Patiromer for Treatment of Hyperkalaemia in Children Under 12 Years of Age

NCT ID: NCT05766839

Last Updated: 2025-10-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

32 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-04-06

Study Completion Date

2030-12-31

Brief Summary

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A study to evaluate the pharmacodynamic effects, safety, and tolerability of patiromer in children under 12 years of age with hyperkalaemia.

Detailed Description

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Conditions

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Hyperkalemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Patiromer

4-week pharmacodynamic /dose-ranging period

Cohort 1: 6 to less than (\<)12 years of age

Cohort 2: 2 to \<6 years of age

Cohort 3: 0 to \<2 years of age; In Cohort 3, a minimum of 3 study participants will be assessed in the subgroup of 0 to \<6 months and another 3 study participants in the subgroup 6 to \<24 months of age.

Group Type EXPERIMENTAL

Patiromer

Intervention Type DRUG

Patiromer will be given once daily; In Cohort 3, depending on the dose and the study participant's age, the total daily dose might be split

Interventions

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Patiromer

Patiromer will be given once daily; In Cohort 3, depending on the dose and the study participant's age, the total daily dose might be split

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Paediatric participants (\<12 years of age) with hyperkalaemia at screening.
* Participant's age should not reach 12 years during the 28 days of the pharmacodynamic/dose-ranging period.
* Participant is able to receive regular external feeding and medication, including via tubes, i.e., percutaneous endoscopic gastrostomy (PEG) or entero-gastric feeding tube.
* At screening/baseline, the results from 2 separate and consecutive potassium assessments using the same measurement method (whole blood, plasma, or serum) need to be above the age-appropriate upper limit of normal (ULN).
* If taking any renin-angiotensin aldosterone system inhibitors (RAASi), beta blockers, fludrocortisone, or diuretic medications, must be on a stable dose for at least 14 days prior to screening.
* Parent(s) or legally authorised representative(s) or another appropriate person delegated by the legally authorised representatives must be available to help the study-site personnel ensure follow-up; accompany the participant to the study site on each assessment day; accurately and reliably dispense investigational product as directed.
* Females of childbearing potential must be non-lactating, must have a negative pregnancy test at screening, and must have used an effective, acceptable form of contraception (e.g., abstinence) for at least 1 month before patiromer administration. Females of childbearing potential must agree to continue using contraception throughout the study and for 1 month after the last dose of patiromer.
* If undergoing peritoneal dialysis, participants must be on a stable treatment plan for a minimum of 4 weeks prior to screening, or at least 8 weeks prior to screening if newly initiated on peritoneal dialysis.

Exclusion Criteria

The following criteria exclude a participant from participating in this trial:

* Preterm birth infants with \<37 weeks of gestation cannot be included in Cohort 3.
* Participants who due to their general condition, e.g., anaemia or low body weight, are not suitable to have blood volume withdrawn.
* Any of the following renal conditions: maintenance haemodialysis, renal artery stenosis, and acute kidney injury (defined by 2012 Kidney Disease Improving Global Outcomes) or a history of acute renal insufficiency in the past 3 months. Note: Chronic kidney disease (CKD) is not excluded.
* A history of or current diagnosis of a severe gastrointestinal (GI) diagnosis or surgery that could affect GI transit of the drug (delayed gastric emptying), such as a severe swallowing disorder, severe gastroesophageal reflux, uncorrected pyloric stenosis, intussusception, any other intestinal obstruction (e.g., Hirschsprung disease, chronic intestinal pseudo-obstruction, clinically significant postsurgical abdominal adhesions) or any gut-shortening surgical procedure prior to screening. Pre-gastric above-mentioned pathologies may be disregarded in case of existence of a PEG or entero-gastric feeding tube, as the PEG or entero-gastric feeding tube will serve for nutrition and investigational product administration.
* Active cancer, currently on cancer treatment, or history of cancer in the past 2 years (except for non-melanoma skin cancer).
* Scheduled for kidney transplant procedure during the first 28 days after Day 1.
* History of sudden infant death in a sibling (only for participants \<2 years of age at screening).
* Use of the following medications if doses have not been stable for at least 14 days prior to screening or if doses are anticipated to change during the 4-week pharmacodynamic/ dose-ranging period: digoxin, bronchodilators, theophylline, heparins (including low molecular heparins), tacrolimus, mycophenolate mofetil, cyclosporine, trimethoprim, or cotrimoxazole.
* Use of any investigational product for an unapproved indication within 30 days prior to screening or within 5 half-lives, whichever is longer.
* Known hypersensitivity to patiromer or its components.
* If the child is being breastfed:

1. There is suspicion of current alcohol or substance misuse/abuse in breastfeeding mother
2. The breastfeeding mother is taking potassium supplements
Maximum Eligible Age

11 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Vifor Pharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Julian Platon, MD, PhD

Role: STUDY_DIRECTOR

Vifor Pharma, Inc.

Locations

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Children's Hospital Colorado Site 84014

Aurora, Colorado, United States

Site Status NOT_YET_RECRUITING

UF Health Pediatric Multispecialty Center Site 84006

Jacksonville, Florida, United States

Site Status RECRUITING

Miller School of Medicine, University of Miami Site 84003

Miami, Florida, United States

Site Status RECRUITING

Arnold Palmer Hospital for Children Site 84010

Orlando, Florida, United States

Site Status NOT_YET_RECRUITING

Augusta University - Children's Hospital of Georgia Site 84015

Augusta, Georgia, United States

Site Status NOT_YET_RECRUITING

University of Illinois College of Medicine Site 84012

Peoria, Illinois, United States

Site Status RECRUITING

Boston Children's Hospital Site 84008

Boston, Massachusetts, United States

Site Status NOT_YET_RECRUITING

Children's Mercy Hospitals and Clinics Site 84004

Kansas City, Missouri, United States

Site Status RECRUITING

Duke University Hospital & Medical Center Site 84002

Durham, North Carolina, United States

Site Status RECRUITING

Duke University Hospital Site 84002

Durham, North Carolina, United States

Site Status RECRUITING

The Children's Hospital of Philadelphia Site 84007

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Vanderbilt Children's Hospital Neurology Site 84013

Nashville, Tennessee, United States

Site Status NOT_YET_RECRUITING

Texas Tech University Health Sciences Center Amarillo Site 84009

Amarillo, Texas, United States

Site Status NOT_YET_RECRUITING

The Royal Children's Hospital (RCH) Site 03601

Parkville, , Australia

Site Status RECRUITING

Children's Hospital Westmead Centre for Kidney Research Site 03602

Westmead, , Australia

Site Status NOT_YET_RECRUITING

Universitair Ziekenhuis Gent Site 05601

Ghent, , Belgium

Site Status RECRUITING

UZ Leuven Site 05602

Leuven, , Belgium

Site Status NOT_YET_RECRUITING

Helsingin Yliopistollinen Keskussairaala Uusi Lastensairaala Site 24601

Helsinki, , Finland

Site Status NOT_YET_RECRUITING

CHRU Montpellier - Arnaud de Villeneuve Site 25001

Montpellier, , France

Site Status RECRUITING

Assistance Publique-Hopitaux de Paris Robert-Debre Site 25003

Paris, , France

Site Status RECRUITING

Hôpital des Enfants - Toulouse Site 25002

Toulouse, , France

Site Status RECRUITING

Ippokratio Thessaloniki General Hospital Site 30002

Thessaloniki, Thessaloniki, Greece

Site Status RECRUITING

Pan and Aglaia Kyriakou Children's Hospital Site 30001

Athens, , Greece

Site Status RECRUITING

Shaare Zedek Medical Center Site 37602

Jerusalem, , Israel

Site Status RECRUITING

Schneider Children's Medical Center of Israel Site 37601

Petach Tikvah, , Israel

Site Status RECRUITING

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico Site 38002

Milan, , Italy

Site Status NOT_YET_RECRUITING

IRCCS Ospedale Pediatrico Bambino Gesù Site 38001

Rome, , Italy

Site Status NOT_YET_RECRUITING

Helse Bergen HF Haukeland Universitetssjukehus Site 57801

Bergen, , Norway

Site Status NOT_YET_RECRUITING

Uniwersytecki Szpital Kliniczny we Wrocławiu Site 61601

Wroclaw, , Poland

Site Status NOT_YET_RECRUITING

Unidade Local de Saude de Santo Antonio, E.P.E. Site 62001

Porto, , Portugal

Site Status NOT_YET_RECRUITING

Sidra Medicine Site 63401

Doha, , Qatar

Site Status NOT_YET_RECRUITING

Spitalul Clinic de Urgenta pentru Copii Louis Turcanu Timisoara Site 64201

Timișoara, , Romania

Site Status RECRUITING

King Saud University Site 68202

Riyadh, , Saudi Arabia

Site Status NOT_YET_RECRUITING

King Faisal Specialist Hospital & Research Centre Site 68201

Riyadh, , Saudi Arabia

Site Status NOT_YET_RECRUITING

King Abdulaziz Medical City Site 68203

Riyadh, , Saudi Arabia

Site Status NOT_YET_RECRUITING

Al Jalila Children's Hospital Site 78401

Dubai, , United Arab Emirates

Site Status NOT_YET_RECRUITING

Countries

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United States Australia Belgium Finland France Greece Israel Italy Norway Poland Portugal Qatar Romania Saudi Arabia United Arab Emirates

Central Contacts

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EMERALD-2 Clinical Study Team

Role: CONTACT

+41 58 851 80 00

Facility Contacts

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Central Contract

Role: primary

Central Contact

Role: primary

Central Contact

Role: primary

Central Contract

Role: primary

Central Contact

Role: primary

Other Identifiers

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2023-505252-21-00

Identifier Type: OTHER

Identifier Source: secondary_id

RLY5016-208p

Identifier Type: -

Identifier Source: org_study_id

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