A Study of Ripretinib vs Sunitinib in Patients With Advanced GIST With Specific KIT Exon Mutations Who Were Previously Treated With Imatinib

NCT ID: NCT05734105

Last Updated: 2025-12-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

54 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-13

Study Completion Date

2028-12-31

Brief Summary

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This is a Phase 3, 2-arm, randomized, open-label, global, multicenter study comparing the efficacy of ripretinib to sunitinib in participants with GIST who progressed on first-line treatment with imatinib, harbor co-occurring KIT exons 11+17/18 mutations, and are without KIT exon 9, 13, or 14 mutations. Upon disease progression as determined by an independent radiologic review, participants randomized to sunitinib will be given the option to either crossover to receive ripretinib 150 mg QD or discontinue sunitinib.

Detailed Description

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Conditions

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GIST

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Ripretinib

150 mg QD of ripretinib (3×50 mg tablets) will be dosed continuously in repeated 42-day cycles.

Group Type EXPERIMENTAL

Ripretinib

Intervention Type DRUG

50 mg tablets

Sunitinib

50 mg QD of sunitinib (4×12.5 mg capsules) will be dosed in 42-day cycles. Sunitinib will be given continuously for 4 weeks with a 2-week break.

Group Type ACTIVE_COMPARATOR

Sunitinib

Intervention Type DRUG

12.5 mg tablets

Interventions

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Ripretinib

50 mg tablets

Intervention Type DRUG

Sunitinib

12.5 mg tablets

Intervention Type DRUG

Other Intervention Names

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QINLOCK, DCC-2618 Sutent

Eligibility Criteria

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Inclusion Criteria

1. Male or female ≥18 years of age.
2. Histologic diagnosis of GIST with co-occurring KIT exons 11+17/18 mutations confirmed by ctDNA sample.
3. Participants must have advanced GIST and radiologic progression on imatinib treatment.
4. Eastern Cooperative Oncology Group (ECOG) performance status (PS) of ≤2 at screening.
5. Female participants of childbearing potential must have a negative pregnancy test at screening and prior to the first dose of study drug.
6. Participants of reproductive potential must agree to follow contraception requirements.
7. Participants must have at least 1 measurable lesion according to mRECIST v1.1 within 21 days prior to the first dose of study drug.
8. Adequate organ function and bone marrow reserve based on laboratory assessments performed at screening.

Exclusion Criteria

1. History of KIT exon 9 mutation or detection of KIT exon 9, 13, or 14 mutations in a ctDNA sample.
2. Has known active central nervous system metastases.
3. New York Heart Association Class II-IV heart disease, myocardial infarction within 6 months of Cycle 1 Day 1, active ischemia or any other uncontrolled cardiac condition such as angina pectoris, clinically significant cardiac arrhythmia requiring therapy, uncontrolled hypertension, or congestive heart failure.
4. Use of strong or moderate inhibitors or inducers of cytochrome P450 (CYP) 3A prior to the first dose of study drug, and consumption of grapefruit or grapefruit juice within 14 days prior to the first dose of study drug.
5. Major surgeries (eg, abdominal laparotomy) within 4 weeks of the first dose of study drug.
6. Known human immunodeficiency virus or hepatitis C infection only if the participant is taking medications that are excluded per protocol, acute or chronic hepatitis B, or acute or chronic hepatitis C infection.
7. Gastrointestinal abnormalities including, but not limited to:

1. inability to take oral medication
2. malabsorption syndromes
3. requirement for intravenous alimentation
8. Any active bleeding excluding hemorrhoidal or gum bleeding.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Deciphera Pharmaceuticals, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Team

Role: STUDY_DIRECTOR

Deciphera Pharmaceuticals, LLC

Locations

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UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

Yale University

New Haven, Connecticut, United States

Site Status

Mayo Clinic Florida

Jacksonville, Florida, United States

Site Status

Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Boston Medical Center

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

M Health Fairview University of Minnesota Medical Center

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Northwell Health Cancer Institute/ R.J. Zuckerberg Cancer Center

New York, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

The James Cancer Hospital and Solove Research Institute at The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States

Site Status

OU Health Stephenson Cancer Center

Oklahoma City, Oklahoma, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Fred Hutchinson Cancer Center

Seattle, Washington, United States

Site Status

Prince of Wales Hospital

Randwick, New South Wales, Australia

Site Status

Alfred Health

Melbourne, Victoria, Australia

Site Status

INCA - Instituto Nacional de Cancer

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

CEPEN - Centro de Pesquisa e Ensino em Saude de Santa Catarina

Florianópolis, Santa Catarina, Brazil

Site Status

Hospital de Cancer de Barretos - Fundacao Pio XII

Barretos, São Paulo, Brazil

Site Status

Hospital Sirio-Libanes

São Paulo, São Paulo, Brazil

Site Status

Hospital 9 de Julho

São Paulo, São Paulo, Brazil

Site Status

AC Camargo Câncer Center

São Paulo, São Paulo, Brazil

Site Status

Arthur J.E. Child Comprehensive Cancer Centre

Calgary, Alberta, Canada

Site Status

Juravinski Cancer Centre

Hamilton, Ontario, Canada

Site Status

University Health Network, Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

McGill University Health Centre

Montreal, Quebec, Canada

Site Status

Clínica San Carlos De Apoquindo Red Salud UC Christus

Las Condes, RM, Chile

Site Status

Centro de Oncología de Precisión

Santiago, RM, Chile

Site Status

CHU Dijon

Dijon, Bourgogone, France

Site Status

Centre Eugène Marquis

Rennes, Ille et Vilaine, France

Site Status

Institut Bergonié

Bordeaux, , France

Site Status

Centre Léon Bérard

Lyon, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Helios Klinikum Berlin-Buch

Berlin, , Germany

Site Status

University Hospital Essen (Universitätsklinikum Essen)

Essen, , Germany

Site Status

Heidelberg University Hospital

Heidelberg, , Germany

Site Status

Universitares Krebszentrum Leipzig

Leipzig, , Germany

Site Status

Istituto Nazionale Tumori IRCCS Fondazione "G Pascale"

Naples, Napoli, Italy

Site Status

U.O.C. Oncologia Medica

Palermo, Palermo, Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Istituto Oncologico Veneto-IOV IRCCS

Padua, , Italy

Site Status

Università Campus Bio-Medico di Roma

Roma, , Italy

Site Status

IRCCS Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

UMC Groningen

Groningen, , Netherlands

Site Status

LUMC

Leiden, , Netherlands

Site Status

Oslo University Hospital

Oslo, Norway, Norway

Site Status

Narodowy Instytut Onkologii Im . Marii Skłodowskiej-Curie - Państwowy Instytut Badawczy

Warsaw, Warszawa, Poland

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, Barcelona, Spain

Site Status

Complejo Hospitalario Universitario de Vigo - Hospital Alvaro Cunqueiro

Vigo, Pontevedra, Spain

Site Status

Instituto Valenciano de Oncologia - IVO

Valencia, Valencia, Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status

Hospital Universitario Centra de Asturias

Oviedo, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

The Royal Marsden Hospital NHS Foundation Trust

London, Greater London, United Kingdom

Site Status

St. James University Hospital

Leeds, West Yorkshire, United Kingdom

Site Status

Countries

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United States Australia Brazil Canada Chile France Germany Italy Netherlands Norway Poland South Korea Spain Taiwan United Kingdom

References

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George S, Blay JY, Chi P, Jones RL, Serrano C, Somaiah N, Gelderblom H, Zalcberg JR, Reichmann W, Sprott K, Cox P, Sherman ML, Ruiz-Soto R, Heinrich MC, Bauer S. The INSIGHT study: a randomized, Phase III study of ripretinib versus sunitinib for advanced gastrointestinal stromal tumor with KIT exon 11 + 17/18 mutations. Future Oncol. 2024;20(27):1973-1982. doi: 10.1080/14796694.2024.2376521. Epub 2024 Sep 4.

Reference Type DERIVED
PMID: 39229786 (View on PubMed)

Related Links

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Other Identifiers

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2022-503058-37-00

Identifier Type: CTIS

Identifier Source: secondary_id

DCC-2618-03-003

Identifier Type: -

Identifier Source: org_study_id