A Study to Examine the Efficacy and Safety of Zanubrutinib Given to Adults With Primary Membranous Nephropathy

NCT ID: NCT05707377

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

178 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-04-17

Study Completion Date

2027-10-31

Brief Summary

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The primary objectives of this study are: In Part 1 to evaluate the efficacy of zanubrutinib as measured by proteinuria reduction, and in Part 2 to evaluate the efficacy of zanubrutinib compared with tacrolimus as measured by complete remission rate, in participants with primary membranous nephropathy (PMN) who are on optimal supportive care.

Detailed Description

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Conditions

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Primary Membranous Nephropathy

Keywords

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BGB-3111 Zanubrutinib BTKi

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

In Part I, participants will be assigned to one treatment group. After enrollment in Part I is complete, enrollment in Part 2 will start. In Part 2, participants will be randomly assigned to 1 of 3 treatment groups.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1: Zanubrutinib High Dose

Participants will receive zanubrutinib twice daily.

Group Type EXPERIMENTAL

Zanubrutinib

Intervention Type DRUG

Zanubrutinib capsules administered orally.

Part 2: Zanubrutinib High Dose

Participants will receive zanubrutinib twice daily.

Group Type EXPERIMENTAL

Zanubrutinib

Intervention Type DRUG

Zanubrutinib capsules administered orally.

Part 2: Zanubrutinib Low Dose

Participants will receive zanubrutinib once daily.

Group Type EXPERIMENTAL

Zanubrutinib

Intervention Type DRUG

Zanubrutinib capsules administered orally.

Part 2: Tacrolimus

Participants will receive tacrolimus capsules twice daily for 64 weeks.

Group Type ACTIVE_COMPARATOR

Tacrolimus

Intervention Type DRUG

Tacrolimus capsules administered orally.

Interventions

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Zanubrutinib

Zanubrutinib capsules administered orally.

Intervention Type DRUG

Tacrolimus

Tacrolimus capsules administered orally.

Intervention Type DRUG

Other Intervention Names

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BGB-3111 Brukinsa

Eligibility Criteria

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Inclusion Criteria

* Biopsy-confirmed PMN within 5 years before the initial screening (ie, the day the informed consent is signed)
* UPCR (based on 24-hour urine collection) \> 3.5 at initial screening and at confirmation assessment
* Treatment with a maximally tolerated or allowed dose of an angiotensin-converting enzyme inhibitor (ACEI) or angiotensin II receptor blocker (ARB) for ≥ 24 weeks before randomization (12 weeks before initiation of study drug for Part 1) and with adequate blood pressure control (blood pressure \< 130/80 mmHg, measured on ≥ 2 occasions \[not on the same day\] within 4 weeks before the assignment of study treatment)
* Anti-PLA2R antibody \> 50 RU/mL at confirmation assessment (Part 1 only)

Exclusion Criteria

* Participants with a secondary cause of membranous nephropathy
* Type 1 or 2 diabetes mellitus with hemoglobin A1c (HbA1c) ≥ 7% at screening
* Severe renal disease as determined by rapid decline in eGFR (defined as \> 15 mL/min/1.73m\^2 within 24 weeks prior to randomization, not otherwise explained)
* A known history of a primary immunodeficiency or an underlying condition such as human immunodeficiency virus (HIV) infection or splenectomy that predisposes the participant to infections
* Patients at risk for tuberculosis at screening
* Known infection with serologic status reflecting active or chronic hepatitis B virus infection, or presence of hepatitis C virus antibody
* Severe hepatic insufficiency (Child-Pugh C)
* Clinically significant cardio-cerebrovascular diseases
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BeOne Medicines

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

BeOne Medicines

Locations

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Amicis Research Center

Northridge, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Intermed Consultants

Minneapolis, Minnesota, United States

Site Status

Kidney Specialist of Southern Nevada (Ksosn)

Las Vegas, Nevada, United States

Site Status

Carolina Nephrology

Spartanburg, South Carolina, United States

Site Status

Investigacion Clinica Aplicada

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Centro de Investigaciones Medicas Mar Del Plata

Mar del Plata, , Argentina

Site Status

Instituto Pro Renal Brasil

Curitiba, , Brazil

Site Status

Hcfmusp Hospital Das Clinicas Da Faculdade de Medicina Da Universidade de Sao Paulo

São Paulo, , Brazil

Site Status

Ott Healthcare, Inc (Corporate Medical Centre)

Scarborough Village, Ontario, Canada

Site Status

Beijing An Zhen Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Site Status

Peking University First Hospital

Beijing, Beijing Municipality, China

Site Status

Peking University Peoples Hospital

Beijing, Beijing Municipality, China

Site Status

Fujian Medical University Union Hospital

Fuzhou, Fujian, China

Site Status

The First Affiliated Hospital of Fujian Medical University

Fuzhou, Fujian, China

Site Status

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, China

Site Status

Guangdong Provincial Peoples Hospital

Guangzhou, Guangdong, China

Site Status

The First Affiliated Hospital, Sun Yat Sen University

Guangzhou, Guangdong, China

Site Status

Peking University Shenzhen Hospital

Shenzhen, Guangdong, China

Site Status

Liuzhou Peoples Hospital

Liuzhou, Guangxi, China

Site Status

The First Affiliated Hospital of Guangxi Medical University

Nanning, Guangxi, China

Site Status

Guizhou Provincial Peoples Hospital

Guiyang, Guizhou, China

Site Status

The First Hospital of Hebei Medical University

Shijiazhuang, Hebei, China

Site Status

The Second Affiliated Hospital of Harbin Medical University

Harbin, Heilongjiang, China

Site Status

The First Affiliated Hospital of Henan University of Science and Technology

Luoyang, Henan, China

Site Status

Nanyang Central Hospital

Nanyang, Henan, China

Site Status

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, China

Site Status

Tongji Hospital of Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status

Renmin Hospital of Wuhan University

Wuhan, Hubei, China

Site Status

Xiangya Hospital of Central South University

Changsha, Hunan, China

Site Status

The First Affiliated Hospital of Baotou Medical College

Baotou, Inner Mongolia, China

Site Status

Jiangsu Province Hospital

Nanjing, Jiangsu, China

Site Status

Wuxi Peoples Hospital

Wuxi, Jiangsu, China

Site Status

The First Affiliated Hospital of Nanchang University Branch Xianghu

Nanchang, Jiangxi, China

Site Status

General Hospital of Ningxia Medical University

Yinchuan, Ningxia, China

Site Status

Shandong Provincial Hospital

Jinan, Shandong, China

Site Status

Affiliated Hospital of Jining Medical University

Jining, Shandong, China

Site Status

The Affiliated Hospital of Qingdao University Branch South

Qingdao, Shandong, China

Site Status

Weifang Peoples Hospital

Weifang, Shandong, China

Site Status

Rui Jin Hospital Shanghai Jiao Tong University School of Medicine

Shanghai, Shanghai Municipality, China

Site Status

Shanghai General Hospital

Shanghai, Shanghai Municipality, China

Site Status

Shanxi Provincial Peoples Hospital

Taiyuan, Shanxi, China

Site Status

Sichuan Academy of Medical Sciences and Sichuan Provincial Peoples Hospital

Chengdu, Sichuan, China

Site Status

Zigong First Peoples Hospital, Zigong Academy of Medical Sciences

Zigong, Sichuan, China

Site Status

The First Affiliated Hospital of Xinjiang Medical University

Ürümqi, Xinjiang, China

Site Status

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status

Zhejiang Provincial Peoples Hospital

Hangzhou, Zhejiang, China

Site Status

The First Affiliated Hospital of Ningbo University

Ningbo, Zhejiang, China

Site Status

Fakultni Nemocnice Olomouc

Olomouc, , Czechia

Site Status

Vseobecna Fakultni Nemocnice V Praze

Prague, , Czechia

Site Status

Istscientifico Di Pavia, Fondazione Smaugeri, Irccs, Clinica Del Lavoro E Della Riabilitazione

Pavia, , Italy

Site Status

Spzoz Centralny Szpital Kliniczny Um W Lodzi

Lodz, , Poland

Site Status

Wojewodzki Specjalistyczny Szpital W Olsztynie

Olsztyn, , Poland

Site Status

Medical Company Llc

Grozny, Chechenskaya Respublika, Russia

Site Status

Erciyes University Medical Faculty

Erciyes, , Turkey (Türkiye)

Site Status

Kocaeli University Research and Application Hospital Department of Nephrology

Kocaeli, , Turkey (Türkiye)

Site Status

Aberdeen Royal Infirmary

Aberdeen, , United Kingdom

Site Status

St Heliers Hospital

Carlshalton, , United Kingdom

Site Status

Royal Derby Hospital

Derby, , United Kingdom

Site Status

Aintree University Hospital

Liverpool, , United Kingdom

Site Status

Manchester Royal Infirmary

Manchester, , United Kingdom

Site Status

Countries

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Mexico Spain United States Argentina Brazil Canada China Czechia Italy Poland Russia Turkey (Türkiye) United Kingdom

References

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Ahmad SB, Jefferson JA. Targeting B Cells and Plasma Cells in Glomerular Disease. J Am Soc Nephrol. 2025 Jun 4;36(9):1844-1857. doi: 10.1681/ASN.0000000772.

Reference Type DERIVED
PMID: 40465397 (View on PubMed)

Other Identifiers

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2022-501147-32-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CTR20230546

Identifier Type: REGISTRY

Identifier Source: secondary_id

BGB-3111-309

Identifier Type: -

Identifier Source: org_study_id