Evaluation of Efficacy and Safety of VX-548 for Painful Diabetic Peripheral Neuropathy (DPN)

NCT ID: NCT05660538

Last Updated: 2025-07-01

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

194 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-12-20

Study Completion Date

2023-10-25

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of VX-548 doses in treating Painful DPN.

Detailed Description

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Conditions

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Diabetic Peripheral Neuropathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Pregabalin

Participants received Pregabalin 100 mg 3 times per day (tid) for 12 weeks

Group Type ACTIVE_COMPARATOR

Pregabalin

Intervention Type DRUG

Capsules for oral administration.

Placebo (matched to SUZ)

Intervention Type DRUG

Placebo matched to SUZ for oral administration.

Suzetrigine (SUZ): Low Dose

Participants received SUZ 23 mg tablet once daily (qd) for 12 weeks.

Group Type EXPERIMENTAL

Suzetrigine

Intervention Type DRUG

Tablets for oral administration.

Placebo (matched to pregabalin)

Intervention Type DRUG

Placebo matched to pregabalin for oral administration.

Suzetrigine (SUZ): Mid Dose

Participants received SUZ 46 mg tablet qd for 12 weeks.

Group Type EXPERIMENTAL

Suzetrigine

Intervention Type DRUG

Tablets for oral administration.

Placebo (matched to pregabalin)

Intervention Type DRUG

Placebo matched to pregabalin for oral administration.

Suzetrigine (SUZ): High Dose

Participants received SUZ 69 mg tablet qd for 12 weeks.

Group Type EXPERIMENTAL

Suzetrigine

Intervention Type DRUG

Tablets for oral administration.

Placebo (matched to pregabalin)

Intervention Type DRUG

Placebo matched to pregabalin for oral administration.

Interventions

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Suzetrigine

Tablets for oral administration.

Intervention Type DRUG

Pregabalin

Capsules for oral administration.

Intervention Type DRUG

Placebo (matched to SUZ)

Placebo matched to SUZ for oral administration.

Intervention Type DRUG

Placebo (matched to pregabalin)

Placebo matched to pregabalin for oral administration.

Intervention Type DRUG

Other Intervention Names

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VX-548 SUZ

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of diabetes mellitus type 1 or type 2 with

* Glycosylated hemoglobin A1c (HbA1c) ≤9%; and
* Presence of bilateral pain in lower extremities due to DPN for at least 1 year

Exclusion Criteria

* Painful neuropathy other than DPN
* History of cardiac dysrhythmias requiring anti-arrhythmia treatment(s)
* History of a clinical atherosclerotic event, such as myocardial infarction or stroke, within the past 12 months
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Vertex Pharmaceuticals Incorporated

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Pinnacle Research Group, LLC

Anniston, Alabama, United States

Site Status

Synexus Clinical Research US - Birmingham

Birmingham, Alabama, United States

Site Status

Synexus Clinical Research US - Phoenix West

Phoenix, Arizona, United States

Site Status

Velocity Clinical Research - Banning

Banning, California, United States

Site Status

Long Beach Clinical Trials Services, Inc.

Long Beach, California, United States

Site Status

University Clinical Investigators

Tustin, California, United States

Site Status

Lynn Institute of the Rockies

Colorado Springs, Colorado, United States

Site Status

Fleming Island Center for Clinical Research

Fleming Island, Florida, United States

Site Status

AMR Fort Myers (The Clinical Study Center)

Fort Myers, Florida, United States

Site Status

Velocity Clinical Research - Hallandale Beach

Hallandale, Florida, United States

Site Status

Westside Center for Clinical Research

Jacksonville, Florida, United States

Site Status

Accel Research Sites - Tampa

Largo, Florida, United States

Site Status

Accel Research Sites - Maitland

Maitland, Florida, United States

Site Status

Suncoast Research Associates

Miami, Florida, United States

Site Status

Synexus - Orlando

Orlando, Florida, United States

Site Status

Synexus - The Villages

The Villages, Florida, United States

Site Status

Accel Research Sites - Neurostudies

Decatur, Georgia, United States

Site Status

Velocity Clinical Research - Boise (Advanced Clinical Research)

Meridian, Idaho, United States

Site Status

Healthcare Research Network - Chicago

Flossmoor, Illinois, United States

Site Status

Synexus Clinical Research - Evansville

Evansville, Indiana, United States

Site Status

AMR El Dorado

El Dorado, Kansas, United States

Site Status

AMR Newton

Newton, Kansas, United States

Site Status

AMR Wichita East, KS

Wichita, Kansas, United States

Site Status

Clinical Trials of America, LLC

Monroe, Louisiana, United States

Site Status

Brigham and Women's Hospital (BWH) - Translational Pain Research

Boston, Massachusetts, United States

Site Status

Boston Neuro Research Center, LLC

North Dartmouth, Massachusetts, United States

Site Status

Boston PainCare Center

Waltham, Massachusetts, United States

Site Status

Revival Research Institute

Dearborn, Michigan, United States

Site Status

StudyMetrix Research, LLC

City of Saint Peters, Missouri, United States

Site Status

Healthcare Research Network - Hazelwood

Hazelwood, Missouri, United States

Site Status

AMR Kansas City

Kansas City, Missouri, United States

Site Status

Synexus Clinical Research US - St. Louis

St Louis, Missouri, United States

Site Status

Synexus Clinical Research - Henderson

Henderson, Nevada, United States

Site Status

Hassman Research Institute

Berlin, New Jersey, United States

Site Status

Synexus Clinical Research- New York

New York, New York, United States

Site Status

Carolina Institute for Clinical Research

Fayetteville, North Carolina, United States

Site Status

Triad Clinical Trials

Greensboro, North Carolina, United States

Site Status

The Center for Clinical Research

Winston-Salem, North Carolina, United States

Site Status

Synexus - Cincinnati

Cincinnati, Ohio, United States

Site Status

Velocity Clinical Research - Cleveland

Cleveland, Ohio, United States

Site Status

Velocity Clinical Research - Medford

Medford, Oregon, United States

Site Status

Velocity Clinical Research - Providence

East Greenwich, Rhode Island, United States

Site Status

Synexus Clinical Research- Anderson

Anderson, South Carolina, United States

Site Status

Clinical Trials of South Carolina - Charleston

Charleston, South Carolina, United States

Site Status

South Carolina Clinical Research

Orangeburg, South Carolina, United States

Site Status

Inquest Clinical Research

Baytown, Texas, United States

Site Status

Synexus - Dallas

Dallas, Texas, United States

Site Status

Diabetes & Glandular Disease Clinic, P.A

San Antonio, Texas, United States

Site Status

Wasatch Clinical Research

Salt Lake City, Utah, United States

Site Status

Northwest Clinical Research Center (NWCRC)

Bellevue, Washington, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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VX21-548-103

Identifier Type: -

Identifier Source: org_study_id

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