A Phase 1/2 Study to Evaluate ALN-KHK in Overweight to Obese Healthy Volunteers and Obese Patients With T2DM

NCT ID: NCT05761301

Last Updated: 2025-05-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

49 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-10

Study Completion Date

2025-04-03

Brief Summary

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To evaluate the safety, tolerability, pharmacokinetics (PK) and pharmacodynamics (PD) of single ascending doses of ALN-KHK and to evaluate the safety, tolerability, efficacy, PK and PD of multiple doses of KHK.

Detailed Description

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Conditions

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Type 2 Diabetes Mellitus (T2DM)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

The single ascending dose part of this study (Part A) will have a sequential interventional study model. The multi-dose part of this study (Part B) will have a parallel interventional study model and will begin after the completion of Part A.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Part A: ALN-KHK

Participants will be administered a single dose of ALN-KHK.

Group Type EXPERIMENTAL

ALN-KHK

Intervention Type DRUG

ALN-KHK will be administered by subcutaneous (SC) injection.

Part A: Placebo

Participants will be administered a single dose of placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered by subcutaneous (SC) injection.

Part B: ALN-KHK

Participants will be administered a multiple doses of ALN-KHK.

Group Type EXPERIMENTAL

ALN-KHK

Intervention Type DRUG

ALN-KHK will be administered by subcutaneous (SC) injection.

Part B: Placebo

Participants will be administered a multiple doses of placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered by subcutaneous (SC) injection.

Interventions

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ALN-KHK

ALN-KHK will be administered by subcutaneous (SC) injection.

Intervention Type DRUG

Placebo

Placebo will be administered by subcutaneous (SC) injection.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Stable euthyroid status (no known changes in thyroid function; stable hormone replacement for at least 4 months) at screening
* Part A: body mass index (BMI) ≥27 kg/m\^2 and ≤34.9 kg/m\^2
* Part B: BMI ≥30 kg/m\^2 to ≤39.9 kg/m\^2, confirmed diagnosis of T2DM, and an HbA1c ≥7.5% to \<10%
* Part B: Confirmed T2DM diagnosis

Exclusion Criteria

* Parts A and B: has received an investigational agent within the last 30 days
* Part A: History of Type 1 or Type 2 diabetes
* Part B: History of Type 1 diabetes
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Alnylam Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Alnylam Pharmaceuticals

Locations

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Clinical Trial Site

Phoenix, Arizona, United States

Site Status

Clinical Trial Site

Vista, California, United States

Site Status

Clinical Trial Site

Lake Worth, Florida, United States

Site Status

Clinical Trial Site

Orlando, Florida, United States

Site Status

Clinical Trial Site

Atlanta, Georgia, United States

Site Status

Clinical Trial Site

Berlin, New Jersey, United States

Site Status

Clinical Trial Site

Monroe, North Carolina, United States

Site Status

Clinical Trial Site

Oklahoma City, Oklahoma, United States

Site Status

Clinical Trial Site

Dallas, Texas, United States

Site Status

Clinical Trial Site

Houston, Texas, United States

Site Status

Clinical Trial Site

San Antonio, Texas, United States

Site Status

Clinical Trial Site

Sarnia, Ontario, Canada

Site Status

Clinical Trial Site

Montreal, Quebec, Canada

Site Status

Clinical Trial Site

Victoriaville, Quebec, Canada

Site Status

Clinical Trial Site

Toronto, , Canada

Site Status

Countries

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United States Canada

Other Identifiers

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ALN-KHK-001

Identifier Type: -

Identifier Source: org_study_id

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