Efficacy and Safety of Inclisiran as Monotherapy in Patients With Primary Hypercholesterolemia Not Receiving Lipid-lowering Therapy.

NCT ID: NCT05763875

Last Updated: 2025-10-16

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

350 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-15

Study Completion Date

2024-06-20

Brief Summary

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CKJX839D12304 was a research study to determine if the study treatment, called inclisiran, in comparison to placebo and ezetimibe effectively reduces Low-Density Lipoprotein Cholesterol (LDL-C) as measured by percentage change from baseline to Day 150. This study was conducted in eligible participants with primary hypercholesterolemia not receiving any lipid-lowering therapy (LLT), with a 10-year Atherosclerotic Cardiovascular Disease (ASCVD) risk of less than 7.5%.

Detailed Description

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This study was a randomized, double-blind, placebo- and active comparator-controlled, multicenter study in 350 adult participants with primary hypercholesterolemia not receiving any LLT with a 10-year ASCVD risk score of less than 7.5%. This study evaluated the efficacy and safety of inclisiran sodium 300 mg, administered as a monotherapy in comparison to ezetimibe and placebo.

The study consisted of:

* a screening period of up to 14 days;
* a double-blind treatment period of 150+/- 5 days during which participants were randomly assigned to either the inclisiran arm, the ezetimibe arm or the placebo arm in a 2:1:1 ratio; and
* a safety follow-up / End of Study visit conducted 30+5 days after the Day 150 visit.

The overall study duration was approximately 190 days.

Conditions

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Hypercholesterolemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Multi-center, randomized, double-blind, placebo- and active comparator-controlled, parallel groups
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Sponsor Personnel participating in the study conduct were also be blinded.

Study Groups

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Inclisiran

Inclisiran s.c and Placebo p.o

Group Type EXPERIMENTAL

Inclisiran

Intervention Type DRUG

284 mg (equivalent to 300 mg inclisiran sodium) subcutaneous injection given on Day 1 and Day 90

Matching Placebo for Ezetimibe

Intervention Type DRUG

0mg over-encapsulated placebo tablet taken once a day from Day 1 through Day 149

Ezetimibe

Placebo s.c. and Ezetimibe p.o.

Group Type ACTIVE_COMPARATOR

Ezetimibe

Intervention Type DRUG

10 mg over-encapsulated tablet taken once a day from Day 1 through Day 149

Matching Placebo for Inclisiran

Intervention Type DRUG

0mg placebo injection solution for subcutaneous injection on Day 1 and Day 90

Placebo

Placebo s.c. and Placebo p.o.

Group Type PLACEBO_COMPARATOR

Matching Placebo for Inclisiran

Intervention Type DRUG

0mg placebo injection solution for subcutaneous injection on Day 1 and Day 90

Matching Placebo for Ezetimibe

Intervention Type DRUG

0mg over-encapsulated placebo tablet taken once a day from Day 1 through Day 149

Interventions

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Inclisiran

284 mg (equivalent to 300 mg inclisiran sodium) subcutaneous injection given on Day 1 and Day 90

Intervention Type DRUG

Ezetimibe

10 mg over-encapsulated tablet taken once a day from Day 1 through Day 149

Intervention Type DRUG

Matching Placebo for Inclisiran

0mg placebo injection solution for subcutaneous injection on Day 1 and Day 90

Intervention Type DRUG

Matching Placebo for Ezetimibe

0mg over-encapsulated placebo tablet taken once a day from Day 1 through Day 149

Intervention Type DRUG

Other Intervention Names

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KJX839 Sandoz ezetimibe Placebo s.c. Placebo p.o.

Eligibility Criteria

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Inclusion Criteria

* informed consent signed prior to participation in study
* fasting LDL-C of \>= 100 mg/dL but \< 190 mg/dL
* fasting triglycerides \<= 400 mg/dL
* 10-year ASCVD risk score \< 7.5%
* not on any lipid-lowering therapy within 90 days of screening

Exclusion Criteria

* history of ASCVD
* diabetes mellitus or fasting plasma glucose of \>= 7.0 mmol/L or HbA1c \>= 6.5%
* secondary hypercholesterolemia, e.g. hypothyroidism (TSH above upper limit of normal)
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Parkway Medical Center

Birmingham, Alabama, United States

Site Status

SEC Clinical Research

Dothan, Alabama, United States

Site Status

Hillcrest Medical Research

DeLand, Florida, United States

Site Status

ClinCloud

Maitland, Florida, United States

Site Status

Alma Clinical Research Inc

Miami, Florida, United States

Site Status

Inpatient Research Clinical LLC

Miami Lakes, Florida, United States

Site Status

Harmony Clinical Research

North Miami Beach, Florida, United States

Site Status

Fam Medical Specialists Of Fl Plc

Plant City, Florida, United States

Site Status

Cozy Research LLC

Zephyrhills, Florida, United States

Site Status

Koch Family Medicine

Morton, Illinois, United States

Site Status

Grace Research LLC

Bossier City, Louisiana, United States

Site Status

Grace Research Llc

Shreveport, Louisiana, United States

Site Status

Southern Clin Research Clinic

Zachary, Louisiana, United States

Site Status

Prime Global Research Inc

The Bronx, New York, United States

Site Status

Monroe Biomedical Research

Monroe, North Carolina, United States

Site Status

Lillestol Research LLC

Fargo, North Dakota, United States

Site Status

WellNow Urgent Care and Research

Huber Heights, Ohio, United States

Site Status

Conrad Clinical Research

Edmond, Oklahoma, United States

Site Status

Compass Point Research

Nashville, Tennessee, United States

Site Status

Mt Olympus Medical Research

Sugar Land, Texas, United States

Site Status

Dominion Medical Associates

Richmond, Virginia, United States

Site Status

Spaulding Clinical Research

West Bend, Wisconsin, United States

Site Status

Novartis Investigative Site

Barranquilla, Atlántico, Colombia

Site Status

Novartis Investigative Site

Floridablanca, Santander Department, Colombia

Site Status

Novartis Investigative Site

Manizales, , Colombia

Site Status

Novartis Investigative Site

San Gil, , Colombia

Site Status

Novartis Investigative Site

Munich, Bavaria, Germany

Site Status

Novartis Investigative Site

Hanover, Lower Saxony, Germany

Site Status

Novartis Investigative Site

Löhne, North Rhine-Westphalia, Germany

Site Status

Novartis Investigative Site

Jerichow, Saxony-Anhalt, Germany

Site Status

Novartis Investigative Site

Berlin, , Germany

Site Status

Novartis Investigative Site

Bochum, , Germany

Site Status

Novartis Investigative Site

Gladbeck, , Germany

Site Status

Novartis Investigative Site

Hamburg, , Germany

Site Status

Novartis Investigative Site

Papenburg, , Germany

Site Status

Novartis Investigative Site

Budapest, , Hungary

Site Status

Novartis Investigative Site

Pécs, , Hungary

Site Status

Novartis Investigative Site

Monterrey, Nuevo León, Mexico

Site Status

Novartis Investigative Site

Monterrey, Nuevo León, Mexico

Site Status

Novartis Investigative Site

Mérida, Yucatán, Mexico

Site Status

Novartis Investigative Site

Culiacan Sinaloa, , Mexico

Site Status

Novartis Investigative Site

Querétaro, , Mexico

Site Status

Countries

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United States Colombia Germany Hungary Mexico

References

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Taub PR, Gutierrez A, Wewers D, Garcia Cantu E, Cao H, Deck C, Lesogor A, Ott D, Mena-Madrazo J, Zang X, Wright RS. Safety and Lipid-Lowering Efficacy of Inclisiran Monotherapy in Patients Without ASCVD: The VICTORION-Mono Randomized Clinical Trial. J Am Coll Cardiol. 2025 Jul 22;86(3):196-208. doi: 10.1016/j.jacc.2025.04.049. Epub 2025 May 5.

Reference Type DERIVED
PMID: 40392667 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.novctrd.com/ctrdweb/patientsummary/patientsummaries?patientSummaryId=2658

A Plain Language Trial Summary is available on www.novctrd.com

Other Identifiers

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CKJX839D12304

Identifier Type: -

Identifier Source: org_study_id

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