Efficacy, Safety, and Tolerability of Two Administrations of COMP360 in Participants With TRD

NCT ID: NCT05711940

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

572 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-02-14

Study Completion Date

2026-12-31

Brief Summary

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Efficacy, Safety, and Tolerability of two administrations of COMP360 in participants with treatment-resistant depression (TRD)

Detailed Description

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This is a phase III, international, multi-centre, randomised, parallel group, fixed repeat dose, double-blind, controlled study. The study population will include participants aged ≥18 years with TRD.

Overall, 568 participants are to be randomised in a 2:1:1 ratio to receive COMP360 25 mg, 10 mg or 1 mg.

The study comprises three parts (A, B, and C) and will last approximately 62 weeks including a three- to ten-week screening period.

Part A will include a nine-week follow-up from initial investigational product (IP) administration.

Part B will include a further 17 weeks follow-up out to 26 weeks from initial IP administration.

Part C will include a further 26 weeks follow-up out to 52 weeks from initial IP administration.

In this study, the aim is to assess the efficacy of COMP360, administered with psychological support in adult participants with TRD, in improving symptoms of depression.

Conditions

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Treatment Resistant Depression

Keywords

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psilocybin

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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25 mg COMP360 Psilocybin

25 mg COMP360 Psilocybin

Group Type EXPERIMENTAL

Psilocybin

Intervention Type DRUG

COMP360 Psilocybin administered under supportive conditions

10 mg COMP360 Psilocybin

10 mg COMP360 Psilocybin

Group Type EXPERIMENTAL

Psilocybin

Intervention Type DRUG

COMP360 Psilocybin administered under supportive conditions

1 mg COMP360 Psilocybin

1 mg COMP360 Psilocybin, active comparator

Group Type ACTIVE_COMPARATOR

Psilocybin

Intervention Type DRUG

COMP360 Psilocybin administered under supportive conditions

Interventions

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Psilocybin

COMP360 Psilocybin administered under supportive conditions

Intervention Type DRUG

Other Intervention Names

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COMP360

Eligibility Criteria

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Inclusion Criteria

1. Aged ≥18 years at Screening
2. Major depression without psychotic features (single or recurrent episode as informed by the Diagnostic and Statistical Manual of Mental Disorders, 5th edition \[DSM-5\])
3. If the current major depressive episode is the participant's first lifetime episode of depression, the length of the current episode must be ≥3 months and ≤2 years at Screening
4. MADRS total score ≥20 at Screening and Baseline to ensure at least moderate severity of depression
5. TRD, defined as failure to respond to an adequate dose and duration of two, three, or four different pharmacological treatments for the current episode as determined through the Massachusetts General Hospital Antidepressant Treatment Response Questionnaire (MGH-ATRQ) and using the supplementary advice on additional antidepressants not included in MGH-ATRQ
6. At Screening, agreement to discontinue all prohibited medications

Exclusion Criteria

1. Prior or ongoing bipolar disorder, any psychotic disorder, including schizophrenia, schizophreniform disorder, schizoaffective disorder, brief psychotic disorder (unless substance induced or due to a medical condition), antisocial personality disorder as assessed by a structured clinical interview (MINI 7.0.2)
2. Lifetime paranoid, schizoid, schizotypal, histrionic, narcissistic personality disorder, or any ongoing serious psychiatric comorbidity based on medical history and clinical judgement
3. Borderline personality disorder as demonstrated by medical history or the Mini International Neuropsychiatric Interview Plus (MINI plus) - borderline personality disorder module
4. Ongoing post-traumatic stress disorder, obsessive-compulsive disorder, or anorexia nervosa as assessed by medical history and a structured clinical interview (MINI 7.0.2)
5. Psychiatric inpatient within the past 12 months prior to Screening
6. Use of electroconvulsive therapy, deep brain stimulation, or vagus nerve stimulation during the current depressive episode
7. Transcranial magnetic stimulation within the past six months prior to Screening
8. Current enrolment in a psychological therapy programme that will not remain stable for the duration of the study. Psychological therapies cannot have been initiated within 30 days prior to Screening
9. Exposure to COMP360 psilocybin therapy prior to Screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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COMPASS Pathways

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Lighthouse Psychiatry Scottsdale

Gilbert, Arizona, United States

Site Status

Clinical Innovations, Inc.

Bellflower, California, United States

Site Status

M3 Wake Research

Encino, California, United States

Site Status

The Regents of the University of California - San Diego

La Jolla, California, United States

Site Status

Kadima Neuropsychiatry Institute

La Jolla, California, United States

Site Status

CalNeuro Research Group, Inc

Los Angeles, California, United States

Site Status

Catalina Research Institute, LLC

Montclair, California, United States

Site Status

Piedmont Hospital Neuroscience Centre

Oakland, California, United States

Site Status

ATP Clinical Research, Inc.

Orange, California, United States

Site Status

CITrials

Riverside, California, United States

Site Status

Lumos Clinical Research Center

San Jose, California, United States

Site Status

Syrentis Clinical Research

Santa Ana, California, United States

Site Status

Stanford University

Stanford, California, United States

Site Status

ASCLEPES Research Centers

Thousand Oaks, California, United States

Site Status

Pacific Clinical Research Management Group, LLC

Upland, California, United States

Site Status

Innovative Clinical Research, Inc.

Lauderhill, Florida, United States

Site Status

Central Miami Medical Institute, LLC

Miami, Florida, United States

Site Status

Behavioral Clinical Research, Inc.

Miami Lakes, Florida, United States

Site Status

Health Synergy Clinical Research

Okeechobee, Florida, United States

Site Status

Clinical Neurosciecne Solutions, Inc. dba CNS Healthcare

Orlando, Florida, United States

Site Status

APG Research, LLC- Advanced Psychiatric Group

Orlando, Florida, United States

Site Status

University South Florida

Tampa, Florida, United States

Site Status

Stedman Clinical Trials

Tampa, Florida, United States

Site Status

Health Synergy Clinical Research, LLC

West Palm Beach, Florida, United States

Site Status

Atlanta Center for Medical Research

Atlanta, Georgia, United States

Site Status

iResearch Atlanta

Decatur, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Uptown Research Institute, LLC

Chicago, Illinois, United States

Site Status

Psychiatric Medicine Associates

Skokie, Illinois, United States

Site Status

Harvard Medical School - McLean Hospital

Belmont, Massachusetts, United States

Site Status

Adams Clinical - Boston (Copley Clinical)

Boston, Massachusetts, United States

Site Status

University of Massachusetts Medical School

North Worcester, Massachusetts, United States

Site Status

Adams Clinical - Boston

Watertown, Massachusetts, United States

Site Status

Michigan Clinical Research Institute PC

Ann Arbor, Michigan, United States

Site Status

University Of Michigan Comprehensive Depression Center

Ann Arbor, Michigan, United States

Site Status

Institute for Integrative Therapies

Eden Prairie, Minnesota, United States

Site Status

St. Charles Psychiatric Associates - Midwest Research Group

Saint Charles, Missouri, United States

Site Status

Alivation Research, LLC.

Lincoln, Nebraska, United States

Site Status

Hassman Research Institute

Berlin, New Jersey, United States

Site Status

Princeton Medical Institute

Princeton, New Jersey, United States

Site Status

Bio Behavioral Health

Toms River, New Jersey, United States

Site Status

Dent Neurosciences Research Center, Inc.

Amherst, New York, United States

Site Status

Fieve Clinical Research, Inc

New York, New York, United States

Site Status

Spectrum Neuroscience and Treatment Institute

New York, New York, United States

Site Status

Adams Clinical - New York

New York, New York, United States

Site Status

New York State Psychiatric Institute

New York, New York, United States

Site Status

Richmond Behavioral Associates

Staten Island, New York, United States

Site Status

Adams Clinical - New York

The Bronx, New York, United States

Site Status

University of Cincinnati, Department of Psychiatry & Behavirol Neuroscience

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic - Lutheran Hospital

Cleveland, Ohio, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Suburban Research Associates

Media, Pennsylvania, United States

Site Status

The University of Texas at Austin - Dell Medical School

Austin, Texas, United States

Site Status

Houston Clinical Trials, LLC

Bellaire, Texas, United States

Site Status

Relaro Medical Trials

Dallas, Texas, United States

Site Status

Center for Depression Research and Clinical Care

Dallas, Texas, United States

Site Status

North Texas Clinical Trials

Fort Worth, Texas, United States

Site Status

Brain Health Consultants and TMS Center

Houston, Texas, United States

Site Status

HCA Healthcare Research Institute - Medical City Green Oaks Hospital

Plano, Texas, United States

Site Status

Cedar Clinical Research

Draper, Utah, United States

Site Status

The University of Utah - Huntsman Mental Health Institute

Salt Lake City, Utah, United States

Site Status

Seattle Neuropsychiatric Treatment Center

Seattle, Washington, United States

Site Status

Diex Recherche Sherbrooke Inc.

Québec, B.C., Canada

Site Status

Medical Arts Health Research Centre, Kamloops

Kamloops, British Columbia, Canada

Site Status

Okanagan Clinical Trials

Kelowna, British Columbia, Canada

Site Status

Medical Arts Research Group - Penticton

Penticton, British Columbia, Canada

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Chatham-Kent Clnical Trials Centre

Chatham, Ontario, Canada

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St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

Centre for Addiction and Mental Health (CAMH)

Toronto, Ontario, Canada

Site Status

Centre for Neurology Studies

Vancouver, , Canada

Site Status

Medical Arts Research Group

Vancouver, , Canada

Site Status

National Institute of Mental Health

Klecany, , Czechia

Site Status

Neuroterapie KH Sro

Kutná Hora, , Czechia

Site Status

Psychiatric Ambulance

Ostrava, , Czechia

Site Status

A-Shine s.r.o.

Pilsen, , Czechia

Site Status

Psychedelicka klinika, s.r.o.

Prague, , Czechia

Site Status

Institut Neuropsychiatricke Pece

Prague, , Czechia

Site Status

Aalborg Universitetshospital-Psykiatrien Region Nordjylland

Aalborg, , Denmark

Site Status

Centre Hospitalier Universitaire de Nimes (CHU) - Hopital Universitaire Caremeau

Nîmes, , France

Site Status

Universite Paris VI Pierre et Marie Curie - Hopital de La Salpetriere - Centre Emotion - USR 3246 (CNRS UMR 7593)

Paris, , France

Site Status

Centre Hospitalier Sainte Anne - Clinique des Maladies Mentales et de l'Encephale (CMME)

Paris, , France

Site Status

Ghu-Centre Hospitalier Sainte Anne, Centre de Recherche Clinique

Paris, , France

Site Status

Charite-Universitaetsmedizin Berlin

Berlin, , Germany

Site Status

Johann Wolfgang Goethe-Universitaet Frankfurt am Main - Klinik fuer Psychiatrie, Psychosomatik und Psychotherapie

Frankfurt, , Germany

Site Status

ZiP Campus Luebeck

Lübeck, , Germany

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Tallaght University Hospital

Dublin, , Ireland

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La Nua Day Hospital Mental Health Centre

Galway, , Ireland

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University Medical Center Groningen

Groningen, , Netherlands

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Leids Universitair Medisch Centrum (LUMC) (Leiden University Medical Center) - Leiden Institute for Brain and Cognition (LIBC)

Leiden, , Netherlands

Site Status

Universitair Medisch Centrum Utrecht (UMC Utrecht)

Utrecht, , Netherlands

Site Status

Promente - Ośrodek Badań Klinicznych

Bydgoszcz, , Poland

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Uniwersyteckle Centrum Kliniczne, Klinika Psychiatrii Doroslych

Gdansk, , Poland

Site Status

Centrum Badan Klinicznych PI-House Sp. z o.o.

Gdansk, , Poland

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Hospital Clinic de Barcelona

Barcelona, , Spain

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Parc Sanitari Sant Joan de Deu (Sant Joan de Deu Serveis de Salut Mental)

Barcelona, , Spain

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Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

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FIDMAG Hermanas Hospitalarias

Sant Boi de Llobregat, , Spain

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Hospital Universitario Río Hortega de Valladolid

Valladolid, , Spain

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Hospital Provincial de Zamora - Servicio de Psiquiatria

Zamora, , Spain

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Vuxenpsykiatrimottagningen

Landskrona, , Sweden

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Lunds Universitet - Medicinska Fakulteten (Lund University Faculty of Medicine)

Lund, , Sweden

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ClinSmart Sweden AB

Solna, , Sweden

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Hälsoklustret

Stockholm, , Sweden

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Cornwall Partnership NHS Foundation Trust

Bodmin, Cornwall, United Kingdom

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Abraham Cowley Unit - Surrey and Borders Partnership NHS Foundation Trust

Chertsey, , United Kingdom

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St. Pancras Clinical Research

Chester, , United Kingdom

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Grounded Research Hub - Rotherham Doncaster & South Humber NHS Foundation Trust

Doncaster, , United Kingdom

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Clinical Research Facility, Royal Devon and Exeter Hospital

Exeter, , United Kingdom

Site Status

Fulbourn Hospital - Cambridgeshire And Peterborough NHS Foundation Trust

Fulbourn, , United Kingdom

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St. Pancras Clinical Research

London, , United Kingdom

Site Status

King's College London - Institute of Psychiatry, Psychology

London, , United Kingdom

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Clerkenwell Health

London, , United Kingdom

Site Status

Cumbria, Northumberland, Tyne and Wear NHS Foundation Trust - Wolfson Research Centre

Newcastle, , United Kingdom

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University Of Nottingham/Nottinghamshire Healthcare Trust, Institute Of Mental Health

Nottingham, , United Kingdom

Site Status

The Warneford Hospital- NIHR Clinical Research Facility

Oxford, , United Kingdom

Site Status

Sheffield Health and Social Care NHS Foundation Trust

Sheffield, , United Kingdom

Site Status

Countries

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United States Canada Czechia Denmark France Germany Ireland Netherlands Poland Spain Sweden United Kingdom

Other Identifiers

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COMP 006

Identifier Type: -

Identifier Source: org_study_id