it has gone through clinical trials and been approved by the Medicines and Healthcare products Regulatory Agency (MHRA) in the UK. Alectinib works in lung cancer patients with a particular mutation in their cancer known as ALK.

Investigators now wish to find out if it will be useful in treating patients with other cancer types which have the same mutation. If the results are positive, the study team will work with the NHS and the Cancer Drugs Fund to see if these drugs can be routinely accessed for patients in the future.

This trial is part of a trial programme called DETERMINE. The programme will also look at other anti-cancer drugs in the same way, through matching the drug to rare cancer types or ones with specific mutations.

Detailed Description

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DETERMINE Treatment Arm 01 (alectinib) aims to evaluate the efficacy of alectinib in ALK-positive rare\* adult, paediatric and teenage/young adult (TYA) cancers and in common cancers where an ALK mutation or amplification is considered to be infrequent.

\*Rare is defined generally as incidence less than 6 cases in 100,000 patients (includes paediatric and teenagers/young adult cancers) or common cancers with rare alterations.

This treatment arm has a target sample size of 30 evaluable patients. Sub-cohorts may be defined and further expanded to a target of 30 evaluable patients each.

The ultimate aim is to translate positive clinical findings to the NHS (Cancer Drugs Fund) to provide new treatment options for rare adult, paediatric and TYA cancers.

OUTLINE:

Pre-screening: The Molecular Tumour Board makes a treatment recommendation for the patient based on molecularly-defined cohorts (See information on Master Screening Protocol below).

Screening: Consenting patients undergo biopsy and collection of blood samples for research purposes.

Treatment: Patients will receive alectinib until disease progression without clinical benefit, unacceptable adverse events (AEs) or withdrawal of consent. Patients will also undergo collection of blood samples at various intervals while receiving treatment and at EoT.

After completion of study treatment, patients are followed up every 3 months for 2 years.

THE DETERMINE TRIAL MASTER (SCREENING) PROTOCOL:

Please see DETERMINE Trial Master (Screening) Protocol record (NCT05722886) for information on the DETERMINE Trial Master Protocol and applicable documents.

Conditions

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Haematological Malignancy Malignant Neoplasm Lymphoproliferative Disorders Neoplasms by Histologic Type Neoplasms by Site Cancer Anaplastic Large Cell Lymphoma Lymphoma Renal Cell Carcinoma Neuroblastoma Solid Tumour

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Treatment Arm 01: Alectinib

This alectinib treatment arm is for adult, paediatric and teenage/young adult (TYA) patients with ALK-positive cancers.

Group Type EXPERIMENTAL

Alectinib

Intervention Type DRUG

Adult patients will be administered alectinib orally at a dose of 600 mg (four 150 mg capsules) twice daily.

Paediatric patients with a body weight ≥40 kg and who are able to swallow the capsules, will be administered alectinib orally at a dose of 600 mg (four 150 mg capsules) twice daily.

Each cycle of treatment will consist of 28 days and patients may continue on treatment until disease progression without clinical benefit, unacceptable AEs or withdrawal of consent.

Interventions

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Alectinib

Adult patients will be administered alectinib orally at a dose of 600 mg (four 150 mg capsules) twice daily.

Paediatric patients with a body weight ≥40 kg and who are able to swallow the capsules, will be administered alectinib orally at a dose of 600 mg (four 150 mg capsules) twice daily.

Each cycle of treatment will consist of 28 days and patients may continue on treatment until disease progression without clinical benefit, unacceptable AEs or withdrawal of consent.

Intervention Type DRUG

Other Intervention Names

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Alecensa

Eligibility Criteria

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Inclusion Criteria

A. Confirmed diagnosis of an ALK-positive malignancy using an analytically validated next-generation sequencing method.

B. Women of childbearing potential are eligible, provided that they meet the following criteria:

* Have a negative serum or urine pregnancy test before enrolment and;
* Agree to use one form of highly effective birth control method such as:

I. combined (oestrogen and progestogen containing) hormonal contraception associated with inhibition of ovulation \[oral, intravaginal or transdermal\]

II. progestogen-only hormonal contraception associated with inhibition of ovulation (oral, injectable or implantable)

III. intrauterine device (IUD)

IV. intrauterine hormone-releasing system (IUS)

V. bilateral tubal occlusion

VI. vasectomised partner

VII. sexual abstinence

Effective from the first administration of alectinib, throughout the trial and for three months after the last administration of alectinib.

C. Male patients with partners who are women of childbearing potential are eligible provided that they agree to the following, from first administration of alectinib, throughout the trial and for three months after the last administration of alectinib:

* Agree to take measures not to father children by using a barrier method of contraception (condom plus spermicide) or sexual abstinence.
* Non-vasectomised male patients with partners who are women of childbearing potential must also be willing to ensure that their partner uses a highly effective method of contraception, as in criterion B, above.
* Male patients with pregnant or lactating partners must be advised to use barrier method contraception (e.g. condom) to prevent drug exposure of the foetus or neonate.

All male patients must refrain from donating sperm for the same period.

D. Patients must be able and willing to undergo a fresh tissue biopsy. Note that for patients with haematological malignancies or neuroblastomas, blood, bone marrow aspiration and/or trephine or lymph node biopsy samples may be taken.

E. Paediatric patients (patients aged \<18 years) must have a body weight ≥40kg.

F. ADULT PATIENTS (≥18 years): Adequate organ function as per haematological and biochemical indices within the ranges defined in the protocol. These measurements should be performed to confirm the patient's eligibility.

G. PAEDIATRIC PATIENTS (\<18 years): Adequate organ function as per haematological and biochemical indices within the ranges shown below. These measurements should be performed to confirm the patient's eligibility.

Exclusion Criteria

A. Diagnosis of ALK-positive non-small cell lung cancer.

B. Female patients who are pregnant, breastfeeding or planning to become pregnant during the trial or for three months following their last dose of alectinib.

C. Prior treatment with the same class of drug unless genetic profile demonstrates a mechanism of resistance known to be potentially sensitive to alectinib. Patients who have previously received crizotinib (Xalkori\^\[®\]) and did not respond, or who responded inadequately or responded adequately and subsequently progressed, are allowed into the trial.

D. History of or radiological evidence of interstitial lung disease and/or pneumonitis. Prior localised radiotherapy related pneumonitis is permitted if resolved and off steroids and asymptomatic for \>6 months.

E. Patients at risk of gastrointestinal (GI) perforation e.g. history of diverticulitis, concomitant use of medicinal product with a recognized risk of GI perforation (unless patient has also been co-prescribed gastric protection).

• Patients who present with a GI primary tumour or metastases to the GI tract may be considered.

F. Patient unable to swallow or tolerate oral medication or any GI disorder that may affect absorption of oral medications, such as malabsorption syndrome or following major bowel resection. Paediatric patients will be excluded if they are unable to swallow the capsules, as per the dosing schedule (150 mg dose strength).

G. Patients with clinically significant pre-existing cardiac conditions, including uncontrolled or symptomatic angina, uncontrolled atrial or ventricular arrhythmias (within three months), or New York Heart Association (NYHA) class III or IV congestive heart failure.

Patients with a cerebrovascular event (including stroke or transient ischaemic attack \[TIA\]), or cardiovascular event (including acute myocardial infarction \[MI\]), within three months before the first dose of alectinib.

• Patients with primary CNS tumours may be considered unless intra-tumoural bleeding has occurred within 2 weeks of the first dose of alectinib, and patients with punctate CNS haemorrhages \<3 mm may be considered.

H. History of organ transplantation.

I. Symptomatic bradycardia for age.

J. Known hypersensitivity to alectinib or any of the excipients. See the current alectinib (Alecensa® 150 mg hard capsules) SmPC for the full list.

K. Patients who were administered a live, attenuated vaccine within 28 days prior to enrolment, or anticipation of need for such a vaccine during alectinib treatment or within six months after the final dose of alectinib.

L. Active hepatitis B or C virus or known human immunodeficiency virus (HIV) positivity or acquired immune deficiency syndrome (AIDS) related illness. Patients with history of testing positive for HIV infection are eligible provided the each of the following conditions are met:

* CD4 count ≥350/μL;
* undetectable viral load;
* receiving antiretroviral therapy (ART) that does not interact with IMP (patients should be on established ART for at least four weeks); and
* no HIV/AIDS-associated opportunistic infection in the last 12 months.

M. Familial or personal history of congenital bone disorders, bone metabolism alterations or known osteopenia in the patient.

N. Any clinically significant concomitant disease or condition (or its treatment) that could interfere with the conduct of the trial or absorption of oral medications or that would, in the opinion of the Investigator, pose an unacceptable risk to the patient in this trial.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Manchester

OTHER

Sponsor Role collaborator

University of Birmingham

OTHER

Sponsor Role collaborator

Royal Marsden NHS Foundation Trust

OTHER

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role collaborator

Cancer Research UK

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Matthew Krebs, Dr

Role: PRINCIPAL_INVESTIGATOR

The Christie Hospital

Locations

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Belfast City Hospital

Belfast, , United Kingdom

Site Status RECRUITING

University Hospital Birmingham

Birmingham, , United Kingdom

Site Status RECRUITING

Birmingham Children's Hospital

Birmingham, , United Kingdom

Site Status NOT_YET_RECRUITING

Bristol Royal Hospital for Children

Bristol, , United Kingdom

Site Status RECRUITING

Bristol Haematology and Oncology Centre

Bristol, , United Kingdom

Site Status RECRUITING

Addenbrooke's Hospital

Cambridge, , United Kingdom

Site Status RECRUITING

Velindre Cancer Centre

Cardiff, , United Kingdom

Site Status RECRUITING

Cardiff Children's Hospital

Cardiff, , United Kingdom

Site Status NOT_YET_RECRUITING

Western General Hospital

Edinburgh, , United Kingdom

Site Status RECRUITING

The Beatson Hospital

Glasgow, , United Kingdom

Site Status RECRUITING

Royal Hospital for Children Glasgow

Glasgow, , United Kingdom

Site Status RECRUITING

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status RECRUITING

Alder Hey Hospital

Liverpool, , United Kingdom

Site Status RECRUITING

University College London Hospital

London, , United Kingdom

Site Status RECRUITING

Guy's Hospital

London, , United Kingdom

Site Status RECRUITING

Great Ormond Street Hospital

London, , United Kingdom

Site Status RECRUITING

Royal Manchester Children's Hospital

Manchester, , United Kingdom

Site Status NOT_YET_RECRUITING

The Christie Hospital

Manchester, , United Kingdom

Site Status RECRUITING

Clatterbridge Cancer Centre

Metropolitan Borough of Wirral, , United Kingdom

Site Status RECRUITING

Great North Children's Hospital

Newcastle, , United Kingdom

Site Status RECRUITING

Freeman Hospital

Newcastle, , United Kingdom

Site Status RECRUITING

Churchill Hospital

Oxford, , United Kingdom

Site Status RECRUITING

John Radcliffe Hospital

Oxford, , United Kingdom

Site Status RECRUITING

Weston Park Hospital

Sheffield, , United Kingdom

Site Status RECRUITING

Sheffield's Children's Hospital

Sheffield, , United Kingdom

Site Status RECRUITING

Southampton General Hospital

Southampton, , United Kingdom

Site Status RECRUITING

The Royal Marsden Hospital

Sutton, , United Kingdom

Site Status RECRUITING

Countries

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United Kingdom

Central Contacts

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Aida Sarmiento Castro

Role: CONTACT

+44 207 242 0200

Facility Contacts

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Vicky Coyle, Prof

Role: primary

Gary Middleton, Prof

Role: primary

0121 371 3573

Gerard Millen, Dr

Role: primary

07921843607

Antony Ng, Dr

Role: primary

0117 342 8044

Antony Ng, Dr

Role: primary

0117 342 8044

Bristi Basu, Dr

Role: primary

01223 596105

Robert Jones, Dr

Role: primary

02920 615888 ext. 6327

Madeline Adams, Dr

Role: primary

02921842285

Stefan Symeonides, Dr

Role: primary

Patricia Roxburgh, Dr

Role: primary

0141 301 7118

Milind Ronghe, Dr

Role: primary

0141 452 6692

Olubukola Ayodele, Dr

Role: primary

0116 2587601

Lisa Howell, Dr

Role: primary

0151 293 3679

Martin Forster, Prof

Role: primary

020 3447 5085

James Spicer, Dr

Role: primary

020 7188 4260

Darren Hargrave, Dr

Role: primary

0207 813 8525

Guy Makin, Dr

Role: primary

0161 701 8419

Matthew Krebs, Dr

Role: primary

01619187672

Dan Palmer, Dr

Role: primary

0151 706 4172 / 0151 706 4177

Alastair Greystoke, Dr

Role: primary

0191 2138476

Alastair Greystoke, Dr

Role: primary

0191 2138476

Sarah Pratap, Dr

Role: primary

01865 235273

Sarah Pratap, Dr

Role: primary

01865 235273

Sarah Danson, Dr

Role: primary

0114 226 5068

Daniel Yeomanson, Dr

Role: primary

01142717366

Juliet Gray, Prof

Role: primary

0238 120 6639

Lynley Marshall, Dr

Role: primary

0208 661 3678

Related Links

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http://CRUK.org/determine

Overview of the DETERMINE trial

https://clinicaltrials.gov/ct2/show/NCT05722886

ClinicalTrials.gov record for DETERMINE Trial Master Screening Protocol (NCT05722886).

Other Identifiers

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IRAS ID: 1004057

Identifier Type: OTHER

Identifier Source: secondary_id

CRUKD/21/004 - Treatment Arm 1

Identifier Type: -

Identifier Source: org_study_id

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