A Study of LY3819469 in Participants With Elevated Lipoprotein(a) [Lp(a)]

NCT ID: NCT05565742

Last Updated: 2025-05-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

320 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-10-20

Study Completion Date

2024-10-17

Brief Summary

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The main purpose of this study is to determine the efficacy and safety of LY3819469 in adults with elevated lipoprotein(a). The study will lasts about 20 months.

Detailed Description

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Conditions

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Lipoprotein Disorder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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16 mg LY3819469

Participants received 16 milligrams (mg) of LY3819469 on day 1 and day 180, administered as a subcutaneous (SC) injection.

Group Type EXPERIMENTAL

LY3819469

Intervention Type DRUG

Administered SC

96 mg LY3819469

Participants received 96 mg of LY3819469 on day 1 and day 180, administered as a SC injection.

Group Type EXPERIMENTAL

LY3819469

Intervention Type DRUG

Administered SC

400 mg LY3819469

Participants received 400 mg of LY3819469 on day 1 and day 180, administered as a SC injection.

Group Type EXPERIMENTAL

LY3819469

Intervention Type DRUG

Administered SC

400 mg LY3819469 + Placebo

Participants received 400 mg of LY3819469 on day 1 and placebo on day 180, administered as a SC injection.

Group Type EXPERIMENTAL

LY3819469

Intervention Type DRUG

Administered SC

Placebo

Intervention Type DRUG

Administered SC

Placebo

Participants received placebo on day 1 and day 180, administered as a SC injection.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered SC

Interventions

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LY3819469

Administered SC

Intervention Type DRUG

Placebo

Administered SC

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participants must be at least 40 years old at the time of signing the informed consent.
* Participants with Lp(a) ≥175 nmol/L at screening, measured at the central laboratory
* Participants on the following medications according to local practice must be on a stable regimen for at least 4 weeks prior to screening and randomization and expected to remain on a stable regimen through the end of the Treatment and Assessment Period:

* lipid-lowering drugs
* testosterone, estrogens, anti-estrogens, progestins, selective estrogen receptor modulators, or growth hormone
* Have a body mass index within the range 18.5 to 40 kilogram/square meter (kg/m²), inclusive.

Male and/or Female

* Males who agree to use highly effective/effective methods of contraception may participate in this trial.
* Women not of childbearing potential (WNOCBP) may participate in this trial.

Exclusion Criteria

* Have a history or presence of an underlying disease, or surgical, physical, medical, or psychiatric condition that, in the opinion of the investigator, would potentially affect participant safety within the study or interfere with participating in or completing the study or with the interpretation of data.
* Any of the following, or other events indicating unstable medical condition in the opinion of the investigator, within 3 months of randomization:

* major surgery
* coronary, carotid, or peripheral arterial revascularization
* stroke or transient ischemic attack
* myocardial infarction or unstable angina
* acute limb ischemia
* Have, in the 6 months prior to day 1, uncontrolled Type 1 or Type 2 diabetes.
* Have uncontrolled hypertension
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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Care Access - 801 South Power Road, Mesa

Mesa, Arizona, United States

Site Status

Care Access - South Pasadena

Pasadena, California, United States

Site Status

Care Access - Santa Clarita

Santa Clarita, California, United States

Site Status

Care Access - Spring Hill

Spring Hill, Florida, United States

Site Status

Care Access - Pebble Beach Boulevard, Tampa

Sun City, Florida, United States

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Care Access - Tamarac

Tamarac, Florida, United States

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Care Access - Tampa

Tampa, Florida, United States

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Care Access - Lake Charles

Lake Charles, Louisiana, United States

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Care Access - Baltimore

Baltimore, Maryland, United States

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Care Access - Dorchester

Dorchester, Massachusetts, United States

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Aventiv Research Inc

Columbus, Ohio, United States

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Care Access - Lima

Lima, Ohio, United States

Site Status

Capital Area Research, LLC

Camp Hill, Pennsylvania, United States

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Lancaster General Hospital

Lancaster, Pennsylvania, United States

Site Status

Cardiology Consultants of Philadelphia Yardley

Yardley, Pennsylvania, United States

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Care Access - Rapid City

Rapid City, South Dakota, United States

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Care Access - Georgetown

Georgetown, Texas, United States

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Care Access - Katy

Katy, Texas, United States

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Virginia Heart

Falls Church, Virginia, United States

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Mautalen Salud e Investigación

Buenos Aires, Buenos Aires F.D., Argentina

Site Status

Centro de Investigaciones Metabólicas (CINME)

Ciudad Autónoma de Buenos Aire, Buenos Air, Argentina

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Glenny Corp. S.A.

Buenos Aires, Ciudad Aut, Argentina

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Investigaciones Medicas Imoba Srl

Balvanera, Ciudad Autónoma de Buenos Aire, Argentina

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CIPREC

Buenos Aires, Ciudad Autónoma de Buenos Aire, Argentina

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Centro Modelo de Cardiología

San Miguel de Tucumán, Tucumán Province, Argentina

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Investigaciones Clínicas Tucumán

San Miguel de Tucumán, Tucumán Province, Argentina

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CEMEDIC

Buenos Aires, , Argentina

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Hospital San Roque

Córdoba, , Argentina

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Centro Cardiovascular Salta

Salta, , Argentina

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Centro de Investigaciones Clinicas del Litoral

Santa Fe, , Argentina

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Third People's Hospital of Hainan Province

Sanya, Hainan, China

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The Second Affiliated Hospital of Nanjing Medical University

Nanjing, Jiangsu, China

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The Third Hospital of Nanchang

Nanchang, Jiangxi, China

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The First Affiliated Hospital of Xi'an Jiaotong University

Xi'an, Shaanxi, China

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Sanos Clinic

Herlev, Capital Region, Denmark

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Sanos Clinic - Nordjylland

Gandrup, North Denmark, Denmark

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Sanos Clinic - Syddanmark

Vejle, Region Syddanmark, Denmark

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Kardiologische Praxis Dr. med. univ. Wolfgang Jungmair

Bad Homburg, Hesse, Germany

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Cardioangiologisches Centrum Bethanien

Frankfurt am Main, Hesse, Germany

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Klinikum Bielefeld Mitte

Bielefeld, North Rhine-Westphalia, Germany

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SMO.MD GmbH

Magdeburg, Saxony-Anhalt, Germany

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Medizinisches Versorgungszentrum am Bahnhof Spandau

Spandau, State of Berlin, Germany

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Kardiologische Praxen im Spreebogen

Berlin, , Germany

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Cardiologicum Hamburg

Hamburg, , Germany

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Diabeteszentrum Hamburg West

Hamburg, , Germany

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Sapporo Medical University Hospital

Sapporo, Hokkaido, Japan

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Hyogo Medical University Hospital

Nishinomiya, Hyōgo, Japan

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Kitasato University Hospital

Sagamihara, Kanagawa, Japan

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Rinku General Medical Center

Izumisano, Osaka, Japan

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Tokyo-Eki Center-building Clinic

Chuo-ku, Tokyo, Japan

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Clinical Research Hospital Tokyo

Shinjuku-ku, Tokyo, Japan

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Heishinkai Medical Group ToCROM Clinic

Shinjuku-ku, Tokyo, Japan

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Miyazaki Medical Association Hospital

Miyazaki, , Japan

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AMC Nishiumeda Clinic

Osaka, , Japan

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Centro de Investigacion Cardiovascular y Metabólica

Tijuana, Estado de Baja California, Mexico

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Virgen Cardiovascular Research SC

Guadalajara, Jalisco, Mexico

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Centro Para El Desarrollo de La Medicina Y de Asistencia Medica Especializada S.C.

Culiacán, Sinaloa, Mexico

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Fundación Cardiovascular de Aguascalientes A.C.

Aguascalientes, , Mexico

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Centro de Estudios Clínicos de Querétaro (CECLIQ)

Querétaro, , Mexico

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Amphia Ziekenhuis, locatie Breda Molengracht

Breda, North Brabant, Netherlands

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Medisch Spectrum Twente

Enschede, Overijssel, Netherlands

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Saxenburgh Medisch Centrum

Hardenberg, Overijssel, Netherlands

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Groene Hart Ziekenhuis

Gouda, South Holland, Netherlands

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Reinier de Graaf Ziekenhuis, locatie Delft

Delft, Zuid-Holla, Netherlands

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Antonius Ziekenhuis, locatie D&A Research and Genetics

Sneek, , Netherlands

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Sal Med Srl

Piteşti, Argeş, Romania

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C.M.D.T.A. Neomed

Brasov, Brașov County, Romania

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Hightech Medical Services SRL-Centrul pentru Studiul Metabolismului

Bucharest, București, Romania

Site Status

Centrul Medical Endocrinologie si Diabet Dr. Paveliu

Bucharest, București, Romania

Site Status

Private Practice - Dr. Mercea Corina Delia

Baia Mare, Maramureş, Romania

Site Status

Cardiomed

Târgu Mureş, Mureș County, Romania

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Private Practice - Dr. Cristian Podoleanu

Târgu Mureş, Mureș County, Romania

Site Status

Centrul Medical Medicalis

Timișoara, Timiș County, Romania

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Cardiomed Iași

Iași, , Romania

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Hospital Universitario Reina Sofia

Córdoba, Andalusia, Spain

Site Status

Hospital Germans Trias i Pujol

Badalona, Barcelona [Barcelona], Spain

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Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Catalunya [Cataluña], Spain

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Hospital Unviersitario Virgen Nieves

Granada, , Spain

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Hospital Universitario Virgen Del Rocio

Seville, , Spain

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Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status

Countries

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United States Argentina China Denmark Germany Japan Mexico Netherlands Romania Spain

References

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Nissen SE, Ni W, Shen X, Wang Q, Navar AM, Nicholls SJ, Wolski K, Michael L, Haupt A, Krege JH; ALPACA Trial Investigators. Lepodisiran - A Long-Duration Small Interfering RNA Targeting Lipoprotein(a). N Engl J Med. 2025 May 1;392(17):1673-1683. doi: 10.1056/NEJMoa2415818. Epub 2025 Mar 30.

Reference Type DERIVED
PMID: 40162643 (View on PubMed)

Makhmudova U, Steinhagen-Thiessen E, Volpe M, Landmesser U. Advances in nucleic acid-targeted therapies for cardiovascular disease prevention. Cardiovasc Res. 2024 Sep 2;120(10):1107-1125. doi: 10.1093/cvr/cvae136.

Reference Type DERIVED
PMID: 38970537 (View on PubMed)

Karp A, Jacobs M, Barris B, Labkowsky A, Frishman WH. Lipoprotein(a): A Review of Risk Factors, Measurements, and Novel Treatment Modalities. Cardiol Rev. 2025 Jul-Aug 01;33(4):352-358. doi: 10.1097/CRD.0000000000000667. Epub 2024 Feb 28.

Reference Type DERIVED
PMID: 38415744 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://trials.lilly.com/en-US/trial/363038

A Study of LY3819469 in Participants With Elevated Lipoprotein(a) \[Lp(a)\]

Other Identifiers

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J3L-MC-EZEB

Identifier Type: OTHER

Identifier Source: secondary_id

2022-501426-38-00

Identifier Type: CTIS

Identifier Source: secondary_id

18547

Identifier Type: -

Identifier Source: org_study_id

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