PROVIDENCE - Prospective Non-interventional Study (NIS) to Examine Patient-reported Outcomes and Real-world Clinical Data in Patients With HER2-positive, HER2-low or HER2-ultralow Unresectable or Metastatic Breast Cancer Treated With Trastuzumab Deruxtecan

NCT ID: NCT05573893

Last Updated: 2025-12-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

800 participants

Study Classification

OBSERVATIONAL

Study Start Date

2023-09-12

Study Completion Date

2031-12-31

Brief Summary

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This is a prospective non-interventional, multicenter study observing patient reported outcomes as well as real-world efficacy and safety of trastuzumab deruxtecan (T-DXd) in patients with documented Human epidermal growth factor receptor 2 (HER2)-positive, HER2-low or HER2-ultralow unresectable or metastatic breast cancer (BC) receiving T-DXd in line with the applicable summary of product characteristics (SmPC) within routine clinical practice in Germany. In addition, patients will be informed about use of digital healthcare application (DiGA).

Detailed Description

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Eligible participants will be those patients with documented HER2-positive, HER2-low or HER2-ultralow unresectable or metastatic BC receiving T-DXd treatment in line with the applicable summary of product characteristics (SmPC) within routine clinical practice.

All diagnostic and treatment procedures including visit frequency are at the discretion of the treating physician and not defined by the protocol. T-DXd treatment is considered as a selection criteria. Patients will be informed about use of digital healthcare application (DiGA).

Approximately 800 eligible participants will be enrolled which includes 400 patients in the HER2-positive cohort and 400 patients in the HER2-low/ HER2-ultralow cohort.

Conditions

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Breast Neoplasms Breast Cancer Neoplasm Metastasis

Keywords

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Trastuzumab-Deruxtecan, Human epidermal growth factor receptor 2 Positive Breast Cancer, Human epidermal growth factor receptor 2 Low Breast Cancer, Human epidermal growth factor receptor 2 Ultralow Breast Cancer,

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Cohort 1

Cohort 1 containing patients with documented HER2-positive unresectable or metastatic BC receiving T-DXd treatment in line with the applicable summary of product characteristics (SmPC) within routine clinical practice.

No interventions assigned to this group

Cohort 2

Cohort 2 containing patients with documented HER2-low or HER2-ultralow unresectable or metastatic BC receiving T-DXd treatment in line with the applicable summary of product characteristics (SmPC) within routine clinical practice.

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

1. Adults ≥ 18 years old
2. Patients (irrespective of sex and gender) with pathologically documented breast cancer that:

* is unresectable or metastatic
* has confirmed HER2+, HER2-low or HER2-ultralow tumor status by local pathology
* was previously treated with one or more anti-HER2 directed therapy if the tumor is HER2+ OR
* was previously treated with at least one endocrine therapy in the metastatic setting and is not considered suitable for endocrine therapy as the next line of treatment if the tumor is HR+, HER2-low or HER2-ultralow OR
* was previously treated with prior chemotherapy in the metastatic setting or developed disease recurrence during or within 6 months of completing adjuvant chemotherapy if the tumor is HER2-low.
3. Has documented radiologic progression (during or after most recent treatment)
4. Patient is eligible for T-DXd treatment in line with the specifications mentioned in the ENHERTU® SmPC and is scheduled for T-DXd treatment \*
5. Patient is able to read and understand either German or English
6. Signed written informed consent

* The prescription of the medicinal product is clearly separated from the decision to include the patient in this NIS.

Exclusion Criteria

1. Start of T-DXd treatment for more than 30 days before enrolment (eCRF registration date)
2. Known hypersensitivity to T-DXd or any of the excipients of the drug
3. Pregnancy or breast feeding
4. Current or planned participation in an interventional clinical trial
5. Current or planned systemic treatment of any tumor other than unresectable or metastatic BC

Patients who have never received any T-DXd dose will be discontinued from the study and will be considered as a late screening failure, no further documentation besides reason and date of discontinuation is needed.
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Daiichi Sankyo

INDUSTRY

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Amberg, , Germany

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Ansbach, , Germany

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Apolda, , Germany

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Aschaffenburg, , Germany

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Augsburg, , Germany

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Augsburg, , Germany

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Bad Reichenhall, , Germany

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Baden-Baden, , Germany

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Balingen, , Germany

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Bamberg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bielefeld, , Germany

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Bonn, , Germany

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Brandenburg, , Germany

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Braunschweig, , Germany

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Bremen, , Germany

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Bremerhaven, , Germany

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Coburg, , Germany

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Dessau, , Germany

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Donauwörth, , Germany

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Dortmund, , Germany

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Dresden, , Germany

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Dresden, , Germany

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Düsseldorf, , Germany

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Eggenfelden, , Germany

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Erfurt, , Germany

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Essen, , Germany

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Filderstadt - Bonlanden, , Germany

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Frankfurt, , Germany

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Freudenstadt, , Germany

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Fürstenfeldbruck, , Germany

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Fürstenwalde, , Germany

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Gerlingen, , Germany

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Giessen, , Germany

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Halle, , Germany

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Hamburg, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Hanover, , Germany

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Heidenheim, , Germany

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Heilbronn, , Germany

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Hildesheim, , Germany

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Homburg/Saar, , Germany

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Jena, , Germany

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Kaiserslautern, , Germany

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Karlsruhe, , Germany

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Kassel, , Germany

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Kassel, , Germany

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Kempten, , Germany

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Kiel, , Germany

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Kulmbach, , Germany

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Landshut, , Germany

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Leer, , Germany

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Leipzig, , Germany

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Loerrach, , Germany

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Lübeck, , Germany

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Lüneburg, , Germany

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Magdeburg, , Germany

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Mainz, , Germany

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Marburg, , Germany

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Memmingen, , Germany

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Mönchengladbach, , Germany

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Mutlangen, , Germany

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Mühlhausen, , Germany

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München, , Germany

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München, , Germany

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München, , Germany

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Neumarkt, , Germany

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Neustadt am Rübenberge, , Germany

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Nordhausen, , Germany

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Nuremberg, , Germany

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Oldenburg, , Germany

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Oranienburg, , Germany

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Potsdam, , Germany

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Recklinghausen, , Germany

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Regensburg, , Germany

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Rosenheim, , Germany

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Rotenburg (Wümme), , Germany

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Saalfeld, , Germany

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Saarbrücken, , Germany

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Salzwedel, , Germany

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Schwäbisch Hall, , Germany

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Siegen, , Germany

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Singen, , Germany

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Solingen, , Germany

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Stade, , Germany

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Stuttgart, , Germany

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Torgau, , Germany

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Troisdorf, , Germany

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Ulm, , Germany

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Walsrode, , Germany

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Weiden, , Germany

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Weinheim, , Germany

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Weisenfels, , Germany

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Westerstede, , Germany

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Wiesbaden, , Germany

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Winnenden, , Germany

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Wolfsburg, , Germany

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Wuppertal, , Germany

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Würzburg, , Germany

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Zittau, , Germany

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Countries

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Germany

Central Contacts

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AstraZeneca Clinical Study Information Center

Role: CONTACT

Phone: 1-877-240-9479

Email: [email protected]

Other Identifiers

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D9673R00028

Identifier Type: -

Identifier Source: org_study_id