Assessment of the Safety and Efficacy of 0.1% RGN-259 Ophthalmic Solution for the Treatment of NK: SEER-2

NCT ID: NCT05555589

Last Updated: 2025-12-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

70 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-04-11

Study Completion Date

2026-05-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The objective of this study is to compare the safety and efficacy of RGN-259 to placebo for the treatment of Neurotrophic Keratopathy (NK)

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Neurotrophic keratopathy (NK) is a degenerative corneal disease that occurs as a result of partial or total impairment of trigeminal innervation. The resulting loss of corneal sensitivity (anesthesia) leads to a reduction in lacrimation and a decline in status, metabolism, and mitosis of corneal epithelial cells.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Neurotrophic Keratopathy

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Neurotrophic Keratitis NK

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

0.1% RGN-259 Opthalmic Solution

It is a preservative-free, sterile eye drop solution containing Tβ4 for direct instillation into study eye(s), five times per day for 28 days

Group Type EXPERIMENTAL

RGN-259

Intervention Type DRUG

A preservative-free, sterile eye drop solution containing Tβ4 for direct instillation into study eye(s), five times per day for 28 days

Placebo Ophthalmic Solution (Vehicle for RGN-259 Ophthalmic Solution)

It is composed of the same excipients as RGN-259 but does not contain Tβ4

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

It is composed of the same excipients as RGN-259 but does not contain Tβ4. Direct instillation into study eye(s), five times per day for 28 days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

RGN-259

A preservative-free, sterile eye drop solution containing Tβ4 for direct instillation into study eye(s), five times per day for 28 days

Intervention Type DRUG

Placebo

It is composed of the same excipients as RGN-259 but does not contain Tβ4. Direct instillation into study eye(s), five times per day for 28 days

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Tβ4 Thymosin Beta 4 Timbetasin Vehicle Control

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Be male or female of any race, at least 18 years of age;
2. Have provided written informed consent;
3. Be able and willing to follow instructions, including participation in all study assessments and visits;
4. At the time of Visit 1, have documentation or observation of a Persistent Epithelial Defect (PED) in one or both eyes, defined as a corneal epithelial defect that has not resolved after 1 week of conventional treatment using non-preserved ocular lubricants, non-preserved topical ophthalmic antibiotics, oral doxycycline, patching, amniotic membrane, serum tears, and/or therapeutic contact lenses;
5. Have stage 2 or 3 neurotrophic keratopathy (Mackie Classification) in at least one eye of which the longest dimension (length or width) of the defect measures a minimum length of 1 mm (study eye) and which is confirmed by the Investigator not to be simply superficial punctate keratitis, at Visit 1;
6. Have evidence of decreased corneal sensitivity ≤40 mm using the Cochet-Bonnet aesthesiometer at Visit 1;
7. Have BCVA score ≤75 letter counts in the study eye based on the ETDRS protocol;
8. Have at least one eye (the same eye) satisfy all criteria for d, e, f, g above;
9. Female subjects of child-bearing potential must be non-lactating and using and agree to continue using an acceptable method of contraception for at least 4 weeks prior to the first dose of study product and until 12 weeks after last dose, and have a negative urine pregnancy test during screening;
10. Male subjects must agree to use an adequate method of contraception.

Exclusion Criteria

1. Have any condition that, in the opinion of the Investigator, would interfere with the subject's ability to complete the study, would interfere with the interpretation of safety or efficacy, or would present an undue risk to the subject.
2. Have any clinically significant slit-lamp findings in the study eye that in the opinion of the Investigator may interfere with the study parameters;
3. Clinically significant active blepharitis, meibomian gland dysfunction (MGD), or lid margin inflammation, or active ocular allergy in study eye that requires treatment that in the opinion of the investigator may interfere with the study parameters;
4. Have a Unanesthetized Schirmer's test score of ≤3 mm at Visit 1;
5. Have a lid function abnormality (ex. Lagophthalmos) which, in the opinion of the Investigator, is the primary cause of the persistent epithelial defect;
6. Have an ongoing ocular infection (bacterial, viral or fungal) or active inflammation (e.g., follicular conjunctivitis) in the study eye.
7. History of any ocular surgery (including laser or refractive surgical procedures) within the three months before study enrollment.
8. Prior surgical procedure(s) for the treatment of NK (e.g., tarsorrhaphy, conjunctival flap, etc.) within the three months before study enrollment with the exception of amniotic membrane transplantation.
9. Have any planned ocular surgical procedures or are likely to require ocular surgery for the study eye during the study;
10. Have received Botox® injection to induce blepharoptosis in the study eye within 90 days prior to Visit 1;
11. Have used contact lenses (for therapeutic or refractive correction) in the study eye within 14 days prior to Visit 1, or anticipate use of contact lenses during the study period.
12. Have used OxervateTM in the study eye within the past 2 months;
13. Anticipate use of serum tears in the study eye during the study period.
14. Have a presence or history of any ocular or systemic disorder or condition that might hinder the efficacy of the study treatment or its evaluation, could possibly interfere with the interpretation of study results, or could be judged by the Investigator to be incompatible with the study visit schedule or conduct;
15. Have used drugs which affect lacrimation or function of the trigeminal nerve within 30 days of Visit 1 or anticipate use of these systemic medication throughout the course of the study;
16. Have any autoimmune or chronic inflammatory disease that might have hindered the efficacy of the study treatment or its evaluation;
17. Be on topical (Ocular/Nasal) immunosuppressive therapy within 30 days prior to screening or is likely to require this during the course of the study;
18. Have a known allergy and/or sensitivity to the study product or its components;
19. History of drug, medication or alcohol abuse or addiction;
20. Have participated in an investigational drug study within 30 days prior to screening;
21. Have fever, inflammation, or systemic signs of illness suggestive of systemic or invasive infection, including COVID-19 or a positive test for COVID-19, within 2 weeks prior to first dose of study drug.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

ReGenTree, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Harvard Eye Associates

Laguna Hills, California, United States

Site Status RECRUITING

Loma Linda University Eye Institute

Loma Linda, California, United States

Site Status RECRUITING

Retina Consultants of Southern Colorado

Colorado Springs, Colorado, United States

Site Status ACTIVE_NOT_RECRUITING

Advance Vision Research Institute

Longmont, Colorado, United States

Site Status RECRUITING

Connecticut Eye Consultants, P.C. Danbury Eye Physicians & Surgeons

Danbury, Connecticut, United States

Site Status RECRUITING

Nature Coast Clinical Research

Crystal River, Florida, United States

Site Status RECRUITING

University of Miami - Bascom Palmer Eye Institute, Miami

Miami, Florida, United States

Site Status RECRUITING

University of South Florida, Ophthalmolgoy

Tampa, Florida, United States

Site Status RECRUITING

Thomas Eye Group, P.C.

Sandy Springs, Georgia, United States

Site Status RECRUITING

Northwestern

Chicago, Illinois, United States

Site Status RECRUITING

Midwest Cornea Associates, LLC.

Carmel, Indiana, United States

Site Status RECRUITING

Huffman & Huffman, PSC

Lexington, Kentucky, United States

Site Status ACTIVE_NOT_RECRUITING

Midwest Vision Research Foundation

Chesterfield, Missouri, United States

Site Status RECRUITING

Washington University Eye Center

St Louis, Missouri, United States

Site Status RECRUITING

Metropolitan Eye Research and Surgery Institute

Palisades Park, New Jersey, United States

Site Status RECRUITING

Montefiore Medical Center

The Bronx, New York, United States

Site Status RECRUITING

Duke Eye Center

Durham, North Carolina, United States

Site Status RECRUITING

Oculus Research

Raleigh, North Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

CORE, Inc. / Vita Eye Clinic

Shelby, North Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

Cleveland Clinic, Cole Eye Institute

Cleveland, Ohio, United States

Site Status RECRUITING

Pacific ClearVision Institute

Eugene, Oregon, United States

Site Status ACTIVE_NOT_RECRUITING

Cataract & Laser Institute of Southern Oregon

Medford, Oregon, United States

Site Status RECRUITING

OHSU Casey Eye Institute

Portland, Oregon, United States

Site Status RECRUITING

UPMC Eye Center

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

MCOA Eye Care

San Antonio, Texas, United States

Site Status RECRUITING

Berkeley Eye Center

Sugar Land, Texas, United States

Site Status RECRUITING

Virginia Eye Consultants

Norfolk, Virginia, United States

Site Status RECRUITING

University of Washington, Department of Ophthalmology

Seatle, Washington, United States

Site Status RECRUITING

Università di Brescia

Brescia, Brescia, Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria Careggi

Florence, Firenze, Italy

Site Status RECRUITING

Gabinet Okulistyczny Prof Edward Wylegala

Katowice, Silesian Voivodeship, Poland

Site Status RECRUITING

IMO Barcelona, Grupo Miranza

Barcelona, Barcelona, Spain

Site Status RECRUITING

Hospital La Arruzafa

Córdoba, Córdoba, Spain

Site Status RECRUITING

Instituto Oftalmológico Fernández-Vega

Oviedo, Principality of Asturias, Spain

Site Status RECRUITING

Aiken Prevención & Cirugía Ocular

Valencia, Valencia, Spain

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Italy Poland Spain

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

ReGenTree, LLC

Role: CONTACT

Phone: 609-734-4328

Email: [email protected]

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

RGN-NK-302

Identifier Type: -

Identifier Source: org_study_id