A Trial Using ARV-471 or Anastrozole in Post-Menopausal Women With Breast Cancer Prior to Surgery

NCT ID: NCT05549505

Last Updated: 2025-08-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

152 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-02-15

Study Completion Date

2024-07-25

Brief Summary

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This trial is a Phase 2 neoadjuvant study evaluating ARV-471 or anastrozole in post-menopausal women with estrogen receptor positive/ human epidermal growth factor receptor 2 (ER+/HER2)- localized breast cancer.

Detailed Description

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This is a Phase 2, open-label, randomized, non-comparative proof of concept study of ARV-471 or anastrozole in participants with ER+/HER2- breast cancer amenable to definitive surgical resection. The main goal of this study is to evaluate the biological activity of ARV-471 and anastrozole, respectively.

Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A: ARV-471 (Experimental)

Participants received 200 mg ARV-471 (2\*100 mg tablets) once daily for approximately 5.5 months prior to undergoing surgical resection (no later than Cycle 6 Day 18 \[C6D18\] + 14 days).

Group Type EXPERIMENTAL

ARV-471

Intervention Type DRUG

100 mg tablet

Surgical resection of breast tumor

Intervention Type PROCEDURE

Surgical resection approximately 5.5 months after starting treatment (C6D18 ± 14 days)

Arm B: Anastrozole

Participants received 1 mg Anastrozole tablet orally once daily for approximately 5.5 months prior to undergoing surgical resection (no later than C6D18 + 14 days).

Group Type ACTIVE_COMPARATOR

Anastrozole

Intervention Type DRUG

1 mg tablet

Surgical resection of breast tumor

Intervention Type PROCEDURE

Surgical resection approximately 5.5 months after starting treatment (C6D18 ± 14 days)

Interventions

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ARV-471

100 mg tablet

Intervention Type DRUG

Anastrozole

1 mg tablet

Intervention Type DRUG

Surgical resection of breast tumor

Surgical resection approximately 5.5 months after starting treatment (C6D18 ± 14 days)

Intervention Type PROCEDURE

Other Intervention Names

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Vepdegestrant PF-07850327 Arimidex

Eligibility Criteria

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Inclusion Criteria

* Post-menopausal females ≥ 18 years.
* Histologically or cytologically confirmed ER+ and HER2- breast cancer (per local assessment). ER and HER2 status must be documented:

* ER+ disease, with ER staining of ≥ 10% of tumor cell nuclei by immunohistochemistry (IHC) per American Society of Clinical Oncology/College of American Pathologists (ASCO/CAP) guidelines.
* HER2- disease by either IHC or in situ hybridization per ASCO/CAP guidelines.
* Ki-67 score ≥ 5%, analyzed locally.
* Clinical T1c-T4c, N0-N2, M0 breast cancer amenable to definitive surgical resection, without bilateral breast ductal carcinoma in situ or invasive breast cancer.
* The primary tumor must be at least 1.5 cm by imaging.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
* Willingness to undergo a screening biopsy, an on-treatment biopsy and surgical resection.

Exclusion Criteria

* Any other active malignancy within 3 years prior to enrollment, except for adequately treated basal cell or squamous cell skin cancer, or cervical carcinoma in situ.
* Any of the following in the previous 6 months: Myocardial infarction; Severe unstable angina; Coronary/peripheral artery bypass graft; Symptomatic congestive heart failure (New York Heart Association class III or IV); Cerebrovascular accident; Transient ischemic attack; Symptomatic pulmonary embolism or other clinically significant episode of thromboembolism.
* Any of the following in the previous 6 months: Congenital long QT syndrome; Torsade de Pointes; Sustained ventricular tachyarrhythmia and ventricular fibrillation; Left anterior hemiblock (bifascicular block); Ongoing cardiac dysrhythmias of NCI CTCAE ≥ Grade 2; Atrial fibrillation of any grade (≥ Grade 2 in the case of asymptomatic lone atrial fibrillation).
* corrected QT (Fridericia method) (QTcF) \> 470 msec.
* Active, uncontrolled bacterial, fungal or viral infection, including (but not limited to) hepatitis B virus (HBV), hepatitis C virus (HCV), and known human immunodeficiency virus (HIV) or acquired immunodeficiency syndrome (AIDS)-related illness.
* Active inflammatory gastrointestinal disease, chronic diarrhea, known uncontrolled diverticular disease, or previous gastric resection or lap band surgery.
* Cirrhosis meeting criteria for Child Pugh B and C.
* Prior treatment for breast cancer including systemic therapy (eg, chemotherapy, hormonal therapy), radiation, surgery, or any investigational agents.
* Any live vaccines within 14 days of planned start of first dose of study drug.
* Major surgery (as defined by the Investigator) within four weeks of first dose of study drug.
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role collaborator

Arvinas Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clinical Trial Site

Springdale, Arkansas, United States

Site Status

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Los Angeles, California, United States

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Torrance, California, United States

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Van Nuys, California, United States

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Fort Lauderdale, Florida, United States

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Fort Myers, Florida, United States

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Orlando, Florida, United States

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West Palm Beach, Florida, United States

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Iowa City, Iowa, United States

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Springfield, Massachusetts, United States

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St Louis, Missouri, United States

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Nashville, Tennessee, United States

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Tacoma, Washington, United States

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Batumi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Augsburg, , Germany

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Berlin, , Germany

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Bonn, , Germany

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Bottrop, , Germany

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Chemnitz, , Germany

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Dresden, , Germany

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Erlangen, , Germany

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Essen, , Germany

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Essen, , Germany

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Esslingen am Neckar, , Germany

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Mannheim, , Germany

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Paderborn, , Germany

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A Coruña, Galicia, Spain

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San Cristóbal de La Laguna, Santa Cruz De Tenerife, Spain

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Alicante, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Castelló, , Spain

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Córdoba, , Spain

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Granada, , Spain

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Granada, , Spain

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Lleida, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Manresa, , Spain

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Seville, , Spain

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Seville, , Spain

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Valencia, , Spain

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Clinical Trial Site

Valencia, , Spain

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Clinical Trial Site

Zaragoza, , Spain

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Countries

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United States Georgia Germany Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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C4891025

Identifier Type: OTHER

Identifier Source: secondary_id

ARV-471-BC-201

Identifier Type: -

Identifier Source: org_study_id

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