DAY101 vs. Standard of Care Chemotherapy in Pediatric Participants With Low-Grade Glioma Requiring First-Line Systemic Therapy (LOGGIC/FIREFLY-2)

NCT ID: NCT05566795

Last Updated: 2025-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

400 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-02-27

Study Completion Date

2030-03-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a 2-arm, randomized, open-label, multicenter, global, Phase 3 trial to evaluate the efficacy, safety, and tolerability of tovorafenib monotherapy versus standard of care (SoC) chemotherapy in participants with pediatric low-grade glioma (LGG) harboring an activating rapidly accelerated fibrosarcoma (RAF) alteration requiring first-line systemic therapy.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Approximately 400 treatment-naïve LGG participants will be randomized 1:1 to either tovorafenib (Arm 1) or an Investigator's choice of SoC chemotherapy (Arm 2).

Arm 1 (tovorafenib): Treatment cycles will repeat every 28 days in the absence of disease progression. Participants will continue tovorafenib until any of the following occurs: disease progression, unacceptable toxicity, withdrawal of consent to treatment, or end of study.

Arm 2 (Investigator's Choice of SoC Chemotherapy): Participants will receive one of 4 SoC chemotherapy options selected by the treating Investigator: Children's Oncology Group - Vincristine/Carboplatin (COG-V/C) regimen, International Society for Paediatric Oncology - Low-Grade Glioma Vincristine/Carboplatin (SIOPe-LGG-V/C) regimen, vinblastine (VBL) regimen, or monthly carboplatin. The choice of SoC chemotherapy regimen will be selected prior to participant randomization. Treatment will continue until completion of therapy or until any of the following occurs: disease progression, unacceptable toxicity, withdrawal of consent to treatment, or end of study.

Participants who discontinue treatment due to disease progression will have (1) radiographic evidence of disease progression, as determined by the Investigator, or (2) clinical progression, as determined by the Investigator. Investigators are encouraged to discuss cases of clinical progression and early radiographic progression without clinical symptoms with the Sponsor Medical Monitor prior to treatment discontinuation or initiation of a different form of treatment for the malignancy. Participants may continue therapy beyond progressive disease (PD).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Low-grade Glioma Rapidly Accelerated Fibrosarcoma (RAF) Altered Glioma Pediatric Low-grade Glioma

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Rapidly accelerated fibrosarcoma RAF alteration glioma Glioneural tumor Ojemda

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Tovorafenib versus standard of care chemotherapy
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Tovorafenib

Group Type EXPERIMENTAL

Tovorafenib

Intervention Type DRUG

Oral Tablet Powder for Oral Suspension

Investigator's choice of Standard of care therapy

Group Type ACTIVE_COMPARATOR

Chemotherapeutic Agent

Intervention Type DRUG

Intravenous solution for injection

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Tovorafenib

Oral Tablet Powder for Oral Suspension

Intervention Type DRUG

Chemotherapeutic Agent

Intravenous solution for injection

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

DAY101, Ojemda COG-V/C SIOPe-LGG-V/C VBL Carboplatin

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Less than 25 years of age with LGG with known activating RAF alteration.
* Histopathologic diagnosis of glioma or glioneuronal tumor.
* At least one measurable lesion as defined by RANO criteria.
* Meet indication for first-line systemic therapy.

Exclusion Criteria

* Participant has any of the following tumor-histological findings:

1. Schwannoma
2. Subependymal giant cell astrocytoma (Tuberous Sclerosis)
3. Diffuse intrinsic pontine glioma, even if histologically diagnosed as World Health Organization (WHO) Grade I-II
* Participant's tumor has additional pathogenic molecular alterations, including but not limited to a) isocitrate dehydrogenase (IDH) 1/2 mutation, b) Histone H3 mutation, and c) neurofibromatosis Type 1 (NF-1) loss of function alteration.
* Known or suspected diagnosis of NF-1/ neurofibromatosis Type 2 (NF-2).
* Prior or ongoing nonsurgical anticancer therapy for this indication (eg, chemotherapy, oral/IV targeted therapy) including radiation.
Maximum Eligible Age

25 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

SIOPe Brain Tumor Group LOGGIC Consortium

UNKNOWN

Sponsor Role collaborator

Day One Biopharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Children's of Alabama

Birmingham, Alabama, United States

Site Status RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

Children's Hospital Los Angeles

Los Angeles, California, United States

Site Status RECRUITING

Children's Hospital of Orange County Main Campus - Orange

Orange, California, United States

Site Status RECRUITING

Packard Children's Hospital Stanford

Palo Alto, California, United States

Site Status RECRUITING

UCSF Benioff Children's Hospital

San Francisco, California, United States

Site Status RECRUITING

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status RECRUITING

Connecticut Children's Medical Center

Hartford, Connecticut, United States

Site Status RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

University of Florida Health

Gainesville, Florida, United States

Site Status RECRUITING

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status RECRUITING

Arnold Palmer Hospital for Children

Orlando, Florida, United States

Site Status RECRUITING

Johns Hopkins All Children's Hospital

St. Petersburg, Florida, United States

Site Status RECRUITING

Children's Healthcare of Atlanta

Atlanta, Georgia, United States

Site Status RECRUITING

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

University of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Riley Hospital for Children at Indiana University Health

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Iowa Hospitals Clinics

Iowa City, Iowa, United States

Site Status RECRUITING

Norton Children's Hospital

Louisville, Kentucky, United States

Site Status RECRUITING

Maine Children's Cancer Program

Scarborough, Maine, United States

Site Status RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

University of Michigan - - C.S. Mott Children's Hospital

Ann Arbor, Michigan, United States

Site Status RECRUITING

Children's Minnesota

Minneapolis, Minnesota, United States

Site Status RECRUITING

Childrens MS Cncr Ctr Bld Dsr

Jackson, Mississippi, United States

Site Status RECRUITING

St. Louis Children's Hospital

St Louis, Missouri, United States

Site Status RECRUITING

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

Albany Medical Center

Albany, New York, United States

Site Status RECRUITING

New York University Langone Health

New York, New York, United States

Site Status RECRUITING

Columbia University

New York, New York, United States

Site Status RECRUITING

University of Rochester

Rochester, New York, United States

Site Status RECRUITING

Duke Cancer Institute

Durham, North Carolina, United States

Site Status RECRUITING

Cleveland Clinic Main Campus

Cleveland, Ohio, United States

Site Status RECRUITING

Oregon Health Science University

Portland, Oregon, United States

Site Status RECRUITING

Dell Children's Medical Center of Central Texas

Austin, Texas, United States

Site Status RECRUITING

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status RECRUITING

Texas Children's Hospital

Houston, Texas, United States

Site Status RECRUITING

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

University of Wisconsin - Madison

Madison, Wisconsin, United States

Site Status RECRUITING

Children's Health Queensland Hospital and Health Service

South Brisbane, Queensland, Australia

Site Status RECRUITING

Perth Children's Hospital

Nedlands, , Australia

Site Status RECRUITING

Women's and Children's Health Network

North Adelaide, , Australia

Site Status RECRUITING

The Royal Children's Hospital - Children's Cancer Centre

Parkville, , Australia

Site Status RECRUITING

Sydney Children's Hospital - Randwick

Randwick, , Australia

Site Status RECRUITING

Children's Hospital at Westmead

Westmead, , Australia

Site Status RECRUITING

Medizinische Universität Innsbruck

Innsbruck, Tyrol, Austria

Site Status RECRUITING

Medizinische Universität Wien

Vienna, , Austria

Site Status RECRUITING

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status RECRUITING

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status RECRUITING

Universitair Ziekenhuis Leuven - Campus Gasthuisberg

Leuven, , Belgium

Site Status RECRUITING

Grupo de Apoio ao Adolescente e à Criança com Câncer (GRAACC)

São Paulo, , Brazil

Site Status RECRUITING

Alberta Children's Hospital

Calgary, Alberta, Canada

Site Status RECRUITING

Stollery Children's Hospital

Edmonton, Alberta, Canada

Site Status RECRUITING

British Columbia Children's Hospital

Vancouver, British Columbia, Canada

Site Status RECRUITING

McMaster Children's Hospital

Hamilton, Ontario, Canada

Site Status RECRUITING

Children's Hospital London Health Sciences Centre

London, Ontario, Canada

Site Status RECRUITING

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

Site Status RECRUITING

CHU Sainte-Justine

Montreal, Quebec, Canada

Site Status RECRUITING

The Montreal Children's Hospital

Montreal, Quebec, Canada

Site Status RECRUITING

Centre Hospitalier de l'Université Laval et Centre Mère-Enfant Soleil

Québec, , Canada

Site Status RECRUITING

SickKids - The Hospital for Sick Children

Toronto, , Canada

Site Status RECRUITING

Fakultní Nemocnice Brno - D?tská Nemocnice

Brno, , Czechia

Site Status RECRUITING

Motol University Hospital

Prague, , Czechia

Site Status RECRUITING

Aarhus Universitetshospital

Aarhus, Central Jutland, Denmark

Site Status RECRUITING

Rigshospitalet

Copenhagen, , Denmark

Site Status RECRUITING

CCHE

Cairo, Cairo Governorate, Egypt

Site Status RECRUITING

Helsingin yliopistollinen sairaala (HUS)

Helsinki, , Finland

Site Status RECRUITING

Tampereen Yliopistollinen Sairaala

Tampere, , Finland

Site Status RECRUITING

Centre de Lutte contre le Cancer - Centre Oscar Lambret

Lille, , France

Site Status RECRUITING

Centre Léon Bérard

Lyon, , France

Site Status RECRUITING

Hôpital de la Timone

Marseille, , France

Site Status RECRUITING

Institut Curie

Paris, , France

Site Status RECRUITING

Gustave Roussy

Villejuif, , France

Site Status RECRUITING

Universitätsklinikum Freiburg

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status RECRUITING

Universitätsklinikum Augsburg

Augsburg, Bavaria, Germany

Site Status RECRUITING

Universitätsklinikum Erlangen

Erlangen, Bavaria, Germany

Site Status RECRUITING

Universitätsklinikum Würzburg

Würzburg, Bavaria, Germany

Site Status RECRUITING

Universitätsklinikum Frankfurt

Frankfurt am Main, Hesse, Germany

Site Status RECRUITING

Medizinische Hochschule Hannover

Hanover, Lower Saxony, Germany

Site Status RECRUITING

Universitaetsklinikum Essen

Essen, North Rhine-Westphalia, Germany

Site Status RECRUITING

Universitätsklinikum Leipzig

Leipzig, Saxony, Germany

Site Status RECRUITING

Charité Universitätsmedizin Berlin

Berlin, , Germany

Site Status RECRUITING

Evangelische Klinikum Bethel (EvKB)

Bielefeld, , Germany

Site Status RECRUITING

Universitätsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status RECRUITING

Universitätsklinikum Heidelberg

Heidelberg, , Germany

Site Status RECRUITING

Universitätsklinikum Tübingen

Tübingen, , Germany

Site Status RECRUITING

Aghia Sofia General Children's Hospital

Athens, , Greece

Site Status RECRUITING

Athens General Children's Hospital

Athens, , Greece

Site Status RECRUITING

Semmelweis Egyetem Tűzoltó utcai II. Sz. Gyermekgyógyászati Kliniká

Budapest, , Hungary

Site Status RECRUITING

Children's Health Ireland at Crumlin

Crumlin, Dublin, Ireland

Site Status RECRUITING

Schneider Children's Medical Center of Israel

Petah Tikva, , Israel

Site Status RECRUITING

The Edmond and Lily Safra Children's Hospital

Ramat Gan, , Israel

Site Status RECRUITING

Fondazione IRCCS - Istituto Nazionale dei Tumori

Milan, Milan, Italy

Site Status RECRUITING

Ospedale Pediatrico Bambino Gesù

Roma, Rome, Italy

Site Status RECRUITING

Ospedale Infantile Regina Margherita

Torino, Turin, Italy

Site Status RECRUITING

Azienda Universitaria Ospedaliera Consorziale - Policlinico di Bari

Bari, , Italy

Site Status RECRUITING

Azienda Ospedaliera U. Meyer

Florence, , Italy

Site Status RECRUITING

Istituto Giannina Gaslini

Genova, , Italy

Site Status RECRUITING

Azienda Ospedaliera di Rilievo Nazional Santobono Pausilipon

Napoli, , Italy

Site Status RECRUITING

Azienda Ospedale Università di Padova

Padua, , Italy

Site Status RECRUITING

Azienda Sanitaria Universitaria Friuli Centrale - P.O. Santa Maria della Misericordia

Udine, , Italy

Site Status RECRUITING

King Hussein Cancer Foundation - King Hussein Cancer Center

Amman, Muhafazat al-Asima, Jordan

Site Status RECRUITING

Prinses Maxima Centrum Kinderoncologie

Utrecht, , Netherlands

Site Status RECRUITING

Starship Paediatric Blood & Cancer Center

Grafton, , New Zealand

Site Status RECRUITING

Universitetssykehuset Nord-Norge - Tromsø

Tromsø, Troms, Norway

Site Status RECRUITING

Oslo Universitetssykehus

Oslo, , Norway

Site Status RECRUITING

Sidra Medicine

Doha, , Qatar

Site Status RECRUITING

SingHealth Group - KK Women's and Children's Hospital

Singapore, , Singapore

Site Status RECRUITING

Univerzitetni Klinini Center Ljubljana

Ljubljana, , Slovenia

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status RECRUITING

Severance Hospital

Seoul, , South Korea

Site Status RECRUITING

Hospital Universitario Cruces

Barakaldo, , Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebrón

Barcelona, , Spain

Site Status RECRUITING

Hospital Sant Joan de Déu Barcelona

Barcelona, , Spain

Site Status RECRUITING

Hospital Infantil Universitario Niño Jesús

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocío

Seville, , Spain

Site Status RECRUITING

Hospital Universitari i Politècnic La Fe

Valencia, , Spain

Site Status RECRUITING

Drottning Silvias barn- och ungdomssjukhus

Gothenburg, , Sweden

Site Status RECRUITING

Skånes Universitetssjukhus - Lund

Lund, , Sweden

Site Status RECRUITING

Astrid Lindgrens Barnsjukhus Solna

Stockholm, , Sweden

Site Status RECRUITING

Centre Hospitalier Universitaire Vaudois Lausanne

Lausanne, , Switzerland

Site Status RECRUITING

Universitaets - Kinderspital Zürich

Zurich, , Switzerland

Site Status RECRUITING

Taipei Medical University Hospital

Taipei, , Taiwan

Site Status RECRUITING

Chang Gung Memorial Hospital - Linkou Branch

Taoyuan District, , Taiwan

Site Status RECRUITING

Birmingham Women's and Children's NHS Foundation Trust

Birmingham, England, United Kingdom

Site Status RECRUITING

Leeds Teaching Hospital NHS Trust

Leeds, England, United Kingdom

Site Status RECRUITING

Alder Hey Children's NHS Foundation Trust

Liverpool, England, United Kingdom

Site Status RECRUITING

Manchester University NHS Foundation Trust

Manchester, England, United Kingdom

Site Status RECRUITING

The Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, England, United Kingdom

Site Status RECRUITING

Great Ormond Street Hospital for Children

Oxford, England, United Kingdom

Site Status RECRUITING

University Hospital Southampton NHS Foundation Trust

Southampton, Hampshire, United Kingdom

Site Status RECRUITING

Royal Belfast Hospital for Sick Children

Belfast, Northern Ireland, United Kingdom

Site Status RECRUITING

NHS Greater Glasgow and Clyde

Glasgow, Scotland, United Kingdom

Site Status RECRUITING

Sheffield Children's Hospital

Sheffield, South Yorkshire, United Kingdom

Site Status RECRUITING

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, United Kingdom

Site Status RECRUITING

University Hospitals Bristol and Weston NHS Foundation Trust

Bristol, , United Kingdom

Site Status RECRUITING

Cambridge University Hospitals NHS Foundation Trust

Cambridge, , United Kingdom

Site Status RECRUITING

The Christie Hospital

Manchester, , United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Austria Belgium Brazil Canada Czechia Denmark Egypt Finland France Germany Greece Hungary Ireland Israel Italy Jordan Netherlands New Zealand Norway Qatar Singapore Slovenia South Korea Spain Sweden Switzerland Taiwan United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Day One Clinical Trials Information

Role: CONTACT

Phone: 650-484-0899

Email: [email protected]

References

Explore related publications, articles, or registry entries linked to this study.

van Tilburg CM, Kilburn LB, Perreault S, Schmidt R, Azizi AA, Cruz-Martinez O, Zapotocky M, Scheinemann K, Meeteren AYNS, Sehested A, Opocher E, Driever PH, Avula S, Ziegler DS, Capper D, Koch A, Sahm F, Qiu J, Tsao LP, Blackman SC, Manley P, Milde T, Witt R, Jones DTW, Hargrave D, Witt O. LOGGIC/FIREFLY-2: a phase 3, randomized trial of tovorafenib vs. chemotherapy in pediatric and young adult patients with newly diagnosed low-grade glioma harboring an activating RAF alteration. BMC Cancer. 2024 Jan 30;24(1):147. doi: 10.1186/s12885-024-11820-x.

Reference Type DERIVED
PMID: 38291372 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2022-001363-27

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

DAY101-002

Identifier Type: -

Identifier Source: org_study_id