A Single and Multiple Ascending Doses Study to Evaluate the Safety and Pharmacokinetics of RBD5044

NCT ID: NCT05539651

Last Updated: 2024-12-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

72 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-11-10

Study Completion Date

2024-10-30

Brief Summary

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This is a randomized, double-blind, placebo-controlled phase I study to evaluate the safety, tolerability, PK profiles and PD effect of single and multiple ascending doses of subcutaneously administered RBD5044 in healthy subjects. The study will be performed in 2 phases: single ascending dose (SAD) phase and multiple ascending doses (MAD) phase in healthy subjects. There are 6 cohorts in SAD phases, the dose levels are 5mg, 20mg, 60mg, 90mg, 120mg and 150mg. There are 3 cohorts in MAD phases, the dose levels are 60mg, 90mg and 120mg.The decision to escalate to subsequent dose levels will be made by the SRC based on the review of all available safety information, including AEs, ECGs, vital signs, and clinical laboratory test results in each cohort.

Detailed Description

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Conditions

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Health Volunteer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
double-blinded

Study Groups

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RBD5044 SAD experimental group

Subjects in SAD experimental groups will receive a single subcutaneous injection of RBD5044 on Day 1.

Group Type EXPERIMENTAL

RBD5044

Intervention Type DRUG

Subcutaneously Administered RBD5044 in Healthy Subjects

RBD5044 MAD experimental group

Subjects in MAD experimental groups will receive one subcutaneous injection of RBD5044 on Day 1 and another subcutaneous injection of RBD5044 on Day 29.

Group Type EXPERIMENTAL

RBD5044

Intervention Type DRUG

Subcutaneously Administered RBD5044 in Healthy Subjects

Placebo SAD group

Subjects in SAD placebo groups will receive a single subcutaneous injection of placebo on Day 1.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Subcutaneously Administered Placebo in Healthy Subjects

Placebo MAD group

Subjects in MAD placebo groups will receive one subcutaneous injection of placebo on Day 1 and another subcutaneous injection of placebo on Day 29.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Subcutaneously Administered Placebo in Healthy Subjects

Interventions

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RBD5044

Subcutaneously Administered RBD5044 in Healthy Subjects

Intervention Type DRUG

Placebo

Subcutaneously Administered Placebo in Healthy Subjects

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

A subject will be eligible for inclusion in this study only if all of the following criteria are met:

1. Willing to comply with protocol required visit schedule and visit requirements and provide written informed consent.
2. Male and female subjects, aged 18 to 65 years (inclusive).
3. Body mass index between 18 and 32 kg/m2, inclusive.
4. Fasting TG ≥ 0.9 mmol/L (80 mg/dL) and ≤ 3.4 mmol/L (300 mg/dL) at screening.
5. Fasting LDL-C \< 4.9 mmol/L (\<190 mg/dL) at screening.
6. Healthy as determined by pre-study medical history, physical examination, clinical laboratory assessments, and 12-lead electrocardiogram (ECG).
7. Satisfy one of the following:

* Females: must be non-pregnant and non-lactating; surgically sterile, post-menopausal, abstinent, or if engaged in sexual relations of child-bearing potential, the subject is using an acceptable contraceptive method (refer to Section 4.6.3) for four weeks before, during, and for at least 6 months after the last dose of study drug administration.
* Males: must be surgically sterile, abstinent, or if engaged in sexual relations of child-bearing potential, the subject is utilizing an acceptable contraceptive method (refer to Section 4.6.3)) during and for at least 6 months after the last dose of study drug administration.
8. Non-smokers and non-nicotine users for at least 90 days before screening

Exclusion Criteria

1. Any uncontrolled or serious disease, or any medical or surgical condition, may interfere with participation in the clinical study and/or put the subject at significant risk (according to the investigator's judgment) if he/she participates in the clinical study.
2. History or presence of cardiovascular disease (including peripheral artery and cerebrovascular disease).
3. Systolic blood pressure (SBP) \> 140 mmHg and/or diastolic blood pressure (DBP) \> 90 mmHg after 10 minutes of supine rest, unless determined by the investigator to be not clinically relevant.
4. Diagnosis of diabetes mellitus.
5. Received any medication or nutraceutical to alter serum lipids within 30 days before screening.
6. Active serious mental illness or psychiatric disorder, including but not limited to schizophrenia, bipolar disorder, or severe depression, which require current pharmacological intervention.
7. Alanine aminotransferase (ALT) and/or total bilirubin are above the upper limit of normal reference range (ULN); no investigator discretion and repeat assessments are allowed.
8. Aspartate aminotransferase (AST), alkaline phosphatase (ALP), or gamma-glutamyl transferase (GGT) \> 2 × ULN (no investigator discretion); or, if AST, ALP, or GGT \> ULN, but ≤ 2 × ULN and considered clinically relevant by the investigator.
9. Used prescription drugs within 14 days or 7 half-lives (whichever is longer) before the first dose of study drug.
10. Used over-the-counter medication, excluding routine vitamins, within 7 days before the first dose of the study drug, unless determined by the investigator to be not clinically relevant, and unlikely to impact blood lipids level.
11. Received an investigational product within 30 days or 7 half-lives (whichever is longer) before the first dose of the study drug or are in the follow-up of another clinical study. If subjects used advanced therapy (ASO/siRNA/gene therapy/cell therapy), it should be judged by the investigator.
12. Hepatitis B virus, hepatitis C virus, human immunodeficiency virus (HIV), syphilis infection, or positive hepatitis B surface antigen (HBsAg), hepatitis B core antibody (HBcAb), hepatitis C virus antibody (HCVAb), HIV antibody (HIVAb), treponema pallidum antibody (TP-Ab) at screening.
13. Clinically significant illness within 7 days before the first dose of the study drug.
14. Consume more than 14 (female) or 21 (male) units of alcohol per week (unit: 1 glass of wine \[125 mL\] = 1 measure of spirits = ½ pint of beer) within the 12 months before screening or positive screen for alcohol abuse.
15. History or clinical evidence of drug abuse within the 12 months before screening or positive screen for drug abuse. Drug abuse is defined as compulsive, repetitive, and/or chronic use of drugs or other substances with or without problems related to their use and/or where stopping or a dose reduction will lead to withdrawal symptoms.
16. Donated more than 500 mL of blood within 90 days before the first dose of the study drug.
17. History of multiple drug allergies or history of allergic reaction to an oligonucleotide or N-acetylgalactosamine (GalNAc).
18. History of intolerance to subcutaneous (SC) injection or relevant abdominal scarring (surgical, burns, etc.).
19. Any conditions which would make the subject unsuitable for enrollment or could interfere with the subject's participation in or completion of the study in the opinion of the investigator.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Suzhou Ribo Life Science Co. Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Q-Pharm Pty Limited

Brisbane, , Australia

Site Status

Countries

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Australia

Other Identifiers

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RBAP1101

Identifier Type: -

Identifier Source: org_study_id