Oral Pooled Fecal Microbiotherapy to Prevent Allogeneic Hematopoietic Cell Transplantation Complications (PHOEBUS Trial)

NCT ID: NCT05762211

Last Updated: 2024-12-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

387 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-10-31

Study Completion Date

2027-02-15

Brief Summary

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This randomized, placebo-controlled phase IIb study (PHOEBUS trial) aims to evaluate the activity of fecal microbiotherapy MaaT033 to improve survival through the prevention of transplant-related complications in eligible alloHCT patients

Detailed Description

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Conditions

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Transplant Complication

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Oral pooled fecal microbiotherapy - MaaT033

3 capsules per day

Group Type EXPERIMENTAL

Pooled allogeneic fecal microbiotherapy

Intervention Type DRUG

Capsule for oral use

Placebo capsule

3 capsules per day

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Capsule for oral use

Interventions

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Pooled allogeneic fecal microbiotherapy

Capsule for oral use

Intervention Type DRUG

Placebo

Capsule for oral use

Intervention Type DRUG

Other Intervention Names

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MaaT033

Eligibility Criteria

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Inclusion Criteria

* Age ≥ 50 years old
* Presence of a hematologic malignancy for which an alloHCT is indicated with a reduced toxicity or reduced intensity conditioning regimen
* Patients with polynuclear neutrophils \> 0.5 G/L
* Patients having received wide spectrum antibiotics within the last 90 days prior to inclusion
* Karnofsky index ≥ 70%
* Availability of a sibling donor, an unrelated stem-cell donor or a familial haploidentical donor
* Written informed consent

Exclusion Criteria

* Patients planned to receive a non-myeloablative conditioning regimen (2 Gray total body irradiation (TBI) +/- purine analog, fludarabine + cyclophosphamide or equivalent)
* Patients planned to receive a conventional myeloablative conditioning regimen (e.g. high dose cyclophosphamide and high dose TBI (≥10Gy); high dose busulfan (12.8 mg/kg IV) + high dose cyclophosphamide)
* Patients receiving a manipulated graft (in-vitro T-cell depletion)
* Patients planned to receive a conditioning regimen with alemtuzumab
* Patients planned to receive alloHCT with cord blood cells
* Patients planned to receive alloHCT from unrelated donor with \>= 3/10 HLA-mismatches
* Patients receiving a large spectrum antibiotic at time of randomization
* Patients planned to receive vedolizumab or abatacept for GvHD prophylaxis
* Creatinine clearance \<30 mL/min
* Bilirubin or amino-transferases abnormalities contra-indicating alloHCT
* Cardiac ejection fraction less than 40%
* Pulmonary impairment with \<50% lung carbon monoxide diffusing capacity (DLCO)
* Pregnancy
* Confirmed or suspected intestinal ischemia
* Confirmed or suspected toxic megacolon or gastrointestinal perforation
* Any history of gastro-intestinal surgery in the past 3 months
* Any history of chronic digestive disease (Crohn's disease, ulcerative colitis, inflammatory bowel disease or other relevant digestive condition according to physician's judgement)
* Known allergy or intolerance to trehalose or maltodextrin
* Patients with EBV-IgG negative serology
* Any condition that would, in the investigator's judgment, interfere with full participation in the study, including administration of study drug and attending required study visits; pose a significant risk to the subject; or interfere with interpretation of study data.
* Vulnerable patients such as: persons deprived of liberty, persons in Intensive Care Unit unable to provide informed consent prior to the intervention.
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MaaT Pharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Florent Malard, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

APHP

Locations

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Universitair Ziekenhuis Antwerpen

Antwerp, , Belgium

Site Status RECRUITING

AZ Sint - Jan Brugge

Bruges, , Belgium

Site Status RECRUITING

Institut Jules Bordet

Brussels, , Belgium

Site Status RECRUITING

Universitair Ziekenhuis Brussel

Brussels, , Belgium

Site Status RECRUITING

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status RECRUITING

Cliniques Universitaires Saint-Luc

Leuven, , Belgium

Site Status RECRUITING

Algemeen Ziekenhuis Delta - Campus Rumbeke

Roeselare, , Belgium

Site Status RECRUITING

CHU Angers

Angers, , France

Site Status RECRUITING

CHU Besançon

Besançon, , France

Site Status RECRUITING

CHU Caen

Caen, , France

Site Status RECRUITING

CHU Grenoble

La Tronche, , France

Site Status RECRUITING

CHRU Lille

Lille, , France

Site Status RECRUITING

Centre Hospitalier Universitaire Limoges

Limoges, , France

Site Status RECRUITING

Institut Paoli Calmettes

Marseille, , France

Site Status RECRUITING

Hôpital Saint-Eloi

Montpellier, , France

Site Status RECRUITING

CHU Nantes Hôtel Dieu

Nantes, , France

Site Status RECRUITING

Hôpital l'Archet

Nice, , France

Site Status RECRUITING

Hôpital Saint-Louis

Paris, , France

Site Status RECRUITING

Hôpital St Antoine

Paris, , France

Site Status RECRUITING

Hôpital Haut-Lévêque

Pessac, , France

Site Status RECRUITING

Centre Hospitalier Lyon-Sud

Pierre-Bénite, , France

Site Status NOT_YET_RECRUITING

Centre Hospitalier Universitaire de Poitiers

Poitiers, , France

Site Status RECRUITING

CHU Rennes - Hôpital Pontchaillou

Rennes, , France

Site Status RECRUITING

CHU St Etienne

Saint-Priest-en-Jarez, , France

Site Status RECRUITING

IUCT Toulouse

Toulouse, , France

Site Status RECRUITING

Centre Hospitalier Régional Universitaire de Tours

Tours, , France

Site Status NOT_YET_RECRUITING

CHU Tours

Tours, , France

Site Status RECRUITING

Universitätsklinikum Augsburg

Augsburg, , Germany

Site Status RECRUITING

Helios Klinikum Berlin-Buch

Berlin, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum Bonn

Bonn, , Germany

Site Status RECRUITING

Universitätsklinikum Essen

Essen, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum Frankfurt

Frankfurt, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum des Saarlandes

Hombourg, , Germany

Site Status RECRUITING

Universitätsklinikum Schleswig-Holstein - Campus Kiel

Kiel, , Germany

Site Status NOT_YET_RECRUITING

Universitätsklinikum Leipzig

Leipzig, , Germany

Site Status NOT_YET_RECRUITING

Universitätsmedizin Mannheim

Mannheim, , Germany

Site Status NOT_YET_RECRUITING

Klinikum rechts der Isar der Technischen Universität

München, , Germany

Site Status RECRUITING

Universitätsklinikum Ulm

Ulm, , Germany

Site Status RECRUITING

Universitair Medisch Centrum Groningen

Groningen, , Netherlands

Site Status RECRUITING

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebrón

Barcelona, , Spain

Site Status RECRUITING

Institut Català d'Oncologia - Hospital Duran i Reynals (ICO L'Hospitalet)

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Virgen de las Nieves

Granada, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Marañón

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Puerta de Hierro - Majadahonda

Majadahonda, , Spain

Site Status RECRUITING

Hospital General Universitario Morales Meseguer

Murcia, , Spain

Site Status RECRUITING

Clinica Universidad de Navarra - Pamplona

Pamplona, , Spain

Site Status RECRUITING

Complejo Asistencial Universitario de Salamanca - Hospital Clínico

Salamanca, , Spain

Site Status RECRUITING

Hospital Universitario Marques de Valdecilla

Santander, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocío

Seville, , Spain

Site Status RECRUITING

Hospital Clínico Universitario de Valencia Avenida Blasco Ibáñez

Valencia, , Spain

Site Status RECRUITING

Hospital Universitario La Fe

Valencia, , Spain

Site Status RECRUITING

Cardiff and Vale University Health Board

Cardiff, , United Kingdom

Site Status RECRUITING

Countries

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Belgium France Germany Netherlands Spain United Kingdom

Central Contacts

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Emilie Plantamura, PharmD, PhD

Role: CONTACT

Phone: 0033 663590186

Email: [email protected]

Romain Collard

Role: CONTACT

Email: [email protected]

Facility Contacts

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Anke Verlinden, MD

Role: primary

Alexander Schauwvlieghe, MD

Role: primary

Fabio Andreozzi, MD

Role: primary

Ann De Becker, MD

Role: primary

Anke Delie, MD

Role: primary

Xavier Poiré, MD

Role: primary

Dries Deeren, MD

Role: primary

Sylvie François, MD

Role: primary

Etienne Daguindau, MD

Role: primary

Sylvain Chantepie, MD

Role: primary

Martin Carré, MD

Role: primary

Leonardo MAGRO, MD

Role: primary

Pascal Turlure, MD

Role: primary

Raynier Devillier

Role: primary

Ludovic Gabellier, MD

Role: primary

Patrice Chevallier

Role: primary

Michael Loschi

Role: primary

David Michonneau, MD

Role: primary

Florent Malard, MD, PhD

Role: primary

Clémence Médiavilla

Role: primary

Hélène Labussiere-Wallet

Role: primary

Déborah Desmier, MD

Role: primary

Jean-Baptiste Méar, MD

Role: primary

Jérôme Cornillon, MD

Role: primary

Anne Huynh

Role: primary

Nicolas Vallet

Role: primary

Nicolas Vallet, MD

Role: primary

Christoph Schmid

Role: primary

Judith Niederland

Role: primary

Tobias Holderried

Role: primary

Thomas Schroeder

Role: primary

Gesine Bug

Role: primary

Sarah Altmeyer, MD

Role: primary

Friedrich Stölzel

Role: primary

Madlen Jentzsch

Role: primary

Daniela Heidenreich

Role: primary

Mareike Verbeek, MD

Role: primary

Elisa Sala, MD

Role: primary

Linde Morsink, MD

Role: primary

Irene Garcia-Cadenas, MD

Role: primary

Maria Sola Soto

Role: primary

Marta Peña Domingo

Role: primary

Manuel Jurado Chacon

Role: primary

Mi Kwon

Role: primary

Karem Humala

Role: primary

Rafael Duarte Palomino

Role: primary

Oriana Jimena Lopez Godino

Role: primary

Jose Rifon, MD

Role: primary

Lucia Lopez Corral, MD

Role: primary

Maria Arancha Bermúdez

Role: primary

Jose Antonio Perez Simon

Role: primary

Rafael Hernani Morales, MD

Role: primary

Jaime Sanz Caballer

Role: primary

Wendy Ingram, MD

Role: primary

Other Identifiers

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MPOH08

Identifier Type: -

Identifier Source: org_study_id