A Randomized Study of XEN1101 Versus Placebo in Focal-Onset Seizures

NCT ID: NCT05614063

Last Updated: 2025-12-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

360 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-11-18

Study Completion Date

2026-02-28

Brief Summary

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The X-TOLE2 Phase 3 clinical trial is a randomized, double-blind, placebo-controlled study that will evaluate the clinical efficacy, safety and tolerability of XEN1101 administered as adjunctive therapy in focal-onset seizures.

Detailed Description

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Approximately 360 subjects will be randomized in a blinded manner to one of two active treatment groups or placebo in a 1:1:1 fashion (XEN1101 25 mg : 15 mg : Placebo). Eligible subjects will have up to 9.5 weeks of baseline to assess frequency of seizures, followed by 12 weeks of blinded treatment. In order to be included in the study, subjects must be treated with a stable dose of 1 to 3 allowable antiseizure medications (ASMs) for at least one month prior to screening, during baseline, and throughout the double-blind treatment period (DBP) of the study. During the DBP, subjects will be instructed to orally take XEN1101 or placebo once daily with an evening meal.

Subjects who complete the 12-week DBP will have the opportunity to qualify and enroll in a separate open-label extension (OLE) study for continued treatment with XEN1101. Subjects who do not enroll in the OLE will enter a 8-week post treatment follow-up period.

Conditions

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Focal Onset Seizures

Keywords

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Epilepsy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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XEN1101 25 mg/day

XEN1101 25 mg/day

Group Type EXPERIMENTAL

XEN1101

Intervention Type DRUG

XEN1101 Capsules

XEN1101 15 mg/day

XEN1101 15 mg/day

Group Type EXPERIMENTAL

XEN1101

Intervention Type DRUG

XEN1101 Capsules

Placebo

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo Capsules

Interventions

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XEN1101

XEN1101 Capsules

Intervention Type DRUG

Placebo

Placebo Capsules

Intervention Type DRUG

Other Intervention Names

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Azetukalner

Eligibility Criteria

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Inclusion Criteria

* Be properly informed of the nature and risks of the study and give informed consent in writing, prior to entering the study
* Diagnosis (≥2 years) of focal epilepsy according to the International League Against Epilepsy (ILAE) Classification of Epilepsy (2017). Subject must have had adequate trials of at least 2 ASMs, which were given (and tolerated) at adequate therapeutic doses, without achieving sustained seizure freedom.
* Treatment with a stable dose of 1 to 3 allowable current ASMs for at least one month prior to screening, during baseline, and throughout the duration of the DBP
* Able to keep accurate seizure diaries

Exclusion Criteria

* Previously documented electroencephalogram which shows any pattern not consistent with focal etiology of seizures.
* History of focal aware non-motor seizures only, non-epileptic psychogenic seizure, primary generalized seizure, developmental and epileptic encephalopathy, including Lennox-Gastaut syndrome.
* Seizures secondary to drug or alcohol use, ongoing infection, neoplasia, demyelinating disease, degenerative neurological disease, metabolic illness, progressive structural lesion, encephalopathy, or progressive central nervous system (CNS) disease.
* History of status epilepticus or repetitive seizures within the 12-month period preceding Visit 1 where the individual seizures cannot be counted.
* History of neurosurgery for seizures \<1 year prior to Visit 1, or radiosurgery \<2 years prior to enrollment.
* Any medical condition or personal circumstance that, in the opinion of the investigator, exposes the subject to unacceptable risk by participating in the study or prevents adherence to the protocol.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Worldwide Clinical Trials

OTHER

Sponsor Role collaborator

Xenon Pharmaceuticals Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Xenon Pharmaceuticals Inc.

Locations

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Strada Patient Care Center

Mobile, Alabama, United States

Site Status

Xenoscience

Phoenix, Arizona, United States

Site Status

University of Arizona, Health Sciences Center

Tucson, Arizona, United States

Site Status

Clinical Trials, Inc

Little Rock, Arkansas, United States

Site Status

Brain Science Research Institute

Los Angeles, California, United States

Site Status

University of California, David Clinical & Translational Science Center Clinical Research (CCRC)

Sacramento, California, United States

Site Status

Anschutz Health Sciences

Aurora, Colorado, United States

Site Status

Floridian Community Research Center

Coral Gables, Florida, United States

Site Status

Serenity Research

Miami, Florida, United States

Site Status

Research Institute of Orlando, LLC

Orlando, Florida, United States

Site Status

Panhandle Research & Medical Clinic

Pensacola, Florida, United States

Site Status

Medsol Clinical Research Center

Port Charlotte, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Encore Medical Research of Weston, LLC

Weston, Florida, United States

Site Status

Emory Brain Health Center

Atlanta, Georgia, United States

Site Status

Hawaii Pacific Neuroscience

Honolulu, Hawaii, United States

Site Status

Consultants in Epilepsy and Neurology

Boise, Idaho, United States

Site Status

Indiana University, IU Health Partners, Adult Neurology Clinic

Indianapolis, Indiana, United States

Site Status

The University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Bluegrass Epilepsy Research, LLC

Lexington, Kentucky, United States

Site Status

University of Kentucky, Dept. of Neurology

Lexington, Kentucky, United States

Site Status

MaineHealth Neurology - Scarborough

Scarborough, Maine, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Mid-Atlantic Epilepsy and Sleep Center

Bethesda, Maryland, United States

Site Status

MedStar Health Research Institute

Clinton, Maryland, United States

Site Status

Medstar Health Research Institute

Hyattsville, Maryland, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

UMass Memorial Medical Center

Worcester, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Michigan State University

East Lansing, Michigan, United States

Site Status

Cornwell Health

Grand Rapids, Michigan, United States

Site Status

Minneapolis Clinic of Neurology

Burnsville, Minnesota, United States

Site Status

Saint Louis University Medical School - Neurosciences Clinical Research Unit

St Louis, Missouri, United States

Site Status

Washington University, St. Louis

St Louis, Missouri, United States

Site Status

Northeast Epilepsy Group

Hackensack, New Jersey, United States

Site Status

Dent Neurosciences Research Center

Buffalo, New York, United States

Site Status

NYU Comprehensive Epilepsy Center (CEC)

New York, New York, United States

Site Status

Weill Cornell Medicine/ New York-Presbyterian Hospital

New York, New York, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Onsite Clinical Solutions, LLC

Charlotte, North Carolina, United States

Site Status

Duke Neurology

Durham, North Carolina, United States

Site Status

Meridian Clinical Research, LLC

Raleigh, North Carolina, United States

Site Status

Wake Forest Baptist Health

Winston-Salem, North Carolina, United States

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Summa Health

Akron, Ohio, United States

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Providence Brain & Spine Institute

Portland, Oregon, United States

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Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Temple University Hospital

Philadelphia, Pennsylvania, United States

Site Status

Austin Epilepsy Care Center (AECC)

Austin, Texas, United States

Site Status

ANESC Research

El Paso, Texas, United States

Site Status

UT Physicians Epilepsy Clinic

Houston, Texas, United States

Site Status

UT Health San Antonio

San Antonio, Texas, United States

Site Status

Carilion Clinic - Neurology

Roanoke, Virginia, United States

Site Status

Sentara Neurology Specialists

Virginia Beach, Virginia, United States

Site Status

University of Washington Main Hospital

Seattle, Washington, United States

Site Status

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, United States

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INECO and Favoloro Fundation

Buenos Aires, , Argentina

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Hospital General de Agudos J.M. Ramos Mejia

Buenos Aires, , Argentina

Site Status

Hospital De Alta Complejidad en Red el Cruce Nestor Kirchner - SAMIC

Buenos Aires, , Argentina

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STAT Research S.A.

Buenos Aires, , Argentina

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Hospital Italiano

Buenos Aires, , Argentina

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CENyR

Caba, , Argentina

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Hospital Córdoba

Córdoba, , Argentina

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Sanatorio del Sur S.A.

San Miguel de Tucumán, , Argentina

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St Vincent's Hospital Melbourne

Fitzroy, Melbourne, Australia

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The Royal Melbourne Hospital

Melbourne, Melbourne, Australia

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Royal Prince Alfred Hospital (RAPH)

Camperdown, New South Wales, Australia

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Prince of Wales Hospital

Sydney, New South Wales, Australia

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Southern Neurology

Sydney, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

The University of Queensland (UQ) - Mater Research Institute (MRI)

Brisbane, Queensland, Australia

Site Status

Austin Health Pharmacy Clinical Trials

Heidelberg, Victoria, Australia

Site Status

The Alfred Hospital (Alfred Health)

Melbourne, Victoria, Australia

Site Status

MHAT Puls AD

Blagoevgrad, , Bulgaria

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Center For Neurologic Research

Lethbridge, Alberta, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Le Centre Hospitalier de l'Universite' de Montreal (CHUM)

Montreal, Quebec, Canada

Site Status

Centro de investigación Clinica UC

Santiago, , Chile

Site Status

Hospital Clínico Vina del Mar

Viña del Mar, , Chile

Site Status

FORBELI s.r.o., Neurologicka ambulance

Prague, , Czechia

Site Status

American Hospital Network LLC

Tbilisi, , Georgia

Site Status

Institute of Neurology and Neuropsychology

Tbilisi, , Georgia

Site Status

Epilepsy Center Bethel

Bielefeld, , Germany

Site Status

Universitatsklinikum Bonn

Bonn, , Germany

Site Status

Epilepsiezentrum Frankfurt Rhein-Main

Frankfurt, , Germany

Site Status

University Medical Center Freiburg

Freiburg im Breisgau, , Germany

Site Status

Philipps-Universität Marburg

Marburg, , Germany

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LMU Munich, Department of Neurology

Munich, , Germany

Site Status

Universitätsklinikum Tübingen

Tübingen, , Germany

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Universitatsklinik fur neurologie, universitats - und Rehabilitationskliniken Ulm

Ulm, , Germany

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Beaumont Hospital

Dublin, , Ireland

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Istituto delle Scienze Neurologiche di Bologna

Bologna, , Italy

Site Status

Università Degli Studi Gabriele d'Annunzio Di Chieti

Pescara, , Italy

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Azienda Ospedaliero Universitaria Pisana

Pisa, , Italy

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Ospedale Pediatrico Bambino Gesu

Roma, , Italy

Site Status

Azienda Ospedaliero-Universitaria Policlinico Umberto I

Rome, , Italy

Site Status

Pauls Stradina Clinical university hospital

Riga, , Latvia

Site Status

Riga East University Hospital

Riga, , Latvia

Site Status

Human Science Research Trials S. de R.L. de C.V.

Mexico City, , Mexico

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Neurocencias Esudios Clinicos SC

Sinaloa, , Mexico

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University of Auckland

Auckland, , New Zealand

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Waikato Hospital

Hamilton, , New Zealand

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Centrum Medyczne Neuromed

Bydgoszcz, , Poland

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NZOZ Novo-Med

Katowice, , Poland

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Twoja Przychodnia NCM

Nowa Sól, , Poland

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Neurosphera Sp. z o.o.

Warsaw, , Poland

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Unidade Local de Saúde de São João

Porto, , Portugal

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Hospital Pedro Hispano

Porto, , Portugal

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Centro Hospitalar de Entre o Douro e Vouga

Santa Maria da Feira, , Portugal

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Unitat d'Assaigs Clínics. Servei de Farmàcia

Barcelona, , Spain

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Hospital Ramón y Cajal

Madrid, , Spain

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Hospital Ruber Internacional

Madrid, , Spain

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Hospital Vithas La Milagrosa

Madrid, , Spain

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Hospital Clinico San Carlos

Madrid, , Spain

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IIS-Fundacion Jimenez Diaz/Farmacia

Madrid, , Spain

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Hospital Universitario 12 de Octubre

Madrid, , Spain

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Hospital Regional De Malaga

Málaga, , Spain

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Hospital Universitario y Politecnico La Fe

Valencia, , Spain

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Hospital Clínico Universitario Valladolid

Valladolid, , Spain

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University Hospitals Birmingham NHS Foundation Trust

Birmingham, , United Kingdom

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University Hospital of Wales

Cardiff, , United Kingdom

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Leeds Teaching Hospitals NHS Trust

Leeds, , United Kingdom

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St. George's Hospital NHS Foundation Trust

London, , United Kingdom

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Royal London Hospital for Integrated Medicine

London, , United Kingdom

Site Status

John Radcliffe Hospital

Oxford, , United Kingdom

Site Status

Northern Care Alliance NHS Foundation Trust, Salford Care Organisation

Salford, , United Kingdom

Site Status

Countries

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United States Argentina Australia Bulgaria Canada Chile Czechia Georgia Germany Ireland Italy Latvia Mexico New Zealand Poland Portugal Spain United Kingdom

Other Identifiers

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2022-502000-73-00

Identifier Type: CTIS

Identifier Source: secondary_id

XPF-010-301

Identifier Type: -

Identifier Source: org_study_id